NCT05540327

Brief Summary

The purpose of the study is to evaluate the long term safety and efficacy of orally administered M5049 in participants with subacute cutaneous lupus erythematosus (SCLE), discoid lupus erythematosus (DLE) and/or systemic lupus erythematosus (SLE) who have completed the 24 week treatment period of Willow study (MS200569\_0003 \[NCT05162586\]).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
379

participants targeted

Target at P75+ for phase_2

Timeline
28mo left

Started Sep 2022

Longer than P75 for phase_2

Geographic Reach
22 countries

122 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress62%
Sep 2022Aug 2028

First Submitted

Initial submission to the registry

September 12, 2022

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 14, 2022

Completed
2 days until next milestone

Study Start

First participant enrolled

September 16, 2022

Completed
5.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 12, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 12, 2028

Last Updated

April 16, 2026

Status Verified

April 1, 2026

Enrollment Period

5.9 years

First QC Date

September 12, 2022

Last Update Submit

April 15, 2026

Conditions

Keywords

Toll-like Receptor 7Toll-like Receptor 8WILLOWAdultsSLECLELupusDiscoid lupus erythematosusSubacute cutaneous lupus erythematosusM5049EnpatoranLTE

Outcome Measures

Primary Outcomes (2)

  • Part 1: Safety Profile as Assessed by Incidence of Treatment-Emergent Adverse Events (TEAEs), Serious Adverse Events (SAEs), Adverse Event of Special Interest (AESIs)

    Baseline up to Week 50 (Long Term Extension Part 1)

  • Part 2: Safety Profile as Assessed by Incidence of Treatment-Emergent Adverse Events (TEAEs), Serious Adverse Events (SAEs), Adverse Event of Special Interest (AESIs)

    Baseline up to Week 194 (LTE Part 1 and LTE Prolongation Part 2))

Secondary Outcomes (1)

  • Part 1 and Part 2: Number of Participants with Abnormalities in Laboratory Parameters and QT Interval Corrected

    Baseline up to Week 50 and LTE Prolongation up to Week 194 (Part 2)

Study Arms (3)

M5049 low dose + Placebo

EXPERIMENTAL

Participants with CLE (active SCLE and/or DLE) or SLE who received low dose of M5049 in WILLOW study will continue to receive M5049 low dose and matching placebo.

Drug: M5049 low doseDrug: Placebo

M5049 medium dose+ Placebo

EXPERIMENTAL

Participants with CLE (active SCLE and/or DLE) or SLE who received medium dose of M5049 in WILLOW study will continue to receive M5049 medium dose and matching placebo.

Drug: M5049 medium doseDrug: Placebo

M5049 high dose + Placebo

EXPERIMENTAL

Participants with CLE (active SCLE and/or DLE) or SLE who received M5049 matched placebo or high dose of M5049 in WILLOW study will receive M5049 high dose .

Drug: M5049 high doseDrug: Placebo

Interventions

Participants will receive film-coated tablets of M5049 at a low dose orally, twice a day (BID) for up to 194 weeks.

Also known as: Enpatoran
M5049 low dose + Placebo

Participants will receive film-coated tablets of M5049 at a medium dose orally, BID for up to 194 weeks.

Also known as: Enpatoran
M5049 medium dose+ Placebo

Participants will receive film-coated tablets of M5049 at a high dose orally, BID for up to 194 weeks.

Also known as: Enpatoran
M5049 high dose + Placebo

Participants will receive M5049 matching placebo orally, BID for up to 194 weeks.

M5049 high dose + PlaceboM5049 low dose + PlaceboM5049 medium dose+ Placebo

Eligibility Criteria

Age18 Years - 76 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Are SCLE, DLE and/or SLE that have completed the 24 week Treatment of the Willow Study
  • Have a Body Mass Index (BMI) within the less than or equal to (\<=) 40 kilograms per meter square (inclusive) at Screening
  • Participants who had successfully completed Week 48 of the Part 1 will have the opportunity to participate in the LTE Part 2. In exceptional cases and after Sponsor review, participants who have completed the Week 48 visit of the Part 1 within the previous 4-weeks may be considered for Part 2 participation based on eligibility review. Previous 4-weeks will be calculated from the Week 48 visit of Part 1

You may not qualify if:

  • Participants who experienced serious event(s) related to the study intervention during the WILLOW study
  • Other severe acute or chronic medical or psychiatric condition or laboratory abnormality that may increase the risk associated with Long Term Extension (LTE) study participation
  • Ongoing or active clinically significant viral (including Severe acute respiratory syndrome coronavirus 2 \[(SARS-CoV-2)\], bacterial or fungal infection, or any major episode of infection requiring hospitalization
  • Received LTE prohibited medication during the WILLOW study or after the WILLOW study Week 24
  • Participation in any other investigational drug study after the WILLOW study Week 24

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (122)

The Lundquist Institute at Harbor-UCLA Medical Center

Torrance, California, 90502, United States

Location

Bay Area Arthritis and Osteoporosis

Brandon, Florida, 33511, United States

Location

Advance Medical Research Center

Miami, Florida, 33135, United States

Location

Dawes Fretzin Dermatology Group, LLC

Indianapolis, Indiana, 46250, United States

Location

AA MRC LLC Ahmed Arif Medical Research Center

Grand Blanc, Michigan, 48439, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

Ohio State University - CTMO Parent

Columbus, Ohio, 43210, United States

Location

Ramesh C Gupta, MD

Memphis, Tennessee, 38119, United States

Location

Centro de Investigaciones Medicas Mar del Plata - CIM

Buenos Aires, Argentina

Location

CINME - Centro De Investigaciones Metabolicas

Buenos Aires, Argentina

Location

Buenos Aires Skin

Ciudad Autonoma Buenos Aires, Argentina

Location

Hospital Militar Central Dr. Cosme Argerich

Ciudad Autonoma Buenos Aires, Argentina

Location

Centro de Investigaciones Medicas Mar del Plata - CIM

Mar del Plata, Argentina

Location

Instituto de Reumatologia

Mendoza, Argentina

Location

Instituto Medico de alta Complejidad San Isidro S.A (IMAC)

San Fernando, Argentina

Location

CER San Juan Centro Polivalente de Asistencia e Inv. Clinica

San Juan, Argentina

Location

Centro Dermatologico Schejtman

San Miguel, Argentina

Location

PSORIAHUE-Medicina Interdisciplinar

San Miguel, Argentina

Location

Centro de Investigaciones Medicas Tucuman

San Miguel de Tucumán, Argentina

Location

Investigaciones Clinicas Tucuman

San Miguel de Tucumán, Argentina

Location

Monash Medical Centre Clayton

Clayton, Australia

Location

Veracity Clinical Research

Woolloongabba, Australia

Location

Santa Casa de Misericórdia de Belo Horizonte

Belo Horizonte, Brazil

Location

Oncovida - Centro de Onco-Hematologia de Mato Grosso

Cuiabá, Brazil

Location

Clínica SER da Bahia

Graça, Brazil

Location

CMiP - Centro Mineiro de Pesquisa

Juiz de Fora, Brazil

Location

Hospital Moinhos de Vento

Moinhos de Vento, Brazil

Location

Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto - CIP - Centro Integrado de Pesquisa

São José, Brazil

Location

CEPIC - Centro Paulista de Investigação Clínica e Serviços Médicos

São Paulo, Brazil

Location

DCC 'Sveti Georgi' EOOD - Cardiology Office

Haskovo, Bulgaria

Location

MC Artmed OOD

Plovdiv, Bulgaria

Location

DCC 1 Sevlievo EOOD

Sevlievo, Bulgaria

Location

DCC Focus 5 - MEOH OOD

Sofia, Bulgaria

Location

Military Medical Academy - MHAT - Sofia

Sofia, Bulgaria

Location

UMHAT "Sv. Ivan Rilski", EAD - Clinic of Rheumatology

Sofia, Bulgaria

Location

UMHAT "Sv. Ivan Rilski", EAD - Clinica of Rheumatology

Sofia, Bulgaria

Location

Clinica Alemana de Osorno - Corporacion de Beneficencia Osorno

Los Lagos, Chile

Location

BioMedica Research Group - Psicomedica Clinical and Research Group

Santiago, Chile

Location

CeCim Biocinetic

Santiago, Chile

Location

Centro Medico Prosalud

Santiago, Chile

Location

CIEC- Centro Internacional de Estudios Clinicos - Valenzuela Y Compania Ltda

Santiago, Chile

Location

Dermacross

Santiago, Chile

Location

The First Affiliated Hospital of Baotou Medical College

Baotou, China

Location

Peking Union Medical College Hospital - Beijing Union Medical College Hospital

Beijing, China

Location

The First Hospital of Jilin University

Changchun, China

Location

Guangdong Provincial People's Hospital

Guangzhou, China

Location

Hainan General Hospital

Haikou, China

Location

The First Affiliated Hospital of Henan University of Science and Technology

Luoyang, China

Location

The Second Affiliated Hospital of Nanchang University

Nanchang, China

Location

The Affiliated Drum Tower Hospital of Nanjing University

Nanjing, China

Location

Huashan Hospital, Fudan University - Neurology

Shanghai, China

Location

Renji Hospital Shanghai Jiaotong University School of Medicine - West Branch

Shanghai, China

Location

Shanghai Skin Disease Hospital

Shanghai, China

Location

West China Hospital, Sichuan University

Sichuan, China

Location

The First Affiliated Hospital of Soochow University

Suzhou, China

Location

Tianjin Medical University General Hospital

Tianjin, China

Location

The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, China

Location

Centro de Investigacion Medico Asistencial S.A.S

Barranquilla, Colombia

Location

Centro de Investigacion en Reumatologia y Especialidades Medicas SAS. CIREEM

Bogotá, Colombia

Location

Servimed S.A.S.

Bucaramanga, Colombia

Location

Centro Integral de Reumatologia del Caribe SAS CIRCARIBE SAS

Medellín, Colombia

Location

Healthy Medical Center

Zipaquirá, Colombia

Location

General Hospital of Athens Laiko

Athens, Greece

Location

General Hospital Papageorgiou

Thessaloniki, Greece

Location

Chaim Sheba Medical Center - pt

Ramat Gan, Israel

Location

NHO Asahikawa Medical Center - Dept of Gastroenterology

Asahikawa-shi, Japan

Location

NHO Chibahigashi National Hospital - Dept of Allergy/Rheumatology

Chiba, Japan

Location

St. Luke's International Hospital - Dept of Immunology/Allergy

Chūōku, Japan

Location

Hiroshima University Hospital

Hiroshima, Japan

Location

Eiraku Clinic - Dept of Rheumatology

Kagoshima, Japan

Location

Saitama Medical Center - Dept of Rheumatology/Immunology

Kawagoe-shi, Japan

Location

Kagawa University Hospital - Dept of Immunology/ Rheumatology

Kita-gun, Japan

Location

Hokkaido University Hospital - Dept of Internal Medicine 2(Rheumatology/Immunolog

Sapporo, Japan

Location

Tohoku University Hospital - Dept of Hematology/Immunology

Sendai, Japan

Location

CAP Research Ltd

Quatre Bornes, Mauritius

Location

Consultorio Privado Dr. Miguel Cortes Hernandez

Cuernavaca, Mexico

Location

Centro de Estudios de Investigacion Basica y Clinica SC

Guadalajara, Mexico

Location

Diseno y Planeacion en Investigacion Medica S.C.

Guadalajara, Mexico

Location

Diseño y Planeacion en Investigacion Medica S.C.

Guadalajara, Mexico

Location

Centro Medico del Angel

Mexicali, Mexico

Location

CAIMED Investigacion en salud S.A de C.V.

Mexico City, Mexico

Location

Clinstile, S.A. de C.V.

Mexico City, Mexico

Location

Medical Care & Research SA de CV

Mérida, Mexico

Location

Centro de Investigacion Clínica GRAMEL S.C

México, Mexico

Location

Clinica para el Diagnostico y Tratamiento de las Enfermedades Reumaticas

México, Mexico

Location

Consultorio de Reumatologia - Hospital Angeles Lindavista Cons. 445B

México, Mexico

Location

Grupo Medico Camino S.C.

México, Mexico

Location

Centro Regiomontano de Estudios Clínicos Roma S.C.

Monterrey, Mexico

Location

CIMAB S.A. de C.V. - Centro de Investigacion Medica Alberto Bazzoni

Torreón, Mexico

Location

ICS ARENSIA Exploratory Medicine SRL - Republican Clinical Hospital "Timofei Mosneaga"

Chisinau, Moldova

Location

Davao Doctors Hospital - Medicine

Davao City, Philippines

Location

Iloilo Doctors Hospital

Iloilo City, Philippines

Location

Mary Mediatrix Medical Center

Lipa City, Philippines

Location

Ospital Ng Makati

Makati City, Philippines

Location

Chinese General Hospital & Medical Center

Manila, Philippines

Location

Far Eastern University - Dr. Nicanor Reyes Medical Foundation - Department of Child Health

Quezon City, Philippines

Location

Nova Reuma Domysławska i Rusiłowicz, Spółka Partnerska Lekarza Reumatologa i Fizjoterapeuty

Bialystok, Poland

Location

Prywatna Praktyka Lekarska prof Pawel Hrycaj

Kościan, Poland

Location

Centrum Medyczne Plejady

Krakow, Poland

Location

Centrum Nowoczesnych Terapii Dobry Lekarz

Krakow, Poland

Location

Twoja Przychodnia PCM

Poznan, Poland

Location

Twoja Przychodnia-Szczecinskie Centrum Medyczne Sp. z o. o

Szczecin, Poland

Location

Clinical Best Solutions - Warszawa

Warsaw, Poland

Location

Centrul Medical Monza SRL - Arensia Exploratory Medicine

Bucharest, Romania

Location

S.C Delta Health Care S.R.L - Ponderas Academic Hospital

Bucharest, Romania

Location

Spitalul Clinic "Sf. Maria" - Clinica de Medicina Interna si Reumatologie

Bucharest, Romania

Location

Spitalul Clinic "Sf. Maria" - parent

Bucharest, Romania

Location

Institute of Rheumatology - Rheumatology

Belgrade, Serbia

Location

Institute of Rheumatology

Belgrade, Serbia

Location

University Clinical Center of Serbia - Clinic of Alergology and Imunology

Belgrade, Serbia

Location

Arthritis Clinical Research Trial Unit - Dr CE Spargo and Dr RB Bhorat

Cape Town, South Africa

Location

University of Pretoria Clinical Research Unit - Parent

Pretoria, South Africa

Location

Naidoo, A - Netcare Umhlanga Hospital

Umhlanga, South Africa

Location

Gachon University Gil Medical Center

Incheon, South Korea

Location

Seoul National University Hospital

Seoul, South Korea

Location

Ajou University Hospital

Suwon, South Korea

Location

Hospital General de Castellon - Servicio de Reumatologia

Castelló, Spain

Location

Hospital Regional Universitario de Malaga - Reumatology Dept

Málaga, Spain

Location

Hospital Universitario Marques de Valdecilla - Servicio de Reumatologia

Santander, Spain

Location

Hospital Universitario Rio Hortega - Servicio de Medicina Interna

Valladolid, Spain

Location

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, Taiwan

Location

Taipei Veterans General Hospital

Taipei, Taiwan

Location

Related Links

MeSH Terms

Conditions

Lupus Erythematosus, SystemicLupus Erythematosus, DiscoidLupus Erythematosus, Cutaneous

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System DiseasesSkin Diseases

Study Officials

  • Medical Responsible

    Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 12, 2022

First Posted

September 14, 2022

Study Start

September 16, 2022

Primary Completion (Estimated)

August 12, 2028

Study Completion (Estimated)

August 12, 2028

Last Updated

April 16, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

We are committed to enhancing public health through responsible sharing of clinical trial data. Following approval of a new product or a new indication for an approved product in both the US and European Union, the study sponsor and/or its affiliated companies will share study protocols, anonymized patient data and study level data, and redacted clinical study reports with qualified scientific and medical researchers, upon request, as necessary for conducting legitimate research. Further information on how to request data can be found on our website bit.ly/IPD21

Shared Documents
STUDY PROTOCOL, SAP, CSR, ANALYTIC CODE
Time Frame
Within six months after the approval of a new product or a new indication for an approved product in both the United States and the European Union
Access Criteria
Qualified scientific and medical researchers can request the data. Such requests must be submitted in writing to the company's portal and will be internally reviewed regarding criteria for researchers' qualification and legitimacy of the research proposal.
More information

Locations