NCT05093153

Brief Summary

Waldenström's macroglobulinemia (WM) is a B-cell lymphoproliferative disorder which is defined by bone marrow infiltration by small lymphocytes, lymphoplasmacytoid and plasma cells together with the presence of a detectable monoclonal immunoglobulin M (IgM).The clinical presentation of WM is variable. Symptoms can be related to tumor infiltration, or they can be related to the monoclonal IgM component. The therapeutic options are heterogeneous and there are no well-established in both first line or relapse/refractory settings. In Spain, the incidence of MGUS-IgM and WM in the last decade is unknown. The aims of this retrospective, observational, multicentric study is:

  • To develop a national registry of patients diagnosed with Waldenström's Macroglobulinemia and Monoclonal Gammopathy of uncertain significance -IgM in Spain in the past 30years.
  • To evaluate the most relevant clinical characteristics, long-term safety and efficacy of different therapeutic schemes and long-term prognosis of patients with WM
  • To help in the design of future therapeutic strategies, risk prognostic factors and clinical trials in Spain. Methods: The investigators will collect data from the patient clinical files after prior Informed Consent providing from patients with diagnosis of MGUS-IgM and WM in the past 30 years in Spain, according to the WHO classification of lymphoid tumors (2008) revised in 2016. Data from patients not able to provide IC (i.e., already dead patients) will be included only after the permission of the ethics review board. The collected data will be included in a database of the Spanish Myeloma and Lymphoma Intergroup (SMALI) team created ad-hoc by the Spanish Society of Hematology and Hemotherapy (SEHH). Each principal investigator in each center will conduct their technical supervision. The evaluation of the treatment protocols will be done following the indications of the intergroup committee according to the guidelines of the International Waldenström's Macroglobulinemia Group.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,000

participants targeted

Target at P75+ for all trials

Timeline
46mo left

Started Oct 2021

Longer than P75 for all trials

Geographic Reach
1 country

51 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress55%
Oct 2021Mar 2030

First Submitted

Initial submission to the registry

September 28, 2021

Completed
3 days until next milestone

Study Start

First participant enrolled

October 1, 2021

Completed
25 days until next milestone

First Posted

Study publicly available on registry

October 26, 2021

Completed
8.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2030

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2030

Last Updated

February 23, 2026

Status Verified

February 1, 2026

Enrollment Period

8.4 years

First QC Date

September 28, 2021

Last Update Submit

February 19, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall survival

    Overall survival evaluation from the date of diagnosis to the death of the patient due to any cause

    through study completion, an average of 4 years

Study Arms (1)

Waldenström's macroglobulinemia cohort patient

Adult patients diagnosed with Waldenström's Macroglobulinemia

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Patients diagnosed with Waldenström's Macroglobulinemia and Monoclonal Gammopathy of uncertain significance

You may qualify if:

  • Age ≥18 years
  • Patients having a confirmed diagnosis of either in the las 30 years:
  • Monoclonal Gammopathy of uncertain significance -IgM
  • Asymptomatic Waldenström's macroglobulinemia
  • Symptomatic Waldenström's macroglobulinemia

You may not qualify if:

  • Other subtypes of Lymphoproliferative diseases.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (51)

Hospital de Mérida

Mérida, Badajoz, 06800, Spain

RECRUITING

Hospital Son Llatzer

Palma, Balearic Islands, Spain

RECRUITING

Hospital Universitario Son Espases

Palma de Mallorca, Balearic Islands, Spain

RECRUITING

ICO Badalona - Hospital Germans Trias i Pujol

Badalona, Barcelona, Spain

RECRUITING

Hospital Mutua Terrassa

Barcelona, Barcelona, 08221, Spain

RECRUITING

Hospital de San Juan Despí Moisès Broggi

Barcelona, Barcelona, 08970, Spain

RECRUITING

Hospital Clínic de Barcelona

Barcelona, Barcelona, Spain

RECRUITING

Hospital del Mar

Barcelona, Barcelona, Spain

RECRUITING

Hospital Vall d'Hebron

Barcelona, Barcelona, Spain

RECRUITING

Hospital Sant Joan de Déu de Manresa

Manresa, Barcelona, Spain

RECRUITING

Hospital Parc Taulí

Sabadell, Barcelona, Spain

RECRUITING

Hospital Universitario Reina Sofía

Córdoba, Córdoba, Spain

RECRUITING

Hospital Virgen de las Nieves

Granada, Granada, 18014, Spain

RECRUITING

Hospital Universitario Clínico San Cecilio

Granada, Granada, Spain

RECRUITING

Hospital Juan Ramón Jiménez

Huelva, Huelva, 21005, Spain

RECRUITING

Complejo Hospitalario Universitario de La Coruña (CHUAC)

A Coruña, La Coruña, Spain

RECRUITING

Hospital San Pedro

Logroño, La Rioja, 26006, Spain

RECRUITING

Hospital Universitario de Gran Canaria Dr. Negrín

Las Palmas de Gran Canaria, Las Palmas, 35010, Spain

RECRUITING

Hospital Insular Materno Infantil- Gran Canaria

Las Palmas de Gran Canaria, Las Palmas, 35016, Spain

RECRUITING

CAU de León

León, León, Spain

RECRUITING

Hospital del Bierzo

Ponferrada, León, 24404, Spain

RECRUITING

Hospital Universitario Arnau de Vilanova

Lleida, Lleida, Spain

RECRUITING

Hospital Universitario Gregorio Marañón

Madrid, Madrid, 28007, Spain

RECRUITING

Hospital Universitario Infanta Leonor

Madrid, Madrid, 28031, Spain

RECRUITING

Hospital Central de La Defensa Gómez Ulla

Madrid, Madrid, 28040, Spain

RECRUITING

Hospital Clinico Universitario Santiago de Compostela

Madrid, Madrid, 28040, Spain

RECRUITING

Hospital de Laredo

Madrid, Madrid, 28040, Spain

RECRUITING

Hospital Marques de Valdecilla

Madrid, Madrid, 28040, Spain

RECRUITING

Hospital Rey Juan Carlos

Madrid, Madrid, 28040, Spain

RECRUITING

Hospital Universitario 12 de Octubre

Madrid, Madrid, 28041, Spain

RECRUITING

Hospital Universitario Fundación Jimenez Diaz

Madrid, Madrid, Spain

RECRUITING

Hospital Universitario Puerta de Hierro

Madrid, Madrid, Spain

RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, Madrid, Spain

RECRUITING

Hospital Santa Lucía de Cartagena

Cartagena, Murcia, 28040, Spain

RECRUITING

Hospital Clinico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

RECRUITING

Hospital Costa del Sol

Marbella, Málaga, Spain

RECRUITING

Hospital de la Serranía de Ronda

Málaga, Málaga, 29400, Spain

RECRUITING

Hospital Regional Universitario de Málaga

Málaga, Málaga, Spain

RECRUITING

Hospital Universitario Virgen de la Victoria

Málaga, Málaga, Spain

RECRUITING

CUN Navarra

Pamplona, Navarre, Spain

RECRUITING

Hospital Vital Álvarez-Buylla

Mieres, Principality of Asturias, Spain

RECRUITING

CAU de Salamanca

Salamanca, Salamanca, Spain

RECRUITING

Hospital Universitario Nuestra Señora de Candelaria

Santa Cruz de Tenerife, Santa Cruz de Tenerife, Spain

RECRUITING

Hospital Virgen de la Macarena

Seville, Sevilla, 41009, Spain

RECRUITING

Hospital Virgen de Valme

Seville, Sevilla, 41014, Spain

RECRUITING

Hospital Clínico de Valencia

Valencia, Valencia, Spain

RECRUITING

Hospital La Fe de Valencia

Valencia, Valencia, Spain

RECRUITING

Hospital Universitario Doctor Peset

Valencia, Valencia, Spain

RECRUITING

Hospital de Galdakao

Galdakao, Vizcaya, 48960, Spain

RECRUITING

Hospital Clínico Universitario Lozano Blesa

Zaragoza, Zaragoza, Spain

RECRUITING

Hospital Miguel Servet

Zaragoza, Zaragoza, Spain

RECRUITING

MeSH Terms

Conditions

Waldenstrom Macroglobulinemia

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Central Study Contacts

RAMON GARCIA SANZ, MD

CONTACT

ELHAM ASKARI ASKARI, MD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 28, 2021

First Posted

October 26, 2021

Study Start

October 1, 2021

Primary Completion (Estimated)

March 1, 2030

Study Completion (Estimated)

March 1, 2030

Last Updated

February 23, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will not share

Locations