NCT03736447

Brief Summary

The purpose of this study is to determine the efficacy and safety of AR101 in peanut-allergic children aged 1 to \< 4 years.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
146

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Dec 2018

Typical duration for phase_3

Geographic Reach
4 countries

23 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 7, 2018

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 9, 2018

Completed
2 months until next milestone

Study Start

First participant enrolled

December 27, 2018

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 5, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 5, 2022

Completed
8 months until next milestone

Results Posted

Study results publicly available

March 2, 2023

Completed
Last Updated

March 2, 2023

Status Verified

February 1, 2023

Enrollment Period

3.5 years

First QC Date

November 7, 2018

Results QC Date

February 2, 2023

Last Update Submit

February 2, 2023

Conditions

Keywords

CODIT™ (characterized oral desensitization immunotherapy™)Peanut-Allergic ChildrenCPNA (Characterized Peanut Allergen)DesensitizationAR101AllergyPeanut AllergyCharacterized Peanut AllergenOral Immunotherapy

Outcome Measures

Primary Outcomes (1)

  • Percentage of Subjects Who Tolerated a Single Highest Dose of at Least 600 mg in the Exit Double-Blind, Placebo-Controlled Food Challenge (DBPCFC)

    The percentage of subjects in the ITT population who achieve desensitization as determined by tolerating specified challenge doses of peanut protein with no more than mild allergy symptoms during the exit double-blind placebo-controlled food challenge (DBPCFC).

    12 months

Secondary Outcomes (3)

  • Percentage of Subjects Who Tolerated a Single Highest Dose of at Least 1000 mg in the Exit Double-Blind, Placebo-Controlled Food Challenge (DBPCFC) [Time Frame: 12 Months]

    12 months

  • Percentage of Subjects Who Tolerated a Single Highest Dose of at Least 300 mg in the Exit Double-Blind, Placebo-Controlled Food Challenge (DBPCFC)

    12 months

  • Maximum Severity of Symptoms in Participants at Any Challenge Dose During the Exit Double-blind Placebo Controlled Food Challenge (DBPCFC)

    12 months

Study Arms (2)

AR101 powder provided in capsules & sachets

ACTIVE COMPARATOR

Study product provided as peanut protein in pull-apart capsules or sachets

Biological: AR101 powder provided in capsules & sachets

Placebo powder provided in capsules & sachets

PLACEBO COMPARATOR

Placebo formulation in pull-apart capsules or sachets containing only inactive ingredients

Biological: Placebo powder provided in capsules & sachets

Interventions

Study product formulated to contain peanut protein at different dosage strengths for use as defined in the protocol

AR101 powder provided in capsules & sachets

Study product formulated to contain only inactive ingredients for use as defined in the protocol

Placebo powder provided in capsules & sachets

Eligibility Criteria

Age1 Year - 3 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Aged 1 to \< 4 years at randomization.
  • Written informed consent from the legal guardian/parent (or both parents where required by local authorities). Provide assent where required and as appropriate per local requirements.
  • Sensitivity to peanut, defined as one of the following:
  • No known history of peanut ingestion and has serum IgE to peanut ≥ 5 kUA/L within 12 months before randomization.
  • Documented history of physician-diagnosed IgE-mediated peanut allergy that includes the onset of characteristic\* signs and symptoms of allergy within 2 hours of known oral exposure to peanut or peanut-containing food, and has a mean wheal diameter on skin prick test (SPT) to peanut of at least 3 mm greater than the negative control (diluent) or serum IgE to peanut ≥ 0.35 kUA/L, obtained within 12 months before randomization.
  • Development of age-appropriate dose-limiting allergy symptoms after consuming single doses of peanut protein \> 3 mg to ≤ 300 mg in a screening DBPCFC.
  • A palatable vehicle food to which the subject is not allergic must be available for administering study product.

You may not qualify if:

  • History of severe or life-threatening anaphylaxis anytime before the screening DBPCFC.
  • History of hemodynamically significant cardiovascular or renovascular disease, including uncontrolled or inadequately controlled hypertension.
  • History of biopsy-confirmed diagnosis of EoE; other eosinophilic GI disease; chronic, recurrent, or severe gastroesophageal reflux disease (GERD); or symptoms of dysphagia (eg, difficulty swallowing, food "getting stuck").
  • Recurrent GI symptoms considered clinically significant in the opinion of the investigator.
  • History of a mast cell disorder including mastocytosis, urticaria pigmentosa, chronic idiopathic or chronic physical urticaria beyond simple dermatographism (eg, cold urticaria, cholinergic urticaria), and hereditary or idiopathic angioedema.
  • Moderate or severe persistent asthma (criteria steps 3-6; National Heart, Lung, and Blood Institute \[NHLBI\], 2007).
  • Mild asthma (criteria steps 1-2; NHLBI, 2007) that is uncontrolled or difficult to control based on NHLBI 2007 criteria.
  • History of high-dose corticosteroid use (eg, 1-2 mg/kg prednisone or equivalent for \> 3 days) by any route of administration as defined by any of the following:
  • Steroid administered daily for \> 1 month within 1 year before screening
  • One steroid course within 6 months before screening
  • More than 2 steroid courses ≥ 1 week in duration within 1 year before screening
  • History of food protein-induced enterocolitis syndrome (FPIES) within 12 months before screening.
  • Recurrent urticaria.
  • History of failure to thrive or any other form of abnormal growth, or developmental or speech delay that precludes age-appropriate communication.
  • History of chronic disease (except mild intermittent asthma, mild persistent asthma that is controlled, atopic dermatitis, or allergic rhinitis) that is or is at significant risk of becoming unstable or requiring a change in a chronic therapeutic regimen.
  • +11 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (23)

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

Location

Sean N. Parker Center for Allergy & Asthma Reseach, LPCH at El Camino Hospital

Mountain View, California, 94040, United States

Location

Peninsula Research Associates, Inc.

Rolling Hills Estates, California, 90274, United States

Location

Allergy & Asthma Medical Group and Research Center

San Diego, California, 92123, United States

Location

Children's Center for Advanced Pediatrics Clinical Research Lab

Atlanta, Georgia, 30329, United States

Location

Atlanta Allergy & Asthma Clinic

Marietta, Georgia, 30060, United States

Location

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

Location

The John Hopkins Hospital

Baltimore, Maryland, 21287, United States

Location

University of Michigan Division of Allergy and Clinical Immunology

Ann Arbor, Michigan, 48106, United States

Location

Atlantic Research Center

Ocean City, New Jersey, 07712, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

UNC-CH School of Medicine, Pediatric Allergy, Immunology & Rheumatology, Food Allergy

Chapel Hill, North Carolina, 27599, United States

Location

Clinical Research of Charlotte

Charlotte, North Carolina, 28277, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

Jeanne de Flandre Hospital

Lille, France

Location

Charité Universitaetsmedizin Berlin

Berlin, 13353, Germany

Location

University of Frankfurt

Frankfurt am Main, 60590, Germany

Location

James Paget University Hospital

Gorleston-on-Sea, Norfolk, NR31 6LA, United Kingdom

Location

Leicester Royal Infirmary

Leicester, LE1 5WW, United Kingdom

Location

Guy's and St. Thomas' NHS Foundation Trust, Snowy Owl, First Floor, Evelina Children's Hospital

London, SEI 7EH, United Kingdom

Location

Royal Manchester Children's Hospital Central Manchester University Hospitals

Manchester, M13 9WL, United Kingdom

Location

Sheffield Children's Hospital

Sheffield, S10 2TH, United Kingdom

Location

University Hospital Southampton Foundation NHS Trust Southampton General Hospital

Southampton, SO16 6YD, United Kingdom

Location

Related Publications (1)

  • Du Toit G, Brown KR, Vereda A, Irani AM, Tilles S, Ratnayake A, Jones SM, Vickery BP. Oral Immunotherapy for Peanut Allergy in Children 1 to Less Than 4 Years of Age. NEJM Evid. 2023 Nov;2(11):EVIDoa2300145. doi: 10.1056/EVIDoa2300145. Epub 2023 Oct 23.

MeSH Terms

Conditions

Peanut HypersensitivityHypersensitivity

Interventions

Capsules

Condition Hierarchy (Ancestors)

Nut and Peanut HypersensitivityFood HypersensitivityHypersensitivity, ImmediateImmune System Diseases

Intervention Hierarchy (Ancestors)

Dosage FormsPharmaceutical Preparations

Results Point of Contact

Title
Director of Regulatory Affairs
Organization
Aimmune Therapeutics, Inc.

Study Officials

  • Director of Regulatory Affairs

    Aimmune Therapeutics

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Masking Details
Double-Blinded
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: 2:1 randomization
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 7, 2018

First Posted

November 9, 2018

Study Start

December 27, 2018

Primary Completion

July 5, 2022

Study Completion

July 5, 2022

Last Updated

March 2, 2023

Results First Posted

March 2, 2023

Record last verified: 2023-02

Locations