NCT04848506

Brief Summary

The purpose of this study is to collect long-term safety and tolerability data for aficamten.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
900

participants targeted

Target at P75+ for phase_2

Timeline
22mo left

Started May 2021

Longer than P75 for phase_2

Geographic Reach
19 countries

129 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress73%
May 2021Mar 2028

First Submitted

Initial submission to the registry

April 9, 2021

Completed
10 days until next milestone

First Posted

Study publicly available on registry

April 19, 2021

Completed
17 days until next milestone

Study Start

First participant enrolled

May 6, 2021

Completed
6.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2028

Last Updated

January 22, 2026

Status Verified

January 1, 2025

Enrollment Period

6.8 years

First QC Date

April 9, 2021

Last Update Submit

January 20, 2026

Conditions

Keywords

Obstructive Hypertrophic CardiomyopathyoHCMCK-3773274CK-274Non obstructive hypertrophic cardiomyopathynHCMHCMHypertrophic cardiomyopathyAficamtenREDWOOD-OLECY 6022FOREST-HCMForest

Outcome Measures

Primary Outcomes (1)

  • Incidence of adverse events observed during dosing of aficamten in patients with HCM

    Patient incidence of reported Adverse Events (AEs)

    Baseline to End of study, up to 5 years

Secondary Outcomes (11)

  • Incidence of serious adverse events observed during dosing of aficamten in patients with HCM

    Baseline to End of study, up to 5 years

  • Incidence of left ventricular ejection fraction (LVEF) < 50% observed during dosing of aficamten in patients with HCM

    Baseline to End of study, up to 5 years

  • Long-term effects of aficamten on left ventricular outflow tract gradient (LVOT G) in patients with oHCM

    Baseline through the end of participation at 12-24 week intervals

  • Long-term effects of aficamten on resting LVOT-G

    Baseline through the end of participation at 12-24 week intervals

  • Long-term effects of aficamten on post Valsalva LVOT-G

    Baseline through the end of participation at 12-24 week intervals

  • +6 more secondary outcomes

Study Arms (1)

Aficamten up to 20 mg

EXPERIMENTAL

Patients in this arm take daily dose of aficamten. Each patient will start at the lowest prespecified dose and titrate up to their maximum tolerated dose.

Drug: Aficamten (5 - 20 mg)

Interventions

Aficamten tablets administered orally. During titration phase, clinic visits will occur approximately every 2-6 weeks. In the maintenance phase clinic visits will occur every 24 weeks, with safety check-in occurring every 12 weeks between visits by phone or, if desirable, in the clinic.

Aficamten up to 20 mg

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Completion of a Cytokinetics trial investigating aficamten
  • LVEF ≥ 55% at the Screening Visit

You may not qualify if:

  • Has received treatment with mavacamten: (a) within 56 days prior to dosing and (b) has not received approval for participation from the Medical Monitor.
  • Has participated in another investigational device or drug study or received an investigational device or drug \< 1 month (or 5 half-lives for drugs, whichever is longer) prior to screening. Other investigational procedures while participating in this study are not permitted.
  • Since completion of a previous trial of aficamten has:
  • Developed new-onset paroxysmal or permanent atrial fibrillation requiring rhythm restoring treatment (eg, direct-current cardioversion, ablation procedure, or antiarrhythmic therapy) \< 30 days prior to screening. Patient may re-screen for CY 6022 after 30 days if heart rate (HR) \< 100 bpm and/or rhythm is stable \> 30 days
  • Undergone septal reduction therapy (surgical myectomy or transcatheter alcohol ablation)
  • Had a confirmed LVEF \< 40% with an associated dose interruption during participation in a prior study with aficamten
  • History of implantable ICD placement within 30 days prior to screening.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (129)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Alaska Heart and Vascular Institute

Anchorage, Alaska, 99508, United States

Location

Mayo Clinic Building - Phoenix

Phoenix, Arizona, 85054, United States

Location

UC San Diego Health - Sulpizio Cardiovascular Center

La Jolla, California, 92037, United States

Location

Cedar-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Cedars-Sinai Medical Center (Smidt Heart Institute)

Los Angeles, California, 90048, United States

Location

UCSF Medical Center

San Francisco, California, 94143, United States

Location

Yale New Haven Hospital

New Haven, Connecticut, 06519, United States

Location

MedStar Washington Hospital Center

Washington D.C., District of Columbia, 20010, United States

Location

Holy Cross Hospital / Cardiology Associates

Fort Lauderdale, Florida, 33308, United States

Location

Emory Clinic

Atlanta, Georgia, 30322, United States

Location

Piedmont Fayette Hospital

Fayetteville, Georgia, 30214, United States

Location

Northwestern University

Evanston, Illinois, 60208, United States

Location

The University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Lahey Hospital & Medical Center

Burlington, Massachusetts, 01805, United States

Location

Michigan Medicine - University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

University of Michigan Health System (UMHS) - University Hospital (University of Michigan Medical Center)

Ann Arbor, Michigan, 48109, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Saint Luke's Hospital of Kansas City

Kansas City, Missouri, 64111, United States

Location

Morristown Medical Center

Morristown, New Jersey, 07960, United States

Location

Northwell Health North Shore University Hospital

Manhasset, New York, 11030, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

Weill Cornell Medicine

New York, New York, 10021, United States

Location

Mount Sinai Hospital

New York, New York, 10029, United States

Location

Columbia University Medical Center/New York Presbyterian Hospital

New York, New York, 10032, United States

Location

Westchester Medical Center

Valhalla, New York, 10595, United States

Location

Sanger Heart & Vascular Institute - HCM Clinic

Charlotte, North Carolina, 28204, United States

Location

Duke Cardiology at Southpoint

Durham, North Carolina, 27710, United States

Location

The Linder Research Center at The Christ Hospital

Cincinnati, Ohio, 45219, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Ascension St. John Clinical Research Institute

Tulsa, Oklahoma, 76104, United States

Location

Providence St. Vincent Medical Center

Portland, Oregon, 97225, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Hospital of the University of Pennsylvania (University of Pennsylvania School of Medicine)

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Presbyterian

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

Greenville Memorial Hospital

Greenville, South Carolina, 29605, United States

Location

Ascension Saint Thomas Heart West

Nashville, Tennessee, 37205, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

The University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, 75390, United States

Location

CHI St. Luke's Health Baylor College of Medicine Medical Center

Houston, Texas, 77030, United States

Location

Houston Methodist Hospital

Houston, Texas, 77030, United States

Location

Intermountain Medical Center

Murray, Utah, 84107, United States

Location

University of Utah Health

Salt Lake City, Utah, 84132, United States

Location

University of Virginia Health System University Hospital

Charlottesville, Virginia, 22908, United States

Location

Inova Health Care Services

Falls Church, Virginia, 22042, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

WVUMedicine

Morgantown, West Virginia, 26506, United States

Location

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, 53215, United States

Location

Instituto Cardiovascular de Buenos Aires(ICBA)

Buenos Aires, C1428, Argentina

Location

Flinders Medical Centre, Cardiology Research

Bedford Park, 5042, Australia

Location

The Prince Charles Hospital

Chermside, 4032, Australia

Location

Fiona Stanley Hospital, AHF Unit

Murdoch, 6150, Australia

Location

Instituto Dante Pazzanese de Cardiologia

São Paulo, 04012-909, Brazil

Location

Institut universitaire de cardiologie et de pneumologie de Quebec-Universite Laval

Québec, Quebec, G1V 4G5, Canada

Location

Royal Alexandra Hospital

Edmonton, T5H 3V9, Canada

Location

QEII Health Science Centre (Halifax Infirmary site)

Halifax, B3H 3A7, Canada

Location

Il. Interni klinika kardiologie a angiologie

Prague, 128 08, Czechia

Location

Department of Cardiology Aalborg University Hospital

Aalborg, 9000, Denmark

Location

Department of Cardiology Aarhus University Hospital

Aarhus, 8200, Denmark

Location

The Heart Center, Department of Cardiology

Copenhagen, 2100, Denmark

Location

Copenhagen University Hospital

Copenhagen, 2400, Denmark

Location

Odense University Hospital

Odense, 5000, Denmark

Location

Hopital de la Timone Service de cardiologie

Marseille, 130005, France

Location

Clinique Du Millenaire

Montpellier, 340000, France

Location

CHU Montpellier - Hopital Arnaud de Villeneuve

Montpellier, 34295, France

Location

CHU de Nantes Institut Du Thorax et du systeme nerveux Clinique Cardiologique et des Maladies Vasculaires

Nantes, 44093, France

Location

Hopital Lariboisiere

Paris, 75010, France

Location

Hopital Europeen Georges Pompidou

Paris, 75015, France

Location

Hopital cardiologique de Haut-Leveque

Pessac, 33604, France

Location

Centre hospitalier universitaire (CHU) de Rennes-Hopital Pontchaillou

Rennes, 35033, France

Location

Centre Hospitalier universitaire de Toulouse - Rangueil Hospital

Toulouse, 31059, France

Location

Charite-Universitaetsmedizin Berlin

Berlin, 13353, Germany

Location

Universitaetsklinikum Essen

Essen, 45147, Germany

Location

Universitaetsmedizin Goettingen Klinik fur Kardiologie und Pneumologie

Goettigen, 37075, Germany

Location

Universitaesklinkum Heidelberg

Heidelberg, 69120, Germany

Location

Universitaetsklinikum Jena

Jena, 07747, Germany

Location

Universitaetskinikum Wuerzburg Deutsches Zentrum fur Herzinsuffzienz Wurzburg (DZHI) Comprehensive Heart Failure Center (CHFC)

Würzburg, 97078, Germany

Location

Evangelismos General Hospital of Athens

Athens, 10676, Greece

Location

"Hippokration" General Hospital of Athens

Athens, 11527, Greece

Location

Onassis Hospital

Athens, 17674, Greece

Location

University General Hospital "ATTIKON"

Attiki, 12462, Greece

Location

Semmelweis Egyetem Varosmajori Sziv es Ergyogyaszati Klinika

Budapest, 1122, Hungary

Location

Szegedi Tudományegyetem, Belgyógyászati Klinika, Kardiológiai Központ

Szeged, 6725, Hungary

Location

Landspitali University Hospital

Reykjavik, 101, Iceland

Location

The Barzilai University Medical Center

Ashkelon, 7830604, Israel

Location

Hadassah Medical Center- Ein Kerem

Jerusalem, 9112001, Israel

Location

Meir Medical Center

Kfar Saba, 4428164, Israel

Location

The Chaim Sheba Medical Center

Ramat Gan, 5265601, Israel

Location

Ziv Medical Center

Safed, 1311001, Israel

Location

Unit Cardiomiopatie, Dipartimento Cardio ToracoVascolare

Florence, 50134, Italy

Location

IRCCS Policlinico San Donato

Milan, 20097, Italy

Location

ASST Grande Ospedale Metropolitano Niguarda

Milan, 20162, Italy

Location

Azienda Ospedaliera Universitaria Federico II di Napoli

Naples, 80131, Italy

Location

Fondazione toscana Gabriele Monesterio per la ricarca medica Dipartimento Cardiotoracico UOC Cardiologia e Medicina Cardiovasculare Ospedale San Cataldo

Pisa, 56124, Italy

Location

Dipartimento di Medicina Clinica e Molecolare Universita Sapienza di Roma Unita di Terapia Intensiva Cardiologica Azienda Ospedaliero Universitaria Sant'Andrea

Roma, 00189, Italy

Location

Azienda Sanitaria Universitaria Giuliano Isontina

Trieste, 34149, Italy

Location

Amsterdam UMC

Amsterdam, 1105, Netherlands

Location

Maastricht University Medical Center (MUMC)

Maastricht, 6229 HX, Netherlands

Location

Erasmus Medical Center Department of Cardiology

Rotterdam, 3015, Netherlands

Location

Kardio Brynow S.C.

Katowice, 40-555, Poland

Location

Narodowy Instytut Kardiologii Stefana Kardynala Wyszynskiego - Panstwowy Instytut Badawczy Centrum Zaburzen Rytmu Serca

Warsaw, 04-628, Poland

Location

Centro Hospitalar Do Baixo Vouga, EPE Cardiology Department

Aveiro, 3814-501, Portugal

Location

Unidade Local De Saude De Sao Jose E.P.E

Lisbon, 1150-199, Portugal

Location

Hospital Cuf Descobertas S.A.

Lisbon, 1998-018, Portugal

Location

Hospital da Luz

Lisbon, Portugal

Location

Complejo Hospitalario Universitario A Coruna

A Coruña, 15006, Spain

Location

Hospital Clinic Barcelona

Barcelona, 08036, Spain

Location

Hospital General Universitario Gregorio Marañón (HGUGM)

Madrid, 28007, Spain

Location

Hospital Clinico Universitario San Carlos

Madrid, 28040, Spain

Location

Hospital Universitario Puerta de Hierro Majadahonda

Madrid, 28220, Spain

Location

Hospital Clinico Universitario Virgen de la Arrixaca

Madrid, 30120, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, 29010, Spain

Location

Hospital Universitario Son Llatzer

Palma, 07198, Spain

Location

Complexo Hospitalario Universitario De Vigo

Pontevedra, 36312, Spain

Location

Hospital Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen Macarena-merge

Seville, 41009, Spain

Location

Hospital Universitario Virgen del Rocío

Seville, 41013, Spain

Location

Queen Elizabeth Hospital Birmingham University Hospitals Birmingham NHS Foundation Trust

Birmingham, B15 2GW, United Kingdom

Location

Ninewells Hospital and Medical School

Dundee, DD2 1SG, United Kingdom

Location

Glasgow Clinical Research Facility Neuroscience Institute

Glasgow, G51 4TF, United Kingdom

Location

Liverpool Heart and Chest Hospital

Liverpool, L14 3PE, United Kingdom

Location

St Bartholomew's Hospital

London, EC1A 7BE, United Kingdom

Location

St George's University Hospitals NHS Foundation Trust

London, SW17 0QT, United Kingdom

Location

Royal Brompton Hospital

London, SW3 6NP, United Kingdom

Location

Oxford Centre for Clinical Magnetic Resonance Research (OCMR) Division of Cardiovascular Medicine Radcliffe Department of Medicine University of Oxford

Oxford, OX3 9DU, United Kingdom

Location

Related Publications (3)

  • Saberi S, Abraham TP, Choudhury L, Barriales-Villa R, Elliott PM, Nassif ME, Oreziak A, Owens AT, Tower-Rader A, Rader F, Garcia-Pavia P, Olivotto I, Coats CJ, Fifer MA, Sherrid MV, Solomon SD, Watkins H, Heitner SB, Jacoby DL, Kupfer S, Malik FI, Melloni C, Meng L, Wei J, Maron MS, Masri A; FOREST-HCM Steering Committee and Investigators. Aficamten Treatment for Symptomatic Obstructive Hypertrophic Cardiomyopathy: 48-Week Results From FOREST-HCM. JACC Heart Fail. 2025 Aug;13(8):102496. doi: 10.1016/j.jchf.2025.03.040. Epub 2025 Jun 19.

  • Masri A, Maron MS, Abraham TP, Nassif ME, Barriales-Villa R, Bilen O, Coats CJ, Elliott P, Garcia-Pavia P, Massera D, Olivotto I, Oreziak A, Owens AT, Saberi S, Solomon SD, Tower-Rader A, Heitner SB, Jacoby DL, Melloni C, Wei J, Sherrid MV; REDWOOD-HCM, SEQUOIA-HCM, and FOREST-HCM Investigators. Concomitant Aficamten and Disopyramide in Symptomatic Obstructive Hypertrophic Cardiomyopathy. JACC Heart Fail. 2026 Feb;14(2):102441. doi: 10.1016/j.jchf.2025.03.008. Epub 2025 Apr 2.

  • Masri A, Choudhury L, Barriales-Villa R, Elliott P, Maron MS, Nassif ME, Oreziak A, Owens AT, Saberi S, Tower-Rader A, Rader F, Garcia-Pavia P, Olivotto I, Nagueh SF, Wang A, Heitner SB, Jacoby DL, Kupfer S, Malik FI, Melloni C, Meng L, Wei J, Sherrid MV, Abraham TP; FOREST-HCM Investigators. Standard-of-Care Medication Withdrawal in Patients With Obstructive Hypertrophic Cardiomyopathy Receiving Aficamten in FOREST-HCM. J Am Coll Cardiol. 2024 Nov 5;84(19):1839-1849. doi: 10.1016/j.jacc.2024.09.002.

MeSH Terms

Conditions

Cardiomyopathy, Hypertrophic

Condition Hierarchy (Ancestors)

CardiomyopathiesHeart DiseasesCardiovascular DiseasesAortic Stenosis, SubvalvularAortic Valve StenosisAortic Valve DiseaseHeart Valve Diseases

Study Officials

  • Cytokinetics, MD

    Cytokinetics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 9, 2021

First Posted

April 19, 2021

Study Start

May 6, 2021

Primary Completion (Estimated)

March 1, 2028

Study Completion (Estimated)

March 1, 2028

Last Updated

January 22, 2026

Record last verified: 2025-01

Data Sharing

IPD Sharing
Will not share

Locations