NCT04957758

Brief Summary

The objective of this study is to evaluate the safety and effectiveness of OC-01 (varenicline) nasal spray as compared to placebo nasal spray for mean change from baseline in corneal fluorescein staining in subjects with Stage 1 (corneal epithelial hyperplasia/punctate keratopathy) neurotrophic keratopathy (NK) in one or both eyes.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
113

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jun 2021

Geographic Reach
1 country

31 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 17, 2021

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

June 28, 2021

Completed
14 days until next milestone

First Posted

Study publicly available on registry

July 12, 2021

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 27, 2023

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 28, 2023

Completed
1 year until next milestone

Results Posted

Study results publicly available

May 7, 2024

Completed
Last Updated

May 7, 2024

Status Verified

March 1, 2024

Enrollment Period

1.6 years

First QC Date

June 28, 2021

Results QC Date

March 8, 2024

Last Update Submit

April 11, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline in Corneal Fluorescein Staining

    Corneal Fluorescein Staining was measured utilizing the Modified Oxford Grading scale. Scores range from a minimum of 0 (no staining) to a maximum of 5. A higher score indicates a worse outcome. The study eye is defined as the eye with the worst staining grade (if both eyes are eligible).

    8 weeks

Secondary Outcomes (1)

  • Mean Change From Baseline in Visual Acuity at Week 8

    8 weeks

Study Arms (2)

OC-01 (varenicline) nasal spray, 1.2 mg/mL

ACTIVE COMPARATOR

OC-01 (varenicline) nasal spray, 1.2 mg/mL

Drug: OC-01 (varenicline) nasal spray 1.2 mg/ml

Placebo (vehicle control) nasal spray

PLACEBO COMPARATOR

Placebo (vehicle control) nasal spray

Drug: Placebo (vehicle) nasal spray

Interventions

OC-01

OC-01 (varenicline) nasal spray, 1.2 mg/mL

Placebo (vehicle)

Placebo (vehicle control) nasal spray

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Be at least 18 years of age at Visit 1.
  • Patients with Stage 1 (corneal epithelial hyperplasia/punctate keratopathy) NK in one or both eyes, as defined by the Mackie Criteria.
  • Evidence of decreased corneal sensitivity (≤ 4 cm using the Cochet-Bonnet aesthesiometer) in at least 1 corneal quadrant.
  • Schirmer's test without anesthesia ≥3 mm/ 5 minutes in the affected eye.
  • If a female is of childbearing potential, they must: use an acceptable means of birth control (acceptable methods of contraception include hormonal - oral, implantable, injectable, or transdermal contraceptives, mechanical - spermicide in conjunction with a barrier such as a diaphragm or condom, IUD, or surgical sterilization of partner), and have a negative urine pregnancy test on Day 1.

You may not qualify if:

  • Have Stage 2 or Stage 3 NK affecting one or both eyes.
  • Have ocular graft versus host disease or Stevens-Johnson syndrome.
  • Have any active ocular infection (COVID-19 conjunctivitis, bacterial, viral, fungal, or protozoal) or active ocular inflammation not related to NK in the affected eye.
  • Be currently receiving autologous serum tears, amniotic membrane, cenegermin, fresh frozen plasma or cord blood derivative tears.
  • Have severe blepharitis and/or severe meibomian gland disease in the study eye.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (31)

Dothan Alabama

Dothan, Alabama, 36301, United States

Location

Irvine, California

Irvine, California, 92697, United States

Location

Los Angeles California

Los Angeles, California, 90095, United States

Location

Mission Hills California

Mission Hills, California, 91345, United States

Location

Aurora Colorado

Aurora, Colorado, 80045, United States

Location

Littleton, Colorado

Littleton, Colorado, 80120, United States

Location

Longmont, Colorado

Longmont, Colorado, 80503, United States

Location

Danbury, Connecticut

Danbury, Connecticut, 06810, United States

Location

Brandon Florida

Brandon, Florida, 33511, United States

Location

Brandon, Florida

Brandon, Florida, 33511, United States

Location

Jacksonville Florida

Jacksonville, Florida, 32256, United States

Location

Miami Florida

Miami, Florida, 33136, United States

Location

Atlanta, Georgia

Atlanta, Georgia, 30339, United States

Location

Hoffman Estates, Illinois

Hoffman Estates, Illinois, 60169, United States

Location

Urbana Illinois

Urbana, Illinois, 61801, United States

Location

Union Kentucky

Edgewood, Kentucky, 41017, United States

Location

Louisville KY

Louisville, Kentucky, 40206, United States

Location

Bowie, Maryland

Bowie, Maryland, 20716, United States

Location

Boston Massachusetts

Boston, Massachusetts, 02114, United States

Location

Kansas City Missouri

Kansas City, Missouri, 64111, United States

Location

Henderson Nevada

Henderson, Nevada, 89052, United States

Location

Bloomfield, New Jersey

Bloomfield, New Jersey, 07003, United States

Location

Dover New Jersey

Dover, New Jersey, 07801, United States

Location

Babylon New York

Babylon, New York, 11702, United States

Location

New York NY

New York, New York, 10029, United States

Location

York, Pennsylvania

York, Pennsylvania, 17408, United States

Location

Houston Texas

Houston, Texas, 77030, United States

Location

Katy, Texas

Katy, Texas, 77494, United States

Location

San Antonio Texas

San Antonio, Texas, 78229, United States

Location

Lynchburg Virginia

Lynchburg, Virginia, 24502, United States

Location

Seattle Washington

Seattle, Washington, 98119, United States

Location

MeSH Terms

Interventions

VareniclineNasal Sprays

Intervention Hierarchy (Ancestors)

BenzazepinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsQuinoxalinesAerosolsColloidsComplex MixturesDosage FormsPharmaceutical Preparations

Results Point of Contact

Title
Marian Macsai, MD
Organization
Oyster Point Pharma Inc

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 28, 2021

First Posted

July 12, 2021

Study Start

June 17, 2021

Primary Completion

January 27, 2023

Study Completion

April 28, 2023

Last Updated

May 7, 2024

Results First Posted

May 7, 2024

Record last verified: 2024-03

Locations