NCT04754321

Brief Summary

This phase I trial is to find out the possible side effects of pembrolizumab and radiation therapy before and during surgery in treating patients with head and neck squamous cell cancer that remains despite treatment (persistent) or has come back (recurrent). Immunotherapy with monoclonal antibodies, such as pembrolizumab, may help the body's immune system attack the cancer, and may interfere with the ability of tumor cells to grow and spread. Radiation therapy uses high energy x-rays or protons to kill tumor cells and shrink tumors. Giving pembrolizumab and radiation therapy before and during surgery may kill more tumor cells.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
45

participants targeted

Target at P50-P75 for phase_1

Timeline
7mo left

Started May 2022

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress86%
May 2022Dec 2026

First Submitted

Initial submission to the registry

February 9, 2021

Completed
6 days until next milestone

First Posted

Study publicly available on registry

February 15, 2021

Completed
1.2 years until next milestone

Study Start

First participant enrolled

May 12, 2022

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2026

Last Updated

February 2, 2026

Status Verified

January 1, 2026

Enrollment Period

4.6 years

First QC Date

February 9, 2021

Last Update Submit

January 29, 2026

Conditions

Outcome Measures

Primary Outcomes (2)

  • Incidence of adverse events

    Evaluated using National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) version 4.0. Summarized by treatment group. All on-study adverse events (AEs), treatment-related AEs, serious (S)AEs, and treatment-related SAEs will be tabulated using worst grade per NCI CTCAE version 4.0 criteria by system organ class and preferred term. On-study lab parameters including hematology, chemistry, liver function, and renal function will also be summarized using worst grade NCI CTCAE v 4.0 criteria. Toxicity will be measured as the rate of grade 3 and 4 adverse events and will be calculated through using the exact binomial distribution method with a 2- sided 95% confidence interval.

    Up to 100 days after last dose of study drug

  • Health related quality of life

    Assessed by European Organization for Research and Treatment of Cancer Quality of Life Questionnaire - Core 30. Analysis will be performed in all randomized participants who have an assessment at baseline and at least one follow-up assessment using linear mixed model for repeated measures to model the changes overtime for each arm.

    Up to 5 years

Secondary Outcomes (5)

  • Objective-response rate (ORR)

    Up to 5 years

  • Local control rate

    From the first day of therapy to the occurrence of a local and/or regional recurrence (whichever comes first), and death from any cause other than distant metastasis, assessed up to 24 months

  • Overall survival

    Up to 5 years

  • Progression-free survival (PFS)

    From the first day of the therapy to the appearance of local or regional recurrence, distant metastases, secondary primary cancer or death from any cause, assessed up to 24 months

  • PD-L1 expression

    Up to 5 years

Study Arms (3)

Arm A (pembrolizumab, salvage surgery, IORT)

EXPERIMENTAL

Patients receive pembrolizumab IV on day 1 of week 1, and undergo salvage surgery during week 4. Beginning week 8, patients receive pembrolizumab IV every 3 weeks for up to 18 doses in the absence of disease progression or unacceptable toxicity. Patients also undergo IORT for 1 fraction during week 9. Treatment with pembrolizumab may continue beyond initial progression per investigator-assessed clinical benefit and if the patient is tolerating pembrolizumab.

Radiation: Intraoperative Radiation TherapyBiological: PembrolizumabOther: Quality-of-Life AssessmentProcedure: Salvage Surgery

Arm B (pembrolizumab, EBRT, salvage surgery, IORT)

EXPERIMENTAL

Patients receive pembrolizumab IV on day 1 of week 1, and undergo low dose EBRT for 2 fractions on 2 consecutive days during week 4. Patients also undergo salvage surgery during week 8. Beginning week 11, patients receive pembrolizumab IV every 3 weeks for up to 18 doses in the absence of disease progression or unacceptable toxicity. Patients also undergo IORT for 1 fraction during week 11. Treatment with pembrolizumab may continue beyond initial progression per investigator-assessed clinical benefit and if the patient is tolerating pembrolizumab.

Radiation: External Beam Radiation TherapyRadiation: Intraoperative Radiation TherapyBiological: PembrolizumabOther: Quality-of-Life AssessmentProcedure: Salvage Surgery

Arm C (pembrolizumab, EBRT, salvage surgery, IORT)

EXPERIMENTAL

Patients receive pembrolizumab IV on day 1 of week 1, and undergo high dose EBRT for 2 fractions on 2 consecutive days during week 4. Patients also undergo salvage surgery during week 8. Beginning week 11, patients receive pembrolizumab IV every 3 weeks for up to 18 doses in the absence of disease progression or unacceptable toxicity. Patients also undergo IORT for 1 fraction during week 11. Treatment with pembrolizumab may continue beyond initial progression per investigator-assessed clinical benefit and if the patient is tolerating pembrolizumab.

Radiation: External Beam Radiation TherapyRadiation: Intraoperative Radiation TherapyBiological: PembrolizumabOther: Quality-of-Life AssessmentProcedure: Salvage Surgery

Interventions

Undergo IORT

Also known as: Intraoperative Radiotherapy, IORT, radiotherapy, intraoperative
Arm A (pembrolizumab, salvage surgery, IORT)Arm B (pembrolizumab, EBRT, salvage surgery, IORT)Arm C (pembrolizumab, EBRT, salvage surgery, IORT)
PembrolizumabBIOLOGICAL

Given IV

Also known as: Keytruda, Lambrolizumab, MK-3475, SCH 900475
Arm A (pembrolizumab, salvage surgery, IORT)Arm B (pembrolizumab, EBRT, salvage surgery, IORT)Arm C (pembrolizumab, EBRT, salvage surgery, IORT)

Undergo EBRT

Also known as: Definitive Radiation Therapy, EBRT, External Beam Radiation, External Beam Radiotherapy, External Beam RT, external radiation, External Radiation Therapy, external-beam radiation, Radiation, External Beam
Arm B (pembrolizumab, EBRT, salvage surgery, IORT)Arm C (pembrolizumab, EBRT, salvage surgery, IORT)

Ancillary studies

Also known as: Quality of Life Assessment
Arm A (pembrolizumab, salvage surgery, IORT)Arm B (pembrolizumab, EBRT, salvage surgery, IORT)Arm C (pembrolizumab, EBRT, salvage surgery, IORT)

Undergo salvage surgery

Also known as: Rescue Surgery, Salvage Resection, Salvage Surgical Resection, Surgical Salvage
Arm A (pembrolizumab, salvage surgery, IORT)Arm B (pembrolizumab, EBRT, salvage surgery, IORT)Arm C (pembrolizumab, EBRT, salvage surgery, IORT)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Pathologically confirmed either persistent and/ or locoregionally recurrent HNSCC of oral cavity, pharynx, larynx, unknown primary head and neck (H\&N) squamous cell carcinoma
  • Resectable disease as determined by the surgeon and team
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) \< 2
  • At least 18 years of age
  • Adequate hematologic, renal, and hepatic function
  • Must have at least 2 week washout period from prior therapy
  • Willingness and ability to provide informed consent
  • Negative pregnancy test for females of reproductive potential
  • Patients who have undergone therapy for their cancer, such as surgery and/or chemotherapy and/or radiotherapy and recurred
  • Disease measurable by computed tomography (CT) or magnetic resonance imaging (MRI) per RECIST 1.1 criteria.
  • Prior definitive and palliative chemotherapy will be allowed
  • Prior radiation therapy will be allowed
  • Tumor tissue from resected site of disease must be provided for biomarker analyses, in addition to urine and blood sample as scheduled per protocol
  • White blood cell (WBC) \>= 2000/uL (obtained within 14 days of randomization)
  • Neutrophils \>= 1500/uL (obtained within 14 days of randomization)
  • +8 more criteria

You may not qualify if:

  • Requirement of immunosuppressive therapy within 14 days of randomization
  • Salivary gland carcinomas, lip carcinoma, adenocarcinoma of the skin
  • Prior use of immune checkpoint blockade agent
  • History of human immunodeficiency virus (HIV), hepatitis B, C: Participants who test positive for hepatitis B virus surface antigen (HBV sAg) or hepatitis C virus ribonucleic acid (HCV antibody) indicating acute or chronic infection, those who test positive for human immunodeficiency virus (HIV) or have known acquired immunodeficiency syndrome (AIDS)
  • Unresectable disease, as determined by the surgeon and team
  • Subjects with history of grade 3 toxicity with prior immunotherapy
  • Patients with distant metastases
  • Subjects with active autoimmune disease
  • Breastfeeding women
  • Additional prior malignancy within the previous 3 years (treated or untreated, except for skin carcinomas treated with excision alone and carcinoma in situ of the cervix)
  • Palliative radiotherapy less than 14 days prior to first dose of study drug
  • Any history of hypersensitivity to any of the trial medications
  • Poorly controlled or serious medical or psychiatric illness likely to interfere with participation and/or compliance in this clinical trial
  • Prisoners or subjects who are involuntarily incarcerated
  • Patients not available for follow-up/future contact as defined in the ICF
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Ohio State University Comprehensive Cancer Center

Columbus, Ohio, 43210, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Squamous Cell Carcinoma of Head and Neck

Interventions

RadiationRadiotherapypembrolizumab

Condition Hierarchy (Ancestors)

Carcinoma, Squamous CellCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsHead and Neck NeoplasmsNeoplasms by Site

Intervention Hierarchy (Ancestors)

Physical PhenomenaTherapeutics

Study Officials

  • Dukagjin M Blakaj, MD, PhD

    Ohio State University Comprehensive Cancer Center

    PRINCIPAL INVESTIGATOR

Central Study Contacts

The Ohio State University Comprehensive Cancer Center

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

February 9, 2021

First Posted

February 15, 2021

Study Start

May 12, 2022

Primary Completion (Estimated)

December 31, 2026

Study Completion (Estimated)

December 31, 2026

Last Updated

February 2, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will not share

Locations