Myotonic Dystrophy 1
45
12
14
20
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 45 trials
100.0%
+13.4% vs benchmark
9%
4 trials in Phase 3/4
10%
2 of 20 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 20 completed trials
Clinical Trials (45)
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
A Clinical Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1
An Ambispective Natural History Study in Myotonic Dystrophy Patients Linking Retrospective Data Captured From the DM-Scope Registry With a Prospective 24-month Follow-up Period
Global Open-Label Extension Study of Del-desiran for the Treatment of DM1
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Chinese Multicenter Clinical Outcome Cohort Study of Myotonic Dystrophy Type 1 (C-DMCOS-DM1)
Myotonic Dystrophy - Vascular and Cognition
An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)
Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients
Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1
Study of ATX-01 in Participants With DM1
The Spanish National Registry for Myotonic Dystrophy Type 1
Global Study of Del-desiran for the Treatment of DM1
Calcium Channel Blocker in Myotonic Dystrophy Type 1
Evaluation of the Efficacy and Safety of Metformin in the Myotonic Dystrophy Type 1 (Steinert's Disease)
Study of ARO-DM1 in Subjects With Type 1 Myotonic Dystrophy
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
Venous Thromboembolism in Myotonic Dystrophy Type 1
Study of Tideglusib in Adolescent and Adult Patients With Myotonic Dystrophy
Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology