NCT04077411

Brief Summary

Approaches and Decisions in Acute Pediatric TBI Trial (ADAPT) is an international research study designed to evaluate the impact of interventions on the outcomes of children with severe traumatic brain injury. Pediatric traumatic brain injury (TBI) is the leading killer of children, resulting in more than 7000 deaths and $2 billion in acute care costs each year. Despite this large burden of disease, advances in the field have been limited due to weak evidenced-based guidelines and the limitations of randomized, controlled trials (RCTs) to demonstrate efficacy of single treatment strategies due to wide treatment variability. ADAPT is a practical study design in a novel approach - an observational cohort study designed to evaluate the association of 6 aspects of pediatric TBI care with outcomes using statistical modeling to correct for confounding variables. Completion of this study will provide compelling evidence to change clinical practices, provide evidence for new Level II recommendations for future guidelines and lead to improved research protocols that would limit variability in TBI treatments - helping children immediately through better clinical practices and ultimately through more effective investigation.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,000

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Feb 2014

Longer than P75 for all trials

Geographic Reach
8 countries

48 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 20, 2014

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 26, 2016

Completed
1.9 years until next milestone

Study Completion

Last participant's last visit for all outcomes

August 28, 2018

Completed
1 year until next milestone

First Submitted

Initial submission to the registry

August 29, 2019

Completed
6 days until next milestone

First Posted

Study publicly available on registry

September 4, 2019

Completed
Last Updated

December 8, 2023

Status Verified

March 1, 2023

Enrollment Period

2.6 years

First QC Date

August 29, 2019

Last Update Submit

December 4, 2023

Conditions

Keywords

Severe Traumatic Brain InjuryTBIIntracranial hypertensionCerebrospinal fluidHypersmolar therapiesProphylactic hyperventilationMetabolismNeuropsychology

Outcome Measures

Primary Outcomes (1)

  • Glasgow Outcome Score - Extended Pediatrics

    Physician-rated assessment of functional outcome. Problems in functioning should have deteriorated from premorbid level. The categories are: 8 - Death 7 - Vegetative State (VS) 6 - Lower Severe Disability (Lower SD) 5 - Upper Severe Disability (Upper SD) 4 - Lower Moderate Disability (Lower MD) 3 - Upper Moderate Disability (Upper MD) 2 - Lower Good Recovery (Lower GR) 1 - Upper Good Recovery (Upper GR)

    6 months

Study Arms (1)

Children with severe TBI

Children with severe Traumatic Brain Injury

Other: Observational

Interventions

This is an observational study with no interventions.

Children with severe TBI

Eligibility Criteria

AgeUp to 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodNon-Probability Sample
Study Population

Children with severe traumatic brain injury (TBI)

You may qualify if:

  • Admission to a study site for treatment of severe traumatic brain injury
  • ICP monitor placed as part of the child's standard care
  • Glasgow Coma Scale (GCS) ≤ 8 after resuscitation
  • Age 0 - 18 y

You may not qualify if:

  • \. ICP Monitor placed at another hospital
  • \. Diagnosis of pregnancy in clinical subject

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (48)

Children's Hospital of Alabama

Birmingham, Alabama, 35294, United States

Location

Phoenix Children's Hospital

Phoenix, Arizona, 85016, United States

Location

University of California, San Diego / Rady's Children's Hospital

La Jolla, California, 92093, United States

Location

Children's Hospital of Los Angeles

Los Angeles, California, 90027, United States

Location

UCLA Mattel Children's Hospital

Los Angeles, California, 90095, United States

Location

UC Davis Medical Center

West Sacramento, California, 95798, United States

Location

Children's Hospital Colorado

Denver, Colorado, 80045, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Miami Children's Hospital

Miami, Florida, 33155, United States

Location

Children's Healthcare of Atlanta

Atlanta, Georgia, 30322, United States

Location

University of Iowa Children's Hospita

Iowa City, Iowa, 52252, United States

Location

John Hopkins Children's Center of Baltimore

Baltimore, Maryland, 21287, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02241, United States

Location

Boston Children's Hospital / Harvard University

Boston, Massachusetts, 414413, United States

Location

Wayne State University in Detroit / Children's Hospital of Michigan

Detroit, Michigan, 13201, United States

Location

Washington University - St. Louis

St Louis, Missouri, 63112, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

Location

Carolinas Medical Center Levine Children's Hospital

Charlotte, North Carolina, 28260, United States

Location

University of Cincinnati / Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43271, United States

Location

Penn State University - Hershey

Hershey, Pennsylvania, 17033, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19178, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15213, United States

Location

University of Tennessee / Le Bonheur Children's Hospita

Memphis, Tennessee, 38163, United States

Location

UT Southwestern / Children's Medical Center at Dallas

Dallas, Texas, 75284, United States

Location

Texas Children's Hospital (Baylor College of Medicine)

Houston, Texas, 77030, United States

Location

Primary Children's Hospital

Salt Lake City, Utah, 84113, United States

Location

Children's Hospital of Richmond at VCU

Richmond, Virginia, 23298, United States

Location

University of Washington - Seattle

Seattle, Washington, 98185, United States

Location

University of Wisconsin - Madison

Madison, Wisconsin, 53715, United States

Location

Children's Health Queensland Hospital and Health Service

Brisbane, Australia

Location

Royal Children's Hospital

Melbourne, Australia

Location

Princess Margaret Hospital

Perth, 6008, Australia

Location

All India Institute of Medical Sciences

New Delhi, 110029, India

Location

Erasmus Medical Center Children's Hospital

Rotterdam, 3015 GJ, Netherlands

Location

Starship Children's Hospital

Auckland, New Zealand

Location

University of Cape Town

Cape Town, South Africa

Location

Hospital Vall d'Hebron

Barcelona, Spain

Location

Birmingham Children's Hospita

Birmingham, 6NH, United Kingdom

Location

University Hospitals Bristol

Bristol, United Kingdom

Location

Addenbrookes Hospital

Cambridge, CB2 0QQ, United Kingdom

Location

Leeds Teaching Hospital

Leeds, LS 7TF, United Kingdom

Location

Alder Hey Children's

Liverpool, L12 2AP, United Kingdom

Location

King's College Hospital

London, SE5 9NY, United Kingdom

Location

Great Ormond Street

London, WC1N 1EH, United Kingdom

Location

Newcastle upon Tyne Hospital

Newcastle upon Tyne, NE7 7DN, United Kingdom

Location

University Hospital Southampton

Southampton, SO16 6YD, United Kingdom

Location

Royal Manchester Children's Hospital

Victoria, 3052, United Kingdom

Location

Related Publications (6)

  • Sarnaik A, Ferguson NM, O'Meara AMI, Agrawal S, Deep A, Buttram S, Bell MJ, Wisniewski SR, Luther JF, Hartman AL, Vavilala MS; Investigators of the ADAPT Trial. Age and Mortality in Pediatric Severe Traumatic Brain Injury: Results from an International Study. Neurocrit Care. 2018 Jun;28(3):302-313. doi: 10.1007/s12028-017-0480-x.

    PMID: 29476389BACKGROUND
  • Bell MJ, Adelson PD, Wisniewski SR; Investigators of the ADAPT Study,. Challenges and opportunities for pediatric severe TBI-review of the evidence and exploring a way forward. Childs Nerv Syst. 2017 Oct;33(10):1663-1667. doi: 10.1007/s00381-017-3530-y. Epub 2017 Sep 6.

    PMID: 29149394BACKGROUND
  • Miller Ferguson N, Sarnaik A, Miles D, Shafi N, Peters MJ, Truemper E, Vavilala MS, Bell MJ, Wisniewski SR, Luther JF, Hartman AL, Kochanek PM; Investigators of the Approaches and Decisions in Acute Pediatric Traumatic Brain Injury (ADAPT) Trial. Abusive Head Trauma and Mortality-An Analysis From an International Comparative Effectiveness Study of Children With Severe Traumatic Brain Injury. Crit Care Med. 2017 Aug;45(8):1398-1407. doi: 10.1097/CCM.0000000000002378.

    PMID: 28430697BACKGROUND
  • Larsen GY, Schober M, Fabio A, Wisniewski SR, Grant MJ, Shafi N, Bennett TD, Hirtz D, Bell MJ. Structure, Process, and Culture Differences of Pediatric Trauma Centers Participating in an International Comparative Effectiveness Study of Children with Severe Traumatic Brain Injury. Neurocrit Care. 2016 Jun;24(3):353-60. doi: 10.1007/s12028-015-0218-6.

    PMID: 26627225BACKGROUND
  • Ahmed N, Russo L, Kuo YH. Levetiracetam or Phenytoin as Prophylaxis for Status Epilepticus: Secondary Analysis of the "Approaches and Decisions in Acute Pediatric Traumatic Brain Injury Trial" (ADAPT) Dataset, 2014-2017. Pediatr Crit Care Med. 2024 Aug 1;25(8):710-719. doi: 10.1097/PCC.0000000000003526. Epub 2024 May 8.

  • Surtees TL, Kumar I, Garton HJL, Rivas-Rodriguez F, Parmar H, McCaffery H, Riebe-Rodgers J, Shellhaas RA. Levetiracetam Prophylaxis for Children Admitted With Traumatic Brain Injury. Pediatr Neurol. 2022 Jan;126:114-119. doi: 10.1016/j.pediatrneurol.2021.10.009. Epub 2021 Oct 19.

MeSH Terms

Conditions

Brain Injuries, TraumaticIntracranial Hypertension

Interventions

Watchful Waiting

Condition Hierarchy (Ancestors)

Brain InjuriesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesCraniocerebral TraumaTrauma, Nervous SystemWounds and Injuries

Intervention Hierarchy (Ancestors)

Outcome Assessment, Health CareOutcome and Process Assessment, Health CareQuality of Health CareHealth Services Administration

Study Officials

  • Michael J Bell, MD

    University of Pittsburgh Medical Center

    PRINCIPAL INVESTIGATOR
  • Stephen R Wisniewski, PhD

    University of Pittsburgh

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

August 29, 2019

First Posted

September 4, 2019

Study Start

February 20, 2014

Primary Completion

September 26, 2016

Study Completion

August 28, 2018

Last Updated

December 8, 2023

Record last verified: 2023-03

Data Sharing

IPD Sharing
Will share

Study data will be released to the general public through FITBIR. ADAPT will adhere to all FITBIR policies and procedures.

Shared Documents
STUDY PROTOCOL, ICF
Time Frame
One year after publication of main results paper.
Access Criteria
Investigators requesting and receiving FITBIR data are expected to: * Submit a Data Access Request; * Protect data confidentiality; * Ensure that data security measures are in place; * Notify the Data Access and Quality Committee of policy violations; * Submit annual progress reports detailing significant research findings; and * Include acknowledgements of the FITBIR Informatics System in all publications and presentations.

Locations