NCT05330325

Brief Summary

The study compares two medicines for treatment of children born small and who stay small, or with Turner Syndrome, Noonan Syndrome, or idiopathic short stature. The purpose of the study is to see how well treatment with somapacitan works compared to treatment with Norditropin®. Somapacitan is a new medicine, and Norditropin® is a medicine doctors can already prescribe in some countries. The study will last for upto 5.5 years. The participants will either get somapacitan once a week up to 5.5 years or Norditropin® once a day for 1 year followed by somapacitan once a week for up to 4.5 years. Which treatment the participants get is decided by chance.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
412

participants targeted

Target at P50-P75 for phase_3

Timeline
18mo left

Started Aug 2022

Longer than P75 for phase_3

Geographic Reach
33 countries

199 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress72%
Aug 2022Oct 2027

First Submitted

Initial submission to the registry

April 8, 2022

Completed
7 days until next milestone

First Posted

Study publicly available on registry

April 15, 2022

Completed
4 months until next milestone

Study Start

First participant enrolled

August 10, 2022

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 5, 2024

Completed
3.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 29, 2027

Expected
Last Updated

April 24, 2026

Status Verified

April 1, 2026

Enrollment Period

2 years

First QC Date

April 8, 2022

Last Update Submit

April 23, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Height velocity reported separately for small for gestational age (SGA), Turner syndrome (TS), Noonan syndrome (NS) and idiopathic short stature (ISS)

    Measured in centimeter per year (cm/year)

    From baseline (week 0) to visit 7 (week 52)

Secondary Outcomes (15)

  • Change in Height standard deviation scores (SDS) reported separately for SGA, TS, NS and ISS

    From baseline (week 0) to visit 7 (week 52)

  • Change in Height Velocity SDS reported separately for SGA, TS, NS and ISS

    From baseline (week 0) to visit 7 (week 52)

  • Change in bone age reported separately for SGA, TS and NS

    From baseline (week 0) to visit 7 (week 52)

  • Change in bone age for ISS

    From screening (visit 1) to visit 7 (week 52)

  • Change in insulin-like growth factor 1 (IGF-1) SDS reported separately for SGA, TS, NA and ISS

    From baseline (week 0) to visit 7 (week 52).

  • +10 more secondary outcomes

Study Arms (2)

Somapacitan

EXPERIMENTAL

Participants will receive Somapacitan for 273 weeks

Drug: Somapacitan

Norditropin®

ACTIVE COMPARATOR

Participants will receive Norditropin® for 52 weeks (main treatment period) and Somapacitan for 221 weeks (extension period)

Drug: Norditropin®

Interventions

Somapacitan will be administered subcutaneously (s.c.) once weekly using PDS290 pen-injector.

Somapacitan

Norditropin® will be administered s.c. once daily using FlexPro® pen-injector.

Norditropin®

Eligibility Criteria

Age2 Years - 10 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Informed consent of parent or legally acceptable representative of participant and child assent, as age appropriate must be obtained before any study-related activities. Study-related activities are any procedures that are carried out as part of the study, including activities to determine suitability for the study.
  • No prior exposure to growth promoting therapy, including but not limited to growth hormone, IGF-I and ghrelin analogues.
  • Applicable to children with SGA:
  • Born small for gestational age (birth length below -2 SDS OR birth weight below -2 SDS OR both) (according to national standards).
  • Prepubertal children:
  • Boys:
  • Age above or equal to 2 years and 26 weeks and below 11.0 years at screening.
  • Testis volume below 4 mL
  • Girls:
  • Age above or equal to 2 years and 26 weeks and below 10.0 years at screening.
  • Tanner stage 1 for breast development: No palpable glandular breast tissue)
  • Impaired height defined as at least 2.5 standard deviations below the mean height for chronological age and sex at screening according to the standards of Centers for Disease Control and Prevention.
  • Impaired height velocity defined as annualized height velocity below the 50th percentile for chronological age and sex according to the standards of Prader calculated over a time span of minimum 6 months and maximum 18 months prior to screening.
  • Body Mass Index below the 95th percentile according to Centers for Disease Control and Prevention, Body Mass Index-for-age growth charts.
  • Applicable to girls with TS:
  • +38 more criteria

You may not qualify if:

  • Known or suspected hypersensitivity to study intervention(s) or related products.
  • Previous randomization into same sub-study in this study.
  • Receipt of any investigational medicinal product within 3 months before screening or participation in another clinical study at the time of randomization.
  • Children with suspected or confirmed growth hormone deficiency according to local practice.
  • laboratory of
  • fasting plasma glucose above or equal to 126 mg/dL (7.0 mmol/L) or
  • HbA1c above or equal to 6.5%.
  • Current inflammatory diseases requiring systemic corticosteroid treatment for longer than 2 consecutive weeks within the last 3 months prior to screening.
  • Children requiring inhaled glucocorticoid therapy at a dose greater than 400 µg/day of inhaled budesonide or equivalent (i.e., 250 µg/day for fluticasone propionate) for longer than 4 consecutive weeks within the last 12 months prior to screening.
  • Concomitant administration of other treatments that may have an effect on growth, e.g., but not limited to methylphenidate for treatment of attention deficit hyperactivity disorder (ADHD).
  • Diagnosis of attention deficit hyperactivity disorder (ADHD).
  • History or known presence of any malignancy, intracranial tumour, or intracranial cyst.
  • Any disorder, which in the investigator's opinion, might jeopardize participant's safety or compliance with the protocol.
  • The participant or the parent/legally acceptable representative is likely to be non-compliant in respect to study conduct, as judged by the investigator.
  • Current treatment with sex hormones or aromatase inhibitors.
  • +26 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (199)

Univ of AL at Birmingham_BRM

Birmingham, Alabama, 35233, United States

Location

Children's Hospital Los Angeles - Endocrinology

Los Angeles, California, 90027, United States

Location

Sutter Valley Med Fdt Ped Endo

Sacramento, California, 95821, United States

Location

Rady Childrens Hosp San Diego

San Diego, California, 92123, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Rocky Mt Ped and Endo

Centennial, Colorado, 80112, United States

Location

Ped Endo Assoc PC-G.V

Greenwood Village, Colorado, 80111-2803, United States

Location

Nemours/AI duPont Hosp-Chld

Wilmington, Delaware, 19803, United States

Location

Childrens National Medical Ctr

Washington D.C., District of Columbia, 20010-2978, United States

Location

Nemours Chld Clnc Jacksonville

Jacksonville, Florida, 32207, United States

Location

Atlanta Diabetes Associates

Atlanta, Georgia, 30318, United States

Location

St. Luke's Children's Endo

Boise, Idaho, 83712, United States

Location

Rocky Mt Clin Res, LLC

Idaho Falls, Idaho, 83404-7596, United States

Location

Riley Hosp for Child-Indiana U

Indianapolis, Indiana, 46202, United States

Location

University OF Iowa

Iowa City, Iowa, 52242, United States

Location

UMass Medical School

Worcester, Massachusetts, 01655, United States

Location

Univ of Minnesota M.C.H.

Minneapolis, Minnesota, 55454, United States

Location

Children's Minnesota

Saint Paul, Minnesota, 55102, United States

Location

Univ of Mississippi Med Ctr

Jackson, Mississippi, 39216, United States

Location

The Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Goryeb Children's Hospital

Morristown, New Jersey, 07962, United States

Location

UBMD Peds-Div of Endo/Diabetes

Buffalo, New York, 14203, United States

Location

NYU Langone Hospital-LI

Garden City, New York, 11530, United States

Location

NYU Langone Hospital-LI

Mineola, New York, 11501, United States

Location

WakeMed Childn Endo-Dbt_Raleig

Raleigh, North Carolina, 27610, United States

Location

Akron Children's Hospital

Akron, Ohio, 44308, United States

Location

CCHMC_Cinc

Cincinnati, Ohio, 45229, United States

Location

Univ Oklahoma Sci Ctr OK City

Oklahoma City, Oklahoma, 73104, United States

Location

UPMC Child Hosp-Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

Location

UT Southwestern Med Cntr

Dallas, Texas, 75235, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

Consano Clinical Research, LLC

Shavano Park, Texas, 78231, United States

Location

University Of Virginia Hospital

Charlottesville, Virginia, 22903, United States

Location

MultiCare Inst for Res & Innov

Tacoma, Washington, 98405, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Kepler Universitätsklinikum GmbH - Med Campus IV (vorm.LFKK)

Linz, Upper Austria, 4020, Austria

Location

Krankenhaus der Stadt Dornbirn

Dornbirn, 6850, Austria

Location

LKH St. Poelten, Kinder-und Jugendheilkunde

Sankt Pölten, 3100, Austria

Location

Salzkammergut-Klinikum Vöcklabruck

Vöcklabruck, 4840, Austria

Location

UZ Brussel

Brussels, 1090, Belgium

Location

Cliniques Universitaires Saint-Luc - Serv. Pédiatrie

Brussels, 1200, Belgium

Location

UZA - UZ Antwerpen - Kinderziekenhuis

Edegem, 2650, Belgium

Location

UZ Leuven - Kindergeneeskunde

Leuven, 3000, Belgium

Location

Centro de Diabetes Curitiba

Curitiba, Paraná, 80810-040, Brazil

Location

Santa Casa Sao Paulo

São Paulo, São Paulo, 01223-001, Brazil

Location

CPQuali Pesquisa Clínica Ltda

São Paulo, São Paulo, 01228-000, Brazil

Location

Centro de Pesquisa Clínica do Hospital das Clínicas da Faculdade de Medicina da USP

São Paulo, São Paulo, 05403-000, Brazil

Location

UMHAT - Dr. Georgi Stranski EAD

Pleven, 5800, Bulgaria

Location

UMHAT Sveti Georgi EAD, Plovdiv, Clinic of Pediatrics

Plovdiv, 4002, Bulgaria

Location

SHATPD - Prof. Ivan Mitev EAD

Sofia, 1606, Bulgaria

Location

UMHAT Sveta Marina EAD, First Pediatric Clinic

Varna, 9010, Bulgaria

Location

Children's Hosp-East Ontario

Ottawa, Ontario, K1H 8L1, Canada

Location

Beijing Children's Hospital, Capital Medical University

Beijing, Beijing Municipality, 100045, China

Location

The First Affiliated Hospital, Sun Yat-sen University

Guangzhou, Guangdong, 510080, China

Location

Liuzhou Maternity and Child Healthcare Hospital-Child Healthcare

Liuchow, Guangxi, 545001, China

Location

Sanya Central Hospital (Hainan Third People's Hospital)-Pediatric

Sanya, Hainan, 572032, China

Location

Henan Children's Hospital Zhengzhou Children's Hospital-Endocrine Genetics and Metabolism

Zhengzhou, Henan, 450018, China

Location

Wuhan Children Hospital-Endocrine Genetics and Metabolism

Wuhan, Hubei, 430019, China

Location

Wuhan Children Hospital

Wuhan, Hubei, 430019, China

Location

Tongji Hospital, Tongji Medical College of HUST-Pediatric

Wuhan, Hubei, 430030, China

Location

Hunan Children's Hospital-Child Health Center

Changsha, Hunan, 410007, China

Location

The First Bethune Hospital of Jilin University-Pediatric

Changchun, Jilin, 130021, China

Location

Shandong Provincial Hospital-Pediatric

Jinan, Shandong, 250098, China

Location

Shanghai Children's Hospital -Endocrine Genetics and Metabolism

Shanghai, Shanghai Municipality, 200062, China

Location

Shanghai Children's Medical Center-Endocrine Genetics and Metabolism

Shanghai, Shanghai Municipality, 200127, China

Location

Chengdu Women's and Children's Central Hospital

Chengdu, Sichuan, 610000, China

Location

KBC "Sestre Milosrdnice"

Zagreb, 10 000, Croatia

Location

KBC Zagreb, Zavod za dječju endokrinologiju i dijabetes

Zagreb, 10000, Croatia

Location

HUS Pediatric Unit

Helsinki, 00290, Finland

Location

Centre Hospitalier Régional Universitaire d' Angers

Angers, 49033, France

Location

Centre Hospitalier Universitaire D'Angers-2

Angers, 49100, France

Location

Centre Hospitalier Universitaire de Bordeaux-Hopital Pellegrin

Bordeaux, 33000, France

Location

CHU Pellegrin

Bordeaux, 33076, France

Location

Ap-Hp-Hopital de Bicetre

Le Kremlin-Bicêtre, 94270, France

Location

Hopital de Bicetre_Le Kremlin-Bicetre

Le Kremlin-Bicêtre, 94275, France

Location

Assistance Publique Hopitaux de Marseille-Hopital de La Timone-2

Marseille, 13005, France

Location

Hopital de La Timone

Marseille Cédex 05, 13385, France

Location

Ap-Hp-Hopital Necker

Paris, 75015, France

Location

Hôpital Necker

Paris, 75015, France

Location

CHU de Toulouse

Toulouse, 31059, France

Location

Hopital Des Enfants

Toulouse, 31059, France

Location

Universitätsklinikum Bonn - Kinderklinik

Bonn, 53127, Germany

Location

Universitätsklinikum Erlangen - Kinder- und Jugendklinik

Erlangen, 91054, Germany

Location

Endokrinologikum Frankfurt

Frankfurt am Main, 60596, Germany

Location

Klinik für Allgemeine Pädiatrie und Neonatologie

Homburg, 66421, Germany

Location

Universität des Saarlandes - Pädiatrie und Neonatologie

Homburg, 66424, Germany

Location

U.G.H. "Attikon", Pediatric Endocrinology Outpatient Clinic

Athens, 12462, Greece

Location

Childrens' Hospital of Athens "Agia Sofia"

Goudi/Athens, 115-27, Greece

Location

P & A Kyriakou Childrens' Hospital - Department of Endocrinology Growth and Development

Goudi/Athens, 115-27, Greece

Location

General University of Patra - Paediatric Department

Pátrai, 26504, Greece

Location

'Ippokrateio' General Hospital of Thessaloniki

Thessaloniki, 546-42, Greece

Location

"AHEPA" University General Hospital of Thessaloniki

Thessaloniki, 54636, Greece

Location

Ippokrateio Gen Hosp of Thessaloniki, 1st Pediatric Clinic

Thessaloniki, 54642, Greece

Location

Ippokrateio Gen Hosp of Thessaloniki, 1st Pediatric Clinic

Thessaloniki, GR 54642, Greece

Location

"AHEPA" University General Hospital of Thessaloniki

Thessaloniki, GR-54636, Greece

Location

Amrita Institute Of Medical Sciences & Research Centre

Kochi, Kerala, 682041, India

Location

Jehangir Clinical Development Centre

Pune, Maharashtra, 411001, India

Location

All India Institute of Medical Sciences

New Dehli, New Delhi, 110029, India

Location

Cork University Hospital

Cork, Ireland

Location

CHI at Temple Street

Dublin, D01 XD99, Ireland

Location

CHI Crumlin Dept of Endocrinology

Dublin, D12 N512, Ireland

Location

CHI Tallaght University Hospital

Dublin, D24NR0A, Ireland

Location

Soroka MC - Pediatric Endocrinology

Beersheba, 84101, Israel

Location

Rambam MC - Department of Pediatrics A

Haifa, 31096, Israel

Location

Schneider MC - Endrocrinology and Diabetes

Petah Tikva, 49202, Israel

Location

Sheba MC - Pediatric endocrinology and adolescent diabetes clinics

Tel Litwinsky, 52621, Israel

Location

Shamir MC - Pediatric and Adolescents Endocrinology unit

Ẕerifin, 7033001, Israel

Location

Ospedale San Raffaele S.r.l. - Unità Clinica Pediatria e neonatologia

Milan, Lombardy, 20132, Italy

Location

IRCCS Meyer Firenze

Florence, 50139, Italy

Location

Ospedale Pediatrico Gaslini

Genova, 16147, Italy

Location

Ospedale San Raffaele UO di Pediatria e UO di Neonatologia

Milan, 20132, Italy

Location

Università degli Studi della Campania "L. Vanvitelli"

Naples, 80138, Italy

Location

Bambin Gesù

Roma, 00165, Italy

Location

Ospedale Pediatrico Bambino Gesu

Roma, 00165, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Rome, 00168, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli IRCS

Rome, 00168, Italy

Location

Fukuoka Children's Hospital_Endocrinology and Metabolism

Fukuoka-shi, Fukuoka, 813-0017, Japan

Location

Fukuoka Children's Hospital

Fukuoka-shi, Fukuoka, 813-0017, Japan

Location

Hyogo Prefectual Kobe Children's Hospital Dept. Metab & endo

Kobe-shi, Hyogo, 650-0047, Japan

Location

Hyogo Prefectual Kobe Children's Hospital_Metab & endo

Kobe-shi, Hyogo, 650-0047, Japan

Location

Univ.HP, Kyoto Pref Univ of Medicine, Dept. of Pediatrics

Kyoto, 602-8566, Japan

Location

Nara Prefecture General Medical Center_Nephrology

Nara-shi, Nara, 630-8581, Japan

Location

Nara Prefecture General Medical Center

Nara-shi, Nara, 630-8581, Japan

Location

Niigata University Medical & Dental Hospital_Pediatrics

Niigata-shi, Niigata, 951 8520, Japan

Location

Okayama Medical Center_Cardiology

Okayama-shi, Okayama, 701-1192, Japan

Location

Osaka City General Hospital, Pediatric Endocrinology and Me

Osaka, 534-0021, Japan

Location

Osaka Women's and Children's Hospital

Osaka, 594-1101, Japan

Location

Saitama Children's Medical Center, Endocrinorogy&Metabolism

Saitama-shi, Saitama, 330-8777, Japan

Location

Hokkaido University Hospital, Pediatrics

Sapporo, Hokkaido, 060-8648, Japan

Location

Hokkaido University Hospital_Pediatrics

Sapporo, Hokkaido, 060-8648, Japan

Location

Shizuoka Children's Hospital, Department of Diabetes and metabolism

Shizuoka-shi, Shizuoka, 420-8660, Japan

Location

Institute of Science Tokyo Hospital_Pediatrics

Tokyo, 113-8519, Japan

Location

Institute of Science Tokyo Hospital

Tokyo, 113-8519, Japan

Location

National Center for Child Health and Development_Endo and Metabo

Tokyo, 157 8535, Japan

Location

Keio University Hospital_Pediatrics

Tokyo, 160-8582, Japan

Location

Fujita Health University Hospital, Pediatrics

Toyoake, Aichi, 470-1192, Japan

Location

Children's Clinical University Hospital

Riga, 1004, Latvia

Location

Hospital of Lithuanian University of Health Sciences Kauno klinikos

Kaunas, 50161, Lithuania

Location

Hospital Universiti Sains Malaysia_Kota Bharu, Kelantan

Kota Bharu, Kelantan, 16150, Malaysia

Location

University Malaya Medical Centre

Kuala Lumpur, Kuala Lumpur, 59100, Malaysia

Location

University Malaya Medical Centre

Lembah Pantai, Kuala Lumpur, 59100, Malaysia

Location

Hospital Al-Sultan Abdullah UiTM

Bandar Puncak Alam, Selangor, 42300, Malaysia

Location

University Technology MARA (UiTM) - Puncak Alam

Bandar Puncak Alam Selangor Darul Ehsan, 42300, Malaysia

Location

Consultorio de Endocrinología y Pediatría

Puebla City, 72190, Mexico

Location

Erasmus MC

Rotterdam, 3015 GD, Netherlands

Location

Kliniczny Szpital Wojewodzki nr 2 im. Sw. Jadwigi Krolowej w Rzeszowie

Rzeszów, Podkarpackie Voivodeship, 35-301, Poland

Location

Uniwer. Szpital Dzieciecy Klinika Endokry. Dzieci i Mlodzie

Cracow, 30-663, Poland

Location

Uniwersytecki Szptal Dziecięcy w Krakowie

Cracow, 30-663, Poland

Location

UCK, Klinika Pediatrii, Diabetologii i Endokrynologii,

Gdansk, 80-952, Poland

Location

Górnośląskie Centrum Zdrowia Dziecka Szpital Kliniczny Nr 6

Katowice, 40-752, Poland

Location

Klinika Endokrynologii i Chorób Metabolicznych

Lodz, 93-338, Poland

Location

SPSK nr 1 im Prof. T Sokolowskiego

Szczecin, 71-252, Poland

Location

Klinika Pediatrii SUM, SPSK nr 1 im. prof.S.Szyszko w Zabrzu_LOC#1

Zabrze, 41-800, Poland

Location

SPSK nr 1 im. prof.S.Szyszko w Zabrzu

Zabrze, 41-800, Poland

Location

Unidade Local De Saúde De São José, E.P.E.- Hospital D. Estefânia

Lisbon, 1169-045, Portugal

Location

Centro Hospitalar Lisboa Norte

Lisbon, 1649-035, Portugal

Location

Unidade Local De Saúde De Santa Maria E.P.E.

Lisbon, 1649-035, Portugal

Location

ULS De Santo António, E.P.E. - Hospital de Santo António

Porto, 4050-651, Portugal

Location

ULS De Gaia/Espinho_H.Santos Silva_Pediatria

Vila Nova de Gaia, 4400-129, Portugal

Location

King Faisal Specialist Hospital & Research Centre, Riyadh

Riyadh, 12713, Saudi Arabia

Location

National Guard Hospital

Riyadh, 14812, Saudi Arabia

Location

University Clinical Centre Nis

Niš, RS, 18 000, Serbia

Location

University Children's Hospital Tirsova

Belgrade, 11000, Serbia

Location

Institute for Mother and Child Health Care of Serbia

Belgrade, 11070, Serbia

Location

University Clinical Centre Kragujevac

Kragujevac, 34000, Serbia

Location

University Clinical Centre Nis

Niš, 18 000, Serbia

Location

Institute for Health Care of Children and Adolescents

Novi Sad, 21000, Serbia

Location

PeK - Dept. of Paediatric Endocrinology, Diabetes and Metabolism

Ljubljana, 1525, Slovenia

Location

University Children's Hospital

Ljubljana, 1525, Slovenia

Location

Department of Peadiatrics CHBAH

Johannesburg, Gauteng, 1864, South Africa

Location

Dr JC van Dyk's Rooms

Pretoria, Gauteng, 0181, South Africa

Location

Dr Y Ganie's site

Mayville, KwaZulu-Natal, 4058, South Africa

Location

Dr K Pillay's site

Westville, KwaZulu-Natal, 3600, South Africa

Location

Pusan National University Yangsan Hospital

Yangsan, Gyeongsangnam-do, 50612, South Korea

Location

Chungnam National University Sejong Hospital

Sejong-si, 30099, South Korea

Location

Severance Hospital, Yonsei University Health System

Seoul, 03722, South Korea

Location

Asan Medical Center

Seoul, 05505, South Korea

Location

Complejo Hospitalario Universitario de Santiago

Santiago de Compostela, A Coruña, 15706, Spain

Location

H.Madrid Montepríncipe

Boadilla del Monte, Madrid, 28660, Spain

Location

Hospital Madrid Montepríncipe

Boadilla del Monte, Madrid, 28660, Spain

Location

Hospital Sant Joan de Déu

Esplugues de Llobregat, 08950, Spain

Location

Med. Kinder- und Poliklinik

Bern, 3010, Switzerland

Location

Ramathibodi Hospital - Ped-Endo and Metabolism

Ratchathewi, Bangkok, 10400, Thailand

Location

Ramathibodi Hospital - Ped-Endo and Metabolism

Bangkok, Ratchathewi, 10400, Thailand

Location

King Chulalongkorn Memorial hospital-Ped-Endocrinology

Bangkok, 10330, Thailand

Location

King Chulalongkorn Memorial hospital_Ped-Endocrinology

Bangkok, 10330, Thailand

Location

Phramongkutklao Hospital_Ped-Endo_Pediatrics

Bangkok, 10400, Thailand

Location

PMK - Paediatrics Endocrinology Centre

Bangkok, 10400, Thailand

Location

Siriraj Hospital_Dept of Paediatrics

Bangkok, 10700, Thailand

Location

Maharaj Nakorn Chiang Mai Hospital_Pediatric Endocrinology

Chiang Mai, 50200, Thailand

Location

Srinagarind Hospital

Khon Kaen, 40002, Thailand

Location

Addenbrooke's Hospital_Cambridge

Cambridge, CB2 0QQ, United Kingdom

Location

Hull Royal Infirmary

Hull, HU3 2JZ, United Kingdom

Location

Alder Hey Children's Hospital

Liverpool, L12 2AP, United Kingdom

Location

Evelina Children's Hospital - St Thomas'

London, SE1 7EH, United Kingdom

Location

Evelina London Children's Hospital

London, SE1 7EH, United Kingdom

Location

Royal Manchester Children's Hospital

Manchester, M13 9WL, United Kingdom

Location

St George's Hospital

Tooting, SW17 0RE, United Kingdom

Location

St Georges Hospital

Tooting, SW17 0RE, United Kingdom

Location

Related Publications (2)

  • Jorge AAL, Albanese A, Hojby M, Soltysik K, Edouard T, Grandone A, Tansey M, Mori J. Once-weekly somapacitan in children with Noonan syndrome: randomized controlled phase 3 trial. Eur J Endocrinol. 2026 Mar 4;194(3):393-403. doi: 10.1093/ejendo/lvag041.

  • Abuzzahab J, Dauber A, Hojby M, Soltysik K, Kawai M, Murray PG, Phillip M, Battelino T. Somapacitan in children with idiopathic short stature: a randomized controlled phase 3 study. Eur J Endocrinol. 2026 Feb 4;194(2):242-253. doi: 10.1093/ejendo/lvag027.

MeSH Terms

Conditions

Turner SyndromeNoonan Syndrome

Interventions

somapacitanHuman Growth Hormone

Condition Hierarchy (Ancestors)

Gonadal DysgenesisDisorders of Sex DevelopmentUrogenital AbnormalitiesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesSex Chromosome Disorders of Sex DevelopmentMale Urogenital DiseasesHeart Defects, CongenitalCardiovascular AbnormalitiesCardiovascular DiseasesHeart DiseasesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesSex Chromosome DisordersChromosome DisordersGenetic Diseases, InbornGonadal DisordersEndocrine System DiseasesCraniofacial AbnormalitiesMusculoskeletal AbnormalitiesMusculoskeletal DiseasesConnective Tissue DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Growth HormonePituitary Hormones, AnteriorPituitary HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and Proteins

Study Officials

  • Clinical Transparency dept. 2834

    Novo Nordisk A/S

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 8, 2022

First Posted

April 15, 2022

Study Start

August 10, 2022

Primary Completion

August 5, 2024

Study Completion (Estimated)

October 29, 2027

Last Updated

April 24, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

According to the Novo Nordisk disclosure commitment on novonordisk-trials.com

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