NCT04736199

Brief Summary

The purpose of the study is to assess the efficacy and safety of darolutamide in combination with standard androgen deprivation therapy (ADT) in patients with metastatic hormone sensitive prostate cancer.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
669

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Feb 2021

Longer than P75 for phase_3

Geographic Reach
15 countries

131 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 29, 2021

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 3, 2021

Completed
20 days until next milestone

Study Start

First participant enrolled

February 23, 2021

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 7, 2024

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

August 8, 2025

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 23, 2026

Completed
Last Updated

February 27, 2026

Status Verified

January 1, 2026

Enrollment Period

3.3 years

First QC Date

January 29, 2021

Results QC Date

May 22, 2025

Last Update Submit

February 9, 2026

Conditions

Keywords

Metastatic hormone-sensitive prostate cancer

Outcome Measures

Primary Outcomes (1)

  • Radiological Progression-free Survival (rPFS) Assessed by Central Review

    rPFS used conventional imaging method (99mTc-phosphonate bone scan, CT/MRI scan). rPFS was defined as the time from the date of randomization to the date of progressive disease in malignant soft tissue lesions, progressive disease in malignant bone lesions, or death due to any cause, whichever occurs first. Malignant soft tissue lesions were assessed by Response Evaluation Criteria in Solid Tumors (RECIST) 1.1 criteria and malignant bone lesions were assessed by Prostate Cancer Clinical Trials Working Group (PCWG3) criteria.

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

Secondary Outcomes (7)

  • Overall Survival (OS)

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

  • Time to Castration-Resistant Prostate Cancer (CRPC)

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

  • Time to Initiation of Subsequent Anti-cancer Therapy

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

  • Time to PSA Progression

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

  • PSA Undetectable Rates (<0.2 ng/mL)

    From randomization to the date when 222 rPFS events were observed, approximately 36 months

  • +2 more secondary outcomes

Study Arms (2)

Darolutamide+ADT

EXPERIMENTAL

Participants will receive darolutamide 600 mg (2 tablets of 300 mg) twice daily with food and ADT of investigator's choice as standard therapy

Drug: Darolutamide (Nubeqa, BAY1841788)Other: Androgen deprivation therapy (ADT)

Placebo+ADT

PLACEBO COMPARATOR

Participants will receive placebo twice daily with food and ADT of investigator's choice as standard therapy

Drug: PlaceboOther: Androgen deprivation therapy (ADT)

Interventions

Coated tablet, oral administration

Darolutamide+ADT

Coated tablet matching Darolutamide in appearance, oral administration

Placebo+ADT

Luteinizing hormone-releasing hormone (LHRH) agonist/antagonists or orchiectomy

Darolutamide+ADTPlacebo+ADT

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed adenocarcinoma of prostate
  • Metastatic disease
  • Started ADT (LHRH agonist/antagonist or orchiectomy) with or without first generation anti-androgen, but not earlier than 12 weeks before randomization
  • Eastern Cooperative Oncology Group (ECOG) Performance Status (PS) of 0, 1 or 2
  • Adequate bone marrow, liver and renal function

You may not qualify if:

  • Prior treatment with: LHRH agonist/antagonists except neoadjuvant and /or adjuvant therapy; Second-generation androgen receptor (AR) inhibitors such as enzalutamide, darolutamide, apalutamide or other investigational AR inhibitors; Cytochrome P17 enzyme inhibitor such as abiraterone acetate or oral ketoconazole as anti-cancer treatment for prostate cancer; Chemotherapy including docetaxel or immunotherapy for prostate cancer; Use of systemic corticosteroid with dose greater than the equivalent 10 mg of prednisone/day within 28 days prior to randomization; Radiopharmaceuticals; Any other anti-cancer treatment for prostate cancer, excluding local therapies and ADT.
  • Treatment with radiotherapy within 2 weeks before randomization
  • Contraindication to iodinated CT and gadolinium chelate MRI intravenous contrast agent(s)
  • Had any of the following within 6 months before randomization: stroke, myocardial infarction, severe/unstable angina pectoris, coronary/peripheral artery bypass graft, congestive heart failure (New York Heart Association Class III or IV)
  • Uncontrolled hypertension as indicated by a resting systolic BP ≥ 160 mmHg or diastolic BP ≥ 100 mmHg despite medical management
  • A gastrointestinal (GI) disorder or procedure which is expected to interfere significantly with absorption of study drug
  • Any prior malignancy (other than adequately treated basal cell or squamous cell skin cancer, superficial bladder cancer, or any other cancer in situ currently in complete remission) within 5 years prior to randomization
  • Inability to swallow oral medications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (131)

Nepean Hospital

Kingswood, New South Wales, 2747, Australia

Location

Northern Cancer Institute

St Leonards, New South Wales, 2065, Australia

Location

Macquarie University Hospital - Oncology Department

Sydney, New South Wales, 2109, Australia

Location

Cancer Research South Australia

Adelaide, South Australia, 5000, Australia

Location

Peninsula Oncology Centre

Frankston, Victoria, 3199, Australia

Location

Austin Health

Heidelberg, Victoria, 3084, Australia

Location

Assistência Multidisciplinar em Oncologia (AMO)

Salvador, Estado de Bahia, 41950-640, Brazil

Location

Hosp. Araujo Jorge da Associação de Combate ao Câncer

Goiânia, Goiás, 74605-070, Brazil

Location

Hospital da Universidade Federal de Minas Gerais

Belo Horizonte, Minas Gerais, 30130-100, Brazil

Location

Cetus Oncologia Hospital Dia

Belo Horizonte, Minas Gerais, 30150-270, Brazil

Location

Liga Paranaense de Combate ao Cancer-Hosp Erasto Gaertner

Curitiba, Paraná, 81520-060, Brazil

Location

Liga Norte Riograndense Contra o Cancer | Centro de Pesquisa Clínica

Natal, Rio Grande do Norte, 59040-000, Brazil

Location

Unidade de Pesquisas Clinicas em Oncologia

Pelotas, Rio Grande do Sul, 96020-080, Brazil

Location

Santa Casa de Porto Alegre | Hospital Sao Francisco - Centro Medico Pesquisa Clinica Cardiologia

Porto Alegre, Rio Grande do Sul, 90020-090, Brazil

Location

Hospital Mae de Deus

Porto Alegre, Rio Grande do Sul, 90850-170, Brazil

Location

FZ Pesquisa e Servicos em Cardiologia | Porto Alegre, Brazil

Porto Alegre, Rio Grande do Sul, 91350-280, Brazil

Location

Fundacao Pio XII - Hospital de Cancer de Barretos

Barretos/SP, São Paulo, 14784-400, Brazil

Location

Hospital de Base | Funfarme - Centro Integrado de Pesquisa - Cardiologia

São José do Rio Preto, São Paulo, 15090-000, Brazil

Location

Urobrasil

São Paulo, São Paulo, 01243-020, Brazil

Location

IBCC - Instituto Brasileiro de Controle do Cancer

São Paulo, São Paulo, 03102-002, Brazil

Location

Inst. de Assistência Médica ao Sérvidor Público Estadual

São Paulo, São Paulo, 04039-004, Brazil

Location

Instituto COI de Educação e Pesquisa

Rio de Janeiro, 22793-080, Brazil

Location

G. Kenneth Jansz Medicine Professional Corporation

Burlington, Ontario, L7N 3V2, Canada

Location

Centre de Recherche du Centre Hospitalier de l'Universite de Montreal (CRCHUM)

Montreal, Quebec, H2X 0A9, Canada

Location

Centro de Investigación Clínica del Sur

Temuco, Región de la Araucanía, 4781156, Chile

Location

OncoCentro

Viña del Mar, Región de Valparaíso, 2520598, Chile

Location

Centro de Estudios Clínicos SAGA SpA

Providencia, Santiago Metropolitan, 7500653, Chile

Location

Fundación Arturo López Perez

Santiago, 7500921, Chile

Location

Oncovida

Santiago, 7510032, Chile

Location

Hospital Clínico de la Pontificia Univ. Católica de Chile

Santiago, TBC, Chile

Location

UROMED

Santiago, Chile

Location

Anhui Provincial Hospital

Hefei City, Anhui Province, Anhui, 230031, China

Location

Beijing Hospital

Beijing, Beijing Municipality, 100730, China

Location

Sun Yat-sen University Cancer Center

Guangzhou, Guangdong, 510000, China

Location

Guangzhou First People Hospital

Guangzhou, Guangdong, 510180, China

Location

Cancer Hospital Chinese Academy of Medical Sciences, Shenzhen Center

Shenzhen, Guangdong, 518172, China

Location

Tongji Hosp. of Tongji Med Coll, Huazhong Uni of Sci & Tech.

Wuhan, Hubei, 430030, China

Location

Zhongnan hospital ,Wuhan University

Wuhan, Hubei, 430071, China

Location

Hubei Cancer Hospital

Wuhan, Hubei, 430079, China

Location

Hunan Cancer Hospital - Oncology Department

Changsha, Hunan, 410013, China

Location

NJ Drum Tower Hospital, the Affil Hos of NJ Univ Med School

Nanjing, Jiangsu, 210008, China

Location

Nantong tumor hospital

Nantong, Jiangsu, 226361, China

Location

The 2nd Affiliated Hospital of Soochow University

Suzhou, Jiangsu, 215004, China

Location

1st Hospital of Jilin University

Changchun, Jilin, 130021, China

Location

Liaoning Cancer Hospital and Institute

Shengyang, Liaoning, 110042, China

Location

Yantai Yuhuangding Hospital

Yantai, Shandong, 264000, China

Location

The First Affiliated Hospital of Xi'an Jiaotong University

Xi’an, Shanxi, 710061, China

Location

SichuanAcademyofMedicalSciences&SichuanProvincialPeople'sHos

Chengdu, Sichuan, 610072, China

Location

Sichuan University West China Hospital

Chengdu, Sichuan, MISSING, China

Location

The 1st Affiliated Hospital of Zhejiang University

Hangzhou, Zhejiang, 310000, China

Location

ZheJiang Provincial People's Hospital

Hangzhou, Zhejiang, 310014, China

Location

Ningbo First Hospital

Ningbo, Zhejiang, 315010, China

Location

The First Affiliated Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, 325000, China

Location

Cancer Hospital, Chinese Academy of Medical Sciences

Beijing, 100000, China

Location

Peking University Third Hospital

Beijing, 100083, China

Location

Beijing Cancer Hospital

Beijing, 100142, China

Location

Mahatma Gandhi Cancer Hospital & Research Institute

Visakhapatnam, Andhra Pradesh, 530017, India

Location

The Gujarat Cancer & Research Institute

Ahmedabad, Gujarat, 380016, India

Location

HCG Cancer Centre - Ahmedabad

Ahmedabad, Gujarat, 380060, India

Location

Cancer Care Clinic - Vadodara

Vadodara, Gujarat, 390007, India

Location

K.L.E.S. Dr. Prabhakar Kore Hospital & Medical Research Centre

Belagavi, Karnataka, 590010, India

Location

Healthcare Global Enterprises Ltd

Bengaluru, Karnataka, 560027, India

Location

Amrita Institute of Medical Sciences

Kochi, Kerala, 682 041, India

Location

Regional Cancer Centre - Thiruvananthapuram

Thiruvananthapuram, Kerala, 695011, India

Location

Marathwada Regional Cancer Centre and Research Institute

Aurangabad, Maharashtra, 431001, India

Location

Jaslok Hospital and Research Centre

Mumbai, Maharashtra, 400026, India

Location

Curie Manavata Cancer Centre

Nashik, Maharashtra, 422004, India

Location

Jehangir Hospital

Pune, Maharashtra, 411001, India

Location

Sparsh Hospital & Critical Care

Bhubaneswar, Odisha, 751007, India

Location

All India Institute of Medical Sciences

Bhubaneswar, Odisha, 751019, India

Location

Jawaharlal Institute Of Postgraduate Medical Education and R

Gorimedu, Puducherry, 605006, India

Location

Christian Medical Center & Hospital

Ludhiana, Punjab, 141008, India

Location

Sawami Man Singh (SMS) Medical College & Attached Hospitals

Jaipur, Rajasthan, 302017, India

Location

Apollo Speciality Hospitals

Madurai, Tamil Nadu, 625020, India

Location

Meenakshi Mission Hospital & Research Centre

Madurai, Tamil Nadu, 625107, India

Location

Post Graduate Institute of Medical Education and Research

Chandigarh, 160012, India

Location

Tata Medical Center

Kolkata, 700156, India

Location

Apex Wellness Hospital

Nashik, 422009, India

Location

Rajiv Gandhi Cancer Institute & Research Centre

New Delhi, 110 085, India

Location

Daugavpils Regional Hospital

Daugavpils, LV-5417, Latvia

Location

RAKUS Hospital Gailezers

Riga, 1038, Latvia

Location

URO Ltd.

Riga, LV-1001, Latvia

Location

P. Stradins Clinical University Hospital

Riga, LV-1002, Latvia

Location

Vidzemes Hospital

Valmiera, LV-4201, Latvia

Location

The Hospital of Lithuanian University of Health SciencesLUHS

Kaunas, LT-50009, Lithuania

Location

PI Klaipedos University Hospital

Klaipėda, LT-92288, Lithuania

Location

National Cancer Institute

Vilnius, LT-08660, Lithuania

Location

Vilnius University Hospital Santaros Klinikos

Vilnius, LT-08661, Lithuania

Location

Tauranga Urology Research Limited

Tauranga, Bay of Plenty, 3112, New Zealand

Location

Canterbury Urology Research Trust

Christchurch, Canterbury, 8013, New Zealand

Location

Waikato Hospital

Hamilton, Waikato Region, 3240, New Zealand

Location

Aliada

San Isidro, Lima region, 15036, Peru

Location

Hospital Guillermo Almenara Irigoyen

Santiago de Surco, Lima region, 15033, Peru

Location

Hospital Militar Luis Arias Schreiber

Lima, LIMA 11, Peru

Location

Clínica El Golf

Lima, LIMA 27, Peru

Location

Arkhangelsk Clinical Oncology Dispensary

Arkhangelsk, 163045, Russia

Location

Ltd "EVIMED"

Chelyabinsk, 454048, Russia

Location

Chelyabinsk Regional Oncology Dispensary

Chelyabinsk, 454087, Russia

Location

Ivanovo Regional Oncology Dispensary

Ivanovo, 153040, Russia

Location

Republican Clinical Oncology Dispensary Kazan

Kazan', 420029, Russia

Location

Research Centre of X-ray and Radiology

Moscow, 117997, Russia

Location

Volga District Med Center FMBA

Nizhny Novgorod, 603109, Russia

Location

LLC Reafan

Novosibirsk, 630099, Russia

Location

Medical Center "Avicenna"

Novosibirsk, 630099, Russia

Location

Clinical Oncological Dispensary of Omsk Region

Omsk, 644013, Russia

Location

AV Medical Group

Saint Petersburg, 196006, Russia

Location

Russian Scientific Radiology and Surgery Technologies Center

Saint Petersburg, 197758, Russia

Location

Scientific Research Instutute of Oncology n.a. N.N. Petrov

Saint Petersburg, 197758, Russia

Location

Multi-Field Clinical Medical Center "Medical City"

Tyumen, 625041, Russia

Location

Republican Clinical Oncology Dispensary

Ufa, 450054, Russia

Location

Vologda Regional Hospital

Vologda, 160022, Russia

Location

Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, 620102, Russia

Location

Cancercare Langenhoven

Port Elizabeth, Eastern Cape, 6045, South Africa

Location

East Rand Medical Research Unit

Johannesburg, Gauteng, 1475, South Africa

Location

University of Pretoria, Clinical Research Unit

Pretoria, Gauteng, 2, South Africa

Location

Cape Town Oncology Trials

Cape Town, 7570, South Africa

Location

Hospital Universitario Fundacion Alcorcon | Urologia

Alcorcón, Madrid, 28922, Spain

Location

Fundacio Puigvert | Urologia

Barcelona, 08025, Spain

Location

Parc Tauli Hospital Universitari | Oncologia

Barcelona, 08208, Spain

Location

Hospital San Pedro De Alcantara | Oncologia

Cáceres, 10003, Spain

Location

Hospital Universitario Virgen De La Victoria | Urologia

Málaga, 20910, Spain

Location

Hospital Universitario Virgen Del Rocio S.L. | Urologia

Seville, 41013, Spain

Location

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, Kaohsiung, 807377, Taiwan

Location

Changhua Christian Hospital

Changhua, 50006, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

National Cheng Kung University Hospital

Tainan, 704, Taiwan

Location

Taipei Veterans General Hospital

Taipei, 11217, Taiwan

Location

CNE "Clinical Center of Oncology, Hematology, Transplantology and Palliative Care of the Cherkasy Regional Council"

Cherkasy, 18009, Ukraine

Location

City Dnipropetrovsk Multi- field Clinical Hosp. 4 DSMA

Dnipro, 49102, Ukraine

Location

Kyiv City Hospital #3 - Department of Urology

Kyiv, 02660, Ukraine

Location

Kyiv Regional Oncological Dispensary

Kyiv, 4107, Ukraine

Location

Related Publications (1)

  • Saad F, Vjaters E, Shore N, Olmos D, Xing N, Pereira de Santana Gomes AJ, Cesar de Andrade Mota A, Salman P, Jievaltas M, Ulys A, Jakubovskis M, Kopyltsov E, Han W, Nevalaita L, Testa I, Le Berre MA, Kuss I, Haresh KP; ARANOTE Study Investigators. Darolutamide in Combination With Androgen-Deprivation Therapy in Patients With Metastatic Hormone-Sensitive Prostate Cancer From the Phase III ARANOTE Trial. J Clin Oncol. 2024 Dec 20;42(36):4271-4281. doi: 10.1200/JCO-24-01798. Epub 2024 Sep 16.

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

darolutamideAndrogen Antagonists

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

Hormone AntagonistsHormones, Hormone Substitutes, and Hormone AntagonistsPhysiological Effects of DrugsPharmacologic ActionsChemical Actions and Uses

Results Point of Contact

Title
Therapeutic Area Head
Organization
Bayer AG

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 29, 2021

First Posted

February 3, 2021

Study Start

February 23, 2021

Primary Completion

June 7, 2024

Study Completion

January 23, 2026

Last Updated

February 27, 2026

Results First Posted

August 8, 2025

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will not share

Availability of this study's data will be determined according to Bayer's commitment to the EFPIA/PhRMA "Principles for responsible clinical trial data sharing". This pertains to scope, timepoint and process of data access. As such, Bayer commits to sharing upon request from qualified researchers patient-level clinical trial data, study-level clinical trial data, and protocols from clinical trials in patients for medicines and indications approved in the US and EU as necessary for conducting legitimate research. This applies to data on new medicines and indications that have been approved by the EU and US regulatory agencies on or after January 01, 2014. Interested researchers can use www.clinicalstudydatarequest.com to request access to anonymized patient-level data and supporting documents from clinical studies to conduct research. Information on the Bayer criteria for listing studies and other relevant information is provided in the Study sponsors section of the portal.

Locations