NCT04906421

Brief Summary

This is a Phase 2, multi-center, double-blind, randomized, placebo-controlled study to evaluate the safety and efficacy on TVB-2640 in subjects with non-alcoholic steatohepatitis (NASH). Subjects will be randomly assigned toTVB-2640 or matching placebo PO QD for 52 weeks, with the first dose administered on Day 1.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
168

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2021

Geographic Reach
4 countries

117 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 20, 2021

Completed
8 days until next milestone

First Posted

Study publicly available on registry

May 28, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

August 12, 2021

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 2, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 2, 2023

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

May 9, 2025

Completed
Last Updated

May 9, 2025

Status Verified

April 1, 2025

Enrollment Period

2.1 years

First QC Date

May 20, 2021

Results QC Date

April 28, 2025

Last Update Submit

April 28, 2025

Conditions

Keywords

NASHNonalcoholic SteatohepatitisFatty Liver DiseaseBiopsy ConfirmedFASNFatty LiverLiver DiseaseDigestive System DiseasesMASHMetabolic dysfunction-associated steatohepatitis

Outcome Measures

Primary Outcomes (2)

  • Histological Improvement in Nonalcoholic Fatty Liver Disease (NAFLD) Activity Score (NAS) Without Worsening of Fibrosis (by NASH Clinical Research Network [CRN] Fibrosis Score).

    Histological improvement is defined as ≥2 points improvement in NAS with ≥1 point improvement in ballooning or inflammation

    52 Weeks

  • Subjects With Resolution of Steatohepatitis and No Worsening of Liver Fibrosis by NASH CRN Fibrosis Score and Histological Improvement in NAS.

    NASH resolution defined as absence of fatty liver disease or isolated or simple steatosis without steatohepatitis and a score of either 0 or 1 for inflammation, 0 for ballooning and any value for steatosis and no worsening of liver fibrosis (by NASH CRN fibrosis score). Histological improvement defined as ≥2 point improvement in NAS (with ≥1 point improvement in ballooning or inflammation).

    52 Weeks

Secondary Outcomes (4)

  • Proportion of Subjects Experiencing Fibrosis Improvement of ≥1 Stage by NASH CRN Score Without Worsening of Steatohepatitis

    52 Weeks

  • Proportion of Subjects Experiencing Resolution of Steatohepatitis and no Worsening of Liver Fibrosis (by NASH CRN Fibrosis Score)

    52 Weeks

  • Proportion of Subjects With Improvement in Liver Fibrosis >=1 Stage by NASH CRN Fibrosis Score Without Worsening of Steatohepatitis at 52 Weeks OR Resolution of Steatohepatitis and No Worsening of Liver Fibrosis by NASH CRN Fibrosis Score

    52 Weeks

  • Proportion of MRI-PDFF ≥30% Responders.

    52 Weeks

Study Arms (2)

TVB-2640 50 mg

EXPERIMENTAL

Subjects will receive TVB-2640 PO QD for 52 weeks, with the first dose administered on Day 1.

Drug: TVB-2640

Placebo

PLACEBO COMPARATOR

Subjects will receive matching placebo PO QD for 52 weeks, with the first dose administered on Day 1.

Other: Placebo

Interventions

Oral dose, tablet

TVB-2640 50 mg
PlaceboOTHER

Oral dose, tablet

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must be willing and able to participate in the study and provide written informed consent.
  • Male and female adults ≥18 years of age on the date that written informed consent to take part in the study is provided.
  • Body mass index (BMI) ≥23 kg/m2 for Asians and ≥25 kg/m2 for other races.
  • Female subjects must be either:
  • Not of childbearing potential OR
  • Women of childbearing potential (WOCBP) must have a negative serum pregnancy (beta-human chorionic gonadotropin \[β-HCG\]) test during Screening, a negative urine pregnancy test within 24 hours before the first dose of study drug on Day 1, and must agree to perform urine home pregnancy tests monthly between study visits. WOCBP must not be breastfeeding, not plan to become pregnant during the study, and must use birth control.
  • Must have liver stiffness measurement ≥8.5 kPa measured by FibroScan and CAP score measured by FibroScan ≥280 dB/m during the Screening period.
  • Histologic confirmation of NASH: must have had prior liver biopsy within 180 days before randomization (randomization is within 24 hours of Baseline \[Day1\]) with fibrosis stage F2-F3 and a NAS of ≥4 with at least a score of 1 in each of the following NAS components: steatosis, ballooning degeneration, and lobular inflammation.

You may not qualify if:

  • History of harmful alcohol intake for a period of more than 3 consecutive months within 1 year prior to Screening in the judgement of the Investigator.
  • Active substance abuse.
  • Gain or loss of \>5% of body weight in the 6 months prior to Baseline (Day 1) or \>10% of body weight in the 12 months prior to Screening.
  • Type 1 diabetes mellitus by history.
  • Uncontrolled T2DM, defined as HbA1c ≥9.5% at Screening.
  • Presence of cirrhosis on liver histology (stage 4 fibrosis), according to the judgement of the central reader, and/or cross sectional imaging evidence consistent with cirrhosis and/or portal hypertension.
  • Use of glucagon-like peptide-1 (GLP-1) agonists or a sodium-glucose co-transporter-2 (SGLT2) inhibitor, unless on a stable daily dose for at least 6 months prior to the Screening visit date, or on a complex oral anti-diabetic (OAD) regimen (3 or more OADs \[except for a GLP-1 agonist or an SGLT2 inhibitor\]), unless on a stable dose for at least 3 months prior to the Screening visit date.
  • Subjects with active or quiescent chronic liver disease of etiologies other than NASH (eg, viral or autoimmune hepatitis, primary sclerosing cholangitis, primary biliary cholangitis, and 'autoimmune hepatitis-overlap' syndromes, hemochromatosis, Wilson's disease, alpha 1 antitrypsin deficiency, alcohol-related liver disease, drug-induced liver disease, and/or infiltrative conditions \[eg, sarcoidosis\]).
  • Current or historic clinically evident hepatic decompensation event (eg, ascites formation, variceal hemorrhage, hepatic encephalopathy).
  • Any subject who has sustained a clinically evident cardiovascular, cerebrovascular, and/or peripheral vascular event during the 12 months prior to anticipated Baseline (Day 1) visit date is not eligible for study participation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (117)

North Alabama Health Research

Huntsville, Alabama, 35801, United States

Location

North Alabama GI Research Center

Madison, Alabama, 35758, United States

Location

GI Alliance Arizona Digestive Health-Sun City

Sun City, Arizona, 85351, United States

Location

ARcare Center for Clinical Research, LLC - Conway

Conway, Arkansas, 72032, United States

Location

Arkansas Diagnostic Center

Little Rock, Arkansas, 72205, United States

Location

Liver Wellness Center

Little Rock, Arkansas, 72205, United States

Location

Citrus Valley Gastroenterology

Covina, California, 91723, United States

Location

UCSD, NAFLD Research Center / Altman Clinical and Translational Research Institute

La Jolla, California, 92093, United States

Location

Om Research LLC

Lancaster, California, 93534, United States

Location

Clinical Trials Research

Lincoln, California, 95648, United States

Location

Digestive Health Research of Southern California LLC

Long Beach, California, 90808, United States

Location

Digestive Health Research of Southern California

Long Beach, California, 90808, United States

Location

Catalina Research Institute, LLC

Montclair, California, 91763, United States

Location

United Medical Doctors

Murrieta, California, 92563, United States

Location

Palmtree Clinical Research, INC

Palm Springs, California, 92262, United States

Location

IVGI

Ventura, California, 93003, United States

Location

Gastro Florida

Clearwater, Florida, 33761, United States

Location

Tampa Bay Medical Research, Inc.

Clearwater, Florida, 33761, United States

Location

American Research Institute, Inc

Cutler Bay, Florida, 33157, United States

Location

Top Medical Research, Inc

Cutler Bay, Florida, 33189, United States

Location

Covenant Metabolic Specialists, LLC

Fort Myers, Florida, 33912, United States

Location

Direct Helpers Research Center

Hialeah, Florida, 33012, United States

Location

Miguel A Rebollar, MD PA

Hialeah, Florida, 33012, United States

Location

Global Research Associates

Homestead, Florida, 33030, United States

Location

Ocala GI Research dba Lake Center for Clinical Research, LLC

Lady Lake, Florida, 32159, United States

Location

Accel Research Site - Maitland

Maitland, Florida, 32751, United States

Location

CPMI

Miami, Florida, 33014, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Sanchez Clinical Research, Inc

Miami, Florida, 33157, United States

Location

Genoma Research Group, Inc

Miami, Florida, 33173, United States

Location

Panax Clinical Research

Miami Lakes, Florida, 33014, United States

Location

San Marcus Research Clinic, Inc.

Miami Lakes, Florida, 33014, United States

Location

Professional Medical Research

Miramar, Florida, 33025, United States

Location

Ocala GI Research, LLC

Ocala, Florida, 34471, United States

Location

Innovation Medical Research Center, Inc

Palmetto Bay, Florida, 33157, United States

Location

Pensacola GI Research Center, LLC

Pensacola, Florida, 32503, United States

Location

Covenant Metabolic Specialists, LLC

Sarasota, Florida, 34240, United States

Location

Headlands Research Sarasota

Sarasota, Florida, 34243, United States

Location

Conquest Research

Winter Park, Florida, 32789, United States

Location

Summit Clinical Research

Athens, Georgia, 30607, United States

Location

Southeast Clinical Research Center

Dalton, Georgia, 30720, United States

Location

Care Access Research

Fairview Heights, Illinois, 62208, United States

Location

Gastroenterology Health Partners, PLLC

New Albany, Indiana, 47150, United States

Location

Digestive Research Alliance of Michiana

South Bend, Indiana, 46635, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

Kansas Medical Clinic, PA

Topeka, Kansas, 66606, United States

Location

Tandem Clinical Research

Marrero, Louisiana, 70072, United States

Location

Louisiana Research Center LLC

Shreveport, Louisiana, 71105, United States

Location

Woodholme Gastroenterology Associates

Glen Burnie, Maryland, 21061, United States

Location

Greater Boston Gastroenterology

Boston, Massachusetts, 01702, United States

Location

Greater Boston Gastroenterology

Framingham, Massachusetts, 01702, United States

Location

FC Research LLC

South Dartmouth, Massachusetts, 02747, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

GI Associates Research, LLC

Columbia, Missouri, 65201, United States

Location

Sierra Clinical Research

Las Vegas, Nevada, 89106, United States

Location

Jubilee Clinical Research, Inc.

Las Vegas, Nevada, 899106, United States

Location

Care Access

Yonkers, New York, 10701, United States

Location

University of North Carolina at Chapel Hill. UNC Liver Center

Chapel Hill, North Carolina, 27599, United States

Location

Northeast GI Research Division

Concord, North Carolina, 28027, United States

Location

ACME Medical Specialties PLCC

Lumberton, North Carolina, 28358, United States

Location

Care Access Research

Lumberton, North Carolina, 28358, United States

Location

Lucas Research, Inc.

Morehead City, North Carolina, 28557, United States

Location

Trial Management Associates, LLC

Wilmington, North Carolina, 28403, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

DSI Research, LLC - Northridge

Dayton, Ohio, 45414, United States

Location

Care Access Research

Poland, Ohio, 44514, United States

Location

DDSI Clinical Trials

Oklahoma City, Oklahoma, 73112, United States

Location

University of Gastroenterology

Providence, Rhode Island, 02905, United States

Location

Care Access Research

Warwick, Rhode Island, 02886, United States

Location

Ralph H. Johnson Veterans Affairs Medical Center

Charleston, South Carolina, 29401, United States

Location

Columbia Digestive Health Research, LLC

Columbia, South Carolina, 29204, United States

Location

Digestive Disease Research Center LLC

Greenwood, South Carolina, 29646, United States

Location

Rapid City Medical Center, LLP

Rapid City, South Dakota, 57701, United States

Location

WR-ClinSearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

Gastro One

Cordova, Tennessee, 38018, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Digestive Health Research

Lebanon, Tennessee, 37090, United States

Location

Texas Clinical Research Institute, LLC

Arlington, Texas, 76012, United States

Location

Pinnacle Clinical Research

Austin, Texas, 78557, United States

Location

Apex Mobile Clinical Research, LLC

Bellaire, Texas, 77401, United States

Location

Texas Digestive Disease Consultants - Cedar Park

Cedar Park, Texas, 78613, United States

Location

The Liver Institute at Methodist Health System

Dallas, Texas, 75203, United States

Location

GI Alliance -Texas Digestive Disease Consultants

Dallas, Texas, 75246, United States

Location

South Texas Research Institute

Edinburg, Texas, 78539, United States

Location

Texas Digestive Disease Consultants - Fort Worth

Fort Worth, Texas, 76104, United States

Location

Baylor College of Medicine - Advanced Liver Therapies

Houston, Texas, 77030, United States

Location

Pioneer Research Solutions

Houston, Texas, 77099, United States

Location

GI Alliance / Texas Digestive Disease Consultants

Lubbock, Texas, 79410, United States

Location

Centex Studies

McAllen, Texas, 78504, United States

Location

ClinRx Research LLC

Plano, Texas, 75023, United States

Location

American Research Corporation

San Antonio, Texas, 78215, United States

Location

Clinical Trials of Texas Inc.

San Antonio, Texas, 78229, United States

Location

Diabetes and Glandular Disease Clinic, P.A.

San Antonio, Texas, 78229, United States

Location

Endeavor Clinical Trials, LLC

San Antonio, Texas, 78229, United States

Location

Pinnacle Clinical Research

San Antonio, Texas, 78240, United States

Location

Sherman Clinical Research

Sherman, Texas, 75092, United States

Location

Impact Research Institute

Waco, Texas, 76710, United States

Location

Digestive Health Research of North Texas

Wichita Falls, Texas, 76301, United States

Location

Care Access

Ogden, Utah, 84403, United States

Location

Bon Secours Richmond Community Hospital LLC d/b/a Bon Secours Liver Institute of Richmond

Richmond, Virginia, 23226, United States

Location

GI Select Health Research, LLC

Richmond, Virginia, 23236, United States

Location

McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

Gastroenterology Consultants of SW Virginia

Roanoke, Virginia, 24014, United States

Location

University of Calgary Liver Unit

Calgary, Alberta, T2N 4Z6, Canada

Location

GI Research Institute

Vancouver, British Columbia, V6Z 2K5, Canada

Location

Office of Dr. Gauthier

North Bay, Ontario, P1B 2H3, Canada

Location

Toronto Liver Centre

Toronto, Ontario, M6H 3M1, Canada

Location

Office of Dr. Gauthier

Toronto, Ontario, M6H-3M1, Canada

Location

McGill University Health Centre

Montreal, Quebec, H4A 3J1, Canada

Location

Centrum Medyczne Pratia

Katowice, 40-081, Poland

Location

Krakowskie Centrum Medyczne sp z o.o.

Krakow, 31-501, Poland

Location

Hepatology Outpatient Clinic

Śląskie, 41-400, Poland

Location

ID Clinic Arkadiusz Pisula

Śląskie, 41-400, Poland

Location

Warsaw IBD Point Profesor Kierkus

Warsaw, 00-728, Poland

Location

Centrum Medyczne K2J2

Wołomin, 05-200, Poland

Location

FutureMeds

Wroclaw, 50-088, Poland

Location

FDI Clinical Research

San Juan, 00927, Puerto Rico

Location

Related Publications (1)

  • Loomba R, Bedossa P, Grimmer K, Kemble G, Bruno Martins E, McCulloch W, O'Farrell M, Tsai WW, Cobiella J, Lawitz E, Rudraraju M, Harrison SA. Denifanstat for the treatment of metabolic dysfunction-associated steatohepatitis: a multicentre, double-blind, randomised, placebo-controlled, phase 2b trial. Lancet Gastroenterol Hepatol. 2024 Dec;9(12):1090-1100. doi: 10.1016/S2468-1253(24)00246-2. Epub 2024 Oct 11.

    PMID: 39396529BACKGROUND

Related Links

MeSH Terms

Conditions

Non-alcoholic Fatty Liver DiseaseFatty LiverLiver DiseasesDigestive System Diseases

Interventions

TVB-2640

Results Point of Contact

Title
Study Director
Organization
Sagimet Biosciences, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Subjects with liver fibrosis stage F2-F3, will be enrolled and randomized in a 2:1 ratio to receive TVB-2640, or placebo PO QD
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 20, 2021

First Posted

May 28, 2021

Study Start

August 12, 2021

Primary Completion

October 2, 2023

Study Completion

October 2, 2023

Last Updated

May 9, 2025

Results First Posted

May 9, 2025

Record last verified: 2025-04

Data Sharing

IPD Sharing
Will not share

Locations