NCT04157348

Brief Summary

This is a randomized, double blind, active-controlled, parallel group, multicenter 52-week Phase 3 study to compare the efficacy and safety of benralizumab 30 mg versus mepolizumab 300 mg administered by subcutaneous (SC) injection in patients with relapsing or refractory EGPA on corticosteroid therapy with or without stable immunosuppressive therapy. All patients who complete the 52-week double-blind treatment period on IP may be eligible to continue into an open label extension (OLE) period. The OLE period is intended to allow each patient at least 1 year of treatment with open-label benralizumab 30 mg administered SC (earlier enrolled patients may therefore be in the OLE for longer than 1 year).

Trial Health

62
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
140

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Oct 2019

Longer than P75 for phase_3

Geographic Reach
9 countries

50 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 29, 2019

Completed
1 month until next milestone

Study Start

First participant enrolled

October 29, 2019

Completed
10 days until next milestone

First Posted

Study publicly available on registry

November 8, 2019

Completed
3.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 10, 2023

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

January 14, 2025

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2026

Completed
Last Updated

February 3, 2026

Status Verified

January 1, 2026

Enrollment Period

3.8 years

First QC Date

September 29, 2019

Results QC Date

July 16, 2024

Last Update Submit

January 15, 2026

Conditions

Keywords

BenralizumabInhaled corticosteroidsEosinophilic Granulomatous Vasculitis

Outcome Measures

Primary Outcomes (2)

  • Number of Subjects Who Achieved Main Remission at Both Weeks 36 and 48

    Percentage of patients with relapsing or refractory EGPA, achieving remission, defined as BVAS = 0 and OCS dose ≤ 4 mg/day (main remission definition) at both Weeks 36 and 48.

    Week 36 and Week 48

  • Supportive Endpoint: Proportion of Subjects Who Achieved Supportive Remission at Both Weeks 36 and 48

    Supportive endpoint: Proportion of patients with relapsing or refractory EGPA, achieving remission, defined as BVAS = 0 and OCS dose ≤ 7.5 mg/day (supportive remission definition) at both Weeks 36 and 48.

    Week 36 and Week 48

Secondary Outcomes (30)

  • Total Accrued Duration of Remission During DB Treatment Period

    from baseline to end of DB period, 52 Weeks.

  • Total Accrued Duration of Sustained Remission During DB Treatment Period

    from baseline to end of DB period, 52 Weeks

  • Time From Randomization to First Eosinophilic Granulomatosis With Polyangiitis (EGPA) Relapse

    from baseline to end of DB period, 52 Weeks

  • Annualized Eosinophilic Granulomatosis With Polyangiitis (EGPA) Relapse Rate

    from baseline to end of DB period, 52 Weeks

  • Average Daily Dose of Prednisolone/Prednisone and Change From Baseline During Week 48 Through 52

    last 4 weeks of DB period

  • +25 more secondary outcomes

Study Arms (2)

Benralizumab arm

EXPERIMENTAL

1x benralizumab SC injection + 3x placebo to mepolizumab SC injections

Biological: BenralizumabBiological: Placebo to Mepolizumab

Mepolizumab arm

ACTIVE COMPARATOR

3x mepolizumab SC injections + 1x placebo to benralizumab SC injection

Biological: MepolizumabBiological: Placebo to Benralizumab

Interventions

BenralizumabBIOLOGICAL

30 mg/mL solution for injection in a single accessorized prefilled syringe (APFS) will be administered subcutaneously (SC)

Benralizumab arm
MepolizumabBIOLOGICAL

3x100 mg vials of powder for solution for injection reconstituted into 3 separate 1 mL syringes for administration on each dosing occasion. Injection volume per syringe is 1 mL. Mepolizumab active solution will be administered subcutaneously (SC)

Mepolizumab arm

Matching placebo solution for injection in APFS, 1 mL fill volume. Placebo solution will be administered subcutaneously (SC)

Mepolizumab arm

Matching placebo: 0.9% sodium chloride, solutions for injection in 1mL syringes (3 syringes will be used on each dosing occasion). Injection volume per syringe is 1mL. Placebo to Mepolizumban will be administered subcutaneously (SC)

Benralizumab arm

Eligibility Criteria

Age18 Years - 130 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects age 18 years or older.
  • EGPA diagnosis based on history or presence asthma and eosinophilia (\>1.0x10\^9/L and/or \>10% of leucocytes) and at least 2 of; biopsy with eosinophilic vasculitis or perivascular/granulomatous inflammation; mono-or polyneuropathy, non-fixed pulmonary infiltrates, sino-nasal abnormality; cardiomyopathy; glomerulonephritis; alveolar haemorrhage; palpable purpura; anti neutrophil cytoplasmic anti-body (ANCA) positivity (Myeloperoxidase or proteinease 3).
  • History of relapsing (at least 1 confirmed EGPA relapse within last 2 years and \> 12 weeks prior to screening), or refractory (failure to attain remission, defined as BVAS=0 and oral corticosteroid (OCS) dose \<=7.5 mg/day of prednisolone or equivalent, following standard induction regimen for at least 3 months and within 6 months prior to screening, or recurrence of symptoms upon OCS tapering at any dose of ≥7.5 mg/day prednisolone or equivalent.
  • If induction with glucocorticoidsalone, patient must have failed to attain remission after 3 months and the glucocorticoid dose must be ≥15 mg/day prednisolone or equivalent for the 4 weeks prior to randomization.
  • Must be on a stable dose of oral prednisolone or prednisone of ≥7.5 mg/day (but not \>50mg/day) for at least 4 weeks prior to randomization.
  • If receiving immunosuppressive therapy (excluding cyclophosphamide) the dose must be stable for the 4 weeks prior to randomization and during the study (dose reductions for safety reasons will be permitted).
  • QTc(F)\<450 msec or QTc(F)\<480 msec for patients with bundle branch block.
  • Females of childbearing potential must use an acceptable method of birth control from randomization for at least 12 weeks after the last study drug administration.

You may not qualify if:

  • Diagnosed with granulomatosis with polyangiitis (GPA) or microscopic polyangiitis (MPA)
  • Organ or life-threatening EGPA \< 3 months prior to screening
  • Currently pregnant or breastfeeding, or planning to become pregnant during study participation.
  • Current malignancy or history of malignancy, unless received curative therapy \>5 years ago, or \>1 year ago for basal cell carcinoma, localized squamous cell carcinoma of the skin or in situ carcinoma of the cervix
  • An untreated or refractory helminth parasitic infection \< 24 weeks prior to screening
  • Unstable liver disease
  • Severe or clinically significant, uncontrolled cardiovascular disease
  • Other concurrent disease that may put the patient at risk, or may influence the results of the study, or the patients' ability to complete entire duration of the study
  • Chronic or ongoing infectious disease requiring systemic anti-infective treatment
  • Known immunodeficiency disorder or positive HIV test
  • Prior receipt of mepolizumab, reslizumab, dupilumab or benralizumab. Receipt of intravenous/intramuscular/subcutaneous corticosteroids within 4 weeks prior to randomization, receipt of omalizumab within 130 days prior to screening, rituximab within 6 months prior to screening (or B-cells not recovered), interferon-α or alemtuzumab within 6 months prior to screening, receipt of anti-tumor necrosis factor therapy within 12 weeks prior to screening or an investigational non-biologic product within 30 days or 5 half-lives prior to screening, whichever is longer. Receipt of any other marketed or investigational biologic products within 4 months or 5 half-lives prior to screening, whichever is longer.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

Research Site

Denver, Colorado, 80206, United States

Location

Research Site

Ann Arbor, Michigan, 48109, United States

Location

Research Site

Rochester, Minnesota, 55905-0001, United States

Location

Research Site

Albuquerque, New Mexico, 87106, United States

Location

Research Site

Great Neck, New York, 11021, United States

Location

Research Site

New York, New York, 10021, United States

Location

Research Site

Philadelphia, Pennsylvania, 19104, United States

Location

Research Site

Denison, Texas, 75020, United States

Location

Research Site

Seattle, Washington, 98115, United States

Location

Research Site

Brussels, 1070, Belgium

Location

Research Site

Brussels, 1090, Belgium

Location

Research Site

Calgary, Alberta, T2N 4Z6, Canada

Location

Research Site

Hamilton, Ontario, L8N 4A6, Canada

Location

Research Site

Toronto, Ontario, M5G 1E2, Canada

Location

Research Site

Toronto, Ontario, M5T 3A9, Canada

Location

Research Site

Dijon, 21079, France

Location

Research Site

Marseille, 13915, France

Location

Research Site

Montpellier, 34090, France

Location

Research Site

Nantes, 44093, France

Location

Research Site

Paris, 75014, France

Location

Research Site

Paris, 75877, France

Location

Research Site

Suresnes, 92151, France

Location

Research Site

Toulouse, 31059, France

Location

Research Site

Bamberg, 96049, Germany

Location

Research Site

Freiburg im Breisgau, 79106, Germany

Location

Research Site

Hamburg, 20251, Germany

Location

Research Site

Kirchheim, 73230, Germany

Location

Research Site

Lübeck, 23538, Germany

Location

Research Site

Ashkelon, 7830604, Israel

Location

Research Site

Beersheba, 84101, Israel

Location

Research Site

Jerusalem, 91120, Israel

Location

Research Site

Ramat Gan, 52621, Israel

Location

Research Site

Rehovot, 7661041, Israel

Location

Research Site

Tel Aviv, 6423906, Israel

Location

Research Site

Cuneo, 12100, Italy

Location

Research Site

Florence, 50141, Italy

Location

Research Site

Milan, 20132, Italy

Location

Research Site

Milan, 20162, Italy

Location

Research Site

Naples, 80131, Italy

Location

Research Site

Roma, 00168, Italy

Location

Research Site

Torino, 10128, Italy

Location

Research Site

Chiba, 260-0877, Japan

Location

Research Site

Kita-gun, 761-0793, Japan

Location

Research Site

Sagamihara-shi, 228-0815, Japan

Location

Research Site

Sendai, 980-8574, Japan

Location

Research Site

Shinjuku-ku, 162-8666, Japan

Location

Research Site

Cambridge, CB2 0QQ, United Kingdom

Location

Research Site

Leicester, LE3 9QP, United Kingdom

Location

Research Site

London, SE19RT, United Kingdom

Location

Research Site

Portsmouth, PO6 3LY, United Kingdom

Location

Related Publications (2)

  • Wechsler ME, Nair P, Terrier B, Walz B, Bourdin A, Jayne DRW, Jackson DJ, Roufosse F, Borjesson Sjo L, Fan Y, Jison M, McCrae C, Necander S, Shavit A, Walton C, Merkel PA; MANDARA Study Group. Benralizumab versus Mepolizumab for Eosinophilic Granulomatosis with Polyangiitis. N Engl J Med. 2024 Mar 7;390(10):911-921. doi: 10.1056/NEJMoa2311155. Epub 2024 Feb 23.

  • Serling-Boyd N, Wallace ZS. Management of primary vasculitides with biologic and novel small molecule medications. Curr Opin Rheumatol. 2021 Jan;33(1):8-14. doi: 10.1097/BOR.0000000000000756.

Related Links

MeSH Terms

Conditions

Churg-Strauss Syndrome

Interventions

benralizumabmepolizumab

Condition Hierarchy (Ancestors)

Anti-Neutrophil Cytoplasmic Antibody-Associated VasculitisSystemic VasculitisVasculitisVascular DiseasesCardiovascular DiseasesGranulomaLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesSkin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Global Clinical Head
Organization
AstraZeneca

Study Officials

  • Michael Wechsler, MD

    National Jewish Health, 1400 Jackson St Denver, CO 80206

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 29, 2019

First Posted

November 8, 2019

Study Start

October 29, 2019

Primary Completion

August 10, 2023

Study Completion

March 31, 2026

Last Updated

February 3, 2026

Results First Posted

January 14, 2025

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal Vivli.org. All requests will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. "Yes", indicates that AZ are accepting requests for IPD, but this does not mean all requests will be approved.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA/PhRMA Data-Sharing Principles. For details of our timelines, please refer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the anonymized individual patient-level data via secure research environment Vivli.org. A Signed Data Usage Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information.
More information

Locations