NCT03918915

Brief Summary

Myopia, or nearsightedness, is the most common eye disorder, often affecting more than 40% of adults in Europe, Asia and the USA. Severe myopia is associated with an increased risk of developing other eye conditions such as glucoma, cataracts and retinal detachment, which may lead to blindness. Early treatment of myopia in children could help slow the condition and minimize the risk of complications later in life. This study investigates the use of SYD-101, an eye solution, in slowing-down the progression of myopia in children.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
852

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Apr 2019

Longer than P75 for phase_3

Geographic Reach
3 countries

47 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 12, 2019

Completed
6 days until next milestone

First Posted

Study publicly available on registry

April 18, 2019

Completed
6 days until next milestone

Study Start

First participant enrolled

April 24, 2019

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 2, 2024

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2025

Completed
Last Updated

January 15, 2026

Status Verified

January 1, 2026

Enrollment Period

5 years

First QC Date

April 12, 2019

Last Update Submit

January 12, 2026

Conditions

Keywords

ChildrenMyopia

Outcome Measures

Primary Outcomes (1)

  • Myopic progression >0.75 D (diopters)

    Proportion of participants with confirmed myopic progression \>0.75 D (diopters), based on SE (spherical equivalent) as measured by cycloplegic autorefraction

    Month 36

Secondary Outcomes (6)

  • Mean annual myopic progression

    Month 36

  • Proportion of participants with annual myopia progression rate <=0.50 D/year

    Through Month 36

  • Proportion of participants with annual myopia progression rate <=0.25 D/year

    Through Month 36

  • Proportion of participants with annual myopia progression rate > 0.50 D/year

    Month 36

  • Time to progression of myopia >0.75 D (diopters)

    Up to 36 months (from date of randomization until date myopia progresses >0.75 D)

  • +1 more secondary outcomes

Study Arms (3)

SYD-101 0.01%

EXPERIMENTAL

1 drop in each eye at bedtime. Part 1: participants will be randomized to SYD-101 0.01% Part 2: participants will be re-randomized to SYD-101 0.01% or Vehicle

Drug: SYD-101 0.01%

SYD-101 0.03%

EXPERIMENTAL

1 drop in each eye at bedtime. Part 1: participants will be randomized to SYD-101 0.03% Part 2: participants will be re-randomized to SYD-101 0.03% or Vehicle

Drug: SYD-101 0.03%

Vehicle

PLACEBO COMPARATOR

1 drop in each eye at bedtime. Part 1: participants will be randomized to Vehicle Part 2: participants will be re-randomized to SYD-101 0.03%

Drug: Vehicle

Interventions

Sterile topical ophthalmic solution

Also known as: atropine sulfate
SYD-101 0.01%

Sterile topical ophthalmic solution

Also known as: atropine sulfate
SYD-101 0.03%

Sterile topical ophthalmic solution without active ingredient

Also known as: Placebo
Vehicle

Eligibility Criteria

Age3 Years - 14 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Myopia of 0.5 D (diopters) to 6.00 D (inclusive) in both eyes.
  • Astigmatism ≤1.50 D in both eyes.
  • Anisometropia ≤1.00 D in both eyes.
  • If myopia is ≥0.75 D, participant must be wearing single vision eyeglasses or soft, daily-wear, single-vision contact lenses that meet study investigator's criteria.
  • BCVA (best-corrected visual acuity) Snellen equivalent of 20/32 or better.

You may not qualify if:

  • Participants with a history or current evidence of a medical condition predisposing them to degenerative myopia (e.g. Marfan syndrome, Stickler syndrome), or a condition that may affect visual function or development (e.g. diabetes mellitus, chromosome anomaly).
  • Current use of a monoamine oxidase inhibitor.
  • Evidence of any ocular inflammation or infection in either eye, including blepharitis, conjunctivitis, keratitis, and scleritis.
  • Past, present or future plans to use orthokeratology (orthoK), rigid gas-permeable, bifocal, progressive-addition, multi-focal, or other lenses to reduce myopia progression; or the use of atropine, pirenzepine or other anti-muscarinic agent for myopia.
  • History or evidence of ocular surgery or planned future ocular surgery in either eye.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (47)

Site 143

Irwindale, California, 91706, United States

Location

Site 144

Pasadena, California, 91105, United States

Location

Site 148

San Diego, California, 92127, United States

Location

Site 104

San Diego, California, 92131, United States

Location

Site 110

Santa Barbara, California, 93110, United States

Location

Site 133

Sunnyvale, California, 94087, United States

Location

Site 130

Colorado Springs, Colorado, 80920, United States

Location

Site 100

Fort Collins, Colorado, 80528, United States

Location

Site 102

Danbury, Connecticut, 06810, United States

Location

Site 150

Waterbury, Connecticut, 06708, United States

Location

Site 122

Fort Lauderdale, Florida, 33309, United States

Location

Site 109

Jupiter, Florida, 33477, United States

Location

Site 119

Sweetwater, Florida, 33182, United States

Location

Site 120

Tamarac, Florida, 33321, United States

Location

Site 124

Marietta, Georgia, 30060, United States

Location

Site 116

Chicago, Illinois, 60616, United States

Location

Site 106

Wilmette, Illinois, 60091, United States

Location

Site 135

Indianapolis, Indiana, 46202, United States

Location

Site 131

Munster, Indiana, 46321, United States

Location

Site 137

Pittsburg, Kansas, 66762, United States

Location

Site 138

Bangor, Maine, 04401, United States

Location

Site 123

Boston, Massachusetts, 02111, United States

Location

Site 114

Washington, Missouri, 63090, United States

Location

Site 132

Henderson, Nevada, 89052, United States

Location

Site 139

Albuquerque, New Mexico, 87109, United States

Location

Site 127

Buffalo, New York, 14209, United States

Location

Site 117

Chapel Hill, North Carolina, 27517, United States

Location

Site 121

Raleigh, North Carolina, 27603, United States

Location

Site 105

Fargo, North Dakota, 58103, United States

Location

Site 111

Medford, Oregon, 97504, United States

Location

Site 147

Tigard, Oregon, 97223, United States

Location

Sie 136

Bala-Cynwyd, Pennsylvania, 19004-1108, United States

Location

Site 128

Cranberry Township, Pennsylvania, 16066, United States

Location

Site 108

Charleston, South Carolina, 29425, United States

Location

Site 126

Lakeway, Texas, 78734, United States

Location

Site 142

San Antonio, Texas, 78215, United States

Location

Site 101

San Antonio, Texas, 78240, United States

Location

Site 115

The Woodlands, Texas, 77380, United States

Location

Site 149

Ogden, Utah, 84403, United States

Location

Site 140

Ogden, Utah, 84405, United States

Location

Site 113

Virginia Beach, Virginia, 23452, United States

Location

Site 204

Graz, Styria, 8036, Austria

Location

Site 203

Linz, Upper Austria, 4021, Austria

Location

Site 205

Vienna, 1140, Austria

Location

Site 202

Bratislava, 833 40, Slovakia

Location

Site 201

Trebišov, 075 01, Slovakia

Location

Site 200

Trenčín, 91108, Slovakia

Location

Related Publications (3)

  • Johnson P, Widder K, Cheetham J, Kirkeby L. Methods and baseline of a large, multicenter, phase 3 study with low-dose atropine (SYD-101) for the treatment of myopia progression in over 800 children (STAR Study). Invest Ophthalmol Vis Sci. 2025; 66(8), 2825

    BACKGROUND
  • Cheetham JK, Gieschen L, Kirkeby L, Widder K, Johnson P. The natural history of myopia progression in a large diverse pediatric population. Invest Ophthalmol Vis Sci. 2025; 66(8), 2824

    BACKGROUND
  • Korenfeld M, Hurcikova M, Tatsuoka K, Tomcikova D, Cheetham J, Kacerik M; STAR Study Investigators. STudy of Atropine to Reduce (STAR) Myopia Progression in Children: 24-Month Results of a Randomized, Double-Masked, Vehicle-Controlled Trial of Atropine Sulfate 0.01% and 0.03. Ophthalmol Ther. 2026 Mar 23. doi: 10.1007/s40123-026-01341-0. Online ahead of print.

Related Links

MeSH Terms

Conditions

Myopia

Interventions

Atropine

Condition Hierarchy (Ancestors)

Refractive ErrorsEye Diseases

Intervention Hierarchy (Ancestors)

Atropine DerivativesTropanesAzabicyclo CompoundsAza CompoundsOrganic ChemicalsBelladonna AlkaloidsSolanaceous AlkaloidsAlkaloidsHeterocyclic CompoundsBridged Bicyclo Compounds, HeterocyclicHeterocyclic Compounds, Bridged-Ring

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 12, 2019

First Posted

April 18, 2019

Study Start

April 24, 2019

Primary Completion

May 2, 2024

Study Completion

May 1, 2025

Last Updated

January 15, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will not share

Locations