NCT03972280

Brief Summary

Study CSL324\_1002 will investigate the safety and pharmacokinetics of repeat doses of CSL324 in subjects with hidradenitis suppurativa and palmoplantar pustulosis. CSL324 is a novel, recombinant therapy that may treat diseases caused by increased numbers of neutrophils at sites of inflammation.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
39

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Jul 2019

Typical duration for phase_1

Geographic Reach
3 countries

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 31, 2019

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 3, 2019

Completed
1 month until next milestone

Study Start

First participant enrolled

July 4, 2019

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 4, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 4, 2022

Completed
Last Updated

May 26, 2023

Status Verified

May 1, 2023

Enrollment Period

3.3 years

First QC Date

May 31, 2019

Last Update Submit

May 25, 2023

Conditions

Outcome Measures

Primary Outcomes (7)

  • Incidence of treatment-emergent adverse events (TEAEs)

    Up to 24 weeks

  • TEAEs by severity

    Up to 24 weeks

  • TEAEs by casuality

    Up to 24 weeks

  • Incidence of adverse events of special interest (AESIs): Grade 3 and 4 neutropenia

    Up to 24 weeks

  • AESIs: Grade 3 and 4 neutropenia by causality

    Up to 24 weeks

  • Incidence of AESIs: Grade 3 and 4 infection

    Up to 24 weeks

  • AESIs: Grade 3 and 4 infection by causality

    Up to 24 weeks

Secondary Outcomes (12)

  • Maximum concentration (Cmax) of CSL324 in serum for the first dose administered

    Up to 22 days after dose

  • Time to maximum concentration (Tmax) of CSL324 in serum for the first dose administered

    Up to 22 days after dose

  • Area under the concentration-time curve during a dosing interval (AUCtau) of CSL324 in serum for the first dose administered

    Up to 22 days after dose

  • Cmax of CSL324 in serum for the last dose administered

    Up to 22 days after dose

  • Tmax of CSL324 in serum for the last dose administered

    Up to 84 days after dose

  • +7 more secondary outcomes

Study Arms (6)

Dose Level 1 (HS)

EXPERIMENTAL

Dose 1 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with HS

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Dose Level 1 (PPP)

EXPERIMENTAL

Dose 1 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with PPP

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Dose Level 1 (Total)

EXPERIMENTAL

Dose 1 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with HS or PPP

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Dose Level 2 (HS)

EXPERIMENTAL

Dose 2 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with HS

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Dose Level 2 (PPP)

EXPERIMENTAL

Dose 2 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with PPP

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Dose Level 2 (Total)

EXPERIMENTAL

Dose 2 of recombinant anti-G-CSF receptor monoclonal antibody administered intravenously to subjects with HS or PPP

Biological: Recombinant anti-granulocyte colony-stimulating factor (G-CSF) receptor monoclonal antibody

Interventions

Recombinant anti-G-CSF receptor monoclonal antibody is a preservative-free, sterile liquid formulation that is suitable for intravenous infusion

Also known as: CSL324
Dose Level 1 (HS)Dose Level 1 (PPP)Dose Level 1 (Total)Dose Level 2 (HS)Dose Level 2 (PPP)Dose Level 2 (Total)

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects between 18 and 75 years of age, inclusive
  • Confirmed clinical diagnosis of moderate to severe HS as per International Hidradenitis Suppurativa Severity Score System (IHS4) guidelines (ie, IHS4 ≥ 4)
  • PPP differentiated from other forms of pustulosis
  • Psoriasis with a Palmoplantar Pustulosis Psoriasis Area and Severity Index (ppPASI) score of ≥ 12.
  • Subjects with HS only: inadequate response to at least a 3-month (90 days) trial of oral antibiotics for treatment of HS
  • Subjects with PPP only: confirmed clinical diagnosis of PPP at least 6 months before Screening and inadequate response to topical therapy, phototherapy, and / or previous systemic therapy for the treatment of PPP

You may not qualify if:

  • Treatment with any medications and therapies not permitted during the study.
  • History of myeloproliferative disease.
  • Malignancy within 5 years at Screening with the exception of nonmelanoma skin cancer, carcinoma in situ, or prostate cancer not requiring treatment.
  • Current, or a recent clinically significant history of, uncontrolled renal, hepatic(including currently active hepatitis B virus and / or hepatitis C virus), hematologic, endocrine, pulmonary, psychiatric, or cardiac disease, assessed as potentially having an effect on study outcomes as determined by the Investigator and / or Sponsor.
  • Congenital or acquired immunosuppressive condition(s), including human immunodeficiency virus infection.
  • Clinical signs of active infection and / or fever \> 38°C during the 7 days before Day 1.
  • Clinically significant abnormalities on physical examination, ECG, or laboratory assessments, or neutropenia (defined as absolute neutrophil count \< 2.0 × 109/L) at Screening.
  • Subjects with PPP only: concurrent psoriasis vulgaris (not including scaly scalp and / or ears).
  • Subjects with HS only: \> 20 draining fistulas."

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Holdsworth House Medical Practice

Darlinghurst, 2010, Australia

Location

Fremantle Dermatology

Fremantle, 6160, Australia

Location

The Royal Melbourne Hospital

Parkville, 3052, Australia

Location

Westmead Hospital

Westmead, 2145, Australia

Location

Bispebjerg Hospital

Copenhagen, 2400, Denmark

Location

Gentofte Hospital

Hellerup, 2900, Denmark

Location

Zealand University Hospital

Roskilde, 4000, Denmark

Location

Charité - Universitätsmedizin Berlin

Berlin, 10117, Germany

Location

St. Josef Hospital

Bochum, 44791, Germany

Location

Klinikum Darmstadt

Darmstadt, 64283, Germany

Location

Universitätsklinikum Carl Gustav Carus

Dresden, 01307, Germany

Location

MeSH Terms

Conditions

Hidradenitis SuppurativaPsoriasis

Interventions

Granulocyte Colony-Stimulating Factor

Condition Hierarchy (Ancestors)

Skin Diseases, BacterialBacterial InfectionsBacterial Infections and MycosesInfectionsSkin Diseases, InfectiousSuppurationSkin DiseasesSkin and Connective Tissue DiseasesHidradenitisSweat Gland DiseasesSkin Diseases, Papulosquamous

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 31, 2019

First Posted

June 3, 2019

Study Start

July 4, 2019

Primary Completion

October 4, 2022

Study Completion

October 4, 2022

Last Updated

May 26, 2023

Record last verified: 2023-05

Data Sharing

IPD Sharing
Will share

CSL will consider requests to share Individual Patient Data (IPD) from systematic review groups or bona-fide researchers. For information on the process and requirements for submitting a voluntary data sharing request for IPD, please contact CSL at clinicaltrials@cslbehring.com. Applicable country specific privacy and other laws and regulations will be considered and may prevent sharing of IPD. If the request is approved and the researcher has executed an appropriate data sharing agreement, IPD that has been appropriately anonymized will be available.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
IPD requests may be submitted to CSL no earlier than 12 months after publication of the results of this study via an article made available on a public website.
Access Criteria
Requests may only be made by systematic review groups or bona-fide researchers whose proposed use of the IPD is non-commercial in nature and has been approved by an internal review committee. An IPD request will not be considered by CSL unless the proposed research question seeks to answer a significant and unknown medical science or patient care question as determined by CSL's internal review committee. The requesting party must execute an appropriate data sharing agreement before IPD will be made available.

Locations