NCT04799002

Brief Summary

The purpose of this study is to evaluate topotecan and melphalan for retinoblastoma patients.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at below P25 for phase_3

Timeline
19mo left

Started Mar 2021

Longer than P75 for phase_3

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress77%
Mar 2021Dec 2027

Study Start

First participant enrolled

March 11, 2021

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

March 12, 2021

Completed
4 days until next milestone

First Posted

Study publicly available on registry

March 16, 2021

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 30, 2024

Completed
3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 30, 2027

Expected
Last Updated

March 16, 2021

Status Verified

March 1, 2021

Enrollment Period

3.8 years

First QC Date

March 12, 2021

Last Update Submit

March 12, 2021

Conditions

Keywords

RetinoblastomatopotecanMelphalan

Outcome Measures

Primary Outcomes (1)

  • Eyeball-sparing rate

    Eyeball-sparing rate during chemotherapy in retinoblastoma patients

    5 years after chemotherapy

Secondary Outcomes (1)

  • Side effects

    5 years after chemotherapy

Study Arms (2)

Topotecan

ACTIVE COMPARATOR

Topotecan intraocular injection during chemotherapy

Drug: Topotecan

Melphalan

EXPERIMENTAL

Melphalan intraocular injection during chemotherapy

Drug: Melphalan

Interventions

Topotecan intraocular injection for chemotherapy in retinoblastoma

Also known as: Topotecan intraocular injection
Topotecan

Melphalan intraocular injection for chemotherapy in retinoblastoma

Also known as: Melphalan intraocular injection
Melphalan

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • diagnosed as retinoblastoma
  • receiving eyeball-sparing treatment

You may not qualify if:

  • disease progression during follow-up

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Sun Yat-sen University

Guangzhou, Guangdong, 510000, China

RECRUITING

MeSH Terms

Conditions

Retinoblastoma

Interventions

TopotecanMelphalan

Condition Hierarchy (Ancestors)

Neoplasms, NeuroepithelialNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Glandular and EpithelialNeoplasms, Nerve TissueRetinal NeoplasmsEye NeoplasmsNeoplasms by SiteEye Diseases, HereditaryEye DiseasesRetinal Diseases

Intervention Hierarchy (Ancestors)

CamptothecinAlkaloidsHeterocyclic CompoundsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and Proteins

Study Officials

  • Huashen Yang

    Sun Yat-sen University

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

March 12, 2021

First Posted

March 16, 2021

Study Start

March 11, 2021

Primary Completion

December 30, 2024

Study Completion (Estimated)

December 30, 2027

Last Updated

March 16, 2021

Record last verified: 2021-03

Data Sharing

IPD Sharing
Will not share

Locations