NCT04960579

Brief Summary

Phase 1 study comprised of open-label, dose escalation, multiple cohorts of P-BCMA-ALLO1 allogeneic T stem cell memory (Tscm) CAR-T cells in subjects with relapsed / refractory Multiple Myeloma (RRMM).

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
275

participants targeted

Target at P75+ for phase_1 multiple-myeloma

Timeline
192mo left

Started May 2022

Longer than P75 for phase_1 multiple-myeloma

Geographic Reach
1 country

23 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress20%
May 2022Mar 2042

First Submitted

Initial submission to the registry

June 24, 2021

Completed
20 days until next milestone

First Posted

Study publicly available on registry

July 14, 2021

Completed
10 months until next milestone

Study Start

First participant enrolled

May 5, 2022

Completed
6.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2029

Expected
13 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2042

Last Updated

April 24, 2026

Status Verified

April 1, 2026

Enrollment Period

6.8 years

First QC Date

June 24, 2021

Last Update Submit

April 22, 2026

Conditions

Outcome Measures

Primary Outcomes (3)

  • Phase 1 Part 1: Assess the safety and maximum tolerated dose (MTD) of P-BCMA-ALLO1 based on dose limiting toxicities (DLT)

    Rate of dose limiting toxicities (DLT)

    Baseline through Day 28

  • Phase 1 Part 2: Assess the safety and tolerability of P-BCMA-ALLO1 when administered as a fixed dose of cells.

    Frequency and severity of adverse events, including cytokine release syndrome.

    Baseline through 36 months

  • Phase 1b: The effect of cell dose and study arm

    Overall response rate (ORR) based on International Myeloma Working Group (IMWG) uniform response criteria

    Baseline through 36 months

Secondary Outcomes (3)

  • The safety of P-BCMA-ALLO1

    Baseline through 15 years

  • The anti-myeloma effect of P-BCMA-ALLO1 (ORR) in Phase 1 Parts 1 and 2

    Baseline through 15 years

  • Safety and Efficacy (anti-myeloma effect) will be used to guide the selection of RP2D

    Baseline through 15 years

Study Arms (18)

P-BCMA-ALLO1 CAR-T cells (Arm S)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen S. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm F)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen F. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm N)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm P1)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen P1. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm P2)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen P2. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm R)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen R. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm RS)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen RS. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm C)

EXPERIMENTAL

Cyclic weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen C. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm160)

EXPERIMENTAL

Single fixed dose IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen S, P1, P1.5 or P2. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm480)

EXPERIMENTAL

Single fixed dose IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen S, P1, P1.5 or P2. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm P1.5)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen P1.5. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm RP1)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen RP1. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm RP1.5)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen RP1.5. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm RP2)

EXPERIMENTAL

Single weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen RP2. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm CP1)

EXPERIMENTAL

Cyclic weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen CP1. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm CP1.5)

EXPERIMENTAL

Cyclic weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen CP1.5. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm CP2)

EXPERIMENTAL

Cyclic weight-based IV administration of P-BCMA-ALLO1 following conditioning chemotherapy regimen CP2. Rimiducid may be administered as indicated.

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: Rimiducid

P-BCMA-ALLO1 CAR-T cells (Arm MP1.5)

EXPERIMENTAL

Single weight based IV administration of P-BCMA-ALLO1 and methotrexate following conditioning chemotherapy regimen MP1.5 Rimiducid may be administered as indicated

Biological: P-BCMA-ALLO1 CAR-T cellsDrug: RimiducidDrug: Methotrexate

Interventions

Allogeneic BCMA-targeted chimeric antigen receptor (CAR) T-cell therapy

P-BCMA-ALLO1 CAR-T cells (Arm C)P-BCMA-ALLO1 CAR-T cells (Arm CP1)P-BCMA-ALLO1 CAR-T cells (Arm CP1.5)P-BCMA-ALLO1 CAR-T cells (Arm CP2)P-BCMA-ALLO1 CAR-T cells (Arm F)P-BCMA-ALLO1 CAR-T cells (Arm MP1.5)P-BCMA-ALLO1 CAR-T cells (Arm N)P-BCMA-ALLO1 CAR-T cells (Arm P1)P-BCMA-ALLO1 CAR-T cells (Arm P1.5)P-BCMA-ALLO1 CAR-T cells (Arm P2)P-BCMA-ALLO1 CAR-T cells (Arm R)P-BCMA-ALLO1 CAR-T cells (Arm RP1)P-BCMA-ALLO1 CAR-T cells (Arm RP1.5)P-BCMA-ALLO1 CAR-T cells (Arm RP2)P-BCMA-ALLO1 CAR-T cells (Arm RS)P-BCMA-ALLO1 CAR-T cells (Arm S)P-BCMA-ALLO1 CAR-T cells (Arm160)P-BCMA-ALLO1 CAR-T cells (Arm480)

Safety switch activator

P-BCMA-ALLO1 CAR-T cells (Arm C)P-BCMA-ALLO1 CAR-T cells (Arm CP1)P-BCMA-ALLO1 CAR-T cells (Arm CP1.5)P-BCMA-ALLO1 CAR-T cells (Arm CP2)P-BCMA-ALLO1 CAR-T cells (Arm F)P-BCMA-ALLO1 CAR-T cells (Arm MP1.5)P-BCMA-ALLO1 CAR-T cells (Arm N)P-BCMA-ALLO1 CAR-T cells (Arm P1)P-BCMA-ALLO1 CAR-T cells (Arm P1.5)P-BCMA-ALLO1 CAR-T cells (Arm P2)P-BCMA-ALLO1 CAR-T cells (Arm R)P-BCMA-ALLO1 CAR-T cells (Arm RP1)P-BCMA-ALLO1 CAR-T cells (Arm RP1.5)P-BCMA-ALLO1 CAR-T cells (Arm RP2)P-BCMA-ALLO1 CAR-T cells (Arm RS)P-BCMA-ALLO1 CAR-T cells (Arm S)P-BCMA-ALLO1 CAR-T cells (Arm160)P-BCMA-ALLO1 CAR-T cells (Arm480)

Anti-metabolite

P-BCMA-ALLO1 CAR-T cells (Arm MP1.5)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have signed written, informed consent.
  • Males or females, ≥18 years of age.
  • Must have a confirmed diagnosis of active MM.
  • Must have measurable MM.
  • Must have relapsed / refractory MM, having received treatment with a proteasome inhibitor, immunomodulatory agent (IMiD), and anti-CD38 therapy.
  • Must be willing to practice birth control from the time of Screening and throughout the first year of the study after P-BCMA-ALLO1 administration.
  • Must have a negative serum pregnancy test at Screening and a negative urine pregnancy test within 3 days prior to initiating the lymphodepletion therapy regimen (females of childbearing potential).
  • Must be at least 90 days since autologous stem cell transplant, if performed.
  • Must have adequate vital organ function within pre-determined parameters.
  • Must have recovered from toxicities due to prior therapies.
  • Must have an Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 1.

You may not qualify if:

  • Is pregnant or lactating.
  • Has inadequate venous access.
  • Has active hemolytic anemia, plasma cell leukemia, Waldenstrom\'s macroglobulinemia, POEMS syndrome, disseminated intravascular coagulation, leukostasis, or amyloidosis.
  • Has an active second malignancy (not disease-free for at least 5 years) in addition to MM, excluding low-risk neoplasms such as non-metastatic basal cell or squamous cell skin carcinoma.
  • Has active autoimmune disease.
  • Has a history of significant central nervous system (CNS) disease, such as stroke, epilepsy, etc.
  • Has an active systemic infection.
  • Has a history of hepatitis B, hepatitis C virus, human immunodeficiency virus (HIV), or human T-lymphotropic virus (HTLV) infection, or any immunodeficiency syndrome. Subjects with a history of treated hepatitis C can be enrolled if negative by Hepatitis C PCR on multiple occasions.
  • Is positive for cytomegalovirus (CMV) by PCR, CMV immunoglobulin M (IgM) antibody, or Coronavirus disease 2019 (COVID-19) by PCR.
  • Has New York Heart Association (NYHA) Class III or IV heart failure, unstable angina, or a history of myocardial infarction or significant arrhythmia.
  • Has any psychiatric or medical disorder that would preclude safe participation in and/or adherence to the protocol.
  • Has received prior allogeneic cellular therapy or gene therapy.
  • Has received anti-cancer medications within 2 weeks of the time of initiating conditioning LD therapy.
  • Has received monoclonal antibody therapy within 4 weeks of initiating conditioning LD therapy.
  • Has received immunosuppressive medications within 2 weeks of the time of administration of P-BCMA-ALLO1, and/or expected to require them while on study.
  • +7 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

City of Hope

Goodyear, Arizona, 85338, United States

Location

University of California San Diego

San Diego, California, 92093, United States

Location

University of California San Francisco

San Francisco, California, 94143, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Blood Marrow and Transplant Group of Georgia

Atlanta, Georgia, 30342, United States

Location

City of Hope

Chicago, Illinois, 60099, United States

Location

Advocate Aurora Health

Park Ridge, Illinois, 66068, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Maryland Greenebaum Comprehensive Cancer Center

Baltimore, Maryland, 21201, United States

Location

Wayne State - Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Hackensack Meridian Health

Hackensack, New Jersey, 07601, United States

Location

Roswell Park Comprehensive Cancer Center

Buffalo, New York, 14263, United States

Location

Mount Sinai

New York, New York, 10029, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599-1350, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45221, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

University of Oklahoma, Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104-4238, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Sarah Cannon Research Institute - St. David's South Austin Medical Center

Austin, Texas, 78704, United States

Location

Houston Methodist Research Institute

Houston, Texas, 77030, United States

Location

Sarah Cannon Research Institute - Methodist Healthcare

San Antonio, Texas, 78229, United States

Location

Related Publications (1)

  • Tseng H, Dholaria B, Cranert SA, Richter M, Marquez KS, Cho BS, Bacong A, McArthur K, Eskew JD, McCaigue J, Haag S, Krasny A, Solimine B, Coffey MJ, Loyola A, Kwong J, Shune L, Kin A, Costello CL, Kocoglu MH, Ramakrishnan A, Namini H, Martin CE, Belani R, Coronella J, Shedlock DJ. TSCM-predominant allogeneic anti-BCMA CAR-T therapy for relapsed/refractory multiple myeloma: preclinical characterization and interim results from a phase 1 trial. Nat Commun. 2025 Nov 24;16(1):10050. doi: 10.1038/s41467-025-65267-0.

MeSH Terms

Conditions

Multiple Myeloma

Interventions

Methotrexate

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

AminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Study Officials

  • Maika Onishi, M.D.

    Senior Medical Director

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 24, 2021

First Posted

July 14, 2021

Study Start

May 5, 2022

Primary Completion (Estimated)

March 1, 2029

Study Completion (Estimated)

March 1, 2042

Last Updated

April 24, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations