NCT04523220

Brief Summary

In this study researchers want to learn about the safety of drug Osocimab at lower-dose and higher-doses in adult participants with kidney disease undergoing regular dialysis (a procedure that uses a machine to get rid of toxins and extra fluids in the blood). Patients with kidney disease undergoing regular dialysis are at high risk for heart and blood vessels diseases. Osocimab is a human monoclonal antibody under development for the prevention of events caused by blood clots like heart attack, stroke and death due to heart or blood vessels diseases. It works by binding to and blocking the activated form of clotting factor XI which increases the formation and stability of clots. Researchers also want to find out how drug Osocimab works in human body and how the body absorbs, distributes and excretes the drug. Participants in this study will receive monthly injection of either Osocimab at a lower-dose or higher-dose or placebo (a placebo looks like a treatment but does not have any medicine in it). Both Osocimab and placebo will be injected into the tissue under the skin of the belly. Observation for each participant will last up to 23 months. Blood samples will be collected from the participants to monitor the safety and measure the blood level of the study drug.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
704

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2020

Geographic Reach
18 countries

147 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 20, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

August 21, 2020

Completed
7 days until next milestone

Study Start

First participant enrolled

August 28, 2020

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 28, 2021

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 30, 2022

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

July 21, 2023

Completed
Last Updated

July 21, 2023

Status Verified

July 1, 2023

Enrollment Period

1.3 years

First QC Date

August 20, 2020

Results QC Date

May 5, 2023

Last Update Submit

July 13, 2023

Conditions

Keywords

End-stage renal disease (ESRD)Hemodialysis

Outcome Measures

Primary Outcomes (2)

  • Cumulative Incidence Risk of the First Composite of Major Bleeding (MB) and Clinically-relevant Non-major Bleeding (CRNMB) Events as Assessed by Blinded Central Independent Adjudication Committee (CIAC)

    Cumulative incidence risk of the first Composite of MB and CRNMB (ISTH) at month 6 is reported in the table. Descriptive time to composite of MB and CRNMB Events is reported in statistical analysis. Descriptive time to composite of treatment emergent major and CRNMB events \[in alignment with International Society on Thrombosis and Haemostatsis (ISTH) guidelines\] analyses were performed. The cumulative incidence function for the event-of-interest together with the corresponding confidence interval were estimated for each treatment arm using Aalen-Johansen estimators. Cumulative incidence of events up to the day, inclusive.

    From the first dose of study intervention up till 30 days after last study intervention in the main treatment period, up to 6 months

  • Cumulative Incidence Risk of Composite of Moderate and Severe Adverse Events (AEs) and Serious Adverse Events (SAEs)

    Cumulative incidence risk of composite of moderate and severe AEs and SAEs at month 6 is reported in the table. Descriptive time to the composite of Moderate and Severe AEs and SAEs is reported in statistical analysis. An AE was any untoward medical occurrence in a patient or clinical study participant, whether or not considered related to the study intervention.

    From the first dose of study intervention up until 30 days after last study intervention in the main treatment period, up to 6 months

Secondary Outcomes (2)

  • Ratio of Activated Partial Thromboplastin Time (aPTT) at 6 Months Trough Levels Versus Baseline.

    At 6 months (Visit 19 / Day 30 of the 6th month)

  • Ratio of Factor XI (FXI) Activity at 6 Months Trough Levels Versus Baseline

    At 6 months (Visit 19 / Day 30 of the 6th month)

Study Arms (4)

BAY1213790 low dose

EXPERIMENTAL

Participants will receive Osocimab (BAY1213790) 105 mg single loading dose as subcutaneous abdominal injection, followed by monthly maintenance doses of 52.5 mg until the end of the extension treatment period.

Drug: BAY1213790 (Osocimab)

Placebo low dose

PLACEBO COMPARATOR

Placebo will be administered subcutaneously in the same manner as Osocimab.

Drug: Placebo

BAY1213790 high dose

EXPERIMENTAL

Participants will receive Osocimab (BAY1213790) 210 mg single loading dose as subcutaneous abdominal injection, followed by monthly maintenance doses of 105 mg until the end of the extension treatment period.

Drug: BAY1213790 (Osocimab)

Placebo high dose

EXPERIMENTAL

Placebo will be administered subcutaneously in the same manner as Osocimab.

Drug: Placebo

Interventions

Single loading dose as subcutaneous abdominal injection followed by monthly maintenance doses.

BAY1213790 high doseBAY1213790 low dose

Subcutaneous administration in the same manner as Osocimab.

Placebo high dosePlacebo low dose

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants must be at least 18 years of age
  • Patients with end-stage renal disease on hemodialysis (including hemodiafiltration) for ≥3 months, receiving dialysis at least 9 hours a week and stable in the view of the investigator
  • Body weight of at least 50 kg
  • Male and/or female. Contraceptive use by men or women should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies.

You may not qualify if:

  • Recent (\<6 months before screening) clinically significant bleeding
  • Hemoglobin (Hb) \< 9.0 g/dL at screening
  • Platelet count \< 100 x 10\^9/L
  • aPTT or PT \> ULN (upper limit of normal)
  • Hepatic disease associated with ALT \> 3x ULN, or total bilirubin \>2x ULN with direct bilirubin \> 20% of the total
  • Sustained uncontrolled hypertension (diastolic blood pressure ≥100 mmHg and/or systolic blood pressure ≥ 180 mmHg)
  • Known intracranial neoplasm, arteriovenous malformation or aneurysm
  • Known bleeding disorders e.g. von-Willebrand disease or Hemophilia A, B or C
  • Recent (\<3 months before screening) thromboembolic event, e.g. acute coronary syndrome, stroke or VTE (except dialysis access thrombosis)
  • Recent (\<3 months before screening) major surgery or scheduled major surgery during study participation
  • Scheduled living donor renal transplant during study participation
  • Persistent heart failure as classified by the New York Heart Association (NYHA) classification of 3 or higher
  • Receiving antiplatelet therapy except daily ASA ≤ 150 mg/day
  • Receiving anticoagulation in therapeutic doses, other than standard anticoagulation during the hemodialysis procedure

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (151)

North America Research Institute - Azusa

Azusa, California, 91702, United States

Location

Fresenius Kidney Care - Brawley

Brawley, California, 92227, United States

Location

DaVita South Valley Dialysis

Encino, California, 91316, United States

Location

Fresenius Kidney Care - La Mesa

La Mesa, California, 91942, United States

Location

East L.A. Dialysis Center

Los Angeles, California, 90022, United States

Location

Van Buren Dialysis Center

Riverside, California, 92503, United States

Location

Fresenius Kidney Care Kearny Mesa

San Diego, California, 92111, United States

Location

FMC San Ysidro

San Diego, California, 92154, United States

Location

Queen's Dialysis Unit

West Covina, California, 91790, United States

Location

DaVita Greater Waterbury Dialysis

Waterbury, Connecticut, 06708, United States

Location

ARA Plantation Dialysis, LLC

Ellenton, Florida, 34222, United States

Location

ARA Augusta

Augusta, Georgia, 30901, United States

Location

Liberty Dialysis- Caldwell

Caldwell, Idaho, 83605, United States

Location

Fresenius Kidney Care Evergreen Park

Evergreen Park, Illinois, 60805, United States

Location

Fresenius Kidney Care Baton Rouge Mancuso Lane

Baton Rouge, Louisiana, 70808, United States

Location

Fresenius Kidney Care South Dialysis

Shreveport, Louisiana, 71106, United States

Location

ARA Holyoke Dialysis Center

Holyoke, Massachusetts, 01040, United States

Location

Davita Hospital Hill Dialysis

Kansas City, Missouri, 64108, United States

Location

Renal Medicine Associates

Albuquerque, New Mexico, 87109, United States

Location

Durham Nephrology Associates, Pa

Durham, North Carolina, 27704, United States

Location

Waterloo Dialysis

Austin, Texas, 78756, United States

Location

Fresenius North Austin Dialysis Center

Austin, Texas, 78758, United States

Location

Fresenius Kidney Care - Mission Bend (FMCNA #3971)

Houston, Texas, 77083, United States

Location

Fresenius Kidney Care Sugar Land

Sugar Land, Texas, 77479, United States

Location

Liberty Dialysis St. George

St. George, Utah, 84790, United States

Location

DaVita Butler Farm Dialysis

Hampton, Virginia, 23666, United States

Location

Sydney Adventist Hospital

Wahroonga, New South Wales, 2076, Australia

Location

Westmead Hospital

Westmead, New South Wales, 2145, Australia

Location

Eastern Health Integrated Renal Service

Box Hill, 3128, Australia

Location

John Hunter Hospital

New Lambton Heights, 2305, Australia

Location

Klinikum Klagenfurt am Wörthersee

Klagenfurt, Carinthia, 9020, Austria

Location

Privatklinik Wehrle-Diakonissen

Salzburg, 5026, Austria

Location

Klinik Landstraße - Krankenhaus Rudolfstiftung

Vienna, 1030, Austria

Location

Universitätsklinikum AKH Wien

Vienna, 1090, Austria

Location

Epicura

Baudour, 7331, Belgium

Location

Imeldaziekenhuis - St-Elisabethkliniek

Bonheiden, 2820, Belgium

Location

AZ St-Lucas Campus St-Lucas

Ghent, 9000, Belgium

Location

UZ Leuven Gasthuisberg

Leuven, 3000, Belgium

Location

CHU de Liege | CHR Citadel - Department of Nephrology

Liège, 4000, Belgium

Location

AZ Nikolaas Campus Sint-Niklaas

Sint-Niklaas, 9100, Belgium

Location

MHAT Sveti Ivan Rilski 2003

Dupnitsa, 2600, Bulgaria

Location

MHAT Haskovo

Haskovo, 6300, Bulgaria

Location

UMHAT Kanev AD

Rousse, 7002, Bulgaria

Location

MHAT Shumen AD

Shumen, 9700, Bulgaria

Location

Multiprofile Hospital for Active Treatment Hristo Botev AD

Vratsa, 3000, Bulgaria

Location

Krajska Nemocnice Liberec

Liberec, 460 63, Czechia

Location

Fakultni nemocnice Ostrava

Ostrava, 708 52, Czechia

Location

Privamed s.r.o.

Pilsen, 323 33, Czechia

Location

Fresenius Nephro Care s.r.o. - Sokolov

Sokolov, 356 01, Czechia

Location

General Hospital of Arta

Arta, 47100, Greece

Location

HIPPOKRATION General Hospital of Athens

Athens, 115 27, Greece

Location

General Hospital of Athens LAIKO

Athens, 11527, Greece

Location

Ioannina University General Hospital

Ioannina, 45500, Greece

Location

University General Hospital of Larissa

Larissa, 41110, Greece

Location

Hippokration General Hospital of Thessaloniki

Thessaloniki, 54642, Greece

Location

General Hospital of Thessaloniki Papageorgiou

Thessaloniki, 56403, Greece

Location

Bajai Szent Rokus Korhaz

Baja, 6500, Hungary

Location

Fresenius Medical Care Egeszsegugyi Kft.

Budapest, 1083, Hungary

Location

Eszak-Pesti Centrumkorhaz-Honvedkorhaz

Budapest, 1134, Hungary

Location

Csongrad Megyei Egeszsegugyi Ellato Kozpont,Hodmezovasarhely

Hódmezővásárhely, 6800, Hungary

Location

Keszthelyi Korhaz

Keszthely, 8360, Hungary

Location

Fresenius Medical Care Egeszsegugyi Kft.

Miskolc, 3526, Hungary

Location

Fresenius Medical Care Egeszsegugyi Kft.

Pécs, 7624, Hungary

Location

Barzilai Medical Center | Nephrology & Hypertension Dept.

Ashkelon, 7830604, Israel

Location

Lady Davis Carmel Medical Center

Haifa, 3436212, Israel

Location

Health Corporation of Galilee Medical Center

Nahariya, 2210001, Israel

Location

Rabin Medical Center, HaSharon (Golda) Campus

Petah Tikva, 4937211, Israel

Location

Clalit Health Services Rabin Medical Center-Beilinson Campus

Petah Tikva, 4941492, Israel

Location

Poriya Medical Center | Nephrology and Hypertension Dept.

Tiberius, 1528001, Israel

Location

Shamir Medical Center (Assaf Harofeh)

Ẕerifin, 7030000, Israel

Location

A.O.U. di Bologna Policlinico S.Orsola Malpighi

Bologna, Emilia-Romagna, 40138, Italy

Location

A.O.U. di Parma

Parma, Emilia-Romagna, 43126, Italy

Location

AUSL-IRCCS di Reggio Emilia

Reggio Emilia, Emilia-Romagna, 42123, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Rome, Lazio, 00168, Italy

Location

IRCCS Ospedale Policlinico San Martino

Genoa, Liguria, 16132, Italy

Location

IRCCS Istituti Clinici Scientifici Maugeri SpA SB

Pavia, Lombardy, 27100, Italy

Location

A.O.U. Careggi

Florence, Tuscany, 50134, Italy

Location

Ibaraki Seinan Medical Center Hospital

Sashima-gun, Ibaraki, 306-0433, Japan

Location

Tsuchiura Beryl Clinic

Tsuchiura, Ibaraki, 300-0062, Japan

Location

Ohishi Naika Clinic

Tsuchiura, Ibaraki, 300-0835, Japan

Location

Kikuchi Medical Clinic

Tsukuba, Ibaraki, 305-0861, Japan

Location

Katta General Hospital

Shiraishi, Miyagi, 989-0231, Japan

Location

Nagaoka Red Cross Hospital

Nagaoka, Niigata, 940-2085, Japan

Location

Saiyu Clinic

Koshigaya, Saitama, 343-0823, Japan

Location

Takemura Medical Nephro Clinic

Kanuma, Tochigi, 322-0029, Japan

Location

Futakotamagawaekimae clinic

Setagaya-ku, Tokyo, 158-0094, Japan

Location

Saint Hill Hospital

Ube, Yamaguchi, 755-0155, Japan

Location

Akebono Clinic

Kumamoto, 861-4112, Japan

Location

Kyoto Station Takeda Dialysis Clinic

Kyoto, 600-8216, Japan

Location

Akagaki Clinic

Osaka, 543-0052, Japan

Location

Yabuki Hospital

Yamagata, 990-0885, Japan

Location

LUHS Kauno Hospital (Josvainiu str.)

Kaunas, LT-47116, Lithuania

Location

Academisch Medisch Centrum (AMC)

Amsterdam, 1105 AZ, Netherlands

Location

Gelre Ziekenhuizen

Apeldoorn, 7334 DZ, Netherlands

Location

Deventer Ziekenhuis

Deventer, 7416 SE, Netherlands

Location

Albert Schweitzer Ziekenhuis, Dordwijk

Dordrecht, 3318 AT, Netherlands

Location

Catharina Ziekenhuis

Eindhoven, 5623 EJ, Netherlands

Location

Maasstad Ziekenhuis | Neurology Department

Rotterdam, 3079DZ, Netherlands

Location

NZOZ Nowy Szpital w Swieciu Sp. z o.o.

Gmina Świecie, 86-100, Poland

Location

Wojewodzki Szpital Zespolony

Kielce, 25-736, Poland

Location

Stacja Dializ Olkusz

Olkusz, 32-300, Poland

Location

Stacja Dializ W-wa Mangalia

Warsaw, 02-758, Poland

Location

Stacja Dializ Zyrardow

Żyrardów, 96-300, Poland

Location

Eurodial Obidos (DaVita)

Gaeiras - Obidos, Leiria District, 2510-702, Portugal

Location

SPD - Amadora (Diaverum Amadora)

Amadora, Lisbon District, 2700-001, Portugal

Location

CHLO - Hospital Santa Cruz

Carnaxide, Lisbon District, 2795-53, Portugal

Location

Pluribus Dialise - Cascais (DaVita)

Cascais, Lisbon District, 2750-663, Portugal

Location

Pluribus Dialise - Sacavem (DaVita)

Sacavém, Lisbon District, 2685-005, Portugal

Location

Caledial - Centro de Hemodialise de Gaia

Canelas, Porto District, 4410-313, Portugal

Location

Centro Hospitalar do Medio Tejo | Unidade de Torres Novas - Nephrology Department

Torres Novas, Santarém District, 2350-754, Portugal

Location

Diaverum Aveiro

Aveiro, 3800-266, Portugal

Location

Eurodial Leiria (DaVita)

Leiria, 2400-441, Portugal

Location

NephroCare APDP

Lisbon, 1250-191, Portugal

Location

Chelyabinsk Regional Clinical Hospital

Chelyabinsk, 454076, Russia

Location

LLC Dialysis center

Kolomna, 140402, Russia

Location

LLC Fresenius medical care Kuban

Krasnodar, 350029, Russia

Location

LLC Dialysis center

Mytishchi, 141007, Russia

Location

City Clinical Hospital #1 Orenburg

Orenburg, 460040, Russia

Location

Republican Hospital n.a. V.A. Baranov

Petrozavodsk, 185019, Russia

Location

Kupchinsky center for outpatient dialysis

Saint Petersburg, 192102, Russia

Location

LLC B. Brown Avitum Russland Clinics

Saint Petersburg, 193318, Russia

Location

City Hospital #31

Saint Petersburg, 197110, Russia

Location

LLC Yaroslavl dialysis center

Yaroslavl, 150062, Russia

Location

Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, 620102, Russia

Location

Hospital Clínico Universitario de Santiago de Compostela

Santiago de Compostela, A Coruña, 15706, Spain

Location

Hospital Universitari Germans Trias i Pujol

Badalona, Barcelona, 08916, Spain

Location

Hospital Althaia, Xarxa Assistencial de Manresa

Manresa, Barcelona, 08243, Spain

Location

Corporació Sanitària Parc Taulí

Sabadell, Barcelona, 08208, Spain

Location

Hospital Clinico Universitario San Carlos | Nefrologia

Madrid, 28040, Spain

Location

Hospital Clínico Universitario de Valencia

Valencia, 46010, Spain

Location

Hospital Universitario Dr. Peset

Valencia, 46017, Spain

Location

Hacettepe Universitesi Tip Fakultesi

Ankara, 06230, Turkey (Türkiye)

Location

Adnan Menderes Universitesi Tip fakultesi

Aydin, 09100, Turkey (Türkiye)

Location

Turk Bobrek Vakfi Memorial Hizmet Hastanesi

Istanbul, 34180, Turkey (Türkiye)

Location

Sisli Hamidiye Etfal Egitim ve Arastirma Hastanesi

Istanbul, 34418, Turkey (Türkiye)

Location

Erciyes Universitesi Tip Fakultesi

Kayseri, 38039, Turkey (Türkiye)

Location

Kocaeli Universitesi Tip Fakultesi

Kocaeli, 41380, Turkey (Türkiye)

Location

Inonu Universitesi Tip Fakultesi

Malatya, 44280, Turkey (Türkiye)

Location

Brovarskaya multidisciplinary clinical hospital

Brovary, 07400, Ukraine

Location

Medical center LLC " Fresenius medical care Ukraine"

Cherkasy, 18009, Ukraine

Location

Dnepropetrovsk regional hospital n.a. I. I. Mechnikov

Dnipro, 49005, Ukraine

Location

Regional Clinical Hospital - Ivano-Frankivsk

Ivano-Frankivsk, 76000, Ukraine

Location

Kharkiv regional Clinical Centre of urology and nephrology

Kharkiv, 61037, Ukraine

Location

Kyiv City Center of Nephrology and Dialysis

Kyiv, 02660, Ukraine

Location

State Institution "Institute of Nephrology" NAMS of Ukraine

Kyiv, 04050, Ukraine

Location

Lutsk city clinical hospital

Lutsk, 43024, Ukraine

Location

Mykolaiv Regional Clinical Hospital

Mykolaiv, 54058, Ukraine

Location

Poltava Regional Clinical Hospital n.a. M.V. Skliphosovskyi

Poltava, 36011, Ukraine

Location

Transcarpatian Regional Clinical Hospital

Uzhhorod, 88018, Ukraine

Location

Vinnitsa Regional Clinical Hospital im. N.I. Pirogov

Vinnytsia, 21018, Ukraine

Location

Zaporizhzhia Regional Clinical Hospital

Zaporizhzhya, 69600, Ukraine

Location

Related Publications (1)

  • Weitz JI, Tanko LB, Floege J, Fox KAA, Bhatt DL, Thadhani R, Hung J, Pap AF, Kubitza D, Winkelmayer WC; CONVERT Investigators. Anticoagulation with osocimab in patients with kidney failure undergoing hemodialysis: a randomized phase 2 trial. Nat Med. 2024 Feb;30(2):435-442. doi: 10.1038/s41591-023-02794-7. Epub 2024 Feb 16.

Related Links

MeSH Terms

Conditions

Kidney Failure, Chronic

Interventions

osocimab

Condition Hierarchy (Ancestors)

Renal Insufficiency, ChronicRenal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Therapeutic Area Head
Organization
Bayer AG

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 20, 2020

First Posted

August 21, 2020

Study Start

August 28, 2020

Primary Completion

December 28, 2021

Study Completion

May 30, 2022

Last Updated

July 21, 2023

Results First Posted

July 21, 2023

Record last verified: 2023-07

Data Sharing

IPD Sharing
Will not share

There are no current plans to share data.

Locations