NCT03126227

Brief Summary

This is a multicenter, randomized, double-blind, placebo-controlled safety study of AR101 using the characterized oral desensitization immunotherapy (CODITâ„¢) regimen in peanut-allergic children.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
506

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started May 2017

Geographic Reach
2 countries

67 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 20, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 24, 2017

Completed
14 days until next milestone

Study Start

First participant enrolled

May 8, 2017

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 31, 2018

Completed
23 days until next milestone

Study Completion

Last participant's last visit for all outcomes

September 23, 2018

Completed
3.1 years until next milestone

Results Posted

Study results publicly available

November 2, 2021

Completed
Last Updated

November 2, 2021

Status Verified

October 1, 2021

Enrollment Period

1.3 years

First QC Date

April 20, 2017

Results QC Date

August 9, 2021

Last Update Submit

October 5, 2021

Conditions

Keywords

AR101Characterized Peanut AllergenCPNA (Characterized Peanut Allergen)OIT (oral immunotherapy)Peanut AllergyPeanut-Allergic ChildrenDesensitizationARC007Characterized Oral Desensitization Immunotherapy (CODITâ„¢)

Outcome Measures

Primary Outcomes (1)

  • Frequency of Treatment Emergent Adverse Events, Including Serious Adverse Events

    Frequency of Treatment Emergent Adverse Events, including Serious Adverse Events, during the overall study period. Treatment-emergent adverse events were defined as adverse events with onset after the first dose of study product.

    Approximately 6 months

Secondary Outcomes (10)

  • Frequency of Premature Discontinuation of Dosing Due to Adverse Events

    Approximately 6 months

  • Frequency of Premature Discontinuation of Dosing Due to Chronic/Recurrent Gastrointestinal Adverse Events

    Approximately 6 months

  • Proportion of Chronic/Recurrent Gastrointestinal Adverse Events Resolving <2, Between 2-4, Between 4-12, and ≥ 12 Weeks Following Discontinuation of Dosing

    Approximately 6 months

  • Frequency of Allergic Hypersensitivity Adverse Events Normalized for Duration of Treatment

    Approximately 6 months

  • Frequency of Anaphylaxis as Defined in the Protocol

    Approximately 6 months

  • +5 more secondary outcomes

Study Arms (2)

AR101 Powder Provided in Capsules

ACTIVE COMPARATOR

Study product formulated to contain peanut protein at different dosage strengths for use as defined in the protocol

Biological: AR101

Placebo powder

PLACEBO COMPARATOR

Placebo formulation in pull-apart capsules containing only excipients color-matched to AR101 study product.

Biological: Placebo

Interventions

AR101BIOLOGICAL

AR101 powder provided in capsules

AR101 Powder Provided in Capsules
PlaceboBIOLOGICAL

Placebo powder provided in capsules

Placebo powder

Eligibility Criteria

Age4 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Ages 4 to 17 years, inclusive
  • History of physician-diagnosed peanut allergy that includes allergic signs and symptoms within two hours of known oral exposure to peanut
  • Mean peanut wheal diameter on SPT of at least 8mm and elevated psIgE of at least 14 kUA/L at screening
  • Written informed consent from the subject's parent/guardian
  • Written assent from the subject as appropriate (per local regulatory requirements)
  • Use of effective birth control by sexually active female subjects of childbearing potential

You may not qualify if:

  • Subjects in whom the clinical diagnosis of peanut allergy is uncertain
  • Severe or uncontrolled asthma
  • History of cardiovascular disease, including uncontrolled or inadequately controlled hypertension
  • History of severe or life-threatening episode of anaphylaxis or anaphylactic shock within 60 days of screening
  • History of eosinophilic esophagitis (EoE), other eosinophilic gastrointestinal disease, chronic, recurrent, or severe gastroesophageal reflux disease (GERD), symptoms of dysphagia or recurrent gastrointestinal symptoms of undiagnosed etiology
  • History of a mast cell disorder, including mastocytosis, urticaria pigmentosa, chronic idiopathic or chronic physical urticaria beyond simple dermatographism (e.g., cold urticaria, cholinergic urticaria), and hereditary or idiopathic angioedema
  • Any other condition that, in the opinion of the Investigator, precludes participation for reasons of safety

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (67)

Clinical Research Center of Alabama

Birmingham, Alabama, 35209, United States

Location

Medical Research of Arizona

Scottsdale, Arizona, 85251, United States

Location

Banner University of Arizona Medical Center

Tucson, Arizona, 85724, United States

Location

Arkansas Children's Hospital

Little Rock, Arkansas, 72202, United States

Location

Jonathan Corren, M.D., Inc.

Los Angeles, California, 90025, United States

Location

Children's Hospital Los Angeles, Division of Clinical Immunology and Allergy

Los Angeles, California, 90027, United States

Location

Allergy & Asthma Associates of Southern California

Mission Viejo, California, 92691, United States

Location

Sean N. Parker Center for Allergy Research, LPCH at El Camino Hospital

Mountain View, California, 94040, United States

Location

Peninsula Research Associates, Inc.

Rolling Hills Estates, California, 90274, United States

Location

Allergy & Asthma Medical Group and Research Center, A.P.C

San Diego, California, 92123, United States

Location

Rady Children's Hospital San Diego

San Diego, California, 92123, United States

Location

University of California, San Francisco

San Francisco, California, 94158, United States

Location

Allergy & Asthma Associates of Santa Clara Valley Research Center

San Jose, California, 95117, United States

Location

UCLA Medical Center, Santa Monica

Santa Monica, California, 90404, United States

Location

Allergy and Asthma Clinical Research, Inc.

Walnut Creek, California, 94598, United States

Location

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

Location

Asthma & Allergy Associates, PC

Colorado Springs, Colorado, 80907, United States

Location

National Jewish Health

Denver, Colorado, 80206-2761, United States

Location

Colorado Allergy & Asthma Centers

Denver, Colorado, 80230, United States

Location

Children's National Health System

Washington D.C., District of Columbia, 20010, United States

Location

Sher Allergy Specialists - Center for Cough

Largo, Florida, 33778, United States

Location

Allergy Associates of the Palm Beaches

North Palm Beach, Florida, 33408, United States

Location

Sarasota Clinical Research

Sarasota, Florida, 34239, United States

Location

University of South Florida Asthma, Allergy, and Immunology Clinical Research Unit

Tampa, Florida, 33613, United States

Location

Atlanta Allergy & Asthma Clinic, PA

Marietta, Georgia, 30060, United States

Location

Idaho Allergy and Research

Eagle, Idaho, 83616, United States

Location

Ann & Robert H. Lurie's Children's Hospital of Chicago

Chicago, Illinois, 60611-2605, United States

Location

The University of Chicago Medicine, Comer Children's Hospital

Chicago, Illinois, 60637, United States

Location

Sneeze, Wheeze, & Itch Associates, LLC

Normal, Illinois, 61761, United States

Location

Deaconess Clinic Downtown

Evansville, Indiana, 47713, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

Family Allergy & Asthma Research Institute

Louisville, Kentucky, 40215, United States

Location

Chesapeake Clinical Research, Inc.

Baltimore, Maryland, 21236, United States

Location

Johns Hopkins Hospital, Pediatric Clinical Research Unit

Baltimore, Maryland, 21287, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

University of Michigan Health System / Michigan Medicine

Ann Arbor, Michigan, 48109, United States

Location

Clinical Research Institute, Inc.

Plymouth, Minnesota, 55441, United States

Location

Children's Mercy on Broadway

Kansas City, Missouri, 64111, United States

Location

Nebraska Medical Research Institute, Inc.

Bellevue, Nebraska, 68123, United States

Location

Atlantic Research Center, LLC

Ocean City, New Jersey, 07712, United States

Location

Princeton Center for Clinical Research

Skillman, New Jersey, 08558, United States

Location

Northwell Health System

Great Neck, New York, 11021, United States

Location

University of Rochester Medical Center

Rochester, New York, 14642, United States

Location

University of North Carolina at Chapel Hill, Clinical & Translational Research Center (CTRC)

Chapel Hill, North Carolina, 27599, United States

Location

National Allergy and Asthma Research, LLC

Charleston, North Carolina, 29420, United States

Location

Clinical Research of Charlotte

Charlotte, North Carolina, 28277, United States

Location

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

Location

Bernstein Clinical Research Center

Cincinnati, Ohio, 45231, United States

Location

Oklahoma Institute of Allergy and Asthma Clinical Research, LLC

Oklahoma City, Oklahoma, 73131, United States

Location

Columbia Asthma & Allergy Clinic

Clackamas, Oregon, 97015, United States

Location

Baker Allergy, Asthma and Dermatology Research Center

Portland, Oregon, 97223, United States

Location

Children's Hospital of Philadelphia: Allergy/Immunology

Philadelphia, Pennsylvania, 19104, United States

Location

Dell Children's Medical Group / Allergy, Asthma & Immunology Clinic

Austin, Texas, 78723, United States

Location

Children's Health

Dallas, Texas, 75235, United States

Location

Western Sky Medical Research

El Paso, Texas, 79903, United States

Location

Texas Children's Hospital / Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Central Texas Health Research

New Braunfels, Texas, 78130, United States

Location

Biogenics Research Institute

San Antonio, Texas, 78229, United States

Location

Sylvana Research Associates

San Antonio, Texas, 78229, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

ASTHMA Inc. Clinical Research Center

Seattle, Washington, 98115, United States

Location

Triple A Lab (Hamilton Allergy)

Hamilton, Ontario, L8S 1G5, Canada

Location

McMaster University Medical Center

Hamilton, Ontario, L8S 4K1, Canada

Location

Cheema Research Inc. (CRI)

Mississauga, Ontario, L5A 3V4, Canada

Location

Ottawa Allergy Research Corp.

Ottawa, Ontario, K1G 6C6, Canada

Location

Gordon Sussman Clinical Research

Toronto, Ontario, M4V 1R2, Canada

Location

Related Publications (1)

  • Nilsson C, Scurlock AM, Dellon ES, Brostoff JM, Pham T, Ryan R, Brown KR, Adelman DC, Aceves SS. Onset of eosinophilic esophagitis during a clinical trial program of oral immunotherapy for peanut allergy. J Allergy Clin Immunol Pract. 2021 Dec;9(12):4496-4501. doi: 10.1016/j.jaip.2021.07.048. Epub 2021 Aug 11. No abstract available.

MeSH Terms

Conditions

Peanut Hypersensitivity

Condition Hierarchy (Ancestors)

Nut and Peanut HypersensitivityFood HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Results Point of Contact

Title
Director of Regulatory Affairs
Organization
Aimmune Therapeutics, Inc.

Study Officials

  • Director of Regulatory Affairs

    Aimmune Therapeutics, Inc.

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: 2:1 randomization to AR101 or placebo
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 20, 2017

First Posted

April 24, 2017

Study Start

May 8, 2017

Primary Completion

August 31, 2018

Study Completion

September 23, 2018

Last Updated

November 2, 2021

Results First Posted

November 2, 2021

Record last verified: 2021-10

Data Sharing

IPD Sharing
Will not share

Locations