NCT05174338

Brief Summary

This registry is a observational, multi-center study designed to collect data and analyze it retrospectively on patients with cardiac amyloidosis who have been evaluated and treated at major amyloid centers across the US and internationally between 1997 and 2025.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
5,000

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jan 2020

Longer than P75 for all trials

Geographic Reach
2 countries

23 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 8, 2020

Completed
1.9 years until next milestone

First Submitted

Initial submission to the registry

December 13, 2021

Completed
17 days until next milestone

First Posted

Study publicly available on registry

December 30, 2021

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2025

Completed
Last Updated

September 6, 2023

Status Verified

September 1, 2023

Enrollment Period

5.9 years

First QC Date

December 13, 2021

Last Update Submit

September 1, 2023

Conditions

Outcome Measures

Primary Outcomes (2)

  • Quantify disease severity at diagnosis, progression and survival in patients with cardiac amyloidosis

    Clinical Outcomes: Disease severity at presentation, progression, and survival \[time frame 3 years\]. Severity and progression determined by change in NYHA Class, NT-ProBNP and troponin.

    1997 - 2025

  • Quantify incidence of complications from cardiac amyloidosis

    Determine incidence of arrhythmias (atrial fibrillation; ventricular arrhythmias) after diagnosis, renal dysfunction (rise in creatinine and development of end-stage renal disease), stroke, bleeding complications \[time frame 3 years\]

    1997 - 2025

Study Arms (1)

AL and TTR amyloidosis

immunoglobulin light chain amyloidosis (AL) and transthyretin amyloidosis (ATTR)

Other: Registry

Interventions

Observational, data collection

AL and TTR amyloidosis

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Established diagnosis of AL or TTR cardiomyopathy identified or treated

You may qualify if:

  • Established diagnosis of AL or TTR cardiomyopathy identified or treated within the timeframe
  • Specific to CSMC: If the individual provided consent while they were alive, and if sufficient information exists in their chart, their data will be included.
  • Information on deceased individuals may be included, but only with the appropriate approval from the external site IRB and/or according to the federal regulations for the protection of human subjects.

You may not qualify if:

  • At Cedars-Sinai, records that specifically state not to be used in research will not be accessed. Patients who have enacted a No Research Flag or are noted as "Break the Glass" will not be included. For external sites, records that indicate No Research Flag or are noted as "Break the Glass" may be included based on institutional policies and appropriate approvals, as applicable.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

University of Arizona Sarver Heart Center

Tucson, Arizona, 85724, United States

Location

UC San Diego Health, Sulpizio Cardiovascular Center

La Jolla, California, 92037, United States

Location

Scripps Health

La Jolla, California, 92137, United States

Location

University of California Davis

Sacramento, California, 95817, United States

Location

University of California, San Francisco

San Francisco, California, 94103, United States

Location

MedStar Health and Vascular Institute/Georgetown University School of Medicine

Washington D.C., District of Columbia, 20010, United States

Location

Johns Hopkins University School of Medicine

Baltimore, Maryland, 21287, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Washington University in St. Louis

St Louis, Missouri, 63110, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

Weill Cornell Medicine

New York, New York, 10021, United States

Location

The Mount Sinai Hospital

New York, New York, 10029, United States

Location

Columbia University Irving Medical Center, Clinical Cardiovascular Research Laboratory for the Elderly (CUMC/CCRLE)

New York, New York, 10032, United States

Location

Duke Health

Durham, North Carolina, 27710, United States

Location

Penn Presbyterian Medical Center

Philadelphia, Pennsylvania, 19104, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84112, United States

Location

University of Calgary

Calgary, Alberta, T2N 4Z6, Canada

Location

MeSH Terms

Conditions

Immunoglobulin Light-chain Amyloidosis

Interventions

Registries

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsAmyloidosisProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesLymphoproliferative DisordersImmunoproliferative DisordersImmune System DiseasesParaproteinemias

Intervention Hierarchy (Ancestors)

Data CollectionEpidemiologic MethodsInvestigative TechniquesRecordsOrganization and AdministrationHealth Services AdministrationHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public Health

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

December 13, 2021

First Posted

December 30, 2021

Study Start

January 8, 2020

Primary Completion

December 1, 2025

Study Completion

December 1, 2025

Last Updated

September 6, 2023

Record last verified: 2023-09

Data Sharing

IPD Sharing
Will share

The study design reflects IPD sharing between researchers based upon agrred set of data elements for study projects in the registry.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
Data will become available upon entry of IPD into the data base and will remain available for the duration of the study.
Access Criteria
Project participants will have access to IPD only relevant to their approved projects. project approval will be determined collectively by the PIs of all the participating sites.

Locations