NCT04634578

Brief Summary

Type 1 retinopathy of prematurity in zone I represents the most severe type of ROP and has the worst prognosis. It is unknown whether low-dose bevacizumab will be successful in these severe cases. Also unknown is the timing and extent of peripheral retinal vascularization after low-dose bevacizumab compared with the standard dose. The current study will evaluate whether doses of 0.063 mg and 0.25mg are effective as treatment for type 1 ROP, with ROP and retinal vessels all in zone I.

Trial Health

78
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
77

participants targeted

Target at P50-P75 for phase_2

Timeline
14mo left

Started May 2022

Longer than P75 for phase_2

Geographic Reach
2 countries

26 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress78%
May 2022Jul 2027

First Submitted

Initial submission to the registry

November 16, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 18, 2020

Completed
1.4 years until next milestone

Study Start

First participant enrolled

May 1, 2022

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2025

Completed
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2027

Expected
Last Updated

February 11, 2026

Status Verified

February 1, 2026

Enrollment Period

3.2 years

First QC Date

November 16, 2020

Last Update Submit

February 9, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Treatment Success at 4 Weeks Post Injection

    Treatment success, determined at 4 weeks, post injection, and meeting all the following criteria: * Improvement by the 4-day exam (3 to 5 days) * No recurrence of type 1 ROP or severe neovascularization requiring additional treatment within 4 weeks of injection.

    4 weeks

Study Arms (2)

Bevacizumab- 0.063 mg

EXPERIMENTAL

Participants will receive a single intravitreal injection of 0.063 mg of bevacizumab in one or both eyes following enrollment into the study. The injection/s should be given as soon as possible but no later than 2 days after the diagnosis of type 1 ROP meeting all of the inclusion criteria and none of the exclusion criteria.

Drug: Bevacizumab

Bevacizumab- 0.25 mg

EXPERIMENTAL

Participants will receive a single intravitreal injection of 0.25 mg of bevacizumab in one or both eyes following enrollment into the study. The injection/s should be given as soon as possible but no later than 2 days after the diagnosis of type 1 ROP meeting all of the inclusion criteria and none of the exclusion criteria.

Drug: Bevacizumab

Interventions

All participants will receive a single intravitreal injection of bevacizumab in one or both eyes following enrollment into the study. The injection/s should be given as soon as possible but no later than 2 days after the diagnosis of type 1 ROP meeting all of the inclusion criteria and none of the exclusion criteria. Eyes meeting eligibility criteria will receive a single dose of 0.063 mg or 0.25mg bevacizumab provided by the pharmacy at the investigator's institution.

Also known as: Avastin
Bevacizumab- 0.063 mgBevacizumab- 0.25 mg

Eligibility Criteria

AgeUp to 6 Months
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Birth weight \< 1251 grams
  • Newly diagnosed (within 2 days) type 1 ROP in zone I in one or both eyes

You may not qualify if:

  • Previous treatment for ROP
  • Stage 4 or 5 ROP in either eye
  • Treatment could not be done within 2 days of diagnosis of type 1 ROP
  • Investigator unwilling to randomize or parent unwilling to accept randomized assignment to either treatment
  • Transfer to another hospital anticipated within the next 4 weeks where exams by study-certified examiners are not available. If hospital discharge is anticipated within the next 4 weeks, parents unable or unwilling to return to the PEDIG site for outpatient follow-up visits.
  • Active ocular infection or purulent nasolacrimal duct obstruction in either eye
  • One eye will be excluded, and other eye may be eligible, if either of the following are present:
  • Visually significant ocular anomaly (e.g., cataract, coloboma)
  • Opacity that precludes an adequate view of the retina

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (26)

Arkansas Childrens Hospital/ University of Arkansas Medical Sciences

Little Rock, Arkansas, 72202, United States

Location

Univ of California, Irvine- Gavin Herbert Eye Institute

Irvine, California, 92697, United States

Location

Jules Stein Eye Institute at the University of California, Los Angeles

Los Angeles, California, 90095, United States

Location

University of California, Davis

Sacramento, California, 95817, United States

Location

University of California San Francisco Department of Ophthalmology

San Francisco, California, 94143, United States

Location

The Emory Eye Center

Atlanta, Georgia, 30322, United States

Location

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

Location

U of Illinois at Chicago Eye and Ear Infirmary

Chicago, Illinois, 60612, United States

Location

University of Chicago

Hyde Park, Illinois, 60637, United States

Location

Indiana University School of Medicine

Indianapolis, Indiana, 46202, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

UK Ophthalmology and Visual Sciences, The Eye Clinic

Lexington, Kentucky, 40508, United States

Location

Greater Baltimore Medical Center

Baltimore, Maryland, 21204-5809, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02215, United States

Location

New York Presbyterian David H Koch Center

New York, New York, 10065, United States

Location

Duke University Eye Center

Durham, North Carolina, 27710, United States

Location

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229, United States

Location

Pediatric Ophthalmology Associates, Inc.

Columbus, Ohio, 43205, United States

Location

Casey Eye Institute

Portland, Oregon, 97239, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

Location

UPMC Children's Eye Center of Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, 15224, United States

Location

Storm Eye Institute

Mt. Pleasant, South Carolina, 29464, United States

Location

Texas Children's Hospital - Dept. Of Ophthalmology

Houston, Texas, 77030, United States

Location

University of Utah Moran Eye Center

Salt Lake City, Utah, 84132, United States

Location

Virginia Pediatric Eye Center

Norfolk, Virginia, 23502, United States

Location

IWK Health Centre

Halifax, Nova Scotia, B3K 6R8, Canada

Location

Related Links

MeSH Terms

Conditions

Retinopathy of Prematurity

Interventions

Bevacizumab

Condition Hierarchy (Ancestors)

Retinal DiseasesEye DiseasesInfant, Premature, DiseasesInfant, Newborn, DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • David K Wallace, MD, MPH

    Vanderbilt University

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 16, 2020

First Posted

November 18, 2020

Study Start

May 1, 2022

Primary Completion

July 1, 2025

Study Completion (Estimated)

July 1, 2027

Last Updated

February 11, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

In accordance with the NIH data sharing policy, a de-identified database is placed in the public domain on the Pediatric Eye Disease Investigator Group (PEDIG) public website after the completion of each protocol and publication of the primary manuscript.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Data will be made available after publication of each primary manuscript.
Access Criteria
Users accessing the data must enter an email address.

Locations