NCT05218772

Brief Summary

Background: Elderly people with serious haemophilia (PwSH), i.e., with moderate or severe haemophilia, have major comorbidities due to consequences of haemophilia. Also, the comorbidities related to age are added. Despite the existence of numerous studies on the objective health status of elderly PwSH, some limitations may be stated (need to update the results in a more contemporary context, no studies conducted in France, highlighted determinants focused on demographic and clinical factors). On the contrary, the perceived health status of elderly PwSH has been little described. Only two studies specifically addressed the quality of life (QoL) of elderly PwSH. These studies reported an altered QoL in some domains, in comparison with reference values from the general population. However, some limitations may also be stated (need to bring results in a more contemporary context, no studies conducted in France, highlighted determinants focused on clinical factors). Since serious haemophilia is a rare disease, studies are often performed on a small number of subjects. The present project relies on the FranceCoag registry, a unique exhaustive national cohort of PwSH followed over time among whom 612 are elderly PwSH. Objectives: Main objective: to describe the objective and perceived health status of elderly (≥60 y.o.) PwSH from of a French exhaustive national registry, and to compare their health status with that of the French general elderly population. Secondary objective: to identify individual (demographic, clinical, social, psycho-cognitive) and collective characteristics (related to healthcare organisation), associated with the objective and perceived health status of elderly PwSH in France. Materials and Methods: A national, multicentric, observational, cross-sectional study will be conducted. It will be based on the participation of elderly PwSH already included in the FranceCoag registry. Each eligible participant will receive a questionnaire to complete concerning: objective health status; perceived health status (QoL assessed by the WHOQOL-Old questionnaire); demographic data; social data; psycho-cognitive data (anxious symptoms, depressive symptoms, use of coping strategies, time perspective). Therapeutic and clinical data related to haemophilia will be collected via the FranceCoag registry database. Data concerning healthcare organisation will be collected directly from investigators of Haemophilia Treatment Centres. The main analysis will consist in the description and comparison of the health status with reference data from the French general elderly population. Standardisation methods will be used to take into account a potential imbalance between the study population and the reference population, related to age and especially to sex, as haemophilia is a predominantly male disease. The secondary analysis will consist in the identification of potential determinants of the health status. Structural equation models will be performed to take into account the complexity of the relationships between the determinants. Impact of the proposal Better understanding the impact of the disease on patients' experience is essential in a systematic global perspective of health, that aims to care and support the individual not only as a patient but also as a person in his/her environment. This study based on a registry will allow to improve the knowledge by updating literature data on the health status of elderly PwSH, adding elements to the rare literature data on the perceived health status, providing data in the French specific context, and identifying both classical and more original determinants of health status of elderly PwSH. These results will be used to better identify elderly PwSH at high risk of poor health status, to propose recommendations and to set up actions to offer them an adapted support, and to elaborate new versions of public health plans dedicated to haemophilia or to rare diseases.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
612

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Apr 2022

Geographic Reach
1 country

28 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 20, 2022

Completed
12 days until next milestone

First Posted

Study publicly available on registry

February 1, 2022

Completed
3 months until next milestone

Study Start

First participant enrolled

April 19, 2022

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2023

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2023

Completed
Last Updated

June 8, 2023

Status Verified

June 1, 2023

Enrollment Period

1.2 years

First QC Date

January 20, 2022

Last Update Submit

June 7, 2023

Conditions

Outcome Measures

Primary Outcomes (2)

  • Objective health status (apart from serious haemophilia)

    Declaration by the participant of at least one chronic disease or health issue (apart from serious haemophilia)

    1 day

  • Perceived health status

    Assessed by the quality of life, which will be measured by the WHOQOL-Old questionnaire

    1 day

Study Arms (1)

Elderly people with moderate or severe haemophilia

Other: Questionnaires

Interventions

Each eligible participant will receive a questionnaire to complete concerning: objective health status; perceived health status (QoL assessed by the WHOQOL-Old questionnaire); demographic data; social data; psycho-cognitive data (anxious symptoms, depressive symptoms, use of coping strategies, time perspective)

Elderly people with moderate or severe haemophilia

Eligibility Criteria

Age60 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Elderly people with moderate or severe haemophilia in France

You may qualify if:

  • People with serious haemophilia, i.e., with (A or B) moderate or severe haemophilia;
  • People aged 60 years or over;
  • People included in the FranceCoag registry;
  • People followed in one of the Haemophilia Treatment Centre participating in the study;
  • People who do not oppose to participate in the study.

You may not qualify if:

  • People with comprehension disabilities;
  • Participants who a posteriori oppose to participate in the study.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

Chu Amiens

Amiens, France

RECRUITING

Ch Annecy - St Julien

Annecy, France

RECRUITING

Chu de Besancon

Besançon, France

RECRUITING

Chu de Bordeaux

Bordeaux, France

RECRUITING

Chu Brest

Brest, France

RECRUITING

Chu de Caen

Caen, France

RECRUITING

Centre hospitalier Métropole Savoie

Chambéry, France

RECRUITING

Chu Clermont-Ferrand

Clermont-Ferrand, France

RECRUITING

Chu de Dijon

Dijon, France

RECRUITING

Chu La Reunion

La Réunion, France

RECRUITING

Chu Le Mans

Le Mans, France

RECRUITING

Chru de Lille

Lille, France

RECRUITING

Hospices Civils de Lyon

Lyon, France

RECRUITING

Ap-Hm

Marseille, 13005, France

RECRUITING

Chu Montpellier

Montpellier, France

RECRUITING

Chu de Nancy

Nancy, France

RECRUITING

Chu Nantes

Nantes, France

RECRUITING

Chu de Nice

Nice, France

RECRUITING

AP-HP

Paris, France

RECRUITING

Chu Poitiers

Poitiers, France

RECRUITING

Chu Reims

Reims, France

RECRUITING

Chu de Rennes

Rennes, France

RECRUITING

Chu de Rouen

Rouen, France

RECRUITING

Chu St Etienne

Saint-Etienne, France

RECRUITING

Chu Strasbourg

Strasbourg, France

RECRUITING

Chu Toulouse

Toulouse, France

RECRUITING

Chru de Tours

Tours, France

RECRUITING

Ch Versailles

Versailles, France

RECRUITING

MeSH Terms

Conditions

Lymphoma, Follicular

Interventions

Surveys and Questionnaires

Condition Hierarchy (Ancestors)

Lymphoma, Non-HodgkinLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Data CollectionEpidemiologic MethodsInvestigative TechniquesHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public Health

Central Study Contacts

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
CROSS SECTIONAL
Target Duration
1 Day
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2022

First Posted

February 1, 2022

Study Start

April 19, 2022

Primary Completion

June 30, 2023

Study Completion

December 31, 2023

Last Updated

June 8, 2023

Record last verified: 2023-06

Locations