NCT05347095

Brief Summary

The purpose of this study to evaluate the clinical efficacy of guselkumab in fistulizing, perianal Crohn's disease and to assess the overall safety of guselkumab.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
288

participants targeted

Target at P50-P75 for phase_3

Timeline
11mo left

Started Sep 2022

Longer than P75 for phase_3

Geographic Reach
23 countries

154 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress80%
Sep 2022Mar 2027

First Submitted

Initial submission to the registry

April 21, 2022

Completed
5 days until next milestone

First Posted

Study publicly available on registry

April 26, 2022

Completed
5 months until next milestone

Study Start

First participant enrolled

September 27, 2022

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 25, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 25, 2027

Last Updated

April 21, 2026

Status Verified

April 1, 2026

Enrollment Period

4.5 years

First QC Date

April 21, 2022

Last Update Submit

April 20, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants who Achieve Combined Fistula Remission at Week 24

    Percentage of participants who achieve combined fistula remission at Week 24 will be reported. Combined fistula remission is defined as 100 percentage (%) closure of all treated external openings without development of new fistulas or abscesses and without any drainage by the external openings \[occurring spontaneously or after gentle finger compression\] and absence of collections greater than (\>) 2 centimeters (cm) of the perianal fistulas in at least two of three dimensions, confirmed by a blinded central review of the magnetic resonance imaging \[MRI\] results.

    Week 24

Secondary Outcomes (38)

  • Percentage of Participants who Achieve Combined Fistula Remission at Week 48

    Week 48

  • Percentage of Participants who Achieve Clinically Assessed Fistula Remission

    Week 24

  • Percentage of Participants who Achieve Radiological Fistula Remission Based on Radiological Findings Assessed by MRI

    Week 24

  • Percentage of Participants who Achieve Clinically Assessed Fistula Response at Week 24

    Week 24

  • Percentage of Participants who Achieve Clinically Assessed Fistula Response at Week 12

    Week 12

  • +33 more secondary outcomes

Study Arms (3)

Group 1: Guselkumab

EXPERIMENTAL

Participants will receive guselkumab Dose 1 intravenous (IV) infusion followed by Dose 2 subcutaneously (SC). Participants will receive matching placebo to maintain the blind. Participants who are eligible and willing to continue guselkumab may enter the Long-Term Extension (LTE) period and continue to receive guselkumab.

Drug: GuselkumabDrug: Placebo

Group 2: Guselkumab

EXPERIMENTAL

Participants will receive guselkumab Dose 1 IV infusion followed by Dose 3 SC. Participants will receive matching placebo to maintain the blind. At Week 24, guselkumab Dose 3 SC non-responders will switch to receive guselkumab dose 2 SC. Participants who are eligible and willing to continue guselkumab may enter the LTE period and continue to receive guselkumab.

Drug: GuselkumabDrug: Placebo

Group 3: Placebo

EXPERIMENTAL

Participants will receive placebo IV infusion followed by placebo SC. At Week 24, placebo non-responders will continue to receive guselkumab Dose 4 followed by guselkumab Dose 2 SC. Participants will receive matching placebo to maintain the blind. Participants who are eligible and willing to continue guselkumab may enter the LTE period and continue to receive guselkumab.

Drug: GuselkumabDrug: Placebo

Interventions

Guselkumab will be administered subcutaneously/IV infusion.

Also known as: CNTO1959
Group 1: GuselkumabGroup 2: GuselkumabGroup 3: Placebo

Matching placebo will be administered subcutaneously/IV infusion.

Group 1: GuselkumabGroup 2: GuselkumabGroup 3: Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have a diagnosis of Crohn's disease with a minimum duration of at least 3 months
  • Has at least one active draining perianal fistula as a complication of Crohn's disease, confirmed by screening magnetic resonance imaging (MRI) results
  • Has previously demonstrated lack of initial response (that is primary non-responders), responded initially but then lost response with continued therapy (that is secondary non-responders), or were intolerant to a maximum of 2 classes of advanced drug therapies at a dose approved for the treatment of Crohn's disease (that is infliximab, adalimumab, certolizumab pegol, vedolizumab, or approved biosimilars for these agents) or JAK inhibitors licensed for Crohn's disease treatment (that is, upadacitinib)

You may not qualify if:

  • Has a very severe luminal disease activity
  • History of concurrent rectovaginal fistulas (other types of concurrent fistula should be confirmed with the sponsor), rectal and/or anal stenosis, stoma or functioning ostomy (include all current stoma types abscess or collections which are not properly drained) colonic mucosal dysplasia or pre-cancerous lesions that have not been removed, demyelinating disease, or systemic lupus erythematosus
  • Has complications of CD, such as symptomatic strictures or stenoses, short gut syndrome, or any other manifestation that might be anticipated to require surgery or preclude fistula evaluation
  • Any medical contraindications preventing study participation
  • Has a history of ongoing, chronic or recurrent enteral or systemic infectious disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (154)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Yale University

New Haven, Connecticut, 06510, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Gastroenterology Group Of Naples

Naples, Florida, 34102, United States

Location

AdventHealth Medical Group Blood & Marrow Transplant at Orlando

Orlando, Florida, 32804, United States

Location

Kansas University Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

Washington University School Of Medicine

St Louis, Missouri, 63110, United States

Location

Mount Sinai School of Medicine

New York, New York, 10029, United States

Location

Digestive Disease Specialists Inc

Oklahoma City, Oklahoma, 73112, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37212, United States

Location

Tyler Research Institute, LLC

Tyler, Texas, 75701, United States

Location

Swedish Medical Center

Seattle, Washington, 98122, United States

Location

Flinders Medical Centre

Adelaide, 5042, Australia

Location

St Vincent's Hospital - Melbourne

Fitzroy, 3065, Australia

Location

Liverpool Hospital

Liverpool, 2170, Australia

Location

Fiona Stanley Hospital

Murdoch, 6150, Australia

Location

Royal Prince Alfred Hospital

Newtown, 2042, Australia

Location

Royal Adelaide Hospital

North Terrace, 5000, Australia

Location

Royal Melbourne Hospital

Parkville, 3050, Australia

Location

Royal Perth Hospital

Perth, 6000, Australia

Location

Mater Hospital

South Brisbane, 4101, Australia

Location

Hopital Erasme

Brussels, 1070, Belgium

Location

Ziekenhuis Oost-Limburg

Genk, 3600, Belgium

Location

UZ Leuven

Leuven, 3000, Belgium

Location

CHU Sart Tilman

Liège, B-4000, Belgium

Location

University of Alberta- Ziedler Ledcor Centre

Edmonton, Alberta, T6G 2X8, Canada

Location

Nova Scotia Health Authority

Halifax, Nova Scotia, B3H2Y9, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 5A5, Canada

Location

Mount Sinai Hospital

Toronto, Ontario, M5G 1X5, Canada

Location

McGill University Health Centre

Montreal, Quebec, H3G 1A4, Canada

Location

Nemocnice Ceske Budejovice a s

České Budějovice, 37001, Czechia

Location

ISCARE a.s.

Prague, 190 00, Czechia

Location

Alexandria University Hospital 1

Alexandria, 21131, Egypt

Location

Alexandria University Hospital

Alexandria, 21131, Egypt

Location

National Hepatology and Tropical Medicine Research Institute

Cairo, 11451, Egypt

Location

Ain Shams University Hospital

Cairo, 11517, Egypt

Location

Cairo university

Giza, 12613, Egypt

Location

Clinique Ambroise Pare

Neuilly-sur-Seine, 92200, France

Location

CHU de Nice Hopital de l Archet

Nice, 06202, France

Location

Hopital Saint Joseph

Paris, 75014, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, 69495, France

Location

CHRU Hopital de Pontchaillou

Rennes, 35033, France

Location

CHRU Nancy Brabois

Vandœuvre-lès-Nancy, 54511, France

Location

Charite - Campus Mitte

Berlin, 10117, Germany

Location

JWG-University Hospital

Frankfurt, 60590, Germany

Location

Universitatsklinikum Schleswig Holstein Kiel

Kiel, 24105, Germany

Location

Universitaetsklinikum Mannheim

Mannheim, 68167, Germany

Location

Universitaetsklinikum Ulm

Ulm, 89081, Germany

Location

Evangelismos General Hospital of Athens

Athens, 10676, Greece

Location

Hippokration Hospital 1

Athens, 11528, Greece

Location

Sotiria General State Hospital of Chest Diseases

Athens, 156 69, Greece

Location

Alexandra General Hospital of Athens

Athens Attica, 115 28, Greece

Location

University Hospital of Heraklion

Heraklion, 71110, Greece

Location

University Hospital Of Larissa

Larissa, 41110, Greece

Location

Patras University Hospital

Pátrai, 26504, Greece

Location

Hippokration Hospital

Thessaloniki, 54642, Greece

Location

Magyar Honvedseg Egeszsegugyi Kozpont

Budapest, 1062, Hungary

Location

Semmelweis Egyetem

Budapest, 1082, Hungary

Location

Semmelweis Egyetem 2

Budapest, 1083, Hungary

Location

Semmelweis Egyetem 1

Budapest, H-1088, Hungary

Location

Pecsi Tudomanyegyetem Orvostudomanyi Es Egeszsegtudomanyi Centrum, I. Belgyogyaszati Klinika

Pécs, 7624, Hungary

Location

Szegedi Tud Egyetem Szent Gyorgyi Albert Klin Kozp

Szeged, 6725, Hungary

Location

Haemek Medical Center

Afula, 1834111, Israel

Location

Rambam Medical Center

Haifa, 31096, Israel

Location

Shaare Zedek Medical Center

Jerusalem, 9103102, Israel

Location

Rabin Medical Center Beilinson Campus

Petah Tikva, 4941492, Israel

Location

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico

Milan, 20122, Italy

Location

Ospedale Classificato Equiparato Sacro Cuore Don Calabria di Negrar

Negrar ( Ve), 37024, Italy

Location

Azienda Ospedaliera Universitaria Pisana

Pisa, 56124, Italy

Location

Azienda Ospedaliera G.Salvini Ospedale di Rho

Rho, Italy

Location

Policlinico Universitario Agostino Gemelli

Roma, 00168, Italy

Location

Istituto Clinico Humanitas

Rozzano, 20089, Italy

Location

Casa Sollievo della Sofferenza

San Giovanni Rotondo, 71013, Italy

Location

KOKIKAI Tokatsu Tsujinaka Hospital

Abiko, 270-1168, Japan

Location

Fukuoka University Chikushi Hospital

Chikushino-shi, 818-8502, Japan

Location

Hospital of the University of Occupational and Environmental Health

Fukuoka, 807-8555, Japan

Location

Fukuoka University Hospital

Fukuoka, 814 0180, Japan

Location

Kitakyushu Municipal Medical Center

Fukuoka-ken, 802-0077, Japan

Location

Hiroshima University Hospital

Hiroshima, 734 8551, Japan

Location

Sameshima Hospital

Kagoshima, 892-0846, Japan

Location

Nara Medical University Hospital

Kashihara, 634-8521, Japan

Location

Tsujinaka Hospital Kashiwanoha

Kashiwa, 277-0871, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8501, Japan

Location

Kojunkai Daido Clinic

Nagoya, 457-8511, Japan

Location

Nagoya University Hospital

Nagoya, 466 8560, Japan

Location

The Hospital of Hyogo College of Medicine

Nishinomiya, 663-8501, Japan

Location

Okayama University Hospital

Okayama, 700 8558, Japan

Location

Kinshukai Infusion Clinic

Osaka, 530-0011, Japan

Location

JOHAS Osaka Rosai Hospital

Sakai, 591-8025, Japan

Location

Sapporo Higashi Tokushukai Hospital

Sapporo, 065-0033, Japan

Location

Tokyo Yamate Medical Center

Shinjuku-ku, 169-0073, Japan

Location

Matsuda Hospital

Shizuoka, 432-8061, Japan

Location

Osaka University Hospital

Suita, 565 0871, Japan

Location

Kyorin University Hospital

Tokyo, 181 8611, Japan

Location

Ieda Hospital

Toyota, 470-1219, Japan

Location

Mie University Hospital

Tsu, 514 8507, Japan

Location

Yokkaichi Hazu Medical Center

Yokkaichi, 510-0016, Japan

Location

Yokohama Municipal Citizen's Hospital

Yokohama, 221 0855, Japan

Location

The Speciality Hospital (TSH) / Advanced Clinical Center

Amman, 11194, Jordan

Location

Jordan University Hospital

Amman, 11942, Jordan

Location

Abdali Hospital

Amman, Jordan

Location

Irbid Specialty Hospital

Irbid, 21110, Jordan

Location

King Abdullah University Hospital

Irbid, 22110, Jordan

Location

Academisch Medisch Centrum Universiteit van Amsterdam

Amsterdam, 1105 AZ, Netherlands

Location

Radboudumc

Nijmegen, 6525 GA, Netherlands

Location

Erasmus MC

Rotterdam, 3015 GD, Netherlands

Location

UMC Utrecht

Utrecht, 3584 CX, Netherlands

Location

Gastromed Kralisz Romatowski Stachurska Sp. j.

Bialystok, 15-322, Poland

Location

Centrum Medyczne Promed

Krakow, 31-513, Poland

Location

Centrum Medyczne Med Gastr

Lodz, 91 034, Poland

Location

Centrum Medyczne Medyk

Rzeszów, 35-326, Poland

Location

Twoja Przychodnia - Szczecinskie Centrum Medyczne

Szczecin, 71-434, Poland

Location

GASTROMED Kopon Zmudzinski i wspolnicy SP j Specjalistyczne Centrum Gastrologii i Endoskopii

Torun, 87 100, Poland

Location

WIP Warsaw IBD Point Profesor Kierkus

Warsaw, 00-728, Poland

Location

Melita Medical Sp. z o.o.

Wroclaw, 50-449, Poland

Location

Centrum Medyczne Oporow

Wroclaw, 52-416, Poland

Location

Uls Braga - Hosp. Braga

Braga, 4710-243, Portugal

Location

Uls Sao Jose - Hosp. Sto Antonio Dos Capuchos

Lisbon, G1R 2J6, Portugal

Location

H. Santo António - Centro Hospitalar do Porto

Porto, 4099-001, Portugal

Location

King Fahad Specialist hospital

Dammam, 31444, Saudi Arabia

Location

King Abdulaziz Medical City

Jeddah, 21423, Saudi Arabia

Location

King Saud University Medical City

Riyadh, 11472, Saudi Arabia

Location

King Faisal Specialist Hospital & Research Center

Riyadh, 12713, Saudi Arabia

Location

Inje University Haeundae Paik Hospital

Busan, 48108, South Korea

Location

Yeungnam University Hospital

Daegu, 42415, South Korea

Location

Seoul National University Bundang Hospital

Gyeonggi-do, 13620, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Gangnam Severance Hospital, Yonsei University Health System

Seoul, 06273, South Korea

Location

Hosp Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hosp. Arquitecto Marcide

Ferrol, 15405, Spain

Location

Hosp. Univ. Dr. Josep Trueta

Girona, 17007, Spain

Location

Hosp. Univ. de La Princesa

Madrid, 28006, Spain

Location

Hosp. Univ. Pta. de Hierro Majadahonda

Majadahonda, 28222, Spain

Location

Hosp. Virgen Macarena

Seville, 41009, Spain

Location

Hosp. Alvaro Cunqueiro

Vigo, 36312, Spain

Location

Hosp. Univ. Miguel Servet

Zaragoza, 50009, Spain

Location

Changhua Christian Hospital

Changhua, 500, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Taiwan University Hospital

Taipei, 10002, Taiwan

Location

Chang Gung Memorial Hospital Linkou Branch

Taoyuan, 333, Taiwan

Location

Gazi University Medical Faculty

Ankara, 06560, Turkey (Türkiye)

Location

Istanbul University Cerrahpasa Medical Faculty

Istanbul, 34098, Turkey (Türkiye)

Location

Acibadem Kozyatagi Hospital

Istanbul, 34734, Turkey (Türkiye)

Location

Ege University Medical Faculty

Izmir, 35100, Turkey (Türkiye)

Location

Mersin University Medical Faculty Hospital

Mersin, 33110, Turkey (Türkiye)

Location

Hull University Teaching Hospitals NHS Trust

Hull, HU3 2JZ, United Kingdom

Location

London North West University Healthcare NHS Trust

London, HA1 3UJ, United Kingdom

Location

Guys and St Thomas NHS Foundation Trust

London, SE1 9RT, United Kingdom

Location

St Georges University Hospital NHS Foundation Trust

London, SW17 0QT, United Kingdom

Location

Newcastle upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, NE3 3HD, United Kingdom

Location

Pennine Acute Hospitals NHS Trust

Salford, M6 8HD, United Kingdom

Location

MeSH Terms

Interventions

guselkumab

Study Officials

  • Janssen-Cilag Ltd. Clinical Trial

    Janssen-Cilag Ltd.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 21, 2022

First Posted

April 26, 2022

Study Start

September 27, 2022

Primary Completion (Estimated)

March 25, 2027

Study Completion (Estimated)

March 25, 2027

Last Updated

April 21, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

The data sharing policy of the Janssen Pharmaceutical Companies of Johnson \& Johnson is available at www.janssen.com/clinical-trials/transparency. As noted on this site, requests for access to the study data can be submitted through Yale Open Data Access (YODA) Project site at yoda.yale.edu

More information

Locations