NCT03784586

Brief Summary

The aim of the study is to evaluate if the electrophysiological study (EPS) guided therapy, including the prophylactic implantation of implantable cardioverter defibrillator (ICD), in inducible patients, is able to improve survival in comparison with conventional therapy (CONV strategy) in Myotonic Dystrophy type 1 patients with conduction disorders.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
70

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Feb 2012

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2012

Completed
6.9 years until next milestone

First Submitted

Initial submission to the registry

December 17, 2018

Completed
7 days until next milestone

First Posted

Study publicly available on registry

December 24, 2018

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2022

Completed
11 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 31, 2023

Completed
Last Updated

June 18, 2021

Status Verified

June 1, 2021

Enrollment Period

10.4 years

First QC Date

December 17, 2018

Last Update Submit

June 13, 2021

Conditions

Keywords

Arrhythmiaselectrophisiological studyprimary prevention

Outcome Measures

Primary Outcomes (1)

  • Sudden Cardiac Death

    24 months

Secondary Outcomes (1)

  • All-cause mortality

    24 months

Study Arms (2)

Positive EPS - ICD

Patients with inducible sustained ventricular tachycardia or ventricular fibrillation at EPS evaluation underwent ICD implantation

Negative EPS - PMK

All non inducible patients underwent PMK implantation

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

MD1 patients with permanent pacing indication and needed of sudden cardiac death screening.

You may qualify if:

  • MD1 diagnosis genetically confirmed
  • LVEF \>35% on two-dimensional echocardiography
  • Permanent pacing indication according to the current guidelines

You may not qualify if:

  • Electrolyte imbalance
  • Thyroid disorders
  • Prior cardiac surgery
  • Prior cardiac arrest
  • Prior spontaneous sustained ventricular arrhythmias

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Vincenzo Russo

Naples, 80136, Italy

RECRUITING

MeSH Terms

Conditions

Myotonic DystrophyDeath, Sudden, CardiacArrhythmias, Cardiac

Condition Hierarchy (Ancestors)

Muscular DystrophiesMuscular Disorders, AtrophicMuscular DiseasesMusculoskeletal DiseasesMyotonic DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesNervous System DiseasesNeuromuscular DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesHeart ArrestHeart DiseasesCardiovascular DiseasesDeath, SuddenDeathPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

Vincenzo Russo, MD,PhD

CONTACT

Andrea Antonio Papa, MD

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
MD, PhD, Assistant Professor

Study Record Dates

First Submitted

December 17, 2018

First Posted

December 24, 2018

Study Start

February 1, 2012

Primary Completion

June 30, 2022

Study Completion

May 31, 2023

Last Updated

June 18, 2021

Record last verified: 2021-06

Data Sharing

IPD Sharing
Will not share

Locations