NCT05334693

Brief Summary

The purpose of this study is to estimate the efficacy of immunotherapy with ex vivo expanded haploidentical NK cells as consolidation therapy for children/young adults with intermediate risk AML.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
15

participants targeted

Target at below P25 for phase_1

Timeline
1mo left

Started Nov 2021

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress99%
Nov 2021Jun 2026

Study Start

First participant enrolled

November 1, 2021

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

April 12, 2022

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 19, 2022

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2025

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2026

Expected
Last Updated

August 28, 2024

Status Verified

August 1, 2024

Enrollment Period

4.1 years

First QC Date

April 12, 2022

Last Update Submit

August 27, 2024

Conditions

Keywords

Natural killer cellsImmunotherapy

Outcome Measures

Primary Outcomes (2)

  • Relapse-free survival (RFS)

    Time from achievement of CR to the time of relapse or death from any cause.

    2 years

  • Overall survival (OS)

    The proportion of patients with overall survival

    2 years

Secondary Outcomes (2)

  • Persistence of donor NK cells

    21 days after the first infusion

  • Number of T, B, NK, activated T and NK cells after immunotherapy

    28 days after the first infusion

Study Arms (1)

Expanded haploidentical NK cell immunotherapy

EXPERIMENTAL

After a lymphodepleting chemotherapy a patient receive two intravenous infusions of expanded haploidentical NK cells.

Biological: Expanded haploidentical NK cells

Interventions

Two doses of expanded haploidentical NK cells (30-100 x 10\^6 cells /kg).

Expanded haploidentical NK cell immunotherapy

Eligibility Criteria

Age6 Months - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients:
  • primary intermediate risk AML in molecular complete remission;
  • primary high risk AML in molecular complete remission awaiting unrelated HSCT;
  • Karnofsky or Lansky performance scale greater or equal to 70;
  • written informed consent.
  • Donors:
  • haploidentical family donor;
  • donor suitable for cell donation and apheresis according to standard criteria;
  • written informed consent.

You may not qualify if:

  • Patients:
  • uncontrolled infection;
  • severe hepatic dysfunction: SGOT or SCPT \>=5x upper limit of normal for age;
  • positive serology for human immunodeficiency virus (HIV).
  • Donors:
  • pregnancy;
  • positive serology for HIV, hepatitis B or C.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Belarussian Research Center for Pediatric Oncology, Hematology and Immunology

Minsk, Minsk Oblast, 223053, Belarus

RECRUITING

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Study Officials

  • Olga Aleinikova, MD, Prof

    Belarussian Research Center for Pediatric Oncology, Hematology and Immunology

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Tatsiana Shman, PhD

CONTACT

Mariya Naumovich, MD

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 12, 2022

First Posted

April 19, 2022

Study Start

November 1, 2021

Primary Completion

December 1, 2025

Study Completion (Estimated)

June 1, 2026

Last Updated

August 28, 2024

Record last verified: 2024-08

Locations