NCT04401267

Brief Summary

This is a randomized unblinded Phase II clinical trial evaluating the impact of intensive antihypertensive control (targeted to the 50-75th percentile for age, sex, and height) compared to conventional antihypertensive control (targeted to the 90-95th percentile for age, sex, and height) on the incidence of radiographically extensive osteonecrosis in children and young adults receiving treatment for newly diagnosed acute lymphoblastic leukemia/lymphoma (ALL). Primary Objective

  • Compare the frequency of radiographically extensive osteonecrosis in patients receiving intensive compared to conventional antihypertensive therapy. Secondary Objectives
  • Evaluate the efficacy of intensive antihypertensive control compared to conventional antihypertensive control in the prevention of clinically significant (CTCAE Grade 2 or higher) and radiologically extensive osteonecrosis, overall and stratified by joints.
  • Compare the frequency of clinically significant and radiographically extensive osteonecrosis in patients receiving antihypertensive therapy and historical controls.
  • Compare blood pressures achieved in intensive and conventional arms using both pressures obtained as part of routine patient care and ambulatory blood pressure monitoring.
  • Compare levels of vascular dysfunction as measured physiologically, radiographically, and in blood samples in patients receiving intensive compared to standard antihypertensive therapy. Exploratory Objectives
  • Identify predictive patterns of blood biomarkers which identify patients at high- risk of developing clinically significant osteonecrosis.
  • Identify MRI findings during late induction which correlate with osteonecrosis lesions seen during reinduction.
  • Identify patterns of diurnal blood pressure variation as measured by ambulatory blood pressure monitoring associated with the later development of osteonecrosis.
  • Compare induction blood pressure control and intervention arm to echocardiographic changes at reinduction II.
  • Evaluate patient-reported, health-related quality of life in patients during induction and after 1.5 years of therapy when many experience the symptoms of osteonecrosis.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
51

participants targeted

Target at P25-P50 for phase_2 hypertension

Timeline
Completed

Started Oct 2020

Longer than P75 for phase_2 hypertension

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 13, 2020

Completed
13 days until next milestone

First Posted

Study publicly available on registry

May 26, 2020

Completed
5 months until next milestone

Study Start

First participant enrolled

October 15, 2020

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 25, 2023

Completed
10 months until next milestone

Results Posted

Study results publicly available

July 11, 2024

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 7, 2025

Completed
Last Updated

November 3, 2025

Status Verified

October 1, 2025

Enrollment Period

2.9 years

First QC Date

May 13, 2020

Results QC Date

June 14, 2024

Last Update Submit

October 29, 2025

Conditions

Keywords

Acute Lymphoblastic LeukemiaChildrenHypertensionOsteonecrosisOsteonecrosis Due to Drug

Outcome Measures

Primary Outcomes (1)

  • Extensive Radiographic Osteonecrosis

    Involvement of \>=30% of the epiphyseal surface of either the hip or knee by prospective MRI during reinduction II

    during reinduction II therapy, approximately 9 months into therapy.

Secondary Outcomes (13)

  • Rate of Clinically Significant Osteonecrosis

    any time during leukemia therapy, approximately 2.5 years

  • Rate of Clinically Significant Osteonecrosis vs. Historical Control

    any time during leukemia therapy, approximately 2.5 years

  • Blood Pressure Control on Trial

    first 9 months of therapy

  • Biomarkers of Vascular Dysfunction - eNO Synthetase (pg/mL)

    3 weeks and 9 months into therapy

  • Biomarker of Vascular Dysfunction - Von Willebrand Factor (%)

    3 weeks and 9 months into therapy

  • +8 more secondary outcomes

Study Arms (2)

Intensive Antihypertensive Therapy

EXPERIMENTAL

Patients will begin Intensive antihypertensive therapy to achieve the targeted blood pressure (targeted to the 50-75th percentile for age, sex, and height) on day 4 of Remission Induction on TOT17 and continue during steroid containing phases until the completion of reinduction II.

Drug: Intensive Antihypertensive TherapyOther: Symptom SurveyOther: Semi-structured interview

Conventional Antihypertensive Therapy

ACTIVE COMPARATOR

Patients will begin Conventional antihypertensive therapy to achieve the targeted blood pressure (targeted to the 90-95th percentile for age, sex, and height) on day 4 of Remission Induction on TOT17 and continue during steroid containing phases until the completion of reinduction II.

Drug: Conventional Antihypertensive TherapyOther: Symptom SurveyOther: Semi-structured interview

Interventions

Receives intensive antihypertensive therapy

Also known as: Hypotensive Therapy
Intensive Antihypertensive Therapy

Receives conventional antihypertensive therapy

Also known as: Hypotensive Therapy
Conventional Antihypertensive Therapy

The symptom survey is comprised of the PROMIS Ped 25 profile, PROMIS pain interference 8a, PROMIS physical activity 8a, and PROMIS mobility 8a during induction (day 23-28), during week 17 of continuation (+/- 2 weeks), and continuation week 49 (+/- 3 weeks).

Also known as: Survey
Conventional Antihypertensive TherapyIntensive Antihypertensive Therapy

Patients will be interviewed by a trained examiner about their treatment and symptom burden on Week 49 of TOT17 Continuation Therapy. The interview will be recorded and will take about 30-45 minutes.

Also known as: Interview
Conventional Antihypertensive TherapyIntensive Antihypertensive Therapy

Eligibility Criteria

Age10 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patient is being treated for newly diagnosed acute lymphoblastic leukemia or lymphoma (ALL) on the TOT17 protocol. Patients do not need to be hypertensive to enroll.
  • Patient is 10 years of age or older at the time of enrollment on TOT17.
  • Patient has completed ≤ 4 days of protocol therapy (patients are eligible on Day 4 of TOT17 therapy).

You may not qualify if:

  • Moderate-severe renal dysfunction (glomerular filtration rate \<45 ml/min/1.73m2).
  • Down's syndrome (germline Trisomy 21) or other syndrome resulting in growth delay or alterations in stature.
  • Chronic inability to ambulate. Patients with limitations in movement due to acute complications of leukemia/lymphoma are not excluded.
  • Permanent contraindication to MRI evaluation.
  • Participants who are pregnant or lactating. Males or females of reproductive potential must agree to use effective contraception for the duration of study participation.
  • Inability or unwillingness of research participant or legal guardian/representative to give written informed consent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

St. Jude Affiliate Clinic - Novant Health Hemby Children's Hospital

Charlotte, North Carolina, 28204, United States

Location

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

Location

Related Links

MeSH Terms

Conditions

HypertensionOsteonecrosisPrecursor Cell Lymphoblastic Leukemia-Lymphoma

Interventions

Surveys and QuestionnairesInterviews as Topic

Condition Hierarchy (Ancestors)

Vascular DiseasesCardiovascular DiseasesBone DiseasesMusculoskeletal DiseasesNecrosisPathologic ProcessesPathological Conditions, Signs and SymptomsLeukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

Data CollectionEpidemiologic MethodsInvestigative TechniquesHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public Health

Results Point of Contact

Title
Seth Karol, MD
Organization
St. Jude Children's Research Hospital

Study Officials

  • Seth E. Karol, MD

    St. Jude Children's Research Hospital

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
Evaluation of the MRIs defining the primary endpoint will be performed by a blinded radiologist.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 13, 2020

First Posted

May 26, 2020

Study Start

October 15, 2020

Primary Completion

September 25, 2023

Study Completion

October 7, 2025

Last Updated

November 3, 2025

Results First Posted

July 11, 2024

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Individual participant de-identified datasets containing the variables analyzed in the published article will be made available (related to the study primary or secondary objectives contained in the publication). Supporting documents such as the protocol, statistical analyses plan, and informed consent are available through the CTG website for the specific study. Data used to generate the published article will be made available at the time of article publication. Investigators who seek access to individual level de-identified data will contact the computing team in the Department of Biostatistics (ClinTrialDataRequest@stjude.org) who will respond to the data request.

Shared Documents
STUDY PROTOCOL, SAP, ICF
Time Frame
Data will be made available at the time of article publication.
Access Criteria
Data will be provided to researchers following a formal request with the following information: full name of requestor, affiliation, data set requested, and timing of when data is needed. As an informational point, the lead statistician and study principal investigator will be informed that primary results datasets have been requested.

Locations