NCT04044690

Brief Summary

This is a phase 3, multicenter, randomized, placebo-controlled, double-blind study of IgPro20 (subcutaneous Ig) treatment in adult subjects with dermatomyositis (DM). The primary objective of this study is to assess the efficacy of IgPro20 subcutaneous (SC) doses in comparison to placebo in adult subjects with DM, as measured by responder status based on Total Improvement Score (TIS) assessments.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
134

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Oct 2019

Longer than P75 for phase_3

Geographic Reach
14 countries

76 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 1, 2019

Completed
4 days until next milestone

First Posted

Study publicly available on registry

August 5, 2019

Completed
3 months until next milestone

Study Start

First participant enrolled

October 21, 2019

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 2, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 2, 2024

Completed
1 year until next milestone

Results Posted

Study results publicly available

December 9, 2025

Completed
Last Updated

December 9, 2025

Status Verified

November 1, 2025

Enrollment Period

5.1 years

First QC Date

August 1, 2019

Results QC Date

October 17, 2025

Last Update Submit

November 24, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Responder Rate

    A responder was defined as a participant with a TIS \>= 20 points at Week 25 and at least 1 of the previous scheduled visits (Week 17 or 21), who completes 24 weeks of randomized IMP treatment without the use of rescue corticosteroid treatment. The TIS was a sum response criterion which incorporates 6 weighted international myositis assessment and clinical studies (IMACS) core set measures (CSMs) including Physician and Patient Global Disease Activity (PGA), Manual Muscle Testing-8 (MMT-8), Health Assessment Questionnaire, Muscle Enzyme, and Extramuscular Global Activity (EGA). Thresholds for minimal, moderate, and major improvement were \>= 20, \>= 40, and \>= 60 points, respectively on the TIS. Percentage of responders at Week 25 based on TIS are reported here. Multiple imputation (MI) was used to impute missing values for participants who discontinued due to the military activities in Ukraine.

    At Week 25

Secondary Outcomes (33)

  • Mean TIS

    At Week 25

  • Mean Changes From Baseline in MMT-8

    From Baseline to Week 25

  • Mean Changes From Baseline in Cutaneous Dermatomyositis Disease Area and Severity Index Total Activity Score (CDASI-A)

    From Baseline to Week 25

  • Percentage of Participants Who Are Able to Reduce the Oral Corticosteroid Dose by >= 25%

    At Week 25

  • Period 1: Mean TIS at Each Visit

    At Week 5, 9, 13, 17, 21, and 25

  • +28 more secondary outcomes

Study Arms (2)

IgPro20

EXPERIMENTAL

human immunoglobulin G administered subcutaneously

Drug: human immunoglobulin G

Placebo

PLACEBO COMPARATOR

human albumin solution administered subcutaneously

Drug: Placebo

Interventions

human immunoglobulin G administered subcutaneously

Also known as: IgPro20, Hizentra
IgPro20

contains 2% human albumin, similar excipients as IgPro20 (Hizentra), same volume, same duration, administered subcutaneously

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects ≥ 18 years of age
  • Diagnosis of at least probable idiopathic inflammatory myopathies (IIM) per European League Against Rheumatism/American College of Rheumatology (EULAR/ACR) Classification Criteria which includes confirmation of dermatomyositis (DM) rash/manifestation, disease activity defined by presence of DM rash / manifestation or an objective disease activity measure
  • Disease severity defined by Physician global activity visual analog scale (VAS) with a minimum value of 2.0 cm on a 10 cm scale and MMT-8 ≤ 142 or CDASI total activity score ≥ 14.
  • Corticosteroid daily dose less than that or equal to 20 mg prednisolone equivalent

You may not qualify if:

  • Cancer-associated myositis
  • Evidence of active malignant disease or malignancies diagnosed within the previous 5 years
  • Physician Global Damage score ≥ 3, or clinically relevant improvement between Screening Visit and Baseline

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (76)

8401117 - Arizona Arthritis & Rheumatology Research

Glendale, Arizona, 85306, United States

Location

8401199 - Neuromuscular Research Center

Phoenix, Arizona, 85028, United States

Location

8401129 - UCLA - Rheumatology Los Angeles

Los Angeles, California, 90095, United States

Location

8401473 - RecioMed Clinical Research Network, Inc.

Boynton Beach, Florida, 33472, United States

Location

8401160 - Center For Rheumatology

Fort Lauderdale, Florida, 33334, United States

Location

8401132 - Omega Research Maitland

Orlando, Florida, 32810, United States

Location

8401107 - Morsani Center for Advanced Health Care (CAHC)

Tampa, Florida, 33616, United States

Location

8401152 - The University of Kansas Medical Center

Fairway, Kansas, 66205, United States

Location

8401476 - DS Research

Louisville, Kentucky, 40241, United States

Location

8401487 - Ohio State University

Columbus, Ohio, 43210, United States

Location

8401486 - Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

8401210 - University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

8401151 - Biomedical Science Tower

Pittsburgh, Pennsylvania, 15261, United States

Location

8401474 - West Tennessee Research Institute, LLC

Jackson, Tennessee, 38305, United States

Location

8401115 - The University of Texas Medical School at Houston

Houston, Texas, 77030, United States

Location

0320083 - Hospital Italiano de Buenos Aires

Ciudad Autónoma Buenos Aires, Buenos Aires, C1181ACH, Argentina

Location

0320084 - DIM Clinica Privada

Buenos Aires, B1704ETD, Argentina

Location

0320081 - Fundacion Respirar

Buenos Aires, C1426ABP, Argentina

Location

0320077 - Centro Medico Privado de Reumatolgia

San Miguel de Tucumán, T4000, Argentina

Location

0560050 - Ghent Universit Hospital (UZ Gent)

Ghent, 9000, Belgium

Location

0560048 - Universitair Ziekenhuis (UZ) Leuven

Leuven, 3000, Belgium

Location

0560056 - Universitair Ziekenhuis Leuven

Leuven, 3000, Belgium

Location

0560049 - CHU de Liège - Sart Tilman

Liège, 4000, Belgium

Location

2500146 - CHU De Dijon Hopital Du Bocage

Dijon, 21079, France

Location

2500188 - Centre Hospitalier Regional Universitaire de Lille

Lille, 59037, France

Location

2500133 - CHU - Hospital de la Timone

Marseille, 13385, France

Location

2500135 - CHU Nice-Hopital Archet I

Nice, 06202, France

Location

2500132 - Hopital Pitie-Salpetriere

Paris, 75013, France

Location

2500144 - Hopitaux Universitaire de Strasbourg

Strasbourg, 67098, France

Location

2760203 - Charité

Berlin, 10117, Germany

Location

2760211 - Charité - Universitätsmedizin Berlin

Berlin, 10117, Germany

Location

2760199 - University Hospital Köln

Cologne, 50937, Germany

Location

2760271 - Universitatsklinikum Carl Gustav Carus TU Dresden

Dresden, 01307, Germany

Location

2760273 - Hautklinik des Uni-Klinikums Erlangen

Erlangen, 91504, Germany

Location

2760036 - University Medicine Göttingen

Göttingen, 37075, Germany

Location

2760201 - Medizinische Hochschule Hannover (MHH)

Hanover, 30625, Germany

Location

2760210 - University of Münster

Münster, 48149, Germany

Location

2760212 - University Hospital Of Tuebingen

Tübingen, 72076, Germany

Location

2760268 - University of Ulm

Ulm, 89081, Germany

Location

3480048 - University of Debrecen

Debrecen, 4032, Hungary

Location

3800133 - Universita degli Studi Di Brescia - Azienda Ospedaliera Spedali Civili di Brescia

Brescia, 25123, Italy

Location

3800132 - Universitaria Vittorio Emanuele

Catania, 95124, Italy

Location

3800139 - Universita degli Studi Firenze

Florence, 50134, Italy

Location

3800134 - Azienda Ospedaliero Universitaria Pisana

Pisa, 56124, Italy

Location

3920096 - Chukyo Hospital

Nagoya, Aichi-ken, 457-8510, Japan

Location

3920090 - University Of Fukui Hospital

Yoshida-Gun, Fukui, 910-1193, Japan

Location

3920088 - Gunma University Hospital

Maebashi, Gunma, 371-6511, Japan

Location

3920089 - Hokkaido University Hospital

Sapporo, Hokkaido, 060-8648, Japan

Location

3920086 - St. Marianna University Hospital

Kawasaki, Kanagawa, 216-8511, Japan

Location

3920125 - Tokyo Medical And Dental University Medical Hospital

Bunkyo, Tokyo, 113-8519, Japan

Location

3920091 - Nippon Medical School Hospital

Bunkyō-Ku, Tokyo, 113-8603, Japan

Location

3920097 - Tokyo Women's Medical University Hospital

Shinjuku-Ku, Tokyo, 162-8666, Japan

Location

3920087 - Wakayama Medical University Hospital

Wakayama, 641-8509, Japan

Location

3920035 - Yamaguchi University Hospital

Yamaguchi, 755-8505, Japan

Location

4840081 - Centro Integral en Reumatologia, SA de CV

Guadalajara, Jalisco, 44160, Mexico

Location

4840082 - CINTRE, Centro de Investigacion y Tratamiento Reumatologico S.C.

Mexico City, Mexico City, 11850, Mexico

Location

4840084 - Centro de Alta Especialidad en Reumatologia e Investigacion del Potosí, S.C.

San Luis Potosí City, 78213, Mexico

Location

6160104 - Zespol Poradni Specjalistycznych REUMED, ONYKSOWA Filia nr 2

Lublin, 20-582, Poland

Location

6160117 - MedicalConcierge Centrum Medyczne

Warsaw, 02-798, Poland

Location

6430124 - ORIS Firm Limited Liability Company

Moscow, 117321, Russia

Location

6430122 - City Clinical Hospital No. 5

Nizhny Novgorod, 603005, Russia

Location

6430125 - Medical Centre-Healthy Family

Novosibirsk, 630099, Russia

Location

6430120 - St. Petersburg City Rheumatological Hospital 25

Saint Petersburg, 190068, Russia

Location

6430123 - Yaroslavl Oblast Clinical Hospital

Yaroslavl, 150007, Russia

Location

7240086 - Complejo Hospitalario Universitario A Coruña

A Coruña, 15006, Spain

Location

7240011 - Hospital Universitario Valle de Hebron

Barcelona, 08035, Spain

Location

7240112 - Hospital Clinic Barcelona

Barcelona, 08036, Spain

Location

7560033 - University Hospital Bern Inselspital

Bern, 3010, Switzerland

Location

7560028 - Kantonsspital St. Gallen

Sankt Gallen, 9007, Switzerland

Location

8040053 - Cherkassy Regional Hospital

Cherkasy, 18009, Ukraine

Location

8040055 - Mechnikov Institute of Microbiology and Immunology

Kharkiv, 61029, Ukraine

Location

8040057 - Khmelnitskiy Regional Hospital

Khmelnytskyi, 29000, Ukraine

Location

8040058 - State Institution National Scientific Center Strazhesko

Kiev, 03151, Ukraine

Location

8040052 - Institute of Rheumatology

Kyiv, 02081, Ukraine

Location

8040051 - Kyiv Railway Clinical Hospital No.2

Kyiv, 03049, Ukraine

Location

8040054 - Modern Clinic LLC

Zaporizhia, 69005, Ukraine

Location

MeSH Terms

Conditions

Dermatomyositis

Interventions

gamma-GlobulinsHizentra

Condition Hierarchy (Ancestors)

PolymyositisMyositisMuscular DiseasesMusculoskeletal DiseasesNeuromuscular DiseasesNervous System DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesSkin Diseases

Intervention Hierarchy (Ancestors)

ImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Limitations and Caveats

A Good Clinical Practice (GCP) breach was identified and reported to regulatory authorities regarding insufficient safety information provided by one site for one Suspected Unexpected Serious Adverse Reaction (SUSAR) and one Adverse Event of Special Interest (AESI). The sponsor made repeated requests to obtain verification of the data, which the site did not provide. This limitation may have impacted the completeness of safety data characterization for these specific events.

Results Point of Contact

Title
Study Director
Organization
CSL Behring

Study Officials

  • Study Director

    CSL Behring

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 1, 2019

First Posted

August 5, 2019

Study Start

October 21, 2019

Primary Completion

December 2, 2024

Study Completion

December 2, 2024

Last Updated

December 9, 2025

Results First Posted

December 9, 2025

Record last verified: 2025-11

Data Sharing

IPD Sharing
Will share

CSL will consider requests to share Individual Patient Data (IPD) from systematic review groups or bona-fide researchers. For information on the process and requirements for submitting a voluntary data sharing request for IPD, please contact CSL at clinicaltrials@cslbehring.com. Applicable country specific privacy and other laws and regulations will be considered and may prevent sharing of IPD. If the request is approved and the researcher has executed an appropriate data sharing agreement, IPD that has been appropriately anonymized will be available.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
IPD requests may be submitted to CSL no earlier than 12 months after publication of the results of this study via an article made available on a public website.
Access Criteria
Requests may only be made by systematic review groups or bona-fide researchers whose proposed use of the IPD is non-commercial in nature and has been approved by an internal review committee. An IPD request will not be considered by CSL unless the proposed research question seeks to answer a significant and unknown medical science or patient care question as determined by CSL's internal review committee. The requesting party must execute an appropriate data sharing agreement before IPD will be made available.

Locations