NCT03689712

Brief Summary

The purpose of the phase 3, clinical study is to determine if GC4419 (avasopasem manganese) administered prior to intensity-modulated radiation therapy (IMRT) reduces the severity of radiation induced oral mucositis in patients who have been diagnosed with locally advanced, non-metastatic squamous cell carcinoma of the head and neck.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
455

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Oct 2018

Longer than P75 for phase_3

Geographic Reach
3 countries

97 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 27, 2018

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 28, 2018

Completed
5 days until next milestone

Study Start

First participant enrolled

October 3, 2018

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 13, 2021

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

April 13, 2023

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 25, 2023

Completed
Last Updated

October 24, 2023

Status Verified

October 1, 2023

Enrollment Period

2.9 years

First QC Date

September 27, 2018

Results QC Date

February 15, 2023

Last Update Submit

October 19, 2023

Conditions

Keywords

Oral MucositisSuperoxide Dismutase MimeticCisplatinIntensity-Modulated Radiation TherapyChemoradiationOMIMRTHead and Neck CancerSquamous Cell CarcinomaSCCOral CavityOropharnyxMouth Soresavasopasem mangenese

Outcome Measures

Primary Outcomes (1)

  • Cumulative Incidence of Severe Oral Mucositis

    Cumulative incidence of severe oral mucositis is defined as the proportion of subjects with any occurrence of WHO Grade 3 to 4 OM, during the Study Treatment Period. Incidence of severe OM is defined as any occurrence of WHO Grade 3 or 4 OM through the last IMRT fraction after the start of IMRT. Incidence was imputed using multiple imputation for subjects with incomplete follow-up for severe OM through 60 Gy who did not have an occurrence of severe OM before the last IMRT fraction.

    From the first IMRT fraction through the end of the study treatment period (completion of study drug administration, IMRT and chemotherapy), which is estimated to be 7 weeks.

Study Arms (2)

GC4419 (avasopasem manganese) 90 mg

EXPERIMENTAL
Drug: GC4419 90mg

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

60 minute IV infusion

Also known as: avasopasem manganese
GC4419 (avasopasem manganese) 90 mg

60 minute IV infusion

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • squamous cell carcinoma of the head and neck
  • treatment plan to receive IMRT delivered as single daily fractions of 2.0 to 2.2 Gy with a cumulative radiation dose of 60-72 Gy
  • Treatment plan to receive standard cisplatin monotherapy
  • Age 18 years or older
  • Eastern Cooperative Oncology Group (ECOG) performance status ≤ 2
  • Adequate hematologic, renal and liver function
  • Negative serum pregnancy test
  • Use of effective contraception

You may not qualify if:

  • Tumor of the lips, larynx, hypopharynx, nasopharynx, sinuses, or salivary glands
  • Metastatic disease
  • Prior radiotherapy to the region of the study cancer or adjacent anatomical
  • Prior induction chemotherapy
  • Receiving any approved or investigational anti-cancer agent other than those provided for in this study
  • Concurrent participation in another interventional clinical study
  • Inability to eat soft solid food at baseline
  • Malignant tumors other than HNC within the last 5 years
  • Active infectious disease excluding oral candidiasis
  • Presence of oral mucositis at baseline
  • Known history of HIV or active hepatitis B/C
  • Female patients who are pregnant or breastfeeding
  • Known allergies or intolerance to cisplatin and similar platinum-containing compounds
  • Requirement for concurrent treatment with nitrates or other drugs that may create a risk for a precipitous decrease in blood pressure

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (97)

Banner MD Anderson Cancer Center

Gilbert, Arizona, 85234, United States

Location

Fowler Family Center for Cancer

Jonesboro, Arkansas, 72401, United States

Location

The Oncology Institute of Hope & Innovation

Corona, California, 92882, United States

Location

Chan Soon-Shiong Institute for Medicine

Costa Mesa, California, 92627, United States

Location

Long Beach Veteran Affairs Healthcare System

Long Beach, California, 90822, United States

Location

USC Norris Cancer Center

Los Angeles, California, 90033, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Clinical Trials and Research Associates, Inc.

Montebello, California, 90640, United States

Location

Hoag Memorial Hospital Presbyterian

Newport Beach, California, 92663, United States

Location

Compassionate Cancer Care

Riverside, California, 92501, United States

Location

Sharp Clinical Oncology Research

San Diego, California, 92123, United States

Location

The Oncology Institute of Hope & Innovation

Whittier, California, 90603, United States

Location

Dignity Health Research Institute

Woodland, California, 95695, United States

Location

St. Mary's Hospital Regional Medical Center

Grand Junction, Colorado, 81501, United States

Location

Bay Pines VA HealthCare System

Bay Pines, Florida, 33744, United States

Location

Boca Raton Regional Hospital, Lynn Cancer Institute

Boca Raton, Florida, 33486, United States

Location

Mayo Clinic Florida

Jacksonville, Florida, 32224, United States

Location

Cancer Specialists of North Florida

Jacksonville, Florida, 32256, United States

Location

Lakeland Regional Cancer Center

Lakeland, Florida, 33805, United States

Location

BRCR Global

Plantation, Florida, 33322, United States

Location

Winship Cancer Institute of Emory University

Atlanta, Georgia, 30322, United States

Location

IACT Health

Columbus, Georgia, 31904, United States

Location

Northwestern University Feinberg School of Medicine

Chicago, Illinois, 60611, United States

Location

SwedishAmerican Regional Cancer Center

Rockford, Illinois, 61114, United States

Location

Parkview Research Center

Fort Wayne, Indiana, 46845, United States

Location

Goshen Center for Cancer Care

Goshen, Indiana, 46526, United States

Location

The University of Iowa Hospitals & Clinics

Iowa City, Iowa, 52242, United States

Location

Appalachian Regional Healthcare, INC.

Hazard, Kentucky, 41701, United States

Location

University of Louisville/James Graham Brown Cancer Center

Louisville, Kentucky, 40202, United States

Location

Norton Cancer Institute

Louisville, Kentucky, 40241, United States

Location

MetroWest Medical Center

Framingham, Massachusetts, 01702, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

Minneapolis VA Healthcare System

Minneapolis, Minnesota, 55417, United States

Location

Hattiesburg Clinic Hematology/Oncology

Hattiesburg, Mississippi, 39401, United States

Location

Henry Ford Allegiance Health Hematology Oncology

Jackson, Mississippi, 49201, United States

Location

Ellis Fischel Cancer Center - University of Missouri

Columbia, Missouri, 65212, United States

Location

Delbert Day Cancer Institute, Phelps County Regional Medical Center

Rolla, Missouri, 65401, United States

Location

Mosaic Life Care/Heartland Regional Medical Center

Saint Joseph, Missouri, 64507, United States

Location

Cox Medical Center

Springfield, Missouri, 65807, United States

Location

St. Vincent Frontier Cancer Center

Billings, Montana, 59102, United States

Location

Benefis Sletten Cancer institute

Great Falls, Montana, 59405, United States

Location

CHI Health St. Francis

Grand Island, Nebraska, 68803, United States

Location

Renown Regional Medical Center

Reno, Nevada, 89502, United States

Location

Exeter Hospital

Exeter, New Hampshire, 03833, United States

Location

Hunterdon Hematology Oncology, LLC

Flemington, New Jersey, 08822, United States

Location

Summit Medical Group

Florham Park, New Jersey, 07932, United States

Location

Jersey Shore University Medical Center

Neptune City, New Jersey, 07753, United States

Location

New York Oncology Hematology, P.C.

Albany, New York, 12206, United States

Location

NY Cancer and Blood Specialists

East Setauket, New York, 11733, United States

Location

New York- Presbyterian Queens/ Weill Cornell

Flushing, New York, 11355, United States

Location

Wilmot Cancer Institute - Univeristy of Rochester

Rochester, New York, 14642, United States

Location

School of Dental Medicine at East Carolina University

Greenville, North Carolina, 27834, United States

Location

Wake Forest Baptist Health

Winston-Salem, North Carolina, 27157, United States

Location

Summa Health

Akron, Ohio, 44304, United States

Location

University Hospitals Seidman Cancer Center

Cleveland, Ohio, 44106, United States

Location

The Ohio State University

Columbus, Ohio, 43210, United States

Location

Willamette Valley Cancer Institue and Research Center

Eugene, Oregon, 97401, United States

Location

VA Portland Health Care System

Portland, Oregon, 97239, United States

Location

St. Luke's Hospital Cancer Center

Easton, Pennsylvania, 18045, United States

Location

Gettysburg Cancer Center

Gettysburg, Pennsylvania, 17325, United States

Location

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, 19107, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Anmed Health Cancer Center

Anderson, South Carolina, 29621, United States

Location

Charleston Cancer Center

Charleston, South Carolina, 29406, United States

Location

St. Francis Cancer Center

Greenville, South Carolina, 29607, United States

Location

Spartanburg Medical Center

Spartanburg, South Carolina, 29303, United States

Location

Mountain States Health Alliance Research Dept

Johnson City, Tennessee, 37604, United States

Location

Tennessee Cancer Specialists

Knoxville, Tennessee, 37909, United States

Location

University of Tennessee Medical Center

Knoxville, Tennessee, 37920, United States

Location

Texas Oncology - Beaumont Mamie McFaddin Ward Cancer Center

Beaumont, Texas, 77702, United States

Location

Texas Oncology- Dallas Presbyterian Hospital

Dallas, Texas, 75231, United States

Location

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, 75246, United States

Location

Texas Oncology - Denton South

Denton, Texas, 76210, United States

Location

Texas Oncology - El Paso Cancer Treatment Center

El Paso, Texas, 79902, United States

Location

SAMMC

Fort Sam Houston, Texas, 78234, United States

Location

Texas Oncology-McAllen

McAllen, Texas, 78503, United States

Location

Texas Oncology - McKinney

McKinney, Texas, 75071, United States

Location

Texas Oncology, Plano West

Plano, Texas, 75093, United States

Location

Baylor Scott & White- Round Rock

Round Rock, Texas, 78665, United States

Location

Texas Oncology - Sugar Land

Sugar Land, Texas, 77479, United States

Location

Texas Oncology - Waco

Waco, Texas, 76712, United States

Location

Fort Belvoir Community Hospital

Fort Belvoir, Virginia, 22060, United States

Location

Oncology and Hematology Associates of Southwest Virginia, Inc., DBA Blue Ridge Cancer Care

Roanoke, Virginia, 24014, United States

Location

Providence Regional Cancer Partnership

Everett, Washington, 98201, United States

Location

Cancer Care Northwest

Spokane, Washington, 99216, United States

Location

West Virginia University

Morgantown, West Virginia, 26506, United States

Location

BC Cancer Center - Vancouver

Vancouver, British Columbia, V574E6, Canada

Location

CIUSS de L'Est-de-I'lle de Montreal - Hopital Maisonneuve- Rosemont

Montreal, Quebec, H1T 2M4, Canada

Location

McGill University Health Center- Cedars Cancer Center

Montreal, Quebec, H4A 3J1, Canada

Location

CHU de Quebec - Universite Laval

Québec, Quebec, G1R 2J6, Canada

Location

Centre Intégré Universitaire de Santé et de Services Sociaux du Saguenay-Lac-Saint-Jean

Chicoutimi, G7H 5H6, Canada

Location

Northeast Cancer Centre of Health Sciences North

Greater Sudbury, P3E 5J1, Canada

Location

Juravinski Cancer Centre

Hamilton, L8V 5C2, Canada

Location

Centre Hospitalier Universitaire de Montreal (CHUM)

Montreal, H2X OC1, Canada

Location

Jewish General Hospital

Montreal, H3T 1E2, Canada

Location

Centre Intégré Universitaire de Santé et de Services Sociaux de la Mauricie et du Centre du Québec

Trois-Rivières, G8Z3R9, Canada

Location

Clinical Research Puerto Rico

San Juan, 00909, Puerto Rico

Location

Related Publications (5)

  • Anderson CM, Lee CM, Kelley JR, et al. ROMAN: Phase 3 trial of avasopasem manganese (GC4419) for severe oral mucositis (SOM) in patients receiving chemoradiotherapy (CRT) for locally advanced, nonmetastatic head and neck cancer (LAHNC). Journal of Clinical Oncology 2022 40:16_suppl, 6005-6005

    BACKGROUND
  • Saunders D, Lee C, Kelley J, et al. ROMAN: Phase 3 trial of avasopasem to reduce chemoradiotherapy (CRT)-related severe oral mucositis (SOM) in patients with head and neck cancer (HNC). Support Care Cancer 30 (Suppl 1), 1-207 (2022).

    BACKGROUND
  • Anderson C, Lee CM, Kelley JR, Walker GV, Dunlap NE, Bar-Ad VC, Miller DA, King VJ, Peddada AV, Ciuba DF, Vincent F, Muzyka BC, Gillespie-Twardy AL, Sonis ST, Holmlund J, Beardsley RA, Kennedy EP, Saunders D. Avasopasem manganese treatment for severe oral mucositis from chemoradiotherapy for locally advanced head and neck cancer: phase 3 randomized controlled trial (ROMAN). EClinicalMedicine. 2025 Oct 8;89:103539. doi: 10.1016/j.eclinm.2025.103539. eCollection 2025 Nov.

  • Squillace S, Salvemini D. Nitroxidative stress in pain and opioid-induced adverse effects: therapeutic opportunities. Pain. 2022 Feb 1;163(2):205-213. doi: 10.1097/j.pain.0000000000002347. No abstract available.

  • Anderson CM, Lee CM, Saunders DP, Curtis A, Dunlap N, Nangia C, Lee AS, Gordon SM, Kovoor P, Arevalo-Araujo R, Bar-Ad V, Peddada A, Colvett K, Miller D, Jain AK, Wheeler J, Blakaj D, Bonomi M, Agarwala SS, Garg M, Worden F, Holmlund J, Brill JM, Downs M, Sonis ST, Katz S, Buatti JM. Phase IIb, Randomized, Double-Blind Trial of GC4419 Versus Placebo to Reduce Severe Oral Mucositis Due to Concurrent Radiotherapy and Cisplatin For Head and Neck Cancer. J Clin Oncol. 2019 Dec 1;37(34):3256-3265. doi: 10.1200/JCO.19.01507. Epub 2019 Oct 16.

MeSH Terms

Conditions

StomatitisHead and Neck NeoplasmsCarcinoma, Squamous CellOral Ulcer

Interventions

avasopasem manganese

Condition Hierarchy (Ancestors)

Mouth DiseasesStomatognathic DiseasesNeoplasms by SiteNeoplasmsCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasms, Squamous Cell

Results Point of Contact

Title
Megan Holm
Organization
Galera Therapeutics

Study Officials

  • Gene Kennedy, MD

    Galera Therapeutics

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
SUPPORTIVE CARE
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 27, 2018

First Posted

September 28, 2018

Study Start

October 3, 2018

Primary Completion

August 13, 2021

Study Completion

August 25, 2023

Last Updated

October 24, 2023

Results First Posted

April 13, 2023

Record last verified: 2023-10

Data Sharing

IPD Sharing
Will not share

Locations