NCT04516291

Brief Summary

This is a multicenter, Phase 2b, double-blind, placebo-controlled, parallel group study to provide data on efficacy, safety, tolerability, and pharmacokinetics (PK) of PF-07285557 (hereafter, vupanorsen) administered subcutaneously (SC) at various doses and regimens in participants with dyslipidemia, defined in this study as participants with elevated non-HDL-C and TG who are receiving a stable dose of a statin. This study is also known as TaRgeting ANGPTL3 with an aNtiSense oLigonucleotide in AdulTs with dyslipidEmia (TRANSLATE-TIMI 70).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
286

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Sep 2020

Shorter than P25 for phase_2

Geographic Reach
3 countries

114 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 13, 2020

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 18, 2020

Completed
1 month until next milestone

Study Start

First participant enrolled

September 28, 2020

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 29, 2021

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 6, 2021

Completed
10 months until next milestone

Results Posted

Study results publicly available

October 4, 2022

Completed
Last Updated

October 4, 2022

Status Verified

September 1, 2022

Enrollment Period

1 year

First QC Date

August 13, 2020

Results QC Date

September 6, 2022

Last Update Submit

September 6, 2022

Conditions

Keywords

Primary hyperlipidemiaMixed dyslipidemiaLipid Metabolism DisordersMetabolic Diseases

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Non-High-Density Lipoprotein-Cholesterol (Non-HDL-C) at Week 24

    Fasting was required at least 10 hours before blood sample collection. Baseline was calculated using the average of all values obtained at Screening and on Day 1 prior to dosing.

    Baseline, Week 24

Secondary Outcomes (4)

  • Percent Change From Baseline in Triglyceride (TG), Apolipoprotein B (ApoB), Low-Density Lipoprotein-Cholesterol (LDL-C), and Non-HDL-C at Week 16

    Baseline, Week 16

  • Percent Change From Baseline in TG, ApoB, and LDL-C at Week 24

    Baseline, Week 24

  • Percent Change From Baseline in Angiopoietin-like Protein 3 (ANGPTL3) at Week 16

    Baseline, Week 16

  • Percent Change From Baseline in ANGPTL3 at Week 24

    Baseline, Week 24

Study Arms (8)

Placebo

PLACEBO COMPARATOR

No drug

Drug: Placebo

Vupanorsen 80 mg every 4 weeks

EXPERIMENTAL

80 milligrams (mg) given subcutaneously every 4 weeks.

Drug: Vupanorsen

Vupanorsen 60 mg every 2 weeks

EXPERIMENTAL

60 mg given subcutaneously every 2 weeks.

Drug: Vupanorsen

Vupanorsen 120 mg every 4 weeks

EXPERIMENTAL

120 mg given subcutaneously every 4 weeks.

Drug: Vupanorsen

Vupanorsen 80 mg every 2 weeks

EXPERIMENTAL

80 mg given subcutaneously every 2 weeks.

Drug: Vupanorsen

Vupanorsen 160 mg every 4 weeks

EXPERIMENTAL

160 mg given subcutaneously every 4 weeks.

Drug: Vupanorsen

Vupanorsen 120 mg every 2 weeks

EXPERIMENTAL

120 mg given subcutaneously every 2 weeks.

Drug: Vupanorsen

Vupanorsen 160 mg every 2 weeks

EXPERIMENTAL

160 mg given subcutaneously every 2 weeks.

Drug: Vupanorsen

Interventions

Vupanorsen and placebo will be provided as prefilled syringes packaged and dispensed in cartons with tamper-evident seals. Only single-use syringes will be used.

Also known as: PF-07285557
Vupanorsen 120 mg every 2 weeksVupanorsen 120 mg every 4 weeksVupanorsen 160 mg every 2 weeksVupanorsen 160 mg every 4 weeksVupanorsen 60 mg every 2 weeksVupanorsen 80 mg every 2 weeksVupanorsen 80 mg every 4 weeks

Vupanorsen and placebo will be provided as prefilled syringes packaged and dispensed in cartons with tamper-evident seals. Only single-use syringes will be used.

Placebo

Eligibility Criteria

Age40 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female participants aged ≥40 years at Screening.
  • Fasting non-HDL-C at Screening ≥100 mg/dL.
  • Fasting TG at Screening of 150 to 500 mg/dL, inclusive, which may be repeated once if deemed necessary.
  • Participants must be on a stable dose of a statin for at least 1 month before Screening and plan to remain on the same medication and dose for the duration of the study.
  • Body weight ≥50 kg and ≤136 kg at Screening.
  • Capable of giving signed informed consent.

You may not qualify if:

  • Participant has active liver disease (other than NAFLD or NASH, which are permitted), including chronic active hepatitis B or C or primary biliary cirrhosis.
  • Uncontrolled hypertension (systolic blood pressure \>180 mmHg or diastolic blood pressure \>100 mmHg). Note: participants who are on an anti-hypertensive medication to treat hypertension should be on a stable dose at least 1 month prior to Screening. The investigator should ensure participant took anti-hypertensive medication as prescribed prior to evaluation of blood pressure.
  • Participant with a known bleeding diathesis or coagulation disorder.
  • Participants with ANY of the following abnormalities in clinical laboratory tests at Screening, as assessed by the central laboratory and confirmed by a single repeat test, if deemed necessary: HbA1c ≥9.5% eGFR \<30 mL/min/1.73 m2 (as determined by the CKD-Epi equation) ALT or AST \>2 × ULN Total bilirubin ≥1.5 × ULN; participants with a history of Gilbert's syndrome may have a direct bilirubin measured and would be eligible for this study provided the direct bilirubin is ≤ULN Platelet count \<LLN
  • History of clinically significant acute cardiac event within 3 months before Screening (includes ischemic stroke, transient ischemic attack, myocardial infarction, revascularization procedures, hospitalization for heart failure).
  • Presence of New York Heart Association Functional Classification IV heart failure symptoms at Screening.
  • Malignancy within 5 years, except for basal or squamous cell carcinoma of the skin or carcinoma in situ of the cervix that has been successfully treated.
  • Current history of alcoholism or drug addiction according to Diagnostic and Statistical Manual of Mental Disorders IV criteria within 12 months prior to Screening. Use of any recreational drugs within 12 months prior to Screening.
  • Other medical or psychiatric condition including recent (within the past year) or active suicidal ideation/behavior or laboratory abnormality that may increase the risk of study participation or, in the investigator's judgment, make the participant inappropriate for the study.
  • Prior/Concomitant Therapy:
  • Prior treatment at any time with vupanorsen.
  • Prior treatment with any oligonucleotide (including small interfering ribonucleic acid) within 6 months of Screening or prior treatment with inclisiran within 12 months of Screening.
  • Use of TG lowering medication (eg, Vascepa \[icosapent ethyl\]), non-prescription dietary supplements (eg, fish oil) or other cholesterol lowering medication (eg, fibric acid derivatives, niacin, PCSK9 inhibitors, bile acid sequestrants, bempedoic acid) 30 days prior to Screening, other than statins and ezetimibe.
  • Use of warfarin or other coumarins, direct thrombin inhibitors, Factor Xa inhibitors, heparins or heparinoids 30 days prior to Screening.
  • Prior/Concurrent Clinical Study Experience:
  • +9 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (114)

Horizon Clinical Research Associates, PLLC

Gilbert, Arizona, 85295, United States

Location

Scottsdale Medical Imaging Research, LLC

Gilbert, Arizona, 85297, United States

Location

CARTI

Little Rock, Arkansas, 72205, United States

Location

Atria Clinical Research

Little Rock, Arkansas, 72209, United States

Location

Clinical Trials Research

Lincoln, California, 95648, United States

Location

Diagnostic Radiological Imaging

Sacramento, California, 95825, United States

Location

West Coast Radiology

Santa Ana, California, 92705, United States

Location

University Clinical Investigators, Inc.

Tustin, California, 92780, United States

Location

Tower Radiology Parsons

Brandon, Florida, 33511, United States

Location

Tower Radiology

Brandon, Florida, 33511, United States

Location

Innovative Research of West Florida, Inc.

Clearwater, Florida, 33756, United States

Location

Westside Center for Clinical Research

Jacksonville, Florida, 32205, United States

Location

Borland-Groover Clinic

Jacksonville, Florida, 32256, United States

Location

Precision Imaging Centers

Jacksonville, Florida, 32256, United States

Location

Care Partners Clinical Research, LLC

Jacksonville, Florida, 32277, United States

Location

Advanced Research Institute, Inc.

New Port Richey, Florida, 34653, United States

Location

Sand Lakes Imaging

Orlando, Florida, 32819, United States

Location

St Johns Center for Clinical Research

Saint Augustine, Florida, 32086, United States

Location

Clinical Research of Central Florida

Winter Haven, Florida, 33880, United States

Location

Alliance for Multispecialty Research, LLC

El Dorado, Kansas, 67042, United States

Location

Susan B. Allen Memorial Hospital

El Dorado, Kansas, 67042, United States

Location

L-MARC Research Center

Louisville, Kentucky, 40213, United States

Location

Heartland Imaging

Louisville, Kentucky, 40222, United States

Location

Maryland Cardiovascular Specialists

Baltimore, Maryland, 21229, United States

Location

Seton Imaging Center

Baltimore, Maryland, 21229, United States

Location

Lahey Clinic Hospital and Medical Center

Burlington, Massachusetts, 01805, United States

Location

Pentucket Medical Associates

Haverhill, Massachusetts, 01830, United States

Location

Regions Hospital - HealthPartners

Saint Paul, Minnesota, 55101, United States

Location

Viable Research Management LLC

Henderson, Nevada, 89014, United States

Location

Pueblo Medical Imaging

Henderson, Nevada, 89074, United States

Location

Capital Cardiology Associates

Albany, New York, 12211, United States

Location

ImageCare Latham

Latham, New York, 12110, United States

Location

Randolph Health Internal Medicine

Asheboro, North Carolina, 27203, United States

Location

Randolph Health MRI Center

Asheboro, North Carolina, 27205, United States

Location

PMG Research of Raleigh, LLC d/b/a PMG Research of Cary

Cary, North Carolina, 27518, United States

Location

Wake Radiology

Cary, North Carolina, 27518, United States

Location

Accellacare - Raleigh

Raleigh, North Carolina, 27609, United States

Location

PMG Research of Raleigh, LLC

Raleigh, North Carolina, 27609, United States

Location

Wake Radiology Diagnostic Imaging Inc

Raleigh, North Carolina, 27609, United States

Location

PMG Research of Winston-Salem, LLC

Winston-Salem, North Carolina, 27103, United States

Location

Hightop Medical Research Center

Cincinnati, Ohio, 45224, United States

Location

Imaging Research Center-Cincinnati Children's

Cincinnati, Ohio, 45229, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Perelman Center for Advanced Medicine, Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Clermont Radiology Orangeburg

Orangeburg, South Carolina, 29118, United States

Location

South Carolina Clinical Research LLC

Orangeburg, South Carolina, 29118, United States

Location

Tennessee Center for Clinical Trials

Tullahoma, Tennessee, 37388, United States

Location

Tullahoma HMA, LLC d\b\a Tennova HealthCare Harton

Tullahoma, Tennessee, 37388, United States

Location

Dallas Diabetes Research Center

Dallas, Texas, 75230, United States

Location

Southwest Diagnostic Imaging Center

Dallas, Texas, 75231, United States

Location

SimonMed Houston

Houston, Texas, 77030, United States

Location

Southwest Clinical Trials

Houston, Texas, 77074, United States

Location

Medical Center Hospital

Odessa, Texas, 79761, United States

Location

Permian Research Foundation

Odessa, Texas, 79761, United States

Location

J. Lewis Research, Inc. / Foothill Family Clinic South

Salt Lake City, Utah, 84121, United States

Location

National Clinical Research, Inc.

Richmond, Virginia, 23294, United States

Location

Rainier Clinical Research Center

Renton, Washington, 98057, United States

Location

Bellevue Medical Imaging

Seattle, Washington, 98166, United States

Location

Universal Research Group, LLC

Tacoma, Washington, 98405, United States

Location

C-endo

Edmonton, Alberta, T6H 2L4, Canada

Location

MIC Medical Imaging

Edmonton, Alberta, T6J 5E5, Canada

Location

Synergy Medical Clinic

Sherwood Park, Alberta, T8H 0N2, Canada

Location

Access MRI

Surrey, British Columbia, V3S 9A5, Canada

Location

SMH Cardiology Clinical Trials Inc.

Surrey, British Columbia, V3V 0C6, Canada

Location

Nova Scotia Health Authority QE II Health Sciences Centre

Halifax, Nova Scotia, B3H 1V7, Canada

Location

Nova Scotia Health Authority QE II Health Sciences Centre

Halifax, Nova Scotia, B3H 2Y9, Canada

Location

LMC Clinical Research Inc. (Barrie)

Barrie, Ontario, L4N 7L3, Canada

Location

Aggarwal and Associates Limited

Brampton, Ontario, L6T 0G1, Canada

Location

LMC Clinical Research Inc. (Thornhill)

Concord, Ontario, L4K 4M2, Canada

Location

LMC Clinical Research Inc. (Etobicoke)

Etobicoke, Ontario, M9R 4E1, Canada

Location

Dawson Clinical Research

Guelph, Ontario, N1H 1B1, Canada

Location

KMH Cardiology Centres Inc.

Kitchener, Ontario, N2M 5N4, Canada

Location

Milestone Research Inc.

London, Ontario, N5W 6A2, Canada

Location

Robarts Research Institute, Western University

London, Ontario, N6A 5B7, Canada

Location

GNMI Medical Imaging

Mississauga, Ontario, L5R 3K6, Canada

Location

GNMI Medical Imaging

Mississauga, Ontario, L5R 3K7, Canada

Location

GNMI MRI and CT Medical Imaging

Mississauga, Ontario, L6R 3K7, Canada

Location

North York Diagnostic and Cardiac Centre

North York, Ontario, M6B 3H7, Canada

Location

Bluewater Clinical Research Group Inc.

Sarnia, Ontario, N7T 4X3, Canada

Location

Holland Bloorview Kids Rehabilitation Hospital

Toronto, Ontario, M4G 1R8, Canada

Location

Dr. Anil K. Gupta Medicine Professional Corporation

Toronto, Ontario, M9V 4B4, Canada

Location

Devonshire Clinical Research Inc.

Woodstock, Ontario, N4S 5P5, Canada

Location

Resonance Magnetique du Saguenay-Lac-Saint-Jean

Chicoutimi, Quebec, G7H 4J1, Canada

Location

Ecogene-21

Chicoutimi, Quebec, G7H 7K9, Canada

Location

Manna Research (Mirabel)

Mirabel, Quebec, J7J 2K8, Canada

Location

Recherche GCP Research

Montreal, Quebec, H1M 1B1, Canada

Location

Montreal Heart Institute

Montreal, Quebec, H1T 1C8, Canada

Location

Research Institute of the McGill University Health Center

Montreal, Quebec, H4A 3J1, Canada

Location

Research Institute of the McGill University Health Centre

Montreal, Quebec, H4A 3J1, Canada

Location

Radimed West Island

Pointe-Claire, Quebec, H9R 4R9, Canada

Location

Diex Recherche Joliette

Saint-Charles-Borromée, Quebec, J6E 2B4, Canada

Location

IRM Quebec - Complexe Synase

Québec, G1J 0H4, Canada

Location

IRM Quebec Synase

Québec, G1J 0H4, Canada

Location

Diex Recherche Quebec Inc.

Québec, G1N 4V3, Canada

Location

Centre de Recherche Saint-Louis

Québec, G1W4R4, Canada

Location

Alpha Recherche Clinique

Québec, G2J 0C4, Canada

Location

NZOZ Kendron

Bialystok, 15-402, Poland

Location

ClinicMed Daniluk, Nowak Spolka Jawna

Bialystok, 15-879, Poland

Location

Malopolskie Centrum Sercowo-Naczyniowe PAKS - Chrzanow

Chrzanów, 32-500, Poland

Location

Centrum Badan Klinicznych PI-House sp. z o.o.

Gdansk, 80-546, Poland

Location

Centrum Medyczne Enel-Med., Oddzial Alfa Plaza - Gdynia

Gdynia, 81-366, Poland

Location

Kardio Brynow

Katowice, 40-555, Poland

Location

Niepubliczny Zaklad Opieki Zdrowotnej "TERAPIA OPTIMA"

Katowice, 40-752, Poland

Location

HELIMED Katowice - Rezonans Magnetyczny, Tomografia Komputerowa (MRI)

Katowice, 40-760, Poland

Location

HELIMED Katowice - Rezonans Magnetyczny, Tomografia Komputerowa

Katowice, 40-760, Poland

Location

"TWOJA PRZYCHODNIA" Sp. z o.o.

Lublin, 20-857, Poland

Location

Top Medical Lublin

Lublin, 20-883, Poland

Location

Centrum Zdrowia Metabolicznego Pawel Bogdanski

Poznan, 60-589, Poland

Location

Arterieart Sp. z o.o.

Puszczykowo, 62-041, Poland

Location

SZPITAL SW. ELZBIETY W KATOWICACH Polsko-Amerykanskie Kliniki Serca

Tychy, 43-100, Poland

Location

Futuremeds

Wroclaw, 50-088, Poland

Location

Skanmex (MRI)

Wroclaw, 50-450, Poland

Location

Wro Medica

Wroclaw, 51-685, Poland

Location

TOMMA Pracownia rezonansu magnetycznego we Wroclawiu

Wroclaw, 53-234, Poland

Location

Related Publications (1)

  • Bergmark BA, Marston NA, Bramson CR, Curto M, Ramos V, Jevne A, Kuder JF, Park JG, Murphy SA, Verma S, Wojakowski W, Terra SG, Sabatine MS, Wiviott SD; TRANSLATE-TIMI 70 Investigators. Effect of Vupanorsen on Non-High-Density Lipoprotein Cholesterol Levels in Statin-Treated Patients With Elevated Cholesterol: TRANSLATE-TIMI 70. Circulation. 2022 May 3;145(18):1377-1386. doi: 10.1161/CIRCULATIONAHA.122.059266. Epub 2022 Apr 3.

Related Links

MeSH Terms

Conditions

DyslipidemiasHyperlipidemiasHyperlipoproteinemiasLipid Metabolism DisordersMetabolic Diseases

Interventions

vupanorsen

Condition Hierarchy (Ancestors)

Nutritional and Metabolic Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 13, 2020

First Posted

August 18, 2020

Study Start

September 28, 2020

Primary Completion

September 29, 2021

Study Completion

December 6, 2021

Last Updated

October 4, 2022

Results First Posted

October 4, 2022

Record last verified: 2022-09

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations