NCT05279872

Brief Summary

This project was undertaken to evaluate the efficacy and safety of BTK inhibitor Zanubrutinib for the secondary treatment of adults with primary immune thrombocytopenia (ITP).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jan 2022

Shorter than P25 for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2022

Completed
23 days until next milestone

First Submitted

Initial submission to the registry

January 24, 2022

Completed
2 months until next milestone

First Posted

Study publicly available on registry

March 15, 2022

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 30, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 30, 2022

Completed
Last Updated

October 10, 2023

Status Verified

October 1, 2023

Enrollment Period

10 months

First QC Date

January 24, 2022

Last Update Submit

October 7, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall response (OR)

    The maintenance of platelet count ≥ 30 x 10\^9/L, at least 2-fold increase of the baseline count, the absence of bleeding, and no need for rescue medication at the 6-week follow-up.

    6 weeks

Secondary Outcomes (4)

  • Complete response (CR)

    6 weeks

  • Time to response

    6 weeks

  • Bleeding events

    6 weeks

  • Side Effects

    6 weeks

Study Arms (1)

Zanubrutinib

EXPERIMENTAL

Zanubrutinib 80mg po qd 6 weeks

Drug: Zanubrutinib

Interventions

Zanubrutinib 80mg po qd 6 weeks

Zanubrutinib

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Confirmed primary refractory ITP
  • Platelet counts \<30×10\^9/L or with bleeding symptoms
  • Willing and able to sign written informed consent

You may not qualify if:

  • Secondary thrombocytopenia
  • Received chemotherapy or anticoagulants or other drugs affecting the platelet counts within 6 months before the screening visit
  • HIV infection or hepatitis B virus or hepatitis C virus infections
  • Malignancy
  • Severe medical condition (e.g., unstable angina, congestive heart failure, uncontrolled hypertension or cardiac arrhythmia)
  • Nursing or pregnant patients
  • Patients who are deemed unsuitable for the study by the investigator

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Peking University Insititute of Hematology, Peking University People's Hospital

Beijing, Beijing Municipality, 100010, China

Location

Related Publications (1)

  • Huang QS, Fu HX, Wang CC, Zhu XL, He Y, Wu J, Chen Q, Zhao P, An ZY, Liu KY, Huang XJ, Zhang XH. Efficacy and Safety of the Bruton's Tyrosine Kinase Inhibitor Zanubrutinib in Immune Thrombocytopenia. Am J Hematol. 2025 Aug;100(8):1314-1322. doi: 10.1002/ajh.27718. Epub 2025 May 20.

MeSH Terms

Conditions

Purpura, Thrombocytopenic, Idiopathic

Interventions

zanubrutinib

Condition Hierarchy (Ancestors)

Purpura, ThrombocytopenicPurpuraBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesThrombotic MicroangiopathiesThrombocytopeniaBlood Platelet DisordersCytopeniaHemorrhagic DisordersAutoimmune DiseasesImmune System DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsSkin ManifestationsSigns and Symptoms

Study Officials

  • Xiao-Hui Zhang, MD

    Peking University People's Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing Key Laboratory of Hematopoietic Stem Cell Transplantation, Collaborative Innovation Center of Hematology

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Vice president of Peking University Institute of Hematology

Study Record Dates

First Submitted

January 24, 2022

First Posted

March 15, 2022

Study Start

January 1, 2022

Primary Completion

October 30, 2022

Study Completion

October 30, 2022

Last Updated

October 10, 2023

Record last verified: 2023-10

Locations