NCT03697265

Brief Summary

The objective of this phase IIb study is to evaluate the effect and safety of Sepranolone (UC1010) on premenstrual symptoms in women with Premenstrual Dysphoric Disorder (PMDD). Patients will be taking Sepranolone or Placebo (blinded to patient and study doctor) during the two weeks preceding the menstruation of three menstrual cycles. Effect (change from baseline) will be assessed by comparison of symptoms recorded daily by the patients using a validated rating scale for assessment of PMDD symptoms. Sepranolone is an endogenous steroid.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
475

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Apr 2018

Geographic Reach
4 countries

12 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 20, 2018

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

September 28, 2018

Completed
7 days until next milestone

First Posted

Study publicly available on registry

October 5, 2018

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 28, 2020

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 23, 2020

Completed
Last Updated

October 28, 2020

Status Verified

October 1, 2020

Enrollment Period

2.3 years

First QC Date

September 28, 2018

Last Update Submit

October 27, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Effect on DRSP Total symptom score

    Change in DRSP Total symptom score (Daily Record of Severity of Problems) measured during the luteal phase (i.e. the week before menstruation) before and during treatment

    Baseline luteal phase score (average from two menstrual cycles) vs. luteal phase score during treatment.

Secondary Outcomes (1)

  • Incidence of Treatment-Emergent Adverse Events

    Starting from first dose given until 1 months after treatment stop

Study Arms (3)

Sepranolone (UC1010) low dose

EXPERIMENTAL

Sepranolone (UC1010) low dose administered subcutaneously (SC) during the luteal phase

Drug: Sepranolone (UC1010) low dose

Sepranolone (UC1010) high dose

EXPERIMENTAL

Sepranolone (UC1010) high dose administered subcutaneously (SC) during the luteal phase

Drug: Sepranolone (UC1010) high dose

Placebo

PLACEBO COMPARATOR

Placebo administered subcutaneously (SC) during the luteal phase

Drug: Placebo

Interventions

Subcutaneous (SC) administration

Sepranolone (UC1010) low dose

Subcutaneous (SC) administration

Sepranolone (UC1010) high dose

Subcutaneous (SC) adminstration

Placebo

Eligibility Criteria

Age18 Years - 45 Years
Sexfemale(Gender-based eligibility)
Gender Eligibility DetailsWoman with regular menstrual cycles
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • have PMDD according to DSM-5 verified in two menstrual cycles
  • have a regular menstrual cycle of 24-35 days cycle,
  • use double barrier contraception, non-hormonal IUD, be truly sexually abstinent, or subject or her partner has been surgically sterilized,

You may not qualify if:

  • steroid hormonal treatment or treatment with psychopharmaceuticals during previous three months
  • treatments for premenstrual syndrome (PMS) or PMDD
  • history of or significant medical condition ongoing
  • be pregnant or plan a pregnancy within the study period

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

Zentrum für Klinische Forschnung

Bad Homburg, Germany

Location

Emovis

Berlin, Germany

Location

Medizentrum Essen Borbeck

Essen, Germany

Location

Klinische Forschung Karlsruhe GmbH

Karlsruhe, Germany

Location

Praxis Dr. Steinwachs

Nuremberg, Germany

Location

Centrum Kliniczno-Badawcze

Elblag, Poland

Location

Centrum Medyczne Angelius Provita

Katowice, Poland

Location

ProCreative

Krakow, Poland

Location

Karolinska University Hospital

Stockholm, 17176, Sweden

Location

Liverpool Women's NHS Foundation Trust

Liverpool, United Kingdom

Location

Imperial College London

London, United Kingdom

Location

Obstetrics and Gynaecology Keele University School of Medicine and University Hospitals of North Staffordshire

Stoke-on-Trent, ST4 6QG, United Kingdom

Location

Related Publications (1)

  • Bixo M, Ekberg K, Poromaa IS, Hirschberg AL, Jonasson AF, Andreen L, Timby E, Wulff M, Ehrenborg A, Backstrom T. Treatment of premenstrual dysphoric disorder with the GABAA receptor modulating steroid antagonist Sepranolone (UC1010)-A randomized controlled trial. Psychoneuroendocrinology. 2017 Jun;80:46-55. doi: 10.1016/j.psyneuen.2017.02.031. Epub 2017 Mar 1.

    PMID: 28319848BACKGROUND

MeSH Terms

Conditions

Premenstrual Dysphoric Disorder

Interventions

Pregnanolone

Condition Hierarchy (Ancestors)

Premenstrual SyndromeMenstruation DisturbancesPathologic ProcessesPathological Conditions, Signs and SymptomsDepressive DisorderMood DisordersMental Disorders

Intervention Hierarchy (Ancestors)

PregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Study Officials

  • Shaughn O'Brien, MD

    Obstetrics and Gynaecology Keele University School of Medicine and University Hospitals of North Staffordshire

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 28, 2018

First Posted

October 5, 2018

Study Start

April 20, 2018

Primary Completion

July 28, 2020

Study Completion

October 23, 2020

Last Updated

October 28, 2020

Record last verified: 2020-10

Data Sharing

IPD Sharing
Will not share

Locations