NCT04770545

Brief Summary

This is a phase 3, open-label, multicenter, extension study to evaluate the long-term safety and efficacy of pegcetacoplan (APL-2) in subjects with geographic atrophy (GA) secondary to age-related macular degeneration (AMD) who participated in Study APL2-103 (NCT03777332) or completed the treatment at Month 24 of either Study APL2-303 (Derby, NCT03525613) or Study APL2-304 (Oaks, NCT03525600).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
792

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Mar 2021

Typical duration for phase_3

Geographic Reach
15 countries

175 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 23, 2021

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 25, 2021

Completed
7 days until next milestone

Study Start

First participant enrolled

March 4, 2021

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 5, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 5, 2025

Completed
Last Updated

October 24, 2025

Status Verified

June 1, 2025

Enrollment Period

4.5 years

First QC Date

February 23, 2021

Last Update Submit

October 23, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence and severity of ocular and systemic adverse events

    Up to 36 Months

Secondary Outcomes (3)

  • Change from baseline in the total area of GA lesion(s) in the study eye (in mm2)

    Up to 36 Months

  • Change from baseline in NL-BCVA score (study eye)

    Up to 36 Months

  • Change from baseline in LL-BCVA score (study eye)

    Up to 36 Months

Study Arms (2)

Pegcetacoplan, 15 mg/100 μL, monthly for up to 36 months

EXPERIMENTAL

Participants from Study APL2-103 (NCT03777332) or those who completed the treatment at Month 24 from either Study APL2-303 (Derby, NCT03525613) or Study APL2-304 (Oaks, NCT03525600) and were administered monthly intravitreal (IVT) pegcetacoplan (15 mg/100 μL) or monthly sham will receive IVT pegcetacoplan (15 mg/100 μL) monthly for up to approximately 36 months.

Drug: PEGCETACOPLAN (APL-2)

Pegcetacoplan, 15 mg/100 μL, every other month (EOM) for up to 36 months

EXPERIMENTAL

Participants from Study APL2-103 (NCT03777332) or those who completed the treatment at Month 24 from either Study APL2-303 (Derby, NCT03525613) or Study APL2-304 (Oaks, NCT03525600) and were administered every other month (EOM) intravitreal (IVT) pegcetacoplan (15 mg/100 μL) or EOM sham will receive IVT pegcetacoplan (15 mg/100 μL) EOM for up to approximately 36 months.

Drug: PEGCETACOPLAN (APL-2)

Interventions

Complement (C3) Inhibitor

Pegcetacoplan, 15 mg/100 μL, every other month (EOM) for up to 36 monthsPegcetacoplan, 15 mg/100 μL, monthly for up to 36 months

Eligibility Criteria

Age60 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants are eligible to be included in the study only if all of the following criteria apply:
  • Subjects must have participated in APL2-103 (NCT03777332) or completed the treatment at Month 24 of either APL2-303 (Derby, NCT03525613) or APL2-304 (Oaks, NCT03525600).
  • For subjects who participated in either the 303 or 304 studies, the condition listed below must also be met for participating in this study.
  • Subjects who did not fully stop study drug treatment, but missed the visit at Month 24, can also participate in the study. However, to participate, subjects must be seen within 60 days from the last day of the period allowed for the 24 months visit in the previous study.
  • The eyes of subjects must have transparency to permit visualization of parts inside the eye such as the retina and subjects must be able to look steadily at a provided target allowing the doctor to get good quality pictures from the eye.
  • Female subjects must be:
  • Women that cannot have children, or
  • Women who can have children must have a negative result of a blood pregnancy test on the first day of the study visit and agree to use ways to avoid pregnancy during the study and 90 days after the last dose of the study medication.
  • Males with female partners who can get pregnant must also agree to use ways to avoid pregnancy and agree not to donate sperm while in the study or until 90 days after administering the last dose of the study medication.
  • Agree to participate in the study by signing the consent document providing information about the study; and take part in all tests and assessments as required.

You may not qualify if:

  • Subjects cannot take part in the study if the eye that will be treated during the study currently meets any of the following conditions:
  • Participants in APL2 303/304 studies who fully stopped study drug treatment before the visit in month 24 but remain in the study to observe the study medication's safety. Those subjects who temporarily paused study drug treatment are still eligible to participate.
  • If, according to your doctor you currently have any disease affecting your eyes that could interfere with your vision, including diseases that affect your retina or macula (the center of the back of your eyes). And, if according to your doctor, the disease in your eyes is benign and does not interfere with the study (e.g. diseases that affects the periphery of the retina), you are also eligible to take part in the study.
  • If, according to your doctor you currently have any inflammation/infection in or around your eyes that could prohibit you from receiving an injection inside your eyes.
  • If, according to your doctor, any current disease that could directly interfere in your participation in the study or that could make it difficult for you to come to the scheduled visits during the next three yearsover the next 36 months.
  • If you have known allergies to fluorescein sodium, a solution that is injected into your body for eye testing; or to pegcetacoplan (the study drug) or any inactive substances in pegcetacoplan solution.
  • If you currently are pregnant, breastfeed or have a positive pregnancy test.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (175)

Retinal Research Institue, LLC

Phoenix, Arizona, 85014, United States

Location

Associated Retina Consultants, Ltd.

Phoenix, Arizona, 85020, United States

Location

California Retina Consultants

Bakersfield, California, 93309, United States

Location

Retinal Diagnostic Center

Campbell, California, 95508, United States

Location

The Retina Partners

Encino, California, 91436, United States

Location

Retina Consultants of Orange County

Fullerton, California, 92835, United States

Location

Atlantis Eyecare

Huntington Beach, California, 92647, United States

Location

Jacobs Retina Center, UCSD

La Jolla, California, 92093, United States

Location

Doheny Eye Center UCLA

Los Angeles, California, 90033, United States

Location

Northern California Retina Vitreous Associates

Mountain View, California, 94040, United States

Location

Retina Institute of California Medical Group

Palm Desert, California, 92260, United States

Location

Byers Eye Institute, Stanford University

Palo Alto, California, 94303, United States

Location

Retina Consultants San Diego

Poway, California, 92064, United States

Location

Orange County Retina Medical Group

Santa Ana, California, 92705, United States

Location

California Retina Consultants

Santa Barbara, California, 93103, United States

Location

Bay Area Retina Associates

Walnut Creek, California, 94598, United States

Location

Southwest Retina Research Center, LLC

Durango, Colorado, 81301, United States

Location

Danbury Eye Physicians & Surgeons, PC

Danbury, Connecticut, 06810, United States

Location

Retina Group of New England - New London

Waterford, Connecticut, 06835, United States

Location

Florida Eye Microsurgical Institute, Inc.

Boynton Beach, Florida, 33426, United States

Location

Blue Ocean Clinical Research

Clearwater, Florida, 33761, United States

Location

Pinnacle Research Insitute

Fort Lauderdale, Florida, 33309, United States

Location

Retina Health Center

Fort Myers, Florida, 33907, United States

Location

National Opthalmic Research Institute

Fort Myers, Florida, 33912, United States

Location

Bascom Palmer Eye Institute

Miami, Florida, 33136, United States

Location

Bascom Palmer Eye Institute at Naples

Naples, Florida, 34103, United States

Location

Palm Beach Gardens

Palm Beach Gardens, Florida, 33418, United States

Location

Retina Specialty Institute

Pensacola, Florida, 32503, United States

Location

Eye Associates of Pinellas

Pinellas Park, Florida, 33782, United States

Location

East Florida Eye Institute

Stuart, Florida, 34994, United States

Location

Retina Associates of Florida

Tampa, Florida, 33609, United States

Location

University of South Florida

Tampa, Florida, 33612, United States

Location

Center for Retina and Macular Disease

Winter Haven, Florida, 33880, United States

Location

Southeast Retina Center, PC

Augusta, Georgia, 30909, United States

Location

Georgia Retina, PC

Marietta, Georgia, 30060, United States

Location

Gailey Eye Clinic Retina Center

Bloomington, Illinois, 61704, United States

Location

Northwestern Feinberg School of Medicine

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Midwest Eye Institute

Indianapolis, Indiana, 46290, United States

Location

Retina and Vitreous Associates of Kentucky, PSC dba Retina Associates of Kentucky

Lexington, Kentucky, 40509, United States

Location

The Retina Care Center

Baltimore, Maryland, 21209, United States

Location

Elman Retina Group

Baltimore, Maryland, 21236, United States

Location

The Retina Group of Washington

Chevy Chase, Maryland, 92705, United States

Location

Cumberland Valley Retina Center

Hagerstown, Maryland, 21740, United States

Location

Mid Atlantic Retina Specialist

Hagerstown, Maryland, 21740, United States

Location

Ophthalmic Consultants of Boston

Boston, Massachusetts, 02114, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02116, United States

Location

New England Retina Consultants, PC

Springfield, Massachusetts, 01107, United States

Location

Michigan Medicine Kellogg Eye Center

Ann Arbor, Michigan, 48105, United States

Location

Associated Retinal Consultants, PC

Grand Rapids, Michigan, 49546, United States

Location

Associated Retinal Consultants, PC

Traverse City, Michigan, 49686, United States

Location

Vitreoretinal Surgery

Minneapolis, Minnesota, 55435, United States

Location

Sierra Eye Associates

Reno, Nevada, 89503, United States

Location

Retina Center of NJ, LLC

Bloomfield, New Jersey, 07003, United States

Location

NJ Retina

Teaneck, New Jersey, 07666, United States

Location

NJ Retina

Toms River, New Jersey, 08755, United States

Location

Vision Research Center Eye Associates of NM

Albuquerque, New Mexico, 87109, United States

Location

Long Island Vitreoretinal Consultants

Great Neck, New York, 11021, United States

Location

Vitreous Retina Macula Consultants of New York

New York, New York, 10022, United States

Location

Ophthalmic Consultants of Long Island

Oceanside, New York, 11572, United States

Location

Western Carolina Retinal Associates

Asheville, North Carolina, 28803, United States

Location

Charlotte Eye Ear Nose and Throat Associates, PS

Charlotte, North Carolina, 28210, United States

Location

Duke University, Duke Eye Center

Durham, North Carolina, 27710, United States

Location

Graystone Eye

Hickory, North Carolina, 28602, United States

Location

Retina Associates of Cleveland, Inc.

Cleveland, Ohio, 44122, United States

Location

Retina Associates of Cleveland

Cleveland, Ohio, 44130, United States

Location

Cleveland Clinic Cole Eye Institute

Cleveland, Ohio, 44195, United States

Location

The Ohio State University

Columbus, Ohio, 43212, United States

Location

Retina Associates of Cleveland, Inc.

Youngstown, Ohio, 44505, United States

Location

Retina Vitreous Center, PLLC

Edmond, Oklahoma, 73013, United States

Location

Oregon Retina LLP

Eugene, Oregon, 97405, United States

Location

Retina Northwest, PC

Portland, Oregon, 97221, United States

Location

Eye Health Northwest

Portland, Oregon, 97225, United States

Location

Mid Atlantic Retina

Bethlehem, Pennsylvania, 18107, United States

Location

Retina Vitreous Consultants

Monroeville, Pennsylvania, 15146, United States

Location

Mid Atlantic Retina

Philadelphia, Pennsylvania, 19006, United States

Location

Mid Atlantic Retina

Philadelphia, Pennsylvania, 19107, United States

Location

AIO Visionary Eye Care

West Mifflin, Pennsylvania, 15122, United States

Location

Black Hills Regional Eye Institute

Rapid City, South Dakota, 57701, United States

Location

Charles Retina Institute

Germantown, Tennessee, 38138, United States

Location

Tennessee Retina, PC

Nashville, Tennessee, 78503, United States

Location

Retina Research Center PLLC

Austin, Texas, 78750, United States

Location

Brown Retina Institute

Bellaire, Texas, 77401, United States

Location

Texas Retina Associates

Dallas, Texas, 75231, United States

Location

Houston Eye Associates

Houston, Texas, 77025, United States

Location

Retina Consultants of Houston, PA

Houston, Texas, 77030, United States

Location

Valley Retina Institute

McAllen, Texas, 78503, United States

Location

Medical Center Ophthalmology Associates

San Antonio, Texas, 78240, United States

Location

Retina Associates of South Texas

San Antonio, Texas, 78240, United States

Location

Retina Consultants of Houston

The Woodlands, Texas, 77384, United States

Location

Retina Associates of Utah, PC

Murray, Utah, 84107, United States

Location

University of Utah - John A. Moran Center

Salt Lake City, Utah, 84312, United States

Location

University of Virginia

Charlottesville, Virginia, 22903, United States

Location

The Retina Group of Washington

Fairfax, Virginia, 22031, United States

Location

Emerson Clinical Research Institute

Falls Church, Virginia, 22046, United States

Location

Vitreoretinal Associates of Washington

Bellevue, Washington, 98004, United States

Location

Spokane Eye Clinical Research

Spokane, Washington, 99204, United States

Location

Retina Health Center

Madison, Wisconsin, 53705, United States

Location

Retina-Vitreous Associates Medical Group

Madison, Wisconsin, 53705, United States

Location

Diagnostico Ocular

Buenos Aires, 1425, Argentina

Location

Organizacion Medica de Investigacion (OMI)

Buenos Aires, C1015 ABO, Argentina

Location

Fundacion Zambrano

Buenos Aires, C1023 AAQ, Argentina

Location

Centro Oftalmologico Dr. Charles S.A.

Buenos Aires, C1116ABA, Argentina

Location

Instituto Oftalmologico de Cordoba

Córdoba, 5000, Argentina

Location

OFTAR

Mendoza, 5500, Argentina

Location

Microcirujia Ocular Rosario

Rosario, 2000, Argentina

Location

Oftalmologos Especialistas

Santa Fe, S2000, Argentina

Location

Marsden Eye Specialist

Parramatta, New South Wales, 2150, Australia

Location

Strathfield Retina Clinic

Strathfield, New South Wales, 2135, Australia

Location

Sydney Retina

Sydney, New South Wales, 2000, Australia

Location

The Ashley Centre

Westmead, New South Wales, 2145, Australia

Location

Centre for Eye Research Australia

East Melbourne, Victoria, 3002, Australia

Location

Retina and Eye Consultantss

Hurstville, 2220, Australia

Location

Lions Eye Institute

Nedlands, 6009, Australia

Location

Save Sight Institute

Westmead, 2145, Australia

Location

IPEPO Instituto Da Visao

São Paulo, 04038-032, Brazil

Location

Ivey Eye Institute

London, Ontario, N6A 4V2, Canada

Location

University of Ottawa Eye Institute

Ottawa, Ontario, K1H 8L6, Canada

Location

Retina Centre of Ottawa

Ottawa, Ontario, K2B 7E9, Canada

Location

Fakultni Nemocnice Ostrava

Ostrava-Poruba, 708 52, Czechia

Location

University hospital Kralovske Vinohrady

Prague, 10034, Czechia

Location

AXON Clinical, s.r.o.

Prague, 150 00, Czechia

Location

Vseobecna fakultni nemocnice v Praze

Prague, 2128 08, Czechia

Location

Gemini Eye Clinic

Zlín, 760 01, Czechia

Location

Centre ophtalmologique Saint-Exupery

Saint-Cyr-sur-Loire, Lyon, 37540, France

Location

CHU de Bordeaux

Bordeaux, 33076, France

Location

Centre Hospitalier Intercommunal de Creteil

Créteil, 94010, France

Location

CHU Dijon

Dijon, 21 079, France

Location

Clinique du Val d'Ouest

Écully, 69130, France

Location

Hopital de la Croix-Rousse

Lyon, 69004, France

Location

Centre monticelli Paradis

Marseille, 13008, France

Location

CHU de Nantes - Hotel Dieu

Nantes, 44093, France

Location

Centre Ophtalmol de l Odeon

Paris, 75006, France

Location

Hopital Lariboisiere

Paris, 75010, France

Location

CHNO des Quinze-Vingts

Paris, 75012, France

Location

Centre Ophtalmo. Image/Laser

Paris, 75015, France

Location

Maison Rouge Ophthalmologic Center

Strasbourg, 67000, France

Location

CHU de Strasbourg Hopital Civil

Strasbourg, 67091, France

Location

Universitats-Augenklinik Bonn

Bonn, 53127, Germany

Location

Uniklinik Koln

Cologne, 50937, Germany

Location

University Opthalmology Clinic

Freiburg im Breisgau, 79106, Germany

Location

Uni-medizin Gottingen Augenklinik 3.B1.261

Göttingen, 37075, Germany

Location

Klinikum der Stadt Ludwigshafen gGmbH

Ludwigshafen, 67063, Germany

Location

Universitatsklinikum Schleswig-Holstein

Lübeck, 23538, Germany

Location

Augenklinik der LMU Munchen

München, 80336, Germany

Location

Klinikum rechts der Isar

München, 81675, Germany

Location

Augenzentrum am St. Franziskus-Hospital

Münster, 48145, Germany

Location

Universitatsklinikum Regensburg

Münster, 48145, Germany

Location

Universitatsklinikum Munster

Münster, 48149, Germany

Location

STZ Eyetrial

Tübingen, 72076, Germany

Location

Assaf ha Rofeh MC

Be’er Ya‘aqov, 7030000, Israel

Location

Rambam Health Care Campus

Haifa, 3109601, Israel

Location

Hadassah Medical Center

Jerusalem, 91120, Israel

Location

Tel Aviv Sourasky Medical Center

Tel Aviv, 64239, Israel

Location

IRCCS San Raffaele

Milan, 20132, Italy

Location

ASST Fatebenefratelli-Sacco Ospedale Luigi Sacco

Milan, 20157, Italy

Location

Academisch Medisch Centrum

Amsterdam, 1105 AZ, Netherlands

Location

Radboud university medical center Oogheelkunde

Nijmegen, 6525 EX, Netherlands

Location

Southern Eye Specialists

Christchurch, 8013, New Zealand

Location

Hamilton Eye Clinic

Hamilton, 3204, New Zealand

Location

Eye Surgery Center Professor Zagorski

Bydgoszcz, 85-316, Poland

Location

Oftalmika Eye Hospital

Bydgoszcz, 85-631, Poland

Location

Grupo Laser Vision

Rzeszów, 35-017, Poland

Location

Oculomedica Eye Centre

Tarnów, 33-100, Poland

Location

UNO-MED Centrum Medyne

Tarnów, 33-100, Poland

Location

Hospital Universitario Puerta de Hierro

Madrid, 28222, Spain

Location

Instituto Oftalmologico Gomez-Ulla

Santiago de Compostela, 15706, Spain

Location

Kings College Hospital NHS Trust

London, London, SE5 9RS, United Kingdom

Location

Huddersfield Royal Infirmary

Huddersfield, West Yorkshire, HD3 3EA, United Kingdom

Location

St James's University Hospital

Leeds, West Yorkshire, LS9 7TF, United Kingdom

Location

Bristol Eye Hospital

Bristol, BS1 2LX, United Kingdom

Location

Royal Liverpool University Hospital

Liverpool, L7 8XP, United Kingdom

Location

London Vision Clinic

London, W1G 7LA, United Kingdom

Location

Oxford Eye Hospital

Oxford, OX3 9DU, United Kingdom

Location

Sunderland Eye Infirmary

Sunderland, SR2 9HP, United Kingdom

Location

MeSH Terms

Interventions

pegcetacoplan

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 23, 2021

First Posted

February 25, 2021

Study Start

March 4, 2021

Primary Completion

September 5, 2025

Study Completion

September 5, 2025

Last Updated

October 24, 2025

Record last verified: 2025-06

Locations