NCT04424914

Brief Summary

This study is a global, multi-center study designed to estimate the global prevalence of transthyretin amyloid cardiomyopathy (ATTR-CM) within a clinically at risk population \[participants with heart failure with preserved ejection fraction (HFpEF)\].

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
347

participants targeted

Target at P75+ for not_applicable

Timeline
Completed

Started Dec 2020

Typical duration for not_applicable

Geographic Reach
8 countries

51 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 27, 2020

Completed
15 days until next milestone

First Posted

Study publicly available on registry

June 11, 2020

Completed
7 months until next milestone

Study Start

First participant enrolled

December 30, 2020

Completed
2.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 2, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 2, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

July 19, 2024

Completed
Last Updated

July 19, 2024

Status Verified

February 1, 2024

Enrollment Period

2.4 years

First QC Date

May 27, 2020

Results QC Date

February 1, 2024

Last Update Submit

February 1, 2024

Conditions

Keywords

prevalencetransthyretin amyloidATTR-CMHFpEFscintigraphy

Outcome Measures

Primary Outcomes (1)

  • Global Prevalence of ATTR-CM in HFpEF Participants Clinically At-Risk of Disease Among Total Evaluable Participants

    Global prevalence of ATTR-CM in HFpEF participants was obtained by dividing the number of participants who were diagnosed with ATTR-CM in the study by the total number of HFpEF participants evaluated. Diagnosis of ATTR-CM was defined as: cardiac scintigraphy Grade 1, with confirmation of ATTR by cardiac biopsy; or cardiac scintigraphy Grade 2 or above. Exact 95% confidence intervals for the prevalence estimates were calculated using the method of Clopper and Pearson.

    Day 1

Secondary Outcomes (4)

  • Global Prevalence of ATTR-CM in Participants With HFpEF Clinically At-Risk of Disease by Subgroups (Regions, Age, Gender) Among Total Evaluable Participants

    Day 1

  • Number of Participants According to TTR Genotypes Among Participants Diagnosed With ATTR-CM

    Day 1

  • Number of HFpEF Participants With and Without ATTR-CM Based on New York Heart Association (NYHA) Classification

    Day 1

  • N-terminal Pro-brain Natriuretic Peptide (NT-proBNP) in Participants With and Without ATTR-CM

    Day 1

Study Arms (2)

ATTR-CM positive

OTHER

Participants diagnosed with ATTR-CM by scintigraphy

Diagnostic Test: Scintigraphy

ATTR-CM negative

OTHER

Participants who are scintigraphy negative for ATTR-CM

Diagnostic Test: Scintigraphy

Interventions

ScintigraphyDIAGNOSTIC_TEST

scintigraphy

ATTR-CM negativeATTR-CM positive

Eligibility Criteria

Age60 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Medical history of heart failure (HF) with:
  • At least 1 episode with clinical evidence of HF (without hospitalization) by signs or symptoms of volume overload or elevated intracardiac pressures that required/requires treatment with a diuretic for improvement; OR
  • prior hospitalization for HF.
  • Left ventricular ejection fraction (LVEF) \>40%.
  • End-diastolic interventricular septal wall thickness (IVST) ≥12 mm.
  • Willing and able to undergo scintigraphy.

You may not qualify if:

  • Diagnosis of heart failure with reduced ejection fraction (HFrEF) (EF ≤40%).
  • Prior clinical history of myocardial infarction, CABG or multi-vessel obstructive coronary disease (\>50% stenosis of ≥2 epicardial coronary arteries).
  • Presence or history of any severe valvular heart disease (obstructive or regurgitant).
  • A confirmed diagnosis of a non-amyloid infiltrative cardiomyopathy (ie, cardiac sarcoidosis, hemochromatosis), muscular dystrophies, cardiomyopathy with reversible causes, hypertrophic obstructive cardiomyopathy with known genetic etiology, or known pericardial constriction.
  • Any type of diagnosed amyloidosis (eg, amyloid A amyloidosis, primary \[light chain\] amyloidosis) or prior diagnosis of ATTR-CM.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (51)

Eastern shore Research Institute LLC

Fairhope, Alabama, 36532, United States

Location

Heart Center Research, LLC

Huntsville, Alabama, 35801, United States

Location

Advance Medical Research Center

Miami, Florida, 33135, United States

Location

Bioclinical Research Alliance Inc.

Miami, Florida, 33155, United States

Location

Biogenix Molecular

Miami, Florida, 33165, United States

Location

CIRA (Nuclear Imaging Facility)

Miami, Florida, 33165, United States

Location

Nucleotron/ Doral Imaging Institute, CIRA DBA

Miami, Florida, 33165, United States

Location

Innova Pharma Research

Miami, Florida, 33175, United States

Location

Ocala Cardiovascular Research

Ocala, Florida, 34471, United States

Location

Chicago Medical Research, LLC

Hazel Crest, Illinois, 60429, United States

Location

Advocate Christ Medical Center

Oak Lawn, Illinois, 60453, United States

Location

Stormont Vail Health

Topeka, Kansas, 66604, United States

Location

Cotton O'Neil Heart Center

Topeka, Kansas, 66606, United States

Location

Ochsner Medical Center

New Orleans, Louisiana, 70121, United States

Location

Corewell Health

Grand Rapids, Michigan, 49503, United States

Location

Spectrum Health Medical Group Cardiovascular Medicine

Grand Rapids, Michigan, 49525, United States

Location

Cardiology Associates of North Mississippi, LLC

Tupelo, Mississippi, 38801, United States

Location

Cardiology Associates Research, LLC

Tupelo, Mississippi, 38801, United States

Location

NYU Langone Health

New York, New York, 10016, United States

Location

WakeMed Health and Hospital

Raleigh, North Carolina, 27610, United States

Location

The Jackson Clinic

Jackson, Tennessee, 38301, United States

Location

Providence Sacred Heart Medical Center and Children's Hospital

Spokane, Washington, 99204, United States

Location

University of Ottawa Heart Institute

Ottawa, Ontario, K1Y 4W7, Canada

Location

CardioVasc HR Inc

Saint-Jean-sur-Richelieu, Quebec, J3A 1C3, Canada

Location

Diex Recherche Trois-Rivieres

Trois-Rivières, Quebec, G9A 4P3, Canada

Location

Hôpital Louis Pradel

Bron, 69677, France

Location

Centre Hospitalier Saint-Joseph Saint-Luc

Lyon, 69365, France

Location

CHU Nimes - Hospital Caremeau

Nîmes, 30029, France

Location

CHU de Toulouse - Hôpital de Rangueil

Toulouse, 50032 - 31059, France

Location

Médecine Nucléaire de la Doua

Villeurbanne, 69100, France

Location

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Policlinico di Sant'Orsola

Bologna, BO, 40138, Italy

Location

U.O. Clinica delle Malattie dell'Apparato Cardiovascolare - Ospedale Policlinico San Martino IRCCS

Genova, Genoa, 16132, Italy

Location

U.O. Clinica delle Malattie dell'Apparato Cardiovascolare - Ospedale Policlinico San Martino IRCCS

Genova, 16132, Italy

Location

Fondazione IRCCS Policlinico San Matteo - Centro per lo Studio e la Cura delle Amiloidosi Sistemiche

Pavia, 27100, Italy

Location

Fondazione Toscana Gabriele Monasterio-UOC Cardiologia e Medicina Cardiovascolare

Pisa, 56124, Italy

Location

Nagoya Tokushukai General Hospital

Kasugai, Aichi-ken, 487-0016, Japan

Location

Fukuoka Tokushukai Hospital

Kasuga, Fukuoka, 816-0864, Japan

Location

Keio University Hospital

Shinjuku-ku, Tokyo, 160-8582, Japan

Location

Okayama University Hospital

Okayama, 700-8558, Japan

Location

Krakowski Szpital Specjalistyczny im. Jana Pawła II

Krakow, Lesser Poland Voivodeship, 31-202, Poland

Location

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wrocławiu

Wroclaw, Lower Silesian Voivodeship, 50-556, Poland

Location

Uniwersytecki Szpital Kliniczny w Białymstoku

Bialystok, Podlaskie Voivodeship, 15-276, Poland

Location

SPZOZ Uniwersytecki Szpital Kliniczny Im. Wojskowej Akademii Medycznej UM W Łodzi Centralny Szpital

Lodz, Łódź Voivodeship, 90-549, Poland

Location

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Madrid, 28222, Spain

Location

Hospital Universitari Vall d´Hebron

Barcelona, 08035, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitari De Bellvitge

Barcelona, 08907, Spain

Location

Hospital Universitario Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Universitario de Salamanca - Complejo Asistencial Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitari i Politècnic La Fe

Valencia, 46026, Spain

Location

St George's Hospital, St George's University Hospitals NHS Foundation Trust

London, SW17 0QT, United Kingdom

Location

Related Publications (1)

  • Yun S, Palladini G, Anderson LJ, Cariou E, Wang R, Angeli FS, Ebede B, Garcia-Pavia P. International prevalence of transthyretin amyloid cardiomyopathy in high-risk patients with heart failure and preserved or mildly reduced ejection fraction. Amyloid. 2024 Dec;31(4):291-301. doi: 10.1080/13506129.2024.2398446. Epub 2024 Sep 8.

Related Links

MeSH Terms

Interventions

Radionuclide Imaging

Intervention Hierarchy (Ancestors)

Diagnostic ImagingDiagnostic Techniques and ProceduresDiagnosisDiagnostic Techniques, Radioisotope

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
SCREENING
Intervention Model
SINGLE GROUP
Model Details: To determine global prevalence of transthyretin amyloid cardiomyopathy in participants diagnosed with heart failure with preserved ejection fraction. No study treatment will be dispensed however, participants will undergo scintigraphy.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 27, 2020

First Posted

June 11, 2020

Study Start

December 30, 2020

Primary Completion

June 2, 2023

Study Completion

June 2, 2023

Last Updated

July 19, 2024

Results First Posted

July 19, 2024

Record last verified: 2024-02

Data Sharing

IPD Sharing
Will not share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

Locations