NCT03981900

Brief Summary

Regarding Tofacitinib, newly introduced on the market, few data on drug retention and no data on the factors predictive of Tofacitinib drug survival in patients with RA are available. Therefore, the primary objective of the DeFacTo study will be to identify the factors predictive of Tofacitinib drug survival in patients with RA. As secondary objectives, the impact of behavioural strategies on drug survival and other clinical parameters as well as Tofacitinib effectiveness and tolerability will be studied under real-life conditions of use in French patients with RA.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
314

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jan 2019

Longer than P75 for all trials

Geographic Reach
1 country

66 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 4, 2019

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

June 7, 2019

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 11, 2019

Completed
3.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 6, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 6, 2023

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

October 1, 2024

Completed
Last Updated

October 1, 2024

Status Verified

June 1, 2024

Enrollment Period

4.1 years

First QC Date

June 7, 2019

Results QC Date

June 5, 2024

Last Update Submit

June 5, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Duration of Tofacitinib Drug Survival

    The duration of tofacitinib drug survival was calculated as: date of permanent drug discontinuation minus date of first taking the drug + 1. If a participant did not present with the event of interest, that is they did not have a permanent drug discontinuation record during the study, then they were censored at the time of their last visit. Kaplan-Meier method was used for estimation.

    Date of initiation of study drug treatment up to date of permanent drug discontinuation or date of censoring (up to a maximum of 48 months)

Secondary Outcomes (23)

  • Change From Baseline in Total Pain Catastrophising Scale (PCS) Score at Month 1, 3, 6, 12, 18 and 24

    Baseline, Month 1, 3, 6, 12, 18 and 24

  • Change From Baseline in Coping Strategies Questionnaire (CSQ) Score at Month 1, 3, 6, 12, 18 and 24

    Baseline, Month 1, 3, 6 12, 18 and 24

  • Percentage of Participants With Low Disease Activity (LDA) According to Disease Activity Index 28 (DAS28)-4 Erythrocyte Sedimentation Rate (ESR) (<=3.2)

    Baseline, Month 1, 3, 6, 12 18, and 24

  • Percentage of Participants With LDA According to DAS28-4 C Reactive Protein (CRP) (<=3.2)

    Baseline, Month 1, 3, 6, 12 18, and 24

  • Percentage of Participants With LDA According to Simplified Disease Activity Index (SDAI) <=11

    Baseline, Month 1, 3, 6, 12 18, and 24

  • +18 more secondary outcomes

Study Arms (1)

Rheumatoid arthritis

All participants with a diagnosis of moderate to severe active rheumatoid arthritis and treated with Tofacitinib

Drug: Tofacitinib

Interventions

5 mg BID, oral administrtaion

Also known as: Xeljanz
Rheumatoid arthritis

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodProbability Sample
Study Population

Patients with a diagnosis of moderate to severe active rheumatoid arthritis for whom the rheumatologist has decided to initiate a treatment with Tofacitinib

You may qualify if:

  • Patient 18 years of age or older
  • Patient in whom the diagnosis of moderate to severe active rheumatoid arthritis has been confirmed by a rheumatologist
  • Patient for whom the rheumatologist decides to initiate treatment with Tofacitinib
  • Patient informed of the study

You may not qualify if:

  • Patient participating in a randomised clinical trial.
  • Patient presenting with a contraindication to prescription of Tofacitinib
  • Patients who are investigational site staff members or patients who are Pfizer employees directly involved in the conduct of the trial.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (66)

Centre Hospitalier D'arras

Arras, 62022, France

Location

Hopital Robert Ballanger

Aulnay-sous-Bois, 93602, France

Location

Cabinet Medical

Aurillac, 15000, France

Location

Centre Hospitalier D Auxerre

Auxerre, 89011, France

Location

Institut Calot Helio Marin

Berck, 62600, France

Location

hopital Avicenne

Bobigny, 93009, France

Location

Centre Hospitalier de Fleyriat

Bourg-en-Bresse, 01012, France

Location

Hopital Jacques Cœur

Bourges, 18020, France

Location

Cabinet Medical

Brest, 29200, France

Location

Cabinet Medical

Brive-la-Gaillarde, 19100, France

Location

Cabinet Medical

Bruges, 33520, France

Location

Centre Hospitalier Jean Rougier

Cahors, 46005, France

Location

Infirmerie Protestante de Lyon

Caluire-et-Cuire, 69641, France

Location

Hopital Pierre Nouveau

Cannes, 06414, France

Location

Centre Hospitalier de Carcassonne

Carcassonne, 11010, France

Location

Hopital Gabriel Montpied

Clermont-Ferrand, 63003, France

Location

Centre Hospitalier de Compiegne

Compiègne, 60321, France

Location

Hopital Henri Mondor

Créteil, 94010, France

Location

Hopital Victor Jousselin

Dreux, 28102, France

Location

Centre Hospitalier des Deux Vallees Juvisy

Juvisy-sur-Orge, 91265, France

Location

Cabinet Medical

La Battie Vieille, 05000, France

Location

Cabinet Medical

La Moutonne, 83260, France

Location

Centre Hospitalier Departemental Vendee Les Oudairies

La Roche-sur-Yon, 85925, France

Location

Hopital Suburbain Du Bouscat

Le Bouscat, 33110, France

Location

Hopital Suburbain

Le Bouscat, 33491, France

Location

Centre Hospitalier Universitaire de Lille - Hopital B Roger Salengro

Lille, 59037, France

Location

Hopital B Roger Salengro-chu De Lille

Lille, 59037, France

Location

Hopital Dupuytren

Limoges, 87042, France

Location

Cabinet Medical

Limoges, 87100, France

Location

Clinique de La Sauvegarde / Cabinet Le Trait D Union

Lyon, 69009, France

Location

Clinique de la Sauvegarde

Lyon, 69337, France

Location

Clinique du Pont de Chaume

Montauban, 82000, France

Location

Centre Hospitalier de Montauban

Montauban, 82013, France

Location

Centre Hospitalier Montceau Les Mines-Hopital Jean Bouveri

Montceau-les-Mines, 71307, France

Location

Hopital Jacques Monod

Montivilliers, 76290, France

Location

Cabinet Medical

Montpellier, 34000, France

Location

Cabinet Medical Saint Roch

Montpellier, 34070, France

Location

Clinique Beau Soleil

Montpellier, 34070, France

Location

Hopital Lapeyronie

Montpellier, 34295, France

Location

Hopital Caremeau

Nîmes, 30029, France

Location

Centre Hospitalier Orleans-Hopital La Source

Orléans, 45067, France

Location

Cabinet Medical

Paris, 75008, France

Location

Centre Hospitalier Pitie Salpetriere

Paris, 75651, France

Location

Hopital Cochin

Paris, 75679, France

Location

Hopital Bichat Claude Bernard

Paris, 75877, France

Location

Centre Hospitalier de Perigueux

Périgueux, 24019, France

Location

Hospices Civils de Lyon - Hopital Lyon Sud- Hematologie

Pierre-Bénite, 69495, France

Location

Cabinet Medical

Poitiers, 86000, France

Location

Centre Hospitalier La Miletrie

Poitiers, 86021, France

Location

Centre Hospitalier Annecy Genevois Site Annecy

Pringy, 74374, France

Location

Hopital Charles Nicolle

Rouen, 76031, France

Location

Cabinet Medical

Saint-Lô, 50000, France

Location

Hopital Inter-armees Begin

Saint-Mandé, 94163, France

Location

Centre Hospitalier Universitaire Saint Pierre

Saint-Pierre, 97410, France

Location

Centre Hospitalier Universitaire Saint Etienne Hopital Nord

Saint-Priest-en-Jarez, 42277, France

Location

Hopital Nord

Saint-Priest-en-Jarez, 42277, France

Location

Centre Hospitalier de Bigorre Site La Gespe

Tarbes, 65013, France

Location

Clinique Medipole Garonne

Toulouse, 31036, France

Location

Hopital Purpan

Toulouse, 31059, France

Location

Cabinet Medical

Toulouse, 31400, France

Location

Cabinet de Rhumatologie

Tours, 37000, France

Location

Cabinet Medical

Tours, 37000, France

Location

Hopital des Hauts Clos

Troyes, 10003, France

Location

Cabinet Medical

Valenciennes, 59322, France

Location

Hopital Psv

Villeneuve-sur-Lot, 47305, France

Location

Cabinet Medical

Vincennes, 94300, France

Location

Related Links

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

tofacitinib

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Pfizer Inc.
Organization
Pfizer ClinicalTrials.gov Call Center

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 7, 2019

First Posted

June 11, 2019

Study Start

January 4, 2019

Primary Completion

February 6, 2023

Study Completion

February 6, 2023

Last Updated

October 1, 2024

Results First Posted

October 1, 2024

Record last verified: 2024-06

Data Sharing

IPD Sharing
Will not share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

Locations