NCT05067140

Brief Summary

A Phase 1/2 study to evaluate the safety and efficacy of ARV-766 given by mouth alone or in combination with abiraterone in men with metastatic prostate cancer.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
152

participants targeted

Target at P75+ for phase_1

Timeline
12mo left

Started Sep 2021

Longer than P75 for phase_1

Geographic Reach
1 country

23 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress84%
Sep 2021May 2027

Study Start

First participant enrolled

September 2, 2021

Completed
21 days until next milestone

First Submitted

Initial submission to the registry

September 23, 2021

Completed
12 days until next milestone

First Posted

Study publicly available on registry

October 5, 2021

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 25, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 25, 2027

Last Updated

May 5, 2026

Status Verified

April 1, 2026

Enrollment Period

5.7 years

First QC Date

September 23, 2021

Last Update Submit

April 30, 2026

Conditions

Keywords

Metastatic Prostate CancerCastrate-ResistantProstate CancermCRPC adenocarcinoma of prostateProstatic NeoplasmsGenital Neoplasms, MaleUrogenital NeoplasmsCastrate-SensitivemCSPC adenocarcinoma of prostate

Outcome Measures

Primary Outcomes (8)

  • Part A: Incidence of Dose Limiting Toxicities of ARV-766

    First Cycle Dose limiting toxicities characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), timing, seriousness, and relationship to study drug

    28 Days

  • Part A: Number of Patients with Adverse Events as a measure of safety and tolerability of ARV-766

    Adverse events as characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), timing, seriousness, and relationship to study drug.

    28 Days

  • Part A: Incidence of laboratory abnormalities as a measure of safety and tolerability of ARV-766

    Laboratory abnormalities as characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), and timing.

    28 Days

  • Part B: To evaluate the clinical anti-tumor activity of ARV-766 in patients with mCRPC

    Evaluate PSA in patients with mCRPC in both dose groups

    12 Weeks

  • Part C: Incidence of Dose Limiting Toxicities of ARV-766 / abiraterone combination

    First Cycle Dose limiting toxicities characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), timing, seriousness, and relationship to study drug

    28 Days

  • Part C: Incidence of laboratory abnormalities as a measure of safety and tolerability of ARV-766 / abiraterone combination

    Laboratory abnormalities as characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), and timing.

    28 Days

  • Part C: Number of Patients with Adverse Events as a measure of safety and tolerability of ARV-766 / abiraterone combination

    Adverse events as characterized by type, frequency, severity (as graded by NCI CTCAE v 5.0), timing, seriousness, and relationship to study drug.

    28 Days

  • Part D: To evaluate the clinical anti-tumor activity of ARV-766 / abiraterone combination in patients with NHA-naïve mPC

    Evaluate PSA in patients with NHA-naïve mPC

    12 Weeks

Study Arms (2)

ARV-766

EXPERIMENTAL

Oral tablets, once daily in 28 day cycles

Drug: ARV-766 Part A&B

ARV-766 + Abiraterone

EXPERIMENTAL

Oral tablets, once daily in 28 day cycles

Drug: ARV-766 + Abiraterone Part C&D

Interventions

Part A: Daily oral dosages are determined by cohort review committee after initial starting dose cohort and each subsequent cohort completes 28 days of treatment. Part B: Oral tablet(s) once daily in 28 day cycles.

ARV-766

Part C: Daily oral combination dosages are determined by cohort review committee after initial starting dose cohort and each subsequent cohort completes 28 days of treatment. Part D: Combination administered once daily in 28 day cycles. Parts C\&D: Participants will also receive concomitant corticosteroid and ADT therapy of investigator choice/patient preference

Also known as: Corticosteroid and ADT
ARV-766 + Abiraterone

Eligibility Criteria

Age18 Years+
Sexmale(Gender-based eligibility)
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Part A,B,C and D:
  • Histological, pathological, or cytological confirmed diagnosis of adenocarcinoma of the prostate.
  • Ongoing androgen deprivation therapy (ADT) with a gonadotropin releasing hormone analog or inhibitor, or orchiectomy (surgical or medical castration).
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
  • Part A:
  • Progression on at least 2 prior approved systemic therapies for metastatic prostate cancer (at least one must be a second-generation androgen inhibitor, e.g., abiraterone, enzalutamide, darolutamide, apalutamide).
  • Progressive mCRPC
  • Part B:
  • Participants must have received at least one but no more than three prior second generation anti-androgen agents (e.g., enzalutamide or abiraterone).
  • Participants must have received no more than two prior chemotherapy regimens.
  • Progressive mCRPC
  • Part C \& D:
  • Metastatic castration resistant or sensitive prostate cancer with radiographic evidence of metastatic disease

You may not qualify if:

  • Part A and B:
  • Known symptomatic brain metastases requiring steroids (above physiologic replacement doses).
  • Active inflammatory gastrointestinal disease, chronic diarrhea, known diverticular disease, or previous gastric resection or lap band surgery.
  • Radiation therapy within 4 weeks of first dose of study drug or prior irradiation to \>25% of the bone marrow.
  • Receipt of an investigational drug(s) within 4 weeks prior to anticipated first dose
  • Part C and D
  • Prior treatment with a second generation NHA

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Clinical Trial Site

Duarte, California, 91010, United States

Location

Clinical Trial Site

Fresno, California, 93720, United States

Location

Clinical Trial Site

La Jolla, California, 92037, United States

Location

Clinical Trial Site

Orange, California, 92868, United States

Location

Clinical Trial Site

Santa Monica, California, 90404, United States

Location

Clinical Trial Site

New Haven, Connecticut, 06510, United States

Location

Clinical Trial Site

Washington D.C., District of Columbia, 20007, United States

Location

Clinical Trial Site

Lake Mary, Florida, 32746, United States

Location

Clinical Trial Site

Chicago, Illinois, 60611, United States

Location

Clinical Trial Site

New Orleans, Louisiana, 70112, United States

Location

Clinical Trial Site

Baltimore, Maryland, 21204, United States

Location

Clinical Trial Site

Boston, Massachusetts, 02114, United States

Location

Clinical Trial Site

Detroit, Michigan, 48201, United States

Location

Clinical Trial Site

Buffalo, New York, 14203, United States

Location

Clinical Trial Site

New York, New York, 10065, United States

Location

Clinical Trial Site

Philadelphia, Pennsylvania, 19144, United States

Location

Clinical Trial Site

Pittsburgh, Pennsylvania, 15232, United States

Location

Clinical Trial Site

Myrtle Beach, South Carolina, 29572, United States

Location

Clinical Trial Site

Nashville, Tennessee, 37203, United States

Location

Clinical Trial Site

San Antonio, Texas, 78229, United States

Location

Clinical Trial Site

Charlottesville, Virginia, 22908, United States

Location

Clinical Trial Site

Fairfax, Virginia, 22031, United States

Location

Clinical Trial Site

Madison, Wisconsin, 53705, United States

Location

MeSH Terms

Conditions

Prostatic NeoplasmsGenital Neoplasms, MaleUrogenital Neoplasms

Interventions

Adrenal Cortex HormonesAndrogen Antagonists

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy Complications

Intervention Hierarchy (Ancestors)

HormonesHormones, Hormone Substitutes, and Hormone AntagonistsHormone AntagonistsPhysiological Effects of DrugsPharmacologic ActionsChemical Actions and Uses

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 23, 2021

First Posted

October 5, 2021

Study Start

September 2, 2021

Primary Completion (Estimated)

May 25, 2027

Study Completion (Estimated)

May 25, 2027

Last Updated

May 5, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations