NCT03975894

Brief Summary

Sickle Cell Disease (SCD) is a serious inherited blood disorder affecting red blood cells. When oxygen levels drop the red cells become abnormally shaped and unable to move through the blood vessels easily. Blood and oxygen do not reach body organs, resulting in episodes of severe pain and other complications. Pregnant women with SCD have an increased risk of both sickle and pregnancy complications, including raised blood pressure. Their babies may grow more slowly in the womb, are more likely to be born early and need special care, and have a higher risk of dying. The only treatments currently available for women with SCD are Hydroxycarbamide (which cannot be used during pregnancy) and blood transfusion. Currently, blood transfusion is only used during pregnancy to treat emergency complications. It has been suggested that giving blood transfusions throughout pregnancy could improve outcomes for both mother and babies. In Serial Prophylactic Exchange Blood Transfusion (SPEBT), sickle blood is mechanically removed and simultaneously replaced with donor red cells. A trial is needed to assess SPEBT given every 6-10 weeks, starting before 18 weeks of pregnancy, compared to standard care. This trial will evaluate outcomes for women (e.g. hospital admission, frequency of crisis) and their infants (e.g. early delivery, birthweight). However, the feasibility of such a study needs to be assessed before embarking on a large multicentre trial. This study is therefore a feasibility study in which we will randomly allocate participants to have either SPEBT or standard care. The study will be carried out in multiple maternity units in England and last two years. The willingness of eligible women to join the study will be assessed, along with how many participants remain part of the study until the end and if participants find the intervention acceptable.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
50

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started May 2019

Geographic Reach
1 country

6 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 2, 2019

Completed
15 days until next milestone

First Submitted

Initial submission to the registry

May 17, 2019

Completed
19 days until next milestone

First Posted

Study publicly available on registry

June 5, 2019

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2020

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2021

Completed
Last Updated

August 2, 2019

Status Verified

June 1, 2019

Enrollment Period

1.6 years

First QC Date

May 17, 2019

Last Update Submit

August 1, 2019

Conditions

Keywords

pregnancyexchange transfusionperinatal complications

Outcome Measures

Primary Outcomes (1)

  • Recruitment rate

    ratio of women eligible:women randomised

    Baseline

Secondary Outcomes (13)

  • Feasibility endpoints

    up to 6 weeks postpartum

  • Maternal hospital admissions

    Every 6-8 weeks from enrolment to 6 weeks postpartum

  • Frequency and severity of painful crisis

    Every 6-8 weeks from enrolment to 6 weeks postpartum

  • Mode of birth

    40 weeks

  • SCD-related complications

    Every 6-8 weeks from enrolment to 6 weeks postpartum

  • +8 more secondary outcomes

Study Arms (2)

Intervention

EXPERIMENTAL

Regular prophylactic blood transfusion given every 6-10 weeks during pregnancy to maintain a HbS% of \<30%.

Biological: Serial prophylactic exchange blood transfusion (SPEBT).

Control

NO INTERVENTION

Symptom directed blood transfusion during pregnancy.

Interventions

Serial prophylactic exchange blood transfusion (SPEBT) will be given via automated apheresis technology. SPEBT will be carried out on the haematology day unit or on the antenatal day unit/ward in accordance with local policies in participating units. The procedure will be carried out using standard operating procedures, by the clinical or research nurse/midwife, haematology day unit staff or specialist sickle nursing staff. Venous access will be via peripheral access if possible or by femoral line access if not. SPEBT will be commenced between 6 and 18+0 weeks gestation. It will be repeated at 6-10 weekly intervals aiming to maintain HbS% \<30%. It will continue throughout pregnancy and be stopped at the end of pregnancy. Number of red cell units used per transfusion will depend on patient weight and pre-transfusion HbS%, but will usually be between 6 and 8 units of red cells on each occasion of exchange transfusion.

Intervention

Eligibility Criteria

Age18 Years+
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Pregnant women with sickle cell disease (all genotypes)
  • Gestation 18+0 weeks or below
  • Willing and able to give informed consent
  • Singleton pregnancy

You may not qualify if:

  • On long term transfusion programme prior to pregnancy for amelioration of SCD
  • Prior Hyperhaemolysis
  • Red cell phenotype or antibodies present prevent likely provision of adequate red cell units to support elective EBT programme
  • Unable to receive blood transfusion for social, religious or clinical reasons
  • Current diagnosis of major medical or psychiatric comorbidity which in the randomising clinicians opinion renders them unable to enter trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

Barts Health NHS Trust

London, United Kingdom

NOT YET RECRUITING

Guy's and St Thomas' NHS Foundation Trust

London, United Kingdom

RECRUITING

King's College Hospital

London, United Kingdom

NOT YET RECRUITING

St George's University Hospitals NHS Foundation Trust

London, United Kingdom

NOT YET RECRUITING

Whittington Health NHS Trust

London, United Kingdom

NOT YET RECRUITING

Manchester University NHS Foundation Trust

Manchester, United Kingdom

NOT YET RECRUITING

Related Publications (2)

  • Oteng-Ntim E, Oakley LL, Robinson V, Brien S, Joseph J, Sharif J, McCabe L, Thompson H, Awogbade M, Johns J, Brunetta DM, Seed PT. Prophylactic exchange transfusion in sickle cell disease pregnancy: a TAPS2 feasibility randomized controlled trial. Blood Adv. 2024 Aug 27;8(16):4359-4369. doi: 10.1182/bloodadvances.2024012923.

  • Oakley LL, Awogbade M, Brien S, Briley A, Chorozoglou M, Drasar E, Johns J, Rhodes E, Robinson V, Seed P, Sharif J, Singh C, Telfer P, Thompson H, Watt-Coote I, Howard J, Oteng-Ntim E. Serial prophylactic exchange blood transfusion in pregnant women with sickle cell disease (TAPS-2): study protocol for a randomised controlled feasibility trial. Trials. 2020 Apr 20;21(1):347. doi: 10.1186/s13063-020-4212-8.

MeSH Terms

Conditions

Anemia, Sickle CellTransfusion Reaction

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesImmune System Diseases

Study Officials

  • Eugene Oteng-Ntim

    Guy's and St Thomas' NHS Foundation Trust

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Regular prophylactic blood transfusion given every 6-10 weeks during pregnancy to maintain a HbS% of \<30%
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 17, 2019

First Posted

June 5, 2019

Study Start

May 2, 2019

Primary Completion

December 1, 2020

Study Completion

May 1, 2021

Last Updated

August 2, 2019

Record last verified: 2019-06

Locations