NCT04084080

Brief Summary

The SCD-CARRE trial is a Phase 3, prospective, randomized, multicenter, controlled, parallel two-arm study aimed to determine if automated exchange blood transfusion and standard of care administered to high mortality risk adult SCD patients reduces the total number of episodes of clinical worsening of SCD requiring acute health care encounters (non-elective infusion center/ER/hospital visits) or resulting in death over 12 months as compared with standard of care.

Trial Health

78
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
173

participants targeted

Target at P25-P50 for phase_3

Timeline
0mo left

Started Feb 2020

Longer than P75 for phase_3

Geographic Reach
3 countries

23 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 26, 2019

Completed
15 days until next milestone

First Posted

Study publicly available on registry

September 10, 2019

Completed
6 months until next milestone

Study Start

First participant enrolled

February 26, 2020

Completed
6.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 31, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 31, 2026

Last Updated

March 4, 2026

Status Verified

March 1, 2026

Enrollment Period

6.3 years

First QC Date

August 26, 2019

Last Update Submit

March 2, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Episodes of clinical worsening

    The efficacy of the intervention will be measured by comparing the total number of episodes of clinical worsening of SCD requiring acute health care encounters (non-elective infusion center/ER/Hospital visits) or resulting in death over 13 months between groups.

    13 months

Secondary Outcomes (17)

  • Acute healthcare event

    13 months

  • Twelve-month survival

    13 months

  • Survival free of acute healthcare encounters

    13 months

  • Total number of acute health care encounters

    13 months

  • Measures of exercise capacity - 6 minute walk distance

    4, 8, and 12 months

  • +12 more secondary outcomes

Study Arms (2)

Exchange transfusion plus standard of care

EXPERIMENTAL

Randomized to standard of care and automated exchange blood transfusion every 3-6 weeks for 12 months.

Biological: Red Blood CellOther: Standard of care

Standard of care

ACTIVE COMPARATOR

Randomized to standard of care

Other: Standard of care

Interventions

Red Blood CellBIOLOGICAL

Red blood cell exchange transfusions will be performed every 3-6 weeks to maintain a target post-transfusion hemoglobin S level of \<20% and a pre-transfusion hemoglobin S of \<30%.

Also known as: Red blood cell (RBC)
Exchange transfusion plus standard of care

NHLBI/ASH/ATS Expert Panel recommended guidelines

Exchange transfusion plus standard of careStandard of care

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18 years or older
  • Diagnosis of SCD: homozygous sickle cell disease, hemoglobin-SC, Sβ-thalassemia, hemoglobin-SO or hemoglobin-SD.
  • Patients not on a chronic exchange transfusion program for at least 60 days.
  • If patients are on a SCD drug (e.g. hydroxyurea, glutamine, or P-selectin inhibitors), the doses must be stable for at least 60 days prior to randomization. At the time of randomization, participants must be off Oxbryta for at least 30 days.
  • Any one of the following vasculopathy biomarker clinical results (a, b, c, d or e) measured in the last 24 months before randomization that indicates a high-risk patient:
  • Both a TRV 2.5- \<3.0 m/sec and NT-proBNP plasma level ≥ 160 pg/mL,
  • TRV ≥ 3.0 m/sec,
  • Both a mean pulmonary artery pressure (PAP) by right heart catheterization 20-24 mmHg and NT-proBNP plasma level ≥ 160 pg/mL,
  • Mean PAP by right heart catheterization ≥ 25 mmHg,
  • Chronic kidney disease (CKD) due to SCD with abnormal measures on 2 separate occasions as defined by: macroalbuminuria (albumin to creatinine ratio (ACR) \>300 mg/g) or proteinuria (protein to creatinine ratio \>30 mg/mmol), or estimated glomerular filtration rate (eGFR) \< 60 mL/min/1.73 m2. (It is recommended that local laboratories use Chronic Kidney Disease Epidemiology Collaboration \[CKD-EPI\] equation without ethnic factors when estimating and reporting GFR).
  • Clinical results of these biomarkers measured locally at sites within 24 months prior to randomization are acceptable to determine eligibility. TRV, PAP, NT-proBNP, albumin to creatinine ratio, protein to creatinine ratio, or eGFR values must be measured in a steady state (defined as measured ≥ 14 days since an acute care pain event) on different days.
  • vi. Written informed consent obtained from patient to participate in the trial.

You may not qualify if:

  • RBC alloimmunization resulting in inability of blood bank to obtain compatible components for chronic exchange transfusions
  • Previous history of hyper-hemolysis syndrome
  • Previous history of severe transfusion reaction resulting in renal failure or due to serious complications such as hypotension or respiratory distress
  • More than 10 vaso-occlusive episodes in the past 12 months requiring admission to a hospital to receive treatment.
  • Religious objection to receiving blood transfusion
  • Diagnosis of ischemic stroke within the past 6 months
  • Clinical evidence of liver failure or advanced cirrhosis or any co-existing medical condition that in the Investigator's judgement will substantially increase the risk associated with the patient's participation in the trial
  • Women of childbearing potential who have a positive pregnancy test at baseline

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

University of Alabama

Tuscaloosa, Alabama, 35401, United States

Location

UCSF Benioff Children's Hospital Oakland

Oakland, California, 94609, United States

Location

Howard University Center for Sickle Cell Disease

Washington D.C., District of Columbia, 20060, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

University of Illinois at Chicago

Chicago, Illinois, 60607, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21206, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

Washington University-St. Louis

St Louis, Missouri, 63110, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Montefiore Medical Center

New York, New York, 10461, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Atrium Health

Charlotte, North Carolina, 28204, United States

Location

Duke University

Durham, North Carolina, 27708, United States

Location

East Carolina University

Greenville, North Carolina, 27834, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15232, United States

Location

University of Texas Health Science Center at Houston

Houston, Texas, 77030, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23284, United States

Location

Hemorio

Rio de Janeiro, Brazil

Location

Kremlin-Bicêtre

Créteil, France

Location

Henri Mondor Hopital

Paris, France

Location

Related Publications (1)

  • Abbasi M, Srivastava A, Saraf SL. Management of Kidney Disease with Sickle Cell Disease. J Am Soc Nephrol. 2025 Oct 1;36(10):2041-2054. doi: 10.1681/ASN.0000000804. Epub 2025 Jun 26.

MeSH Terms

Conditions

Anemia, Sickle Cell

Interventions

Erythrocyte CountStandard of Care

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Blood Cell CountCell CountCytological TechniquesClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisHematologic TestsInvestigative TechniquesCell Physiological PhenomenaBlood Physiological PhenomenaCirculatory and Respiratory Physiological PhenomenaQuality Indicators, Health CareQuality of Health CareHealth Services AdministrationHealth Care Quality, Access, and Evaluation

Study Officials

  • Mark Gladwin, MD

    University of Maryland

    STUDY CHAIR
  • Darrell Triulzi, MD

    University of Pittsburgh

    PRINCIPAL INVESTIGATOR
  • Maria Brooks, PhD

    University of Pittsburgh

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Vice President for Medical Affairs, University of Maryland and Dean, University of Maryland School of Medicine

Study Record Dates

First Submitted

August 26, 2019

First Posted

September 10, 2019

Study Start

February 26, 2020

Primary Completion (Estimated)

May 31, 2026

Study Completion (Estimated)

May 31, 2026

Last Updated

March 4, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Results from research conducted under this project will be shared in several ways. Manuscripts will be submitted for publication in high-quality peer-reviewed journals, following the NIH Public Access Policy guidelines. Findings will be presented at relevant national conferences, public lectures, scientific institutions and meetings. The timeline for participant recruitment, data collection and analysis will foster publication, facilitated by the investigators' Publications Committee, of critically important and clinically relevant data throughout the trial. The study datasets will be archived and made available to qualified individuals after a period of exclusive use by the SCD-CARRE trial research team and after publication of the primary manuscripts, following NIH guidelines.

Shared Documents
CSR
Time Frame
At the end of the trial, study de-identified datasets will be submitted for permanent archive in the NHLBI BioLINCC repository. The trial will also produce deliverables that will be freely available to the sickle cell community including a description of the protocol for automated red blood cell exchange transfusion.
Access Criteria
All publications based on the SCD-CARRE trial will adhere to the NIH Public Access Policy (Notice NOT-OD-08-033). All study data will be de-identified. At the end of the trial, study de-identified datasets will be submitted for permanent archive in the NHLBI BioLINCC repository. The investigators also will work closely with regional and National SCD Foundations to promote recruitment for this study and communicate our results.

Locations