NCT04315025

Brief Summary

The study will perform UC-MSCs and CM transplantation. The first group will be injected by UCMSC+NaCl. the 2nd group will be injected by UC-MSC+CM. the 3rd group will be injected by CM. Each group consists of 6 subjects. all groups will be transplanted via peribulbar route. the dosage of UC-MSC is 1 million cells for each subject. All groups will be observed until 6 months.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
18

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Oct 2018

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 7, 2018

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 20, 2019

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 20, 2019

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

March 8, 2020

Completed
11 days until next milestone

First Posted

Study publicly available on registry

March 19, 2020

Completed
Last Updated

June 4, 2020

Status Verified

March 1, 2020

Enrollment Period

9 months

First QC Date

March 8, 2020

Last Update Submit

June 2, 2020

Conditions

Keywords

Allogeneic Mesenchymal Stem CellUmbilical Cord Mesenchymal Stem CellConditioned MediumAllogeneic Umbilical Cord Mesenchymal Stem Cell

Outcome Measures

Primary Outcomes (18)

  • Visual Acuity Test

    a test to see the sharpness of vision using Snellen Chart which is read at a distance of 6 meters. Normal eye test results are stated in 6/6.

    1 week after injection

  • Visual Acuity Test

    a test to see the sharpness of vision using Snellen Chart which is read at a distance of 6 meters. Normal eye test results are stated in 6/6.

    1 month after injection

  • Visual Acuity Test

    a test to see the sharpness of vision using Snellen Chart which is read at a distance of 6 meters. Normal eye test results are stated in 6/6.

    3 months after injection

  • Visual Field Test

    a test to assess the breadth of views of the lateral, medial, superior and inferior aspects using Humprey's perimetry.

    1 week after injection

  • Visual Field Test

    a test to assess the breadth of views of the lateral, medial, superior and inferior aspects using Humprey's perimetry.

    1 month after injection

  • Visual Field Test

    a test to assess the breadth of views of the lateral, medial, superior and inferior aspects using Humprey's perimetry.

    3 months after injection

  • Funduscopy

    an examination to see and assess the abnormalities and conditions in the ocular fundus using an ophthalmoscope. This examination is carried out by an ophthalmologist.

    1 week after injection

  • Funduscopy

    an examination to see and assess the abnormalities and conditions in the ocular fundus using an ophthalmoscope. This examination is carried out by an ophthalmologist.

    1 month after injection

  • Funduscopy

    an examination to see and assess the abnormalities and conditions in the ocular fundus using an ophthalmoscope. This examination is carried out by an ophthalmologist.

    3 months after injection

  • Electrorectinography

    an examination to provide a picture of objectivity, a quantitative measure of retinal function to monitor the function of stem cells and ganglion cells in the eye. This examination is carried out by a trained ophthalmologist.

    1 week after injection

  • Electrorectinography

    an examination to provide a picture of objectivity, a quantitative measure of retinal function to monitor the function of stem cells and ganglion cells in the eye. This examination is carried out by a trained ophthalmologist.

    1 month after injection

  • Electrorectinography

    an examination to provide a picture of objectivity, a quantitative measure of retinal function to monitor the function of stem cells and ganglion cells in the eye. This examination is carried out by a trained ophthalmologist.

    3 months after injection

  • Optical Coherence Tomography (OCT)

    is a diagnostic test that give the information about posterior segment structure, which is retina and optic nerve papillae so that it can be used to assess macular abnormalities

    1 week after injection

  • Optical Coherence Tomography (OCT)

    is a diagnostic test that give the information about posterior segment structure, which is retina and optic nerve papillae so that it can be used to assess macular abnormalities

    1 month after injection

  • Optical Coherence Tomography (OCT)

    is a diagnostic test that give the information about posterior segment structure, which is retina and optic nerve papillae so that it can be used to assess macular abnormalities

    3 months after injection

  • Angiography

    a process of taking photos of the retina by injecting fluorescent to get a bleeding location on the retina.

    1 week after injection

  • Angiography

    a process of taking photos of the retina by injecting fluorescent to get a bleeding location on the retina.

    1 month after injection

  • Angiography

    a process of taking photos of the retina by injecting fluorescent to get a bleeding location on the retina.

    3 months after injection

Study Arms (3)

Conditioned Medium (CM)

ACTIVE COMPARATOR

a total 2 ml volume of Conditioned Medium derived Umbilical Cord Mesenchymal Stem Cell will be injected by peribulbar

Biological: Conditioned Medium (CM)

UC-MSC + NaCl

ACTIVE COMPARATOR

1.8 ml cell preparations are suspended in physiological NaCl until it reaches a total of 2 ml volume of cell suspension. Umbilical Cord Mesenchymal Stem Cell (UC-MSC) suspension will be injected by peribulbar

Biological: Umbilical Cord Mesenchymal Stem Cell (UC-MSC)

UC-MSC+CM

ACTIVE COMPARATOR

1.8 ml cell preparations are suspended in Conditioned Medium (CM) until it reaches total of 2 ml volume of cell suspension. Umbilical Cord Mesenchymal Stem Cell (UC-MSC) + Conditioned Medium (CM) suspension will be injected by peribulbar

Biological: Umbilical Cord Mesenchymal Stem Cell (UC-MSC)Biological: Conditioned Medium (CM)

Interventions

Umbilical Cord Mesenchymal Stem Cell (UC-MSC) injected by peribulbar

UC-MSC + NaClUC-MSC+CM

Conditioned Medium (CM) injected by peribulbar

Conditioned Medium (CM)UC-MSC+CM

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Visual field defects at initial examination with Humhprey perimetry are between 25% to 50%
  • Willing to sign informed consent as research subjects
  • Willing to do peribulbar injection with mesenchymal stem cells isolated from umbilical cord tissue
  • Willing to do visual field checks with Humphrey's perimetry, vision tests with Snellen boards, Optical Coherrent Tomography (OCT) examinations, electroretinogram examinations and fill out a quality of life questionnaire

You may not qualify if:

  • Pregnant or nursing women
  • Positive result of HIV test
  • Have a history of eye tumors
  • In immunosuppressive treatment or other drugs that can affect the growth of transplanted stem cells
  • Have another eye disease such as diabetic retinopathy, uveitis, cataract, and glaucoma
  • Do not come to control according to the schedule determined by the researcher (loss to follow up)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Jakarta Eye Center Hospital

Jakarta, DKI Jakarta, Indonesia

Location

Sardjito Hospital

Yogyakarta, Special Region, 55284, Indonesia

Location

MeSH Terms

Conditions

Retinitis Pigmentosa

Interventions

Culture Media, Conditioned

Condition Hierarchy (Ancestors)

Eye Diseases, HereditaryEye DiseasesRetinal DystrophiesRetinal DegenerationRetinal DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Culture MediaLaboratory ChemicalsSpecialty Uses of ChemicalsChemical Actions and UsesEquipment and Supplies

Study Officials

  • dr Cosmos O Mangunsong, Sp.M

    Gadjah Mada University, Faculty of Medicine

    PRINCIPAL INVESTIGATOR
  • Professor dr. Yohanes W Wirohadidjojo, Sp.KK(K), PhD

    Gadjah Mada University, Faculty of Medicine

    STUDY DIRECTOR
  • Bayu W Putera, S.Si, M.Kes

    Prodia Stem Cell Indonesia

    STUDY DIRECTOR
  • dr Bayu M Sasongko, Sp.M, PhD

    Gadjah Mada University, Faculty of Medicine

    STUDY DIRECTOR
  • dr Melita S Djaja, Sp.M

    Jakarta Eye Center

    STUDY CHAIR
  • dr Amyra D Costa

    Jakarta Eye Center

    STUDY CHAIR
  • Rima Haifa, B.Sc

    Prodia StemCell Indonesia

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 8, 2020

First Posted

March 19, 2020

Study Start

October 7, 2018

Primary Completion

June 20, 2019

Study Completion

September 20, 2019

Last Updated

June 4, 2020

Record last verified: 2020-03

Locations