NCT04710056|Unknown
Expanded Access to REGN4461 for Patients With Diseases Associated With Deficient Leptin Signaling
1 other identifier
R4461-LEPR
Study Type
expanded_access
Target
N/A
Locations
0 countries
Sites
N/A
Timeline
RegisteredJan 2021
Brief Summary
Provide Expanded Access to REGN4461 for patients with diseases associated with deficient leptin signaling.
Trial Health
Trial Relationships
Click on a node to explore related trials.
Study Timeline
Key milestones and dates
First Submitted
Initial submission to the registry
January 13, 2021
Completed1 day until next milestone
First Posted
Study publicly available on registry
January 14, 2021
CompletedLast Updated
March 12, 2026
Status Verified
March 1, 2026
First QC Date
January 13, 2021
Last Update Submit
March 10, 2026
Conditions
Keywords
Leptin (LEP)Leptin Receptors (LEPR)Biallelic Loss of Function Variants of the LEP Gene
Interventions
Eligibility Criteria
Sexall
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Contact the study team to confirm eligibility.
Sponsors & Collaborators
MeSH Terms
Conditions
LipodystrophyLipodystrophy, Congenital Generalized
Condition Hierarchy (Ancestors)
Skin Diseases, MetabolicSkin DiseasesSkin and Connective Tissue DiseasesLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesLipid Metabolism, Inborn ErrorsMetabolism, Inborn ErrorsGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities
Central Study Contacts
Requests for Expanded Access must be initiated by a treating physician. Physicians should contact
CONTACT
Study Design
- Study Type
- expanded access
- Sponsor Type
- INDUSTRY
- Responsible Party
- SPONSOR
Study Record Dates
First Submitted
January 13, 2021
First Posted
January 14, 2021
Last Updated
March 12, 2026
Record last verified: 2026-03