NCT04706663

Brief Summary

Background: Prostate cancer is the most common cancer and the second leading cause of death in males in the United States. Researchers want to find additional gene mutations that may increase a man s risk for prostate cancer and may affect how aggressive the disease is. Objective: To look at gene mutations in men with prostate cancer as well as the course of their disease to better understand how gene mutations relate to the way the cancer progresses and responds to treatment. Eligibility: Adult males 18 and older with prostate cancer who have at least one of the gene mutations researchers want to study and/or have been treated for their cancer and have had complete elimination of their cancer or stable disease for a long time. Design: Participants will be screened with a review of their medical records. Their gene test results will be reviewed, if available. They will be asked questions over the phone or in person. Participants do not need to visit the NIH for this study. But if they visit NIH for another study, their data and test results will be collected. They may give blood and urine samples. They may give leftover tumor samples. These samples will be used to study their genes. Participants who do not come to NIH on regular basis will be contacted every 6 months by phone or e-mail. They will be asked questions about their health. Data from their medical records will be collected. Participants will have testosterone and prostate-specific antigen (PSA) tests. Participants may be invited to NIH to give blood samples for research. Participants on this study will be followed for life.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2,000

participants targeted

Target at P75+ for all trials

Timeline
14mo left

Started Sep 2021

Longer than P75 for all trials

Geographic Reach
1 country

11 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress80%
Sep 2021Jun 2027

First Submitted

Initial submission to the registry

January 12, 2021

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 13, 2021

Completed
8 months until next milestone

Study Start

First participant enrolled

September 14, 2021

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2026

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2027

Last Updated

April 24, 2026

Status Verified

April 22, 2026

Enrollment Period

4.8 years

First QC Date

January 12, 2021

Last Update Submit

April 23, 2026

Conditions

Keywords

germline variantssomatic variantsGenetic PredispositionMolecular GeneticsNatural History

Outcome Measures

Primary Outcomes (2)

  • natural history of prostate cancer with known germline and/or somatic variants

    clinical presentation, patterns of disease progression, therapeutic response, disease recurrence and participant overall survival

    ongoing

  • natural history of TMB-H prostate cancer

    clinical presentation, patterns of disease progression, therapeutic response, disease recurrence and participant overall survival

    ongoing

Study Arms (2)

Cohort 1

Subjects with histologically confirmed prostate cancer and genomic testing results

Cohort 2

Subjects with histologically confirmed prostate cancer who deemed to be an exceptional responder with or without genomic testing results

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

primary clinical

You may qualify if:

  • Subjects with histologically confirmed prostate cancer.
  • Must have known germline and/or somatic variants in PIK3 and/or AKT, PALB2, BRIP1, RAD50, RAD51, RAD54, RB1, SPOP, Wnt/B-catenin pathway, CDK12, and/or MMR genes: MLH1, MSH2, MSH6, PMS2, and EPCAM and/or TMB-high(\[defined as greater than or equal to 10 mutations/megabase (mut/Mb) and/or bTMB \[greater than or equal to 16 mut/Mb\]. NOTE: any platform for genomics testing is acceptable (research or CLIA-certified)
  • be deemed an exceptional responder. NOTE: an exceptional response is defined as achievement of either a) a complete response, or b) a confirmed partial response in a trial or treatment or a response of exceptionally long duration
  • Age greater than or equal to 18 years old.
  • Ability of subject to understand and the willingness to sign a written informed consent document.

You may not qualify if:

  • None

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

University of California San Diego

La Jolla, California, 92093, United States

RECRUITING

University of California San Francisco

San Francisco, California, 94143, United States

RECRUITING

NorthShore University HealthSystem

Evanston, Illinois, 60201, United States

RECRUITING

National Institutes of Health Clinical Center

Bethesda, Maryland, 20892, United States

RECRUITING

Dana Farber Cancer Institute, Boston, MA

Boston, Massachusetts, 02215, United States

RECRUITING

University of Michigan

Ann Arbor, Michigan, 48109, United States

NOT YET RECRUITING

Memorial Sloan Kettering Cancer Center

New York, New York, 10007, United States

RECRUITING

Mount Sinai Hospital

New York, New York, 10029, United States

NOT YET RECRUITING

Weill Cornell Medicine

New York, New York, 10065, United States

NOT YET RECRUITING

Oregon Health Sciences University

Portland, Oregon, 97239, United States

NOT YET RECRUITING

University of Washington

Seattle, Washington, 98195, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Prostatic NeoplasmsGenetic Predisposition to Disease

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital DiseasesDisease SusceptibilityDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Fatima H Karzai, M.D.

    National Cancer Institute (NCI)

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Katherine O Lee-Wisdom, R.N.

CONTACT

Fatima H Karzai, M.D.

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 12, 2021

First Posted

January 13, 2021

Study Start

September 14, 2021

Primary Completion (Estimated)

June 30, 2026

Study Completion (Estimated)

June 30, 2027

Last Updated

April 24, 2026

Record last verified: 2026-04-22

Data Sharing

IPD Sharing
Will share

All IPD recorded in the medical record will be shared with intramural investigators upon request. @@@@@@ In addition, all large scale genomic sequencing data will be shared with subscribers to dbGaP.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Clinical data available during the study and indefinitely.@@@@@@Genomic data are available once genomic data are uploaded per protocol GDS plan for as long as database is active
Access Criteria
Clinical data will be made available via subscription to BTRIS and with the permission of the study PI. @@@@@@Genomic data are made available via dbGaP through requests to the data custodians.

Locations