NCT04057131

Brief Summary

The objectives of this survey are to collect data to report the safety and efficacy of Firazyr (Icatibant acetate) in the post-marketing phase in participants diagnosed with Hereditary Angioedema (HAE).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
179

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Nov 2018

Longer than P75 for all trials

Geographic Reach
1 country

18 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 20, 2018

Completed
9 months until next milestone

First Submitted

Initial submission to the registry

August 13, 2019

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 15, 2019

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 29, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 29, 2024

Completed
7 months until next milestone

Results Posted

Study results publicly available

February 21, 2025

Completed
Last Updated

February 21, 2025

Status Verified

February 1, 2025

Enrollment Period

5.7 years

First QC Date

August 13, 2019

Results QC Date

January 5, 2025

Last Update Submit

February 2, 2025

Conditions

Outcome Measures

Primary Outcomes (6)

  • Number of Participants With Adverse Events

    An adverse event (AE) is any untoward or undesirable medical occurrence in a participant linked in time with the use of a pharmaceutical/ medicinal product. They are not limited to the events with clear causal relationship with treatment with concerned drug. An adverse event can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease temporally associated with the use of a medicinal product, whether or not related to the medicinal product.

    Baseline up to end of the study (up to approximately 68 months)

  • Number of Participants With Adverse Drug Reaction

    An adverse event (AE) is any untoward or undesirable medical occurrence in a participant linked in time with the use of a pharmaceutical/ medicinal product. They are not limited to the events with clear causal relationship with treatment with concerned drug. Adverse drug reaction refers to AE related to administered drug.

    Baseline up to end of the study (up to approximately 68 months)

  • Time to Treatment for Attack

    Time to treatment for attack defined as the time between the onset of the attack and the first injection of treatment. Time to treatment for attack was assessed and reported.

    Up to 3 months

  • Time to First Symptom Relief

    Time to first symptom relief defined as the time between the first injection of treatment and first symptom relief. Time to first symptom relief was assessed and reported.

    Up to 3 months

  • Time to Complete Resolution of Attack

    Time to complete resolution of attack defined as the time between the first injection of treatment and the complete resolution of all symptoms. Time to complete resolution of attack was assessed and reported.

    Up to 3 months

  • Total Duration of Attack

    Total duration of attack defined as the time between the onset of the attack and the complete resolution of all symptoms. Total duration of attack was assessed and reported.

    Up to 3 months

Study Arms (1)

Firazyr

Participants with Hereditary angioedema (HAE) receiving treatment with Icatibant acetate (Firazyr) as prescribed by their physician following locally approved prescribing information.

Drug: Firazyr

Interventions

Participants with Hereditary angioedema (HAE) receiving treatment with Icatibant acetate (Firazyr) as prescribed by their physician following locally approved prescribing information.

Also known as: Icatibant acetate
Firazyr

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Hereditary angioedema (HAE) patients in Japan who receive FIRAZYR for first time in the real world clinical setting are eligible for enrollment in this survey.

You may qualify if:

  • Hereditary angioedema (HAE) participants in Japan who receive FIRAZYR for first time in the real world clinical setting.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

Nagoya-city

Nagoya, Aichi-ken, 453-0046, Japan

Location

Toyohashi-city

Toyohashi, Aichi-ken, 441-8570, Japan

Location

Maebashi-city

Maebashi, Gunma, 371-8511, Japan

Location

Asahikawa-city

Asahikawa, Hokkaido, 070-0034, Japan

Location

Fukagawa-city

Fukagawa, Hokkaido, 074-0006, Japan

Location

Rumoi-city

Rumoi, Hokkaido, 077-0011, Japan

Location

Sapporo-city

Sapporo, Hokkaido, 002-8072, Japan

Location

Kasama-city

Kasama, Ibaraki, 309-1703, Japan

Location

Maizuru-city

Maizuru, Kyoto, 625-8585, Japan

Location

Kishiwada-city

Kishiwada, Osaka, 596-0042, Japan

Location

Takatsuki-city

Takatsuki, Osaka, 569-0096, Japan

Location

Kawagoe-city

Kawagoe, Saitama, 350-8550, Japan

Location

Soka-city

Sōka, Saitama, 340-0041, Japan

Location

Numazu-city

Numazu, Shizuoka, 410-0302, Japan

Location

Shimada-city

Shimada, Shizuoka, 427-8502, Japan

Location

Yaezu-city

Yaezu, Shizuoka, 425-0088, Japan

Location

Tachikawa-city

Tachikawa, Tokyo, 190-0014, Japan

Location

Niigata-city

Niigata, 950-1197, Japan

Location

Related Links

MeSH Terms

Conditions

Angioedemas, Hereditary

Interventions

icatibant

Condition Hierarchy (Ancestors)

AngioedemaVascular DiseasesCardiovascular DiseasesHereditary Complement Deficiency DiseasesPrimary Immunodeficiency DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesUrticariaSkin Diseases, VascularSkin DiseasesSkin and Connective Tissue DiseasesHypersensitivity, ImmediateHypersensitivityImmune System DiseasesImmunologic Deficiency Syndromes

Results Point of Contact

Title
Study Director
Organization
Takeda

Study Officials

  • Study Director

    Takeda

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 13, 2019

First Posted

August 15, 2019

Study Start

November 20, 2018

Primary Completion

July 29, 2024

Study Completion

July 29, 2024

Last Updated

February 21, 2025

Results First Posted

February 21, 2025

Record last verified: 2025-02

Data Sharing

IPD Sharing
Will share

Takeda provides access to the de-identified individual participant data (IPD) for eligible studies to aid qualified researchers in addressing legitimate scientific objectives (Takeda's data sharing commitment is available on https://clinicaltrials.takeda.com/takedas-commitment?commitment=5). These IPDs will be provided in a secure research environment following approval of a data sharing request, and under the terms of a data sharing agreement.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Access Criteria
IPD from eligible studies will be shared with qualified researchers according to the criteria and process described on https://vivli.org/ourmember/takeda/. For approved requests, the researchers will be provided access to anonymized data (to respect patient privacy in line with applicable laws and regulations) and with information necessary to address the research objectives under the terms of a data sharing agreement.
More information

Locations