NCT05260528

Brief Summary

The trial is a randomized, open-label phase II study comparing CPX-351 vs conventional intensivechemotherapy in patients with newly diagnosed de novo AML and intermediate- or adverse-risk genetics

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
248

participants targeted

Target at P75+ for phase_2

Timeline
45mo left

Started May 2023

Longer than P75 for phase_2

Geographic Reach
1 country

35 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress45%
May 2023Feb 2030

First Submitted

Initial submission to the registry

February 7, 2022

Completed
23 days until next milestone

First Posted

Study publicly available on registry

March 2, 2022

Completed
1.2 years until next milestone

Study Start

First participant enrolled

May 3, 2023

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 2, 2028

Expected
1.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 2, 2030

Last Updated

March 27, 2026

Status Verified

March 1, 2026

Enrollment Period

5.3 years

First QC Date

February 7, 2022

Last Update Submit

March 24, 2026

Conditions

Keywords

CPX-351Acute Myeloid Leukemia

Outcome Measures

Primary Outcomes (1)

  • Improvement in the proportion of patients achieving deep remission (CR)/(CRi) with a standardized flow based MRD in the BM aspirate using the LAIP/Dfn method after the 1st induction

    28-56 days

Secondary Outcomes (18)

  • Rate of CR/CRi with a flow based MRD in the BM aspirate using the LAIP/Dfn method

    28-56 days

  • Analysis of rate of flow-based MRD quantified in the bone marrow according to both the LAIP/DfN method and the LSC method

    10-13 weeks

  • Analysis of flow-based MRD quantified according to both LAIP/DfN method and the LSC methods

    10-13 weeks

  • Overall response rate, and CR and CRi rates

    28-56 days

  • Cumulative incidence of allogeneic HSCT

    4.5 years

  • +13 more secondary outcomes

Study Arms (2)

Standard arm

ACTIVE COMPARATOR

conventional 7+3 chemotherapy

Drug: Cytarabine and Idarubicin

Investigational arm

EXPERIMENTAL

CPX-351

Drug: CPX-315

Interventions

Induction 1:CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine i.v. (90 min) d1,3,5 Induction 2: CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine i.v. (90 min) d1,3 Consolidation therapy:CPX-351 29 mg/m2 daunorubicin / 65 mg/m2 cytarabine i.v. (90 min) d1,3

Also known as: Investigational arm
Investigational arm

Induction 1: Cytarabine 200 mg/m2 i.v. (continuously) d1-7 + Idarubicin 12mg/m2 d1, 2, 3 i.v (60 min) Induction 2: Cytarabine 1500 mg/m2 i.v. q12h d1-3 Consolidation: Cytarabine 1500 mg/m2 i.v. q12h d1-3

Also known as: Standard arm
Standard arm

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • De novo AML
  • No MRC-defining cytogenetic lesion
  • No t(15;17), t(8;21), inv(16) or t(16;16)
  • No NPM1 gene mutation
  • No FLT3 mutated AML (FLT3 ITD or TKD)
  • Not previously treated except for short course hydroxyurea in patients presenting with high WBC count and/or tumor symptoms,
  • Age ≥ 50 years,
  • Performance status ≤ 2 (ECOG grading),
  • Patient must have adequate organ function as indicated detailed with laboratory values in the section IV of the protocol
  • Female patient of childbearing potential with a negative serum pregnancy test (β-hCG) within 72 hours prior to receiving the first dose of CPX-351 or 7+3. Female patient who is not actively breastfeeding at the time of study entry.
  • Female patient is either post-menopausal, free from menses for \> 2 years, surgically sterilized or willing to use 2 adequate barrier methods of contraception to prevent pregnancy, or agrees to not become pregnant throughout the study, starting with study screening
  • Male patient agrees to use an adequate method of contraception for the duration of the study. Men should be advised not to father a child while receiving CPX-351 or 7+3 and for 3 months after the last dose of study treatment .
  • Patient is available for periodic blood sampling, study related assessments, and appropriate clinical management at the treating institution for the duration of the study.
  • Patient has the ability to understand and willingness to sign an informed consent form indicating the investigational nature of the study.
  • Patient registered to the French Social Security.

You may not qualify if:

  • Prior history of documented MDS, MPN or MDS/MPN, tAML
  • Prior history of radiation therapy or chemotherapy for a solid tumor or lymphoma (exceptions to be considered: local radiotherapy for prostate cancer)
  • Patient has active and uncontrolled infection.
  • Patient has uncontrolled intercurrent illness or circumstances that could limit compliance with the study, including but not limited to the following: symptomatic congestive heart failure, unstable angina pectoris, uncontrolled cardiac arrhythmia, pancreatitis, or psychiatric or social conditions that may interfere with patient compliance.
  • Patient is currently participating or has participated in a study with an investigational compound or device within 30 days of initial dosing with study drug.
  • Patient has known human immunodeficiency virus (HIV) infection or HIV-related malignancy.
  • Patient has clinically active hepatitis B or hepatitis C infection.
  • Patient has a known allergy or hypersensitivity to any component of CPX-351, idarubicin or cytarabine.
  • Patient with a "currently active" second malignancy, other than nonmelanoma skin cancer and carcinoma in situ of the cervix, should not be enrolled. Patients are not considered to have a "currently active" malignancy if they have completed therapy for a prior malignancy, are disease free from prior malignancies for \>1 year or are considered by their physician to be at less than 30% risk of relapse.
  • Patients with clinical evidence of CNS leukemia.
  • Cardiac ejection fraction \<50% or considered as abnormal by echocardiography or multi-gated acquisition (MUGA) scan.
  • Patient is pregnant or breastfeeding within the projected duration of the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (35)

CHU Amiens Picardie site Sud

Amiens, France

RECRUITING

CHU d'Angers

Angers, France

NOT YET RECRUITING

CH Avignon

Avignon, France

RECRUITING

CHRU Jean Minjoz

Besançon, France

RECRUITING

Centre Hospitalier de Béziers

Béziers, France

RECRUITING

Hôpital Avicenne APHP

Bobigny, France

RECRUITING

Institut d'hématologie de Basse Normandie (IHBN)

Caen, France

RECRUITING

Hôpital d'Instruction des Armée (HIA)

Clamart, France

RECRUITING

CHU Estaing

Clermont-Ferrand, France

RECRUITING

Centre Hospitalier Sud Francilien (CHSF)

Corbeil-Essonnes, France

RECRUITING

CHU Henri Mondor

Créteil, France

RECRUITING

Centre Hospitalier de Versailles, Site André Mignot

Le Chesnay, France

RECRUITING

Hôpital Claude HURIEZ, CHU Lille

Lille, France

RECRUITING

CHU de Limoges

Limoges, France

RECRUITING

Hoptial de la Conception APHM

Marseille, France

RECRUITING

Institut Paoli Calmettes

Marseille, France

RECRUITING

CHR Metz-Thionville Site Mercy

Metz, France

RECRUITING

Groupe hospitalier de la région de Mulhouse et Sud-Alsace, Hôpital Emile Muller

Mulhouse, France

RECRUITING

CHU de Nantes

Nantes, France

NOT YET RECRUITING

Centre Antoine Lacassagne

Nice, France

NOT YET RECRUITING

CHU de Nice

Nice, France

RECRUITING

Institut de cancérologie du Gard

Nîmes, France

RECRUITING

CHR Orléans

Orléans, France

RECRUITING

Hopital Necker

Paris, France

RECRUITING

Hôpital de la Pitié Salpêtrière

Paris, France

RECRUITING

Hôpital Saint-Antoine

Paris, France

RECRUITING

Hôpital Saint-Louis

Paris, France

RECRUITING

CHU de Bordeaux

Pessac, France

RECRUITING

Hopital Lyon Sud

Pierre-Bénite, France

RECRUITING

CH de Roubaix

Roubaix, France

RECRUITING

Centre Henri Becquerel

Rouen, France

RECRUITING

CHU de Saint Etienne

Saint-Priest-en-Jarez, France

RECRUITING

CHU de Toulouse

Toulouse, France

RECRUITING

Hopital Bretonneau

Tours, France

RECRUITING

Institut Gustave Roussy

Villejuif, France

RECRUITING

MeSH Terms

Conditions

Leukemia, Myeloid, Acute

Interventions

CytarabineIdarubicin

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

CytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsArabinonucleosidesNucleosidesNucleic Acids, Nucleotides, and NucleosidesDaunorubicinAnthracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic CompoundsAminoglycosidesGlycosidesCarbohydrates

Study Officials

  • Thomas Cluzeau, MD

    Centre Hospitalier Universitaire de Nice

    PRINCIPAL INVESTIGATOR

Central Study Contacts

valerie Foussat

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 7, 2022

First Posted

March 2, 2022

Study Start

May 3, 2023

Primary Completion (Estimated)

August 2, 2028

Study Completion (Estimated)

February 2, 2030

Last Updated

March 27, 2026

Record last verified: 2026-03

Locations