NCT04064944

Brief Summary

Neuromyelitis optica spectrum disorder (NMOSD) is one common demyelinating disease of the central nervous system in young adults, with high rate of disability and recurrence, and poor natural course, which can cause a serious burden on families and society. To today, there is still a lack of prospective, multi-center, large sample clinical trial evidence for the treatment and prognosis of acute attack of NMOSD patients. This study will conduct a prospective, multi-center, single-blind, randomized controlled clinical trial of acute attacked NMOSD patients in China. The researchers plan to collect 144 NMOSD patients with acute attack in three research centers of Guangzhou (the Third Affiliated Hospital of Sun Yat-sen University, the Zhongshan Ophthalmic Center of Sun Yat-sen University, and the Guangdong 999 Brain hospital), to study the safety and efficacy of immunoadsorption therapy. The subjects will be randomized into immunoadsorption group and plasma exchange group, and the following indicators will be evaluated: (1) changes in EDSS scores and visual acuity before and after treatment; (2) changes in AQP4-IgG levels; (3) the safety of immunoadsorption treatment. This study is aimed to determine the efficacy and safety of immunoadsorption therapy for acute attack of refractory NMOSD patients, and to provide more sufficient clinical evidence for the therapy selection for acute phase of NMOSD patients.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
144

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Sep 2019

Longer than P75 for phase_2

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 20, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 22, 2019

Completed
10 days until next milestone

Study Start

First participant enrolled

September 1, 2019

Completed
3.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2023

Completed
1.4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2024

Completed
Last Updated

August 22, 2019

Status Verified

August 1, 2019

Enrollment Period

3.9 years

First QC Date

August 20, 2019

Last Update Submit

August 21, 2019

Conditions

Keywords

Neuromyelitis Optica Spectrum Disorderimmunoadsorptionplasma exchangeacute attackrefractory

Outcome Measures

Primary Outcomes (1)

  • Changes in EDSS scores

    Changes in EDSS scores of 4 weeks after the last treatment of plasma exchange or immunoadsorption compared with the first treatment

    4 weeks after the last treatment vs.baseline ( first treatment)

Secondary Outcomes (3)

  • Comparison of follow-up results of EDSS scores

    the next 1 day, 1 week, 2 weeks, 3 months after the last treatment vs. baseline (that of the time before first treatment)

  • Comparison of follow-up results of LogMAR

    the next 1 day, 1 week, 2 weeks, 3 months after the last treatment vs. baseline (that of the time before first treatment)

  • Comparison of follow-up results of AQP4-IgG level

    the next 1 day, 1 week, 2 weeks, 3 months after the last treatment vs. baseline (that of the time before first treatment)

Study Arms (2)

Immunoadsorption group

EXPERIMENTAL

patients' blood purification treatment protocal is Protain A Immunoadsorption method.

Device: blood purification equipment

Plasma exchange group

EXPERIMENTAL

patients' blood purification treatment protocal is Plasma exchange method.

Device: blood purification equipment

Interventions

The subjects enrolled in this study will undergo blood purification treatment, and will be randomized into either immunoadsorption group or plasma exchange group, and the following indicators will be evaluated: (1) changes in EDSS scores and visual acuity before and after treatment; (2) changes in AQP4-IgG levels; (3) the safety of immunoadsorption treatment.

Immunoadsorption groupPlasma exchange group

Eligibility Criteria

Age14 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Patients should meet the 2015 International NMOSD with acute attacks diagnostic criteria (including first episodes and recurrences)
  • When NMOSD Patients with acute attacks undergo a course of hormone shock therapy (5-10g total methylprednisolone), EDSS ≥ 6.0 or visual acuity ≤ 20/200
  • Serum AQP4-IgG positive (CBA test)

You may not qualify if:

  • Weight \<25Kg
  • Nursing or pregnant women
  • Unable to establish a peripheral or central vascular access
  • The use of rituximab and gamma-ball shocks within 3 months prior to enrollment
  • Using immunoadsorption and/or plasma exchange therapy within 3 months before enrollment
  • ACEI drugs must be taken within 1 week before the first treatment and during treatment and cannot be stopped

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Neuromyelitis Optica

Condition Hierarchy (Ancestors)

Myelitis, TransverseDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesOptic NeuritisOptic Nerve DiseasesCranial Nerve DiseasesDemyelinating DiseasesEye DiseasesAutoimmune DiseasesImmune System Diseases

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
professor

Study Record Dates

First Submitted

August 20, 2019

First Posted

August 22, 2019

Study Start

September 1, 2019

Primary Completion

August 1, 2023

Study Completion

December 31, 2024

Last Updated

August 22, 2019

Record last verified: 2019-08

Data Sharing

IPD Sharing
Will not share