NCT04851964

Brief Summary

A Multicentre, Randomised, Double-Blind, Parallel-Group, Placebo-Controlled Phase 3 Efficacy and Safety Study of Tezepelumab in Participants with Severe Chronic Rhinosinusitis with Nasal Polyposis

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
416

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Apr 2021

Typical duration for phase_3

Geographic Reach
10 countries

112 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 18, 2021

Completed
2 months until next milestone

First Posted

Study publicly available on registry

April 21, 2021

Completed
1 day until next milestone

Study Start

First participant enrolled

April 22, 2021

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 23, 2024

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 11, 2024

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

January 27, 2026

Completed
Last Updated

January 27, 2026

Status Verified

January 1, 2026

Enrollment Period

3.4 years

First QC Date

February 18, 2021

Results QC Date

September 12, 2025

Last Update Submit

January 8, 2026

Conditions

Keywords

Chronic rhinosinusitis with nasal polypsNasal polypsNasal polyposis

Outcome Measures

Primary Outcomes (2)

  • Change From Baseline in Total Nasal Polyp Score at Week 52

    The total nasal polyp score (NPS) is the sum of the right and left nostril scores (maximum of 8), as evaluated by nasal endoscopy. Higher scores indicate greater symptom severity. The left and right score will be based on a central read with a scale from 0 to 4. Each nasal endoscopy is evaluated by two independent physician reviewers.

    Baseline to Week 52

  • Change From Baseline in Bi-weekly Mean Nasal Congestion Score (NCS) at Week 52

    The NCS is captured by one item in the NPSD (nasal polyps symptom diary) asking participants to rate the severity of their worst NC over the past 24 hours using the following response options: 0 - None; 1 - Mild; 2 - Moderate; 3 - Severe. Baseline will be the mean of daily responses from Day -13 to Day 0. Bi-weekly (14-day) mean NCS will be calculated if at least 8 days in each 14-day period has evaluable data; otherwise the bi-weekly mean is set to missing.

    Baseline to Week 52

Secondary Outcomes (8)

  • Change From Baseline in Bi-weekly Mean Loss of Smell at Week 52

    Baseline to Week 52

  • Change From Baseline in SinoNasal Outcome Test 22 (SNOT-22) at Week 52

    Baseline to Week 52

  • Change From Baseline in Lund Mackay Score Evaluated by CT at Week 52.

    Week 52

  • Percentage of Participants With Nasal Polyp Surgery Decision and/or Systemic Corticosteroid for Nasal Polyposis up to Week 52

    Up to Week 52

  • Percentage of Participants With Nasal Polyp Surgery Decision up to Week 52

    Up to Week 52

  • +3 more secondary outcomes

Other Outcomes (14)

  • Change From Baseline Over Time in Nasal Polyp Score Through Week 52.

    Baseline to Week 52

  • Proportion of Participants With ≥1 Point Reduction in the Nasal Polyp Score at Week 52

    Baseline to Week 52

  • Proportion of Participants With ≥2 Point Reduction in the Nasal Polyp Score at Week 52

    Baseline to Week 52

  • +11 more other outcomes

Study Arms (2)

Tezepelumab

EXPERIMENTAL

Tezepelumab subcutaneous injection in an accessorized pre-filled syringe every 4 weeks (Q4W) added to background mometasone furoate (MFNS) or equivalent intranasal corticosteroid (INCS).

Biological: Experimental: TezepelumabDrug: Mometasone furoate or equivalent intranasal corticosteroid

Placebo

PLACEBO COMPARATOR

Placebo subcutaneous injection in an accessorized pre-filled syringe Q4W added to background MFNS or equivalent INCS.

Other: PlaceboDrug: Mometasone furoate or equivalent intranasal corticosteroid

Interventions

Tezepelumab subcutaneous injection

Tezepelumab
PlaceboOTHER

Placebo subcutaneous injection

Placebo

Background MFNS or equivalent INCS at stable dose

PlaceboTezepelumab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants with physician-diagnosed CRSwNP for at least 12 months prior to Visit 1 that have:
  • Severity consistent with need for surgery as defined by total NPS ≥ 5 (≥ 2 for each nostril) at screening, as determined by the central reader
  • Nasal Congestion Score (NCS) ≥ 2 at Visit 1
  • Ongoing documented NP symptoms over \> 8 weeks prior to screening such as rhinorrhea and/or reduction/loss of smell
  • SNOT-22 total score ≥ 30 at screening (Visit 1)
  • Any standard of care for treatment of CRSwNP provided the participant is stable on that treatment for 30 days prior to Visit 1
  • Documented treatment of nasal polyposis exacerbation with SCS for at least 3 consecutive days or one IM depo-injectable dose (or contraindications/intolerance to) within the past 12 months prior to Visit 1 but not within the last 3 months prior to Visit 1 and/or any history of NP surgery (or contraindications/intolerance to)

You may not qualify if:

  • Any clinically important comorbidities other than asthma (e.g. active lung infection, bronchiectasis, pulmonary fibrosis, cystic fibrosis, primary ciliary dyskinesia, allergic bronchopulmonary mycosis, hypereosinophilic syndromes, etc.) that could confound interpretation of clinical efficacy results.
  • Sinus surgery within 6 months of screening visit OR any sinus surgery in the past which changed the lateral wall of the nose making NPS evaluation impossible.
  • Positive COVID-19 PCR test (or COVID-19 rapid test) or COVID-19 entry screening questionnaire during the screening visit. Evaluation will be based on on local standard of care as determined by current local guidelines.
  • Regular use of decongestants (topical or systematic) at enrolment is not allowed unless used for endoscopic procedure
  • Use of immunosuppressive medication (including but not limited to: methotrexate, troleandomycin, cyclosporine, azathioprine, mycophenolate, tacrolimus, gold, penicillamine, sulfasalazine, hydroxychloroquine, systemic corticosteroids or any experimental anti-inflammatory therapy) within 3 months prior to Visit 1 and during the study period. Systemic corticosteroid use is defined as treatment with a burst of systemic corticosteroids for at least 3 consecutive days or a single IM depo-injectable dose of corticosteroids (considered equivalent to a 3-day burst of systemic corticosteroids).
  • Receipt of COVID-19 vaccine (regardless of vaccine delivery platform) 28 days prior to date of IP administration at Visit 3 (randomisation visit).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (112)

Research Site

Birmingham, Alabama, 35209, United States

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Bakersfield, California, 93301, United States

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Newport Beach, California, 92663, United States

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Roseville, California, 95661, United States

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Walnut Creek, California, 94598, United States

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Colorado Springs, Colorado, 80923, United States

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Denver, Colorado, 80230, United States

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Boca Raton, Florida, 33487, United States

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Chicago, Illinois, 60657, United States

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Baltimore, Maryland, 21224, United States

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White Marsh, Maryland, 21162, United States

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Boston, Massachusetts, 02115, United States

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Columbia, Missouri, 65212, United States

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New York, New York, 10003, United States

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Winston-Salem, North Carolina, 27103, United States

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Oklahoma City, Oklahoma, 73120, United States

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North Charleston, South Carolina, 29406, United States

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Dallas, Texas, 75231, United States

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Norfolk, Virginia, 23507, United States

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Spokane, Washington, 99201, United States

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Milwaukee, Wisconsin, 53228, United States

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Vancouver, British Columbia, V6Z 1Y6, Canada

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Hamilton, Ontario, L8S 1G5, Canada

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London, Ontario, N6A 4V2, Canada

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Montreal, Quebec, H2V 2K1, Canada

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Montreal, Quebec, H2X 0A9, Canada

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Montreal, Quebec, H4A 3J1, Canada

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Québec, Quebec, G1S 4L8, Canada

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Québec, Quebec, G1V 4G5, Canada

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Québec, Quebec, G1V 4W2, Canada

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Trois-Rivières, Quebec, G8T 7A1, Canada

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Bengbu, 233004, China

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Chengdu, 610072, China

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Guangzhou, 510120, China

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Hangzhou, 310003, China

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Hangzhou, 310014, China

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Hengyang, 421001, China

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Lanzhou, 730030, China

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Nanchang, 330006, China

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Nanjing, 210009, China

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Qingdao, 266011, China

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Shanghai, 200031, China

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Shanghai, 200433, China

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Suzhou, 215006, China

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Taizhou, 225300, China

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Tianjin, 300121, China

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Tianjin, 300211, China

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Wenzhou, 325027, China

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Wuhan, 430060, China

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Xi'an, 710068, China

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Yinchuan, 750001, China

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Zunyi, 563100, China

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Aalborg, 9000, Denmark

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Aarhus N, 8200, Denmark

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Hillerød, 3400, Denmark

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Hvidovre, 2650, Denmark

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København NV, 2400, Denmark

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Køge, 4600, Denmark

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Odense, 5000, Denmark

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Vejle, 7100, Denmark

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Berlin, 10629, Germany

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Berlin, 13353, Germany

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Dresden, 01307, Germany

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Heidelberg, 69120, Germany

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Lübeck, 23538, Germany

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Marburg, 35043, Germany

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Tübingen, 72076, Germany

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Wiesbaden, 65183, Germany

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Budapest, 1046, Hungary

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Budapest, 1083, Hungary

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Budapest, 1134, Hungary

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Nyíregyháza, 4400, Hungary

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Pécs, 7621, Hungary

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Siófok, 8600, Hungary

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Székesfehérvár, 8000, Hungary

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Bunkyō City, 113-8431, Japan

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Chuo-shi, 409-3898, Japan

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Habikino-shi, 583-0886, Japan

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Ichikawa-shi, 272-0111, Japan

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Itabashi-ku, 173-8610, Japan

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Kashiwa-shi, 277-0882, Japan

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Kisarazu-shi, 292-8535, Japan

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Miyazaki, 880-8510, Japan

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Nagaoka-shi, 940-8621, Japan

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Nerima-ku, 177-0035, Japan

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Niigata, 951-8520, Japan

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Osaka, 553-0003, Japan

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Saitama-shi, 336-8522, Japan

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Sapporo, 003-0022, Japan

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Sendai, 983-8512, Japan

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Suwa-shi, 392-8510, Japan

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Toyonaka Shi, 560-0082, Japan

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Yokohama, 227-8501, Japan

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Yokohama, 236-0037, Japan

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Bialystok, 15-879, Poland

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Bydgoszcz, 85-231, Poland

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Krakow, 31-513, Poland

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Nadarzyn, 05-830, Poland

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Wroclaw, 50-556, Poland

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Wroclaw, 53-301, Poland

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Zawadzkie, 47-120, Poland

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Łodź, 90-153, Poland

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Barakaldo, 48903, Spain

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Barcelona, 08036, Spain

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Jerez de la Frontera, 11407, Spain

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Madrid, 28040, Spain

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Santiago de Compostela, 15706, Spain

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Seville, 41009, Spain

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Dundee, DD1 9SY, United Kingdom

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London, SE1 9RT, United Kingdom

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Manchester, M13 9WL, United Kingdom

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Stockport, SK2 7JE, United Kingdom

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Related Publications (1)

  • Lipworth BJ, Han JK, Desrosiers M, Hopkins C, Lee SE, Mullol J, Pfaar O, Li T, Chen C, Almqvist G, Margolis MK, McLaren J, Jagadeesh S, MacKay J, Megally A, Hellqvist A, Mankad VS, Bahadori L, Ponnarambil SS; WAYPOINT Study Investigators. Tezepelumab in Adults with Severe Chronic Rhinosinusitis with Nasal Polyps. N Engl J Med. 2025 Mar 27;392(12):1178-1188. doi: 10.1056/NEJMoa2414482. Epub 2025 Mar 1.

Related Links

MeSH Terms

Conditions

Nasal Polyps

Interventions

Mometasone Furoate

Condition Hierarchy (Ancestors)

Nose DiseasesRespiratory Tract DiseasesOtorhinolaryngologic DiseasesPolypsPathological Conditions, AnatomicalPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

PregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Results Point of Contact

Title
Global Clinical Lead
Organization
AstraZeneca

Study Officials

  • Brian Lipworth, MD

    University of Dundee

    PRINCIPAL INVESTIGATOR
  • Joseph K Han, MD

    Eastern Virginia Medical School

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double-Blind
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Subjects will be randomized in a 1:1 ratio to either tezepelumab or matching placebo both administered subcutaneously.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 18, 2021

First Posted

April 21, 2021

Study Start

April 22, 2021

Primary Completion

September 23, 2024

Study Completion

December 11, 2024

Last Updated

January 27, 2026

Results First Posted

January 27, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please refer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the deidentified individual patient-level data in an approved sponsored tool . Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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