NCT04278417

Brief Summary

The purpose of this study was to evaluate the efficacy and safety of brolucizumab compared to panretinal photocoagulation laser (PRP) in patients with proliferative diabetic retinopathy (PDR). This evaluation will provide information that brolucizumab is non-inferior to PRP with respect to the change in best corrected visual acuity at Week 54.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
689

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Nov 2020

Typical duration for phase_3

Geographic Reach
16 countries

120 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 18, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 20, 2020

Completed
9 months until next milestone

Study Start

First participant enrolled

November 19, 2020

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 30, 2023

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 19, 2024

Completed
1 day until next milestone

Results Posted

Study results publicly available

August 20, 2024

Completed
Last Updated

October 16, 2025

Status Verified

October 1, 2025

Enrollment Period

2.9 years

First QC Date

February 18, 2020

Results QC Date

June 24, 2024

Last Update Submit

October 8, 2025

Conditions

Keywords

proliferative diabetic retinophathy, retinal neovascularization, anti-VEGF, brolucizumab, intravitreal injection, panretinal photocoagulation

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Best-corrected Visual Acuity (BCVA) at Week 54 for the Study Eye

    BCVA was assessed using Early Treatment Diabetic Retinopathy Study (ETDRS) visual acuity testing charts. Visual function of the study eye was assessed using the ETDRS protocol. Participants with a BCVA ETDRS letter score of \>= 34 ETDRS letters (Snellen equivalent 20/200) at Screening / Baseline in the study eye were included. Min and max possible scores are 0-100 respectively. A higher score represents better functioning. Last observation carried forward (LOCF) was used for the imputation of missing values.

    Baseline, Week 54

Secondary Outcomes (12)

  • Number and Percentage of Subjects With no Proliferative Diabetic Retinopathy (PDR) at Week 54 for the Study Eye

    Week 54

  • Number and Percentage of Subjects With no Proliferative Diabetic Retinopathy (PDR) at Week 96 for the Study Eye

    Week 96

  • Number and Percentage of Subjects With Center-involved Diabetic Macular Edema (CI- DME) up to Week 54 for the Study Eye

    Up to Week 54

  • Number and Percentage of Subjects With Center-involved Diabetic Macular Edema (CI- DME) up to Week 96 for the Study Eye

    Up to Week 96

  • Area Under the Curve in Change From Baseline in BCVA up to Week 54 and up to Week 96 - for the Study Eye

    Baseline, up to Week 54 and up to Week 96

  • +7 more secondary outcomes

Study Arms (2)

Brolucizumab 6 mg

EXPERIMENTAL

Intra-vitreal injection. 3 x q6w loading injections, followed by q12w maintenance through Week 90

Biological: Brolucizumab 6 mg

Panretinal photocoagulation laser Arm

ACTIVE COMPARATOR

Initial treatment in 1-4 sessions up to Week 12, followed with additional PRP treatment as needed

Procedure: Panretinal photocoagulation laser

Interventions

3 x q6w loading injections, followed by q12w maintenance through Week 90

Also known as: RTH258
Brolucizumab 6 mg

initial treatment in 1-4 sessions up to Week 12, followed with additional PRP treatment as needed

Also known as: PRP
Panretinal photocoagulation laser Arm

Eligibility Criteria

Age18 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed informed consent must be obtained prior to participation
  • Able to complete adequate fundus photographs and retinal images
  • Diagnosis of type 1 or 2 Diabetes Mellitus (DM) and HbA1c less than or equal to 12% at screening
  • DM treatment stable for at least 3 months
  • PDR diagnosis with no previous PRP treatment in the study eye

You may not qualify if:

  • Concomitant conditions or ocular disorders in the study eye at Screening or Baseline that could compromise a response to study treatment.
  • Presence of diabetic macular edema in the study eye
  • Active infection or inflammation in the study eye
  • Uncontrolled glaucoma (IOP greater than 25 mmHg)
  • Intravitreal anti-VEGF treatment within 6 months
  • Treatment with intraocular corticosteroids
  • End stage renal disease requiring dialysis or kidney transplant
  • Uncontrolled blood pressure
  • Systemic anti-VEGF therapy at any time

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (120)

Retina Associates SW

Tucson, Arizona, 85704, United States

Location

Retina- Vitreous Assoc Medical Group

Beverly Hills, California, 90211, United States

Location

Retina Consultants of Orange County

Fullerton, California, 92835, United States

Location

Salehi Retina Institute

Huntington Beach, California, 92647, United States

Location

Retina Consultants of Southern California

Redlands, California, 92374, United States

Location

Premiere Practice Management LLC

Torrance, California, 90505, United States

Location

Lundquist Inst BioMed at Harbor

Torrance, California, 90509-2910, United States

Location

Miramar Eye Specialists

Ventura, California, 93003, United States

Location

Advanced Research LLC

Deerfield Beach, Florida, 33064, United States

Location

Rand Eye Institute

Deerfield Beach, Florida, 33064, United States

Location

Pinnacle Research Institute

Fort Lauderdale, Florida, 33309, United States

Location

National Ophthalmic Research Institute

Fort Myers, Florida, 33912-7125, United States

Location

Florida Retina Institute

Jacksonville, Florida, 32216, United States

Location

Blue Oc Clin Res at Palm Bch Eye Ct

Lakeland, Florida, 33801, United States

Location

MedEye Associates

Miami, Florida, 33143, United States

Location

Florida Retina Institute

Orlando, Florida, 32804, United States

Location

Eye Center of North Florida

Panama City, Florida, 32405, United States

Location

Fort Lauderdale Eye Institute

Plantation, Florida, 33324, United States

Location

Retina Associates

Elmhurst, Illinois, 60126, United States

Location

Midwest Eye Institute

Indianapolis, Indiana, 46280, United States

Location

John-Kenyon American Eye Institute PC

New Albany, Indiana, 47150, United States

Location

Retina Associates PA

Lenexa, Kansas, 66215, United States

Location

Cumberland Valley Retina Consultants

Hagerstown, Maryland, 21740, United States

Location

University of Mississippi Med Ctr

Jackson, Mississippi, 39216, United States

Location

Retina Associates Of Cleveland

Cleveland, Ohio, 44122, United States

Location

Dean McGee Eye Institute

Oklahoma City, Oklahoma, 73104, United States

Location

Cascade Medical Research Institute

Springfield, Oregon, 97477, United States

Location

Erie Retinal Surgery

Erie, Pennsylvania, 16507, United States

Location

Charleston Neuroscience Institute

Ladson, South Carolina, 29456, United States

Location

Southeastern Retina Associates P C

Knoxville, Tennessee, 37923, United States

Location

Austin Retina Associates

Austin, Texas, 78705, United States

Location

Texan Eye P A

Austin, Texas, 78731, United States

Location

Retina And Vitreous Of Texas

Bellaire, Texas, 77401, United States

Location

Retina Consultants TX Rsrch Ctr

Bellaire, Texas, 77401, United States

Location

Texas Retina Associates

Fort Worth, Texas, 76104, United States

Location

Valley Retina Institute PA

Harlingen, Texas, 78550, United States

Location

Retina Consultants of Houston PA

Houston, Texas, 77030, United States

Location

Medical Center Opthamology Assoc

San Antonio, Texas, 78240, United States

Location

Retina Associates Of South Texas PA

San Antonio, Texas, 78240, United States

Location

Virginia Eye Consultants

Norfolk, Virginia, 23502, United States

Location

Novartis Investigative Site

Caba, Buenos Aires, 1116, Argentina

Location

Novartis Investigative Site

Ciudad Autonoma de Bs As, Buenos Aires, C1015ABO, Argentina

Location

Novartis Investigative Site

Rosario, De Santa Fe, B7602, Argentina

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Novartis Investigative Site

CABA, C1061AAE, Argentina

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Novartis Investigative Site

Albury, New South Wales, 2640, Australia

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Novartis Investigative Site

Liverpool, New South Wales, 2170, Australia

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Novartis Investigative Site

Parramatta, New South Wales, 2150, Australia

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Novartis Investigative Site

Strathfield, New South Wales, 2135, Australia

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Novartis Investigative Site

Porto Alegre, Rio Grande do Sul, 90035-903, Brazil

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Novartis Investigative Site

Blumenau, Santa Catarina, 89052-504, Brazil

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Novartis Investigative Site

São Paulo, São Paulo, 01427-002, Brazil

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Novartis Investigative Site

Sorocaba, São Paulo, 18031-060, Brazil

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Novartis Investigative Site

Ottawa, Ontario, K2B 7E9, Canada

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Novartis Investigative Site

Toronto, Ontario, M5T 2S8, Canada

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Novartis Investigative Site

Boisbriand, Quebec, J7H 1S6, Canada

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Novartis Investigative Site

Québec, Quebec, G1S 4L8, Canada

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Novartis Investigative Site

Santiago, RM, 7560994, Chile

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Novartis Investigative Site

Beijing, Beijing Municipality, 100044, China

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Novartis Investigative Site

Shantou, Guangdong, 515041, China

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Wuhan, Hubei, 430060, China

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Novartis Investigative Site

Wuhan, Hubei, 430070, China

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Nanjing, Jiangsu, 210000, China

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Novartis Investigative Site

Nantong, Jiangsu, 226000, China

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Novartis Investigative Site

Changchun, Jilin, 130041, China

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Novartis Investigative Site

Shenyang, Liaoning, 110000, China

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Novartis Investigative Site

Xi'an, Shaanxi, 710004, China

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Novartis Investigative Site

Chengdu, Sichuan, 610041, China

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Novartis Investigative Site

Tianjin, Tianjin Municipality, 300020, China

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Novartis Investigative Site

Wenzhou, Zhejiang, 325027, China

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Novartis Investigative Site

Beijing, 100050, China

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Novartis Investigative Site

Beijing, 100191, China

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Novartis Investigative Site

Beijing, 100730, China

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Novartis Investigative Site

Shanghai, 200080, China

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Novartis Investigative Site

Ahmedabad, Gujarat, 380 016, India

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Novartis Investigative Site

Coimbatore, Tamil Nadu, 641014, India

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Novartis Investigative Site

Tirunelveli, Tamil Nadu, 627003, India

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Novartis Investigative Site

Chandigarh, 160012, India

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Novartis Investigative Site

New Delhi, 110 029, India

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Novartis Investigative Site

Nagakute, Aichi-ken, 480-1195, Japan

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Novartis Investigative Site

Nagoya, Aichi-ken, 466 8560, Japan

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Novartis Investigative Site

Sakura, Chiba, 285-8741, Japan

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Novartis Investigative Site

Yoshida-gun, Fukui, 910-1193, Japan

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Novartis Investigative Site

Kurume, Fukuoka, 830-0011, Japan

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Novartis Investigative Site

Kōriyama, Fukushima, 963-8052, Japan

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Novartis Investigative Site

Asahikawa, Hokkaido, 078 8510, Japan

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Novartis Investigative Site

Kita-gun, Kagawa-ken, 761-0793, Japan

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Novartis Investigative Site

Tsu, Mie-ken, 514-8507, Japan

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Novartis Investigative Site

Matsumoto, Nagano, 390-8621, Japan

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Novartis Investigative Site

Shimotsuke, Tochigi, 329-0498, Japan

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Novartis Investigative Site

Chiyoda-ku, Tokyo, 101-8309, Japan

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Novartis Investigative Site

Hachiōji, Tokyo, 193-0944, Japan

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Novartis Investigative Site

Meguro-ku, Tokyo, 152-8902, Japan

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Novartis Investigative Site

Akita, 010-8543, Japan

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Novartis Investigative Site

Kobe, 650-0017, Japan

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Novartis Investigative Site

Osaka, 545-8586, Japan

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Novartis Investigative Site

Ciudad de, Mexico City, 06800, Mexico

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Novartis Investigative Site

Mexico City, 06760, Mexico

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Novartis Investigative Site

Tijuana, 22010, Mexico

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Novartis Investigative Site

Makati, NCR, 1229, Philippines

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Novartis Investigative Site

Makati, 1229, Philippines

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Novartis Investigative Site

Pasig, 1605, Philippines

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Emanuelli Research and Development Center LLC

Arecibo, 00612, Puerto Rico

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Novartis Investigative Site

Cheboksary, 428028, Russia

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Novartis Investigative Site

Moscow, 119021, Russia

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Novartis Investigative Site

Moscow, 127473, Russia

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Novartis Investigative Site

Moscow, 127486, Russia

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Novartis Investigative Site

Omsk, 644024, Russia

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Novartis Investigative Site

Sterlitamak, 453128, Russia

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Novartis Investigative Site

Ulyanovsk, 432063, Russia

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Novartis Investigative Site

Yekaterinburg, 620109, Russia

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Novartis Investigative Site

Bundang Gu, Gyeonggi-do, 13620, South Korea

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Novartis Investigative Site

Seoul, Seocho Gu, 06591, South Korea

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Novartis Investigative Site

Daegu, 705703, South Korea

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Novartis Investigative Site

Seoul, 06351, South Korea

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Novartis Investigative Site

Hualien City, 970, Taiwan

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Novartis Investigative Site

Kaohsiung City, 80756, Taiwan

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Novartis Investigative Site

Ankara, 06100, Turkey (Türkiye)

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Novartis Investigative Site

Ankara, 06230, Turkey (Türkiye)

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Novartis Investigative Site

Istanbul, 34420, Turkey (Türkiye)

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Novartis Investigative Site

Izmir, 35340, Turkey (Türkiye)

Location

Related Links

MeSH Terms

Conditions

Retinal Neovascularization

Interventions

brolucizumab

Condition Hierarchy (Ancestors)

Retinal DiseasesEye DiseasesNeovascularization, PathologicMetaplasiaPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 18, 2020

First Posted

February 20, 2020

Study Start

November 19, 2020

Primary Completion

October 30, 2023

Study Completion

August 19, 2024

Last Updated

October 16, 2025

Results First Posted

August 20, 2024

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations. This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com.

More information

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