NCT05061446

Brief Summary

The purpose of this Japan-only study is to assess the safety and efficacy of etrasimod at 2 doses in Japanese subjects with moderately to severely active ulcerative colitis (UC) when administered for 12 weeks.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
54

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Sep 2021

Geographic Reach
1 country

80 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 10, 2021

Completed
10 days until next milestone

First Submitted

Initial submission to the registry

September 20, 2021

Completed
9 days until next milestone

First Posted

Study publicly available on registry

September 29, 2021

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 6, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 6, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

October 29, 2024

Completed
Last Updated

October 29, 2024

Status Verified

October 1, 2024

Enrollment Period

2.1 years

First QC Date

September 20, 2021

Results QC Date

October 3, 2024

Last Update Submit

October 3, 2024

Conditions

Keywords

Ulcerative ColitisAPD334Etrasimod

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Who Achieved Clinical Remission at Week 12

    Clinical remission:Participants with stool frequency (SF)subscore=0(or of 1 with greater than or equal to(\>=)1 point decrease from baseline,rectal bleeding(RB)subscore=0 and endoscopic score(ES)less than or equal to(\<)=1(excluding friability).SF subscore:number of stools in 24-hours relative to normal number of stools for that participant in same period,score ranged from 0(normal number of stools) to 3(5 or more stools than normal),higher scores=more severity.RB subscore:most severe amount of blood passed per rectum in 24-hours,score ranged from 0(no blood seen)to 3(blood alone passes),higher scores=more severity.ES:reported worst appearance of mucosa on flexible sigmoidoscopy or colonoscopy,score ranged from 0(normal or inactive disease) to 3(severe disease \[spontaneous bleeding,ulceration\]),higher scores=more severity.Modified Mayo score:measure disease activity for UC,score:0(normal) to 9(maximum severity),comprised subscores for SF,RB,ES.higher score=more severe disease activity.

    Week 12

Secondary Outcomes (5)

  • Percentage of Participants Who Achieved Endoscopic Improvement at Week 12

    Week 12

  • Percentage of Participants Who Achieved Symptomatic Remission at Week 12

    Week 12

  • Percentage of Participants Who Achieved Mucosal Healing at Week 12

    Week 12

  • Percentage of Participants Who Achieved Clinical Response at Week 12

    Week 12

  • Percentage of Participants Who Achieved Endoscopic Normalization at Week 12

    Week 12

Other Outcomes (1)

  • Number of Participants With Adverse Events According to Severity

    Day 1 of first dose of study treatment up to 4 weeks after administration of the final dose of study treatment (maximum up to 16 weeks)

Study Arms (3)

Etrasimod Dose 1

EXPERIMENTAL
Drug: Etrasimod

Etrasimod Dose 2

EXPERIMENTAL
Drug: Etrasimod

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Etrasimod tablet by mouth, once daily for 12 weeks

Also known as: APD334
Etrasimod Dose 1

Etrasimod matching placebo tablet by mouth, once daily up to 12 weeks

Placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Japanese ancestry
  • Diagnosed with ulcerative colitis (UC) ≥ 3 months prior to screening
  • Having active UC confirmed by endoscopy
  • Moderately to severely active UC

You may not qualify if:

  • Severe extensive colitis
  • Diagnosis of Crohn's disease (CD) or indeterminate colitis or the presence, history of a fistula consistent with CD
  • Diagnosis of microscopic colitis, ischemic colitis, or infectious colitis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (80)

Aichi Medical University Hospital

Nagakute, Aichi-ken, 480-1195, Japan

Location

Kojunkai Daido Clinic

Nagoya, Aichi-ken, 457-8511, Japan

Location

Nagoya City University Hospital

Nagoya, Aichi-ken, 467-8602, Japan

Location

Fujita Health University Hospital

Toyoake, Aichi-ken, 470-1192, Japan

Location

Toyohashi Municipal Hospital

Toyohashi, Aichi-ken, 441-8570, Japan

Location

Kojunkai Daido Hospital

Nagoya, Aixhi-ken, 457-8511, Japan

Location

NHO Hirosaki General Medical Center

Hirosaki-shi, Aomori, 036-8545, Japan

Location

Hirosaki University Hospital(OCT/PFT/DLCO)

Hirosaki-shi, Aomori, 036-8563, Japan

Location

Hirosaki University Hospital

Hirosaki-shi, Aomori, 036-8563, Japan

Location

Tsujinaka Hospital Kashiwanoha

Kashiwa-shi, Chiba, 277-0871, Japan

Location

Ishii Eye Clinic

Nagareyama-shi, Chiba, 270-0116, Japan

Location

Toho University Sakura Medical Center

Sakura, Chiba, 285-8741, Japan

Location

Saiseikai Matsuyama Hospital

Matsuyama, Ehime, 791-8026, Japan

Location

Ehime University Hospital

Toon-shi, Ehime, 791-0295, Japan

Location

Fukuoka University Hospital

Fukuoka, Fukuoka, 814-0180, Japan

Location

Japan Community Health Care Organization Kyushu Hospital

Kitakyushu, Fukuoka, 806-8501, Japan

Location

Kokura Memorial Hospital

Kitakyushu-shi, Fukuoka, 802-8555, Japan

Location

Kitakyushu Municipal Medical Center

Kitakyushu-shi, Fukuoka, 802-8561, Japan

Location

Koyanose Eye Clinic

Kitakyushu-shi, Fukuoka, 807-1266, Japan

Location

Our Lady of the Snow St. Mary's Hospital

Kurume, Fukuoka, 830-8543, Japan

Location

Kurume University Hospital

Kurume-shi, Fukuoka, 830-0011, Japan

Location

Kokura Memorial Hospital

Kutakyushu-shi, Fukuoka, 802-8555, Japan

Location

Fukuoka Shinmizumaki Hospital

Onga-gun, Fukuoka, 807-0051, Japan

Location

Gifu University Hospital

Gifu, Gifu, 501-1194, Japan

Location

SUBARU Health Insurance Society Ota Memorial Hospital

Ota-shi, Gunma, 373-8585, Japan

Location

Nakayama EYE Clinic

Fukuyama-shi, Hiroshima, 720-0822, Japan

Location

NHO Fukuyama Medical Center

Fukuyama-shi, Hiroshima, 720-8520, Japan

Location

Hiroshima University Hospital

Hiroshima, Hiroshima, 734-8551, Japan

Location

Asahikawa City Hospital

Asahikawa-shi, Hokkaido, 070-8610, Japan

Location

Tokushukai Sapporo Tokushukai Hospital

Sapporo, Hokkaido, 004-0041, Japan

Location

Sapporo-Kosei General Hospital

Sapporo, Hokkaido, 060-0033, Japan

Location

NHO Mito Medical Center

Higashiibaraki-gun, Ibaraki, 311-3193, Japan

Location

Yuai Memorial Hospital

Koga-shi, Ibaraki, 306-0232, Japan

Location

Ibaraki Seinan Medical Center Hospital

Sashima-gun, Ibaraki, 306-0433, Japan

Location

Matsumoto Eye Clinic

Toride-shi, Ibaraki, 302-0014, Japan

Location

Tsuchiura Kyodo General Hospital

Tsuchiura-shi, Ibaraki, 300-0028, Japan

Location

NHO Kanazawa Medical Center

Kanazawa, Ishikawa-ken, 920-8650, Japan

Location

Kudo Internist Heart Clinic

Morioka, Iwate, 020-0871, Japan

Location

Iwate Medical University Uchimaru Medical Center

Morioka, Iwate, 020-8505, Japan

Location

Takamatsu Red Cross Hospital

Takamatsu, Kagawa-ken, 760-0017, Japan

Location

JA- Kagoshima Koseiren Hospital (PET/DLCO)

Kagoshima, Kagoshima-ken, 890-0062, Japan

Location

Clinical Pathology Laboratory (Diagnostick center)

Kagoshima, Kagoshima-ken, 892-0813, Japan

Location

Sameshima Eye Clinic (OCT)

Kagoshima, Kagoshima-ken, 892-0825, Japan

Location

Sameshima Hospital

Kagoshima, Kagoshima-ken, 892-0846, Japan

Location

Sagamihara Kyodo Hospital

Sagamihara, Kanagawa, 252-5188, Japan

Location

Social Welfare Organization Imperial Gift Foundation,Inc.Saiseikai Yokohamashi Nanbu Hospital

Yokohama, Kanagawa, 234-0054, Japan

Location

NHO Yokohama Medical Center

Yokohama, Kanagawa, 245-8575, Japan

Location

Japanese Red Cross Kumamoto Hospital

Kumamoto, Kumamoto, 861-8520, Japan

Location

University Hospital Kyoto Prefectural University of Medicine

Kyoto, Kyoto, 602-8566, Japan

Location

National Hospital Organization Kyoto Medical Center

Kyoto, Kyoto, 612-8555, Japan

Location

Mie University Hospital

Tsu, Mie-ken, 514-8507, Japan

Location

Hinaga Nishi Ophthalmology Clinic

Yokkaichi- Shi, Mie-ken, 510-0891, Japan

Location

Mie Prefectural General Medical Center

Yokkaichi-shi, Mie-ken, 510-8561, Japan

Location

Tohoku University Hospital

Sendai, Miyagi, 980-8574, Japan

Location

JOHAS Tohoku Rosai Hospital

Sendai, Miyagi, 981-8563, Japan

Location

Nagaoka Red Cross Hospital

Nagaoka-shi, Niigata, 940-2085, Japan

Location

Kansai Medical University Hospital

Hirakata-shi, Osaka, 573-1191, Japan

Location

Medical Corporation Tokushukai Kishiwada Tokushukai Hospital

Kishiwada-shi, Osaka, 596-0042, Japan

Location

Osaka City University Hospital

Osaka, Osaka, 545-8586, Japan

Location

Japan Community Health care Organization Osaka Hospital

Osaka, Osaka, 553-0003, Japan

Location

Osaka Medical and Pharmaceutical University Hospital

Takatsuki, Osaka, 569-8686, Japan

Location

Saga University Hospital

Saga, Saga-ken, 849-8501, Japan

Location

Saitama Medical University Hospital

Iruma-gun, Saitama, 350-0495, Japan

Location

Japan Community Health care Organization Saitama Medical Center

Saitama-shi, Saitama, 330-0074, Japan

Location

Shiga University of Medical Science Hospital

Ōtsu, Shiga, 520-2192, Japan

Location

Hamamatsu University Hospital

Hamamatsu, Shizuoka, 431-3192, Japan

Location

Matsuda Hospital

Hamamatsu, Shizuoka, 432-8061, Japan

Location

Hamamatsu Medical Centre

Hamamatsu, Shizuoka, 432-8580, Japan

Location

Tokyo Medical and Dental University Hospital

Bunkyo-ku, Tokyo, 113-8519, Japan

Location

Tokai University Hachioji Hospital

Hachiōji, Tokyo, 192-0032, Japan

Location

Showa General Hospital

Kodaira-shi, Tokyo, 187-8510, Japan

Location

Kitasato University Kitasato Institute Hospital

Minato-ku, Tokyo, 108-8642, Japan

Location

JCHO Tokyo Yamate Medical Center

Shinjuku-ku, Tokyo, 169-0073, Japan

Location

Wakayama Medical University Hospital

Wakayama, Wakayama, 641-8510, Japan

Location

Yamanashi Prefectural Central Hospital

Kofu, Yamanashi, 400-8506, Japan

Location

Fukushima Medical University Hospital

Fukushima, 960-1295, Japan

Location

Kagoshima University Hospital

Kagoshima, 890-8520, Japan

Location

NHO Osaka National Hospital

Osaka, 540-0006, Japan

Location

Osaka National Hospital Institutional Review Board

Osaka, 540-0006, Japan

Location

Teikyo University Hospital

Tokyo, 173-8606, Japan

Location

Related Publications (1)

  • Takeuchi K, Nakase H, Hisamatsu T, Matsuoka K, Arai S, Yuasa H, Oe M, Ono R, Keating M, Gu G, Lazin K, McDonnell A, Fukuta K, Hibi T. Efficacy and safety of etrasimod in Japanese patients with ulcerative colitis: results from a phase 2 dose-ranging study. Intest Res. 2025 Apr 25. doi: 10.5217/ir.2024.00213. Online ahead of print.

Related Links

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

etrasimod

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 20, 2021

First Posted

September 29, 2021

Study Start

September 10, 2021

Primary Completion

October 6, 2023

Study Completion

October 6, 2023

Last Updated

October 29, 2024

Results First Posted

October 29, 2024

Record last verified: 2024-10

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations