NCT05310422

Brief Summary

This study will examine the safety of tivanisiran sodium eye drops versus vehicle when dosed once daily for 1 year in subjects with signs and symptoms of dry eye disease (DED).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
301

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Mar 2022

Geographic Reach
1 country

25 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 24, 2022

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

March 25, 2022

Completed
11 days until next milestone

First Posted

Study publicly available on registry

April 5, 2022

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 11, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 11, 2023

Completed
Last Updated

February 20, 2024

Status Verified

February 1, 2024

Enrollment Period

1.6 years

First QC Date

March 25, 2022

Last Update Submit

February 16, 2024

Conditions

Keywords

siRNAoligonucleotidekeratoconjunctivitis siccaSYL1001

Outcome Measures

Primary Outcomes (1)

  • Frequency and percentage of subjects with ocular and non-ocular treatment emergent adverse events (TEAEs) for 1 year

    1 year

Study Arms (2)

Tivanisiran sodium ophthalmic solution

EXPERIMENTAL
Drug: Tivanisiran sodium ophthalmic solution

Vehicle ophthalmic solution

PLACEBO COMPARATOR
Drug: Vehicle ophthalmic solution

Interventions

1 drop in the affected eye(s) once daily

Tivanisiran sodium ophthalmic solution

1 drop in the affected eye(s) once daily

Vehicle ophthalmic solution

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be at least 18 years of age
  • Have given their written consent to participate in the study
  • Use of artificial tears (AT), autologous serum or specific dry eye medications during the last 6 months prior to the selection

You may not qualify if:

  • Pregnant or breast feeding females with a postitive pregnancy test
  • Women of childbearing potential not willing to use a medically acceptable contraceptive method
  • Current, previous chronic or recurrent medical condition that, according to the investigator, might impact on the study
  • Any concomitant treatment or prior ocular procedure or surgery in either eye or alteration of the dose of systemic medications that could interfere in the trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Sylentis Investigative Site

Chandler, Arizona, 85021, United States

Location

Sylentis Investigative Site

Phoenix, Arizona, 85032, United States

Location

FYDES Investigative Site

Glendale, California, 91204, United States

Location

Sylentis Investigative Site

Hemet, California, 92545, United States

Location

Sylentis Investigative Site

Los Angeles, California, 85032, United States

Location

Sylentis Investigative Site

Murrieta, California, 92562, United States

Location

Sylentis Investigative Site

Newport Beach, California, 92663, United States

Location

FYDES Investigative Site

Delray Beach, Florida, 33484, United States

Location

FYDES Investigative Site

Jacksonville, Florida, 32256, United States

Location

Sylentis Investigative Site

Largo, Florida, 33773, United States

Location

Sylentis Investigative Site

Morrow, Georgia, 30260, United States

Location

Sylentis Investigative Site

Fraser, Michigan, 48026, United States

Location

Sylentis Investigative Site

Kansas City, Missouri, 64111, United States

Location

FYDES Investigative Site

St Louis, Missouri, 63131, United States

Location

Sylentis Investigative Site

Washington, Missouri, 63090, United States

Location

Sylentis Investigative Site

Rochester, New York, 14618, United States

Location

Sylentis Investigative Site

Asheville, North Carolina, 28803, United States

Location

Sylentis Investigative Site

Garner, North Carolina, 27529, United States

Location

Sylentis Investigative Site

Cranberry Township, Pennsylvania, 16066, United States

Location

Sylentis Investigative Site

Rapid City, South Dakota, 57701, United States

Location

Sylentis Investigative Site

Memphis, Tennessee, 38119, United States

Location

Sylentis Investigative Site

Austin, Texas, 78731, United States

Location

FYDES Investigative Site

El Paso, Texas, 79902, United States

Location

Sylentis Investigative Site

San Antonio, Texas, 78215, United States

Location

Sylentis Investigative Site

San Antonio, Texas, 78230, United States

Location

Related Publications (1)

  • Mangwani-Mordani S, Goodman CF, Galor A. Novel Treatments for Chronic Ocular Surface Pain. Cornea. 2023 Mar 1;42(3):261-271. doi: 10.1097/ICO.0000000000003193. Epub 2022 Dec 19.

MeSH Terms

Conditions

Dry Eye SyndromesKeratoconjunctivitis Sicca

Condition Hierarchy (Ancestors)

Lacrimal Apparatus DiseasesEye DiseasesKeratoconjunctivitisConjunctivitisConjunctival DiseasesKeratitisCorneal Diseases

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 25, 2022

First Posted

April 5, 2022

Study Start

March 24, 2022

Primary Completion

October 11, 2023

Study Completion

October 11, 2023

Last Updated

February 20, 2024

Record last verified: 2024-02

Locations