NCT04933552

Brief Summary

This study will utilize a prospective, observational, exposure cohort design to examine pregnancy and infant outcomes in women and infants who are exposed to siponimod during pregnancy to treat MS.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
867

participants targeted

Target at P75+ for all trials

Timeline
74mo left

Started Dec 2021

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress42%
Dec 2021May 2032

First Submitted

Initial submission to the registry

June 18, 2021

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 21, 2021

Completed
6 months until next milestone

Study Start

First participant enrolled

December 15, 2021

Completed
10.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2032

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 31, 2032

Last Updated

May 16, 2024

Status Verified

May 1, 2024

Enrollment Period

10.5 years

First QC Date

June 18, 2021

Last Update Submit

May 14, 2024

Conditions

Keywords

Multiple SclerosisMSPASSPost-Authorization Safety StudyMayzentSiponimodPregnancy

Outcome Measures

Primary Outcomes (1)

  • Prevalence of major structural defects

    A major structural defect is defined as a defect that has either cosmetic or functional significance to the child (e.g., a cleft lip).

    Up to 10,5 years

Secondary Outcomes (10)

  • Number of spontaneous abortion/miscarriage

    Up to 10,5 years

  • Number of stillbirth

    Up to 10,5 years

  • Number of elective termination

    Up to 10,5 years

  • Number of premature delivery

    Up to 10,5 years

  • Number of preeclampsia / eclampsia

    Up to 1 10,5 years

  • +5 more secondary outcomes

Study Arms (3)

Siponimod-Exposed

Pregnant women with MS exposed to siponimod during pregnancy

Other: Siponimod

Disease-Matched Comparison

Pregnant women with MS not exposed to siponimod during pregnancy

Healthy Comparison

Pregnant women who are neither diagnosed with MS nor with any other autoimmune disease, and not exposed to siponimod or any known teratogenic agent during pregnancy

Interventions

Prospective observational cohort study. There is no treatment allocation. Patients administered siponimod, that have started before inclusion of the patient into the study will be enrolled.

Also known as: Mayzent
Siponimod-Exposed

Eligibility Criteria

Sexfemale(Gender-based eligibility)
Gender Eligibility DetailsThe study population includes pregnant women.
Healthy VolunteersYes
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

The study population includes pregnant women who reside in the US or Canada.

You may qualify if:

  • Participants must meet all the criteria listed under the respective cohorts to enroll in that particular cohort of the registry:
  • Cohort 1: Siponimod-Exposed Cohort
  • Pregnant women
  • Diagnosed with MS, with the indication validated by medical records when possible
  • Exposure to siponimod for the treatment of MS, for any number of days, at any dose, and at any time from the 4th day post the first day of LMP prior to conception up to and including the end of pregnancy
  • Agree to the conditions and requirements of the study including the interview schedule, release of medical records, the dysmorphology examination of live born infants, and the Ages and Stages Questionnaire (ASQ) in live born children
  • Cohort 2: Disease-Matched Comparison Cohort (Comparison Group 1)
  • Pregnant women
  • Diagnosed with MS, with the indication validated by medical records when possible
  • May or may not have taken another medication for MS in the current pregnancy
  • Agree to the conditions and requirements of the study including the interview schedule, release of medical records, the dysmorphology examination of live born infants, and the ASQ in live born children
  • Cohort 3: Healthy Comparison Cohort (Comparison Group 2):
  • Pregnant women
  • Agree to the conditions and requirements of the study including the interview schedule, release of medical records, the dysmorphology examination of live born infants, and the ASQ in live born children

You may not qualify if:

  • Women meeting any of the following criteria will be excluded from the cohort study:
  • Cohort 1: Siponimod-Exposed Cohort
  • Women who have enrolled in the siponimod cohort study with a previous pregnancy
  • Women who have used siponimod for an indication other than a currently approved indication
  • Women with exposure to any of the following medications within 5 half-lives prior to conception:
  • Cladribine (Mavenclad)
  • Based on the US label, animal studies indicate that there is positive evidence of teratogenicity for Cladribine
  • All other S1P modulators including fingolimod (Gilenya), ozanimod, etc.
  • S1P modulatros are in the same class of drug as siponimod
  • Teriflunomide (Aubagio)
  • The teratogenicity of teriflunomide is unknown and currently under investigation
  • Other anti-CD20 monoclonal antibody: same class as Kesimpta
  • Retrospective enrollment after the outcome of pregnancy is known (i.e. the pregnancy has ended prior to enrollment)
  • Results of a diagnostic test are positive for a major structural defect prior to enrollment. However, women who have had any normal or abnormal prenatal screening or diagnostic test prior to enrollment are eligible as long as the test result does not indicate a major structural defect.
  • Cohort 2: Disease-Matched Comparison Cohort (Comparison Group 1):
  • +18 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Novartis Investigative Site

La Jolla, California, 92093-0934, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Multiple Sclerosis

Interventions

siponimod

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 18, 2021

First Posted

June 21, 2021

Study Start

December 15, 2021

Primary Completion (Estimated)

May 31, 2032

Study Completion (Estimated)

May 31, 2032

Last Updated

May 16, 2024

Record last verified: 2024-05

Data Sharing

IPD Sharing
Will not share

Locations