NCT04614246

Brief Summary

The purpose of this study is to assess safety and efficacy of BAY 1817080 compared to elagolix and placebo in women with symptomatic endometriosis. Study details include:

  • Study duration: 155 up to 285 days
  • Treatment duration: 84 days
  • Visit frequency: 3 laboratory every 2 weeks for participants on BAY 1817080 or placebo

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
215

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jan 2021

Shorter than P25 for phase_2

Geographic Reach
19 countries

143 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 2, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 3, 2020

Completed
3 months until next milestone

Study Start

First participant enrolled

January 29, 2021

Completed
12 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 17, 2022

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 3, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 31, 2023

Completed
Last Updated

August 1, 2023

Status Verified

July 1, 2023

Enrollment Period

12 months

First QC Date

November 2, 2020

Results QC Date

January 13, 2023

Last Update Submit

July 28, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Absolute Change in Mean Worst Endometriosis Associated Pelvic Pain (EAPP), Primary Per Protocol Set (pPPS)

    The worst EAPP was measured daily on the 0-10 Numerical Rating Scale (NRS) by item 1 of the Endometriosis Symptom Diary (ESD). In question 1, participants were asked to rate the pain in the target area during the past 24 hours, where 0= no pain and 10= worst imaginable pain and responses were recorded in ESD. The absolute change in mean worst EAPP was from baseline (last 28 days before the first intake of study drug) to end of intervention (last 28 days ending with the last intake of study drug planned on Day 84 \[+3\]). The time frame of 28 days captures a menstrual cycle on average.

    change from baseline to week 12

Secondary Outcomes (2)

  • Least Squares Mean (SE) Changes in Worst EAPP From Baseline to Week 12, Per Protocol Set

    change from baseline to week 12

  • Number of Participants With Treatment-emergent Adverse Events (TEAE)

    up to 14 days after the last study medication intake

Study Arms (5)

BAY1817080 150 mg

EXPERIMENTAL

Participants will receive 150 mg of BAY1817080 twice daily over a 12-week intervention period

Drug: BAY1817080

BAY1817080 75 mg

EXPERIMENTAL

Participants will receive 75 mg of BAY1817080 twice daily over a 12-week intervention period

Drug: BAY1817080

BAY1817080 25 mg

EXPERIMENTAL

Participants will receive 25 mg of BAY1817080 twice daily over a 12-week intervention period

Drug: BAY1817080

Elagolix

ACTIVE COMPARATOR

Participants will receive 150 mg of Elagolix once daily over a 12-week intervention period

Drug: Elagolix

Placebo

PLACEBO COMPARATOR

Participants will receive placebo matching BAY1817080 twice daily over a 12-week intervention period

Drug: Placebo

Interventions

Tablet, oral administration

BAY1817080 150 mgBAY1817080 25 mgBAY1817080 75 mg

Tablet, oral administration

Elagolix

Tablet, oral administration

Placebo

Eligibility Criteria

Age18 Years+
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participant must be ≥ 18 years of age at the time of signing the informed consent
  • Visually-confirmed endometriosis: detection of endometriotic lesions during laparoscopy or laparotomy (with or without pathological diagnosis) within 10 years but no less than 8 weeks from Visit 1a (surgically diagnosed endometriosis). For Japan only and limited to no more than half of all randomized Japanese participants: the diagnosis can be based on previous imaging (i.e. endometriosis lesion detected by ultrasound or MRI). If the participant was diagnosed by ultrasound, the lesion must be visualized again by ultrasound at the screening visit. If the participant was diagnosed by MRI, the diagnosis must have been made within 12 months before Visit 1a (clinically diagnosed endometriosis).
  • Both sub-criteria regarding pain symptoms must be fulfilled:
  • At Visit 1a, participant presents self-reported moderate to severe pain which - based on the judgement of the investigator - carries a reasonable likelihood to translate into a severity of pain symptoms sufficient to fulfil the eligibility criterion and be caused by endometriosis, and
  • During the screening period at least 24 daily ESD entries during the 28 consecutive days starting on the first day with menstrual bleeding at or after Visit 1a and entries in the ESD item 1a ('worst pain' on the daily numerical rating scale) sum up to 98 or more.
  • Willingness to use standardized rescue pain medications for EAPP (i.e. ibuprofen, acetaminophen and tramadol) and not use any prophylactic pain medication, according to investigator's instruction
  • Ability to swallow the study intervention, i.e., the different kinds of tablets, as complete units
  • Good general health (except for findings related to endometriosis) as proven by medical history, physical and gynecological examinations and laboratory test results
  • Normal or clinically insignificant cervical cytology not requiring further follow-up:
  • A cervical cytology sample has to be obtained during screening, or
  • A documented normal result has to be available from cervical cytology conducted within 12 months prior to Visit 1a.
  • Human papilloma virus (HPV) testing in participants with atypical squamous cells of unknown significance (ASCUS) will be used as an adjunctive test automatically. Participants with ASCUS can be included if they are negative for high-risk HPV strains.

You may not qualify if:

  • Current pregnancy or less than 3 months since delivery, abortion or stop of lactation before Visit 1a
  • Hypersensitivity to any ingredient of the study intervention and/or the standardized rescue medications
  • Known osteoporosis
  • History of a low trauma fracture
  • Contraindications for elagolix or the standardized rescue medications
  • Current malignancy or history of cancer (exception: basal cell or squamous cell carcinoma of the skin) within the last 5 years prior to Visit 1a
  • Any other diseases or conditions that according to the investigator can compromise the function of the body systems and could result in altered absorption, excessive accumulation, impaired metabolism, or altered excretion of the study intervention (e.g. extremely low body weight, chronic bowel disease, Crohn's disease and ulcerative colitis)
  • Any disease or condition that may worsen during the study period according to the assessment and opinion of the investigator
  • Abnormal uterine bleeding in terms of regularity or heaviness (with the exception of heavy menstrual bleeding that does not require treatment)
  • Any findings that require further diagnostic procedures to avoid harm to the participant (e.g. ovarian tumors of uncertain origin or pelvic masses of unclear etiology)
  • Any serious or unstable diseases or medical conditions, including psychiatric disorders, that might interfere with the conduct of the study or the interpretation of the result, including for example:
  • history of hysterectomy and/or bilateral oophorectomy
  • any conditions considered to contribute significantly to pelvic pain by the investigator, e.g. fibromyalgia, uterine fibroids, irritable bowel syndrome or other bowel disorders
  • any other underlying diseases requiring regular use of pain medication (e.g. migraine)
  • history of or current anxiety or depression unless stable with or without medical treatment ≥ 6 months before Visit 1a
  • +11 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (147)

Accel Research Sites - Cahaba Medical Care

Birmingham, Alabama, 35218, United States

Location

University of Alabama at Birmingham

Birmingham, Alabama, 35294-0026, United States

Location

Mobile Ob-Gyn, PC

Mobile, Alabama, 36608-6703, United States

Location

Precision Trials, AZ, LLC

Phoenix, Arizona, 85032, United States

Location

Diagnamics, Inc.

Encinitas, California, 92024, United States

Location

West Coast OB/GYN Associates

San Diego, California, 92123, United States

Location

Advanced Women's Health Institute

Greenwood Village, Colorado, 80111, United States

Location

Office of Dr. James A. Simon, MD

Washington D.C., District of Columbia, 20036, United States

Location

Helix Biomedics, LLC

Boynton Beach, Florida, 33435, United States

Location

Alliance for Multispecialty Research, LLC - Fort Meyers

Fort Myers, Florida, 33912, United States

Location

Suncoast Clinical Research Center, Inc.

New Port Richey, Florida, 34652, United States

Location

A Premier Medical Research of Florida, LLC

Orange City, Florida, 32763, United States

Location

Physician Care Clinical Research

Sarasota, Florida, 34239, United States

Location

Medisense, Inc.

Atlanta, Georgia, 30363, United States

Location

Augusta University Medical Center

Augusta, Georgia, 30912, United States

Location

Paramount Research Solutions-College Park

College Park, Georgia, 30349, United States

Location

Journey Medical Research

Snellville, Georgia, 30078, United States

Location

Clinical Research Prime

Idaho Falls, Idaho, 83404, United States

Location

Southern Clinical Research Associates LLC

Metairie, Louisiana, 70001, United States

Location

Continental Clinical Solutions, LLC

Towson, Maryland, 21204, United States

Location

Wayne State University Physicians Group

Detroit, Michigan, 48201, United States

Location

Essential Women's Health Associates

Las Vegas, Nevada, 89113, United States

Location

Bosque Womens Care

Albuquerque, New Mexico, 87109, United States

Location

SUNY Downstate Medical Center

Brooklyn, New York, 11203, United States

Location

Carolina Women's Research & Wellness Center

Durham, North Carolina, 27713, United States

Location

Lyndhurst Clinical Research

Winston-Salem, North Carolina, 27103, United States

Location

Clinical Inquest Center, Ltd.

Beavercreek, Ohio, 45432, United States

Location

Aventiv Research - Dublin

Dublin, Ohio, 43016, United States

Location

Centricity Research formerly Aventiv - Dublin

Dublin, Ohio, 43016, United States

Location

HWC Women's Research Center

Englewood, Ohio, 45322, United States

Location

University Hospitals Landerbrook Health Center

Mayfield Heights, Ohio, 44124, United States

Location

Palmetto Clinical Research

Summerville, South Carolina, 29485, United States

Location

Chattanooga Medical Research, LLC

Chattanooga, Tennessee, 37404, United States

Location

ClinSearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

Medical Research Center of Memphis, LLC

Memphis, Tennessee, 38120, United States

Location

International Clinical Research-Tennessee LLC.

Murfreesboro, Tennessee, 37130, United States

Location

Discovery Clinical Trials - Dallas

Dallas, Texas, 75230, United States

Location

UT Health Women's Research Center at Memorial City

Houston, Texas, 77024, United States

Location

Biopharma Informatic, Inc.

Houston, Texas, 77043, United States

Location

Centex Studies, Inc.

Houston, Texas, 77058, United States

Location

Centex Studies, Inc.

Houston, Texas, 77090, United States

Location

Advances in Health

Pearland, Texas, 77584, United States

Location

Tidewater Clinical Research, Inc.

Norfolk, Virginia, 23456, United States

Location

Eastern Virginia Medical School | OB/GYN Clinical Research Center

Norfolk, Virginia, 23507, United States

Location

Eastern Virginia Medical School

Norfolk, Virginia, 23507, United States

Location

Virginia Physicians For Women

North Chesterfield, Virginia, 23235, United States

Location

Seattle Clinical Research Center

Seattle, Washington, 98105, United States

Location

Medizinische Universität Graz

Graz, Styria, 8036, Austria

Location

Universitätsklinikum AKH Wien

Vienna, 1090, Austria

Location

AZ Jan Palfijn Gent

Ghent, Oost-Vlaanderen, 9000, Belgium

Location

CU Saint-Luc/UZ St-Luc

Bruxelles - Brussel, 1200, Belgium

Location

Ziekenhuis Oost-Limburg

Genk, 3600, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

MC Asklepii OOD

Dupnitsa, 2600, Bulgaria

Location

Spec. Hospital for Active Treatment of Oncological Diseases

Sofia, 1233, Bulgaria

Location

Medical Center Panaceya

Sofia, 1606, Bulgaria

Location

MHAT Niamed

Stara Zagora, 6000, Bulgaria

Location

SHOGAT Prof Dimitar Stamatov

Varna, 9000, Bulgaria

Location

The Ottawa Hospital

Ottawa, Ontario, K1H 7W9, Canada

Location

The Ottawa Hospital | The Ottawa Hospital Research Institute - Neurology - Ottawa Stroke Program

Ottawa, Ontario, K1Y4E9, Canada

Location

The Ottawa Hospital

Ottawa, Ontario, K1Y4E9, Canada

Location

Clinique OVO

Montreal, Quebec, H4P 2S4, Canada

Location

Alpha Recherche Clinique LB9

Québec, G2J 0C4, Canada

Location

First Affiliated Hospital of Guangzhou Medical University

Guangzhou, Guangdong, 510120, China

Location

Guangzhou Women and Children's Medical Center

Guangzhou, Guangdong, 510623, China

Location

Wuhan Tongji Reproductive Medicine Hospital

Wuhan, Hubei, 430013, China

Location

The Second Affiliated Hospital of Nanjing Medical university

Nanjing, Jiangsu, 210000, China

Location

The Second Affiliated Hospital of Nanjing Medical university

Nanjing, Jiangsu, 210011, China

Location

Women's Hospital School of Medicine Zhejiang University

Hangzhou, Zhejiang, 310006, China

Location

Beijing Obstetrics and Gynecology Hospital,Capital Med.Uni.

Beijing, 100026, China

Location

Peking University First Hospital

Beijing, 100034, China

Location

Fakultni nemocnice Brno

Brno, 625 00, Czechia

Location

Gynekologie Meda s.r.o. - Lidicka

Brno-střed, 60200, Czechia

Location

GYN-MIKA s.r.o.

České Budějovice, 370 01, Czechia

Location

GynCare MUDr. Michael Svec s.r.o.

Pilsen, 326 00, Czechia

Location

Centrum gynekologicke rehabilitace

Písek, 39701, Czechia

Location

GYNERA

Prague, 156 00, Czechia

Location

Gynekologie Studentsky dum s.r.o.

Prague, 160 00, Czechia

Location

Fakultní nemocnice Bulovka

Prague, 180 81, Czechia

Location

Dr. Smrhova-Kovacs

Tábor, 39003, Czechia

Location

Parnu Hospital

Pärnu, 80010, Estonia

Location

Clinic Elite

Tartu, 50407, Estonia

Location

HUS / Naistenklinikka

Helsinki, 00029, Finland

Location

Lääkärikeskus Gyneko

Oulu, 90100, Finland

Location

Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, 69120, Germany

Location

Praxisklinik am Rosengarten

Mannheim, Baden-Wurttemberg, 68165, Germany

Location

Praxis f. Gynäkologie und Geburtshilfe

Bernburg, Saxony-Anhalt, 06406, Germany

Location

emovis GmbH

Berlin, 10629, Germany

Location

Charité - Campus Virchow-Klinikum (CVK)

Berlin, 13353, Germany

Location

ARETAIEION University Hospital

Athens, 11528, Greece

Location

University General Hospital of Patras | Univ Obs & Gynae Cli

Pátrai, 26504, Greece

Location

Cortex Study Center

Budapest, 1026, Hungary

Location

SZTE ÁOK Szent Györgyi Albert Klinikai Kozpont

Szeged, 6725, Hungary

Location

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Rome, Lazio, 00168, Italy

Location

IRCCS Ospedale Policlinico San Martino

Genoa, Liguria, 16132, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Lombardy, 20122, Italy

Location

ASST Sette Laghi

Varese, Lombardy, 21100, Italy

Location

A.O.U. Careggi

Florence, Tuscany, 50134, Italy

Location

A.O.U.I. Verona

Verona, Veneto, 37126, Italy

Location

Aiiku Ladies Clinic

Funabashi, Chiba, 274-0071, Japan

Location

Tokyo Bay Urayasu Ichikawa Medical Center

Urayasu, Chiba, 279-0001, Japan

Location

Sou Clinic

Yotsukaidō, Chiba, 284-0001, Japan

Location

Teine Keijinkai Hospital

Sapporo, Hokkaido, 006-8555, Japan

Location

Social Medical Corporation Tokeidai Memorial Hospital

Sapporo, Hokkaido, 060-0031, Japan

Location

Nishikawa Women's Health Clinic

Sapporo, Hokkaido, 060-0061, Japan

Location

Hitachi General Hospital

Hitachi, Ibaraki, 317-0077, Japan

Location

Ibaraki Prefectural Central Hospital

Kasama, Ibaraki, 309-1793, Japan

Location

Fujisawa City Hospital

Fujisawa, Kanagawa, 251-8550, Japan

Location

Yokosuka Kyosai Hospital

Yokosuka, Kanagawa, 238-8558, Japan

Location

Kurashiki Medical Clinic

Kurashiki, Okayama-ken, 710-0824, Japan

Location

Suita Tokushukai Hospital

Suita, Osaka, 565-0814, Japan

Location

Omi Medical Center

Kusatsu, Shiga, 525-8585, Japan

Location

Kashiwazaki ladies clinic

Saitama, Tokyo, 330-0855, Japan

Location

NTT Medical Center Tokyo

Shinagawa-ku, Tokyo, 141-8625, Japan

Location

Toyama Rosai Hospital

Uozu, Toyama, 937-0042, Japan

Location

JCHO Tokuyama Central Hospital

Shūnan, Yamaguchi, 745-8522, Japan

Location

Japanese Red Cross Kumamoto Hospital

Kumamoto, 861-8520, Japan

Location

Saiseikai Nagasaki Hospital

Nagasaki, 850-0003, Japan

Location

Nagasaki University Hospital

Nagasaki, 852-8501, Japan

Location

Latvian Maritime Medicine Center

Riga, LV-1005, Latvia

Location

Vitols and Vitols Ltd

Riga, LV-1006, Latvia

Location

I.Vasaraudzes Private Practice

Riga, LV-1011, Latvia

Location

I.Dinsbergas Physician Practice

Riga, LV-1013, Latvia

Location

JSC Seimos gydytojas family medical center

Vilnius, LT-01118, Lithuania

Location

V. Jonaitienes private gynecology clinic

Vilnius, LT-01123, Lithuania

Location

JSC Gyvenk Silciau Medical Center Maxmeda

Vilnius, LT-03225, Lithuania

Location

Kirkeparken Spesialistpraksis

Fredrikstad, 1605, Norway

Location

Oslo Universitetssykehus HF, Ullevål

Oslo, 0450, Norway

Location

Sykehuset i Vestfold HF, Tønsberg

Tønsberg, 3116, Norway

Location

Gabinet Ginekologiczny Janusz Tomaszewski

Bialystok, 15-244, Poland

Location

MICS Centrum Medyczne Torun

Bydgoszcz, 85-065, Poland

Location

CLINICAL MEDICAL RESEARCH Sp. z o. o.

Katowice, 40-156, Poland

Location

NZOZ MEDEM Wilk Sp. j.

Katowice, 40-301, Poland

Location

Vita Longa Sp. z o.o.

Katowice, 40-748, Poland

Location

Prywatny Gabinet Lekarski Ginekologia, Poloznictwo i Ultr.

Lodz, 90-602, Poland

Location

Specjalistyczny Gabinet Ginekologiczno-Polozniczy

Lublin, 20-400, Poland

Location

NZOZ NOVITA, Specjalistyczne Gabinety Lekarskie S.C

Lublin, 20-632, Poland

Location

VitroLive Sp. z o.o.

Szczecin, 70-483, Poland

Location

MTZ Clinical Research Sp z o.o.

Warsaw, 02-106, Poland

Location

Medical Concierge Centrum Medyczne

Warsaw, 02-798, Poland

Location

ULMUS, s r.o.

Hlohovec, 920 01, Slovakia

Location

GA Lucenec s.r.o

Lučenec, 984 01, Slovakia

Location

Virina sano, s.r.o. Gynekologicko porodnicka ambulancia

Veľký Krtíš, 990 01, Slovakia

Location

Hospital de Basurto

Bilbao, Vizcaya, 48013, Spain

Location

Hospital de la Santa Creu i de Sant Pau | Ginecologia

Barcelona, 08041, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Hospital General Universitario de Valencia

Valencia, 46014, Spain

Location

Related Publications (2)

  • Parke S, Gude K, Roth K, Messina F. Efficacy and safety of eliapixant in endometriosis-associated pelvic pain: the randomized, placebo-controlled phase 2b SCHUMANN study. BMC Womens Health. 2024 Jun 19;24(1):353. doi: 10.1186/s12905-024-03188-8.

  • Fletcher MC. Selectivity of the P2X3 receptor antagonist Eliapixant, and its potential use in the treatment of endometriosis. Purinergic Signal. 2022 Mar;18(1):1-3. doi: 10.1007/s11302-021-09831-5. Epub 2022 Jan 3. No abstract available.

Related Links

MeSH Terms

Conditions

Endometriosis

Interventions

elagolix

Condition Hierarchy (Ancestors)

Genital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital Diseases

Results Point of Contact

Title
Therapeutic Area Head
Organization
Bayer AG

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double blind to placebo and open-label for active comparator
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 2, 2020

First Posted

November 3, 2020

Study Start

January 29, 2021

Primary Completion

January 17, 2022

Study Completion

May 3, 2022

Last Updated

August 1, 2023

Results First Posted

May 31, 2023

Record last verified: 2023-07

Data Sharing

IPD Sharing
Will not share

Availability of this study's data will be determined according to Bayer's commitment to the EFPIA/PhRMA "Principles for responsible clinical trial data sharing". This pertains to scope, timepoint and process of data access. As such, Bayer commits to sharing upon request from qualified researchers patient-level clinical trial data, study-level clinical trial data, and protocols from clinical trials in patients for medicines and indications approved in the US and EU as necessary for conducting legitimate research. This applies to data on new medicines and indications that have been approved by the EU and US regulatory agencies on or after January 01, 2014. Interested researchers can use www.clinicalstudydatarequest.com to request access to anonymized patient-level data and supporting documents from clinical studies to conduct research. Information on the Bayer criteria for listing studies and other relevant information is provided in the Study sponsors section of the portal.

Locations