NCT03572114

Brief Summary

To generate pilot data to investigate the potential to use in vivo iron- and neuromelanin-quantification as imaging tools for the diagnostic evaluation of movement disorders with predominant dystonia / parkinsonism. To this end we are planning to compare the MR imaging neuromelanin and iron-pattern and content in midbrain, striatum and further brain structures in clinically similar entities and respective, sex- and age-matched healthy controls.

Trial Health

35
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
80

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Jul 2018

Typical duration for all trials

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 8, 2018

Completed
5 months until next milestone

First Posted

Study publicly available on registry

June 28, 2018

Completed
3 days until next milestone

Study Start

First participant enrolled

July 1, 2018

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2021

Completed
Last Updated

June 28, 2018

Status Verified

June 1, 2018

Enrollment Period

3 years

First QC Date

February 8, 2018

Last Update Submit

June 27, 2018

Conditions

Outcome Measures

Primary Outcomes (1)

  • neuromelanin content

    absolute amount of neuromelanin in midbrain, striatum and other areas of the brain

    up to 8 weeks

Secondary Outcomes (3)

  • neuromelanin association

    up to 8 weeks

  • iron association

    up to 8 weeks

  • Iron content

    up to 8 weeks

Study Arms (6)

Sporadic Dystonia

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

Familial Dystonia

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

Parkinson´s disease, juvenile

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

Neurodegeneration with brain iron acc.

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

mitochondrial disease

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

Healthy Controls

3 Tesla MRI Burke-Fahn-Marsden Dystonia Rating scale MDS-United Parkinsons Disease Rating Scale, Part III Beck Depression Inventory MoCA: Montreal Cognitive Assessment

Diagnostic Test: 3Tesla MRIBehavioral: Burke-Fahn-Marsden Dystonia Rating scaleBehavioral: MDS-United Parkinsons Disease Rating Scale, Part IIIBehavioral: Beck Depression InventoryBehavioral: MoCA: Montreal Cognitive Assessment:

Interventions

3Tesla MRIDIAGNOSTIC_TEST

1. A previously validated multi-parameter mapping protocol sensitive to neuromelanin and iron content 2. Iron mapping and micro-bleed detection: QSM (quantitative susceptibility mapping), a fully flow-compensated, susceptibility-weighted gradient-echo sequence (5 minutes). 3. 1-mm isotropic anatomical MPRAGE (magnetization-prepared rapid gradient-echo) 4. conventional FLAIR sequence

Familial DystoniaHealthy ControlsNeurodegeneration with brain iron acc.Parkinson´s disease, juvenileSporadic Dystoniamitochondrial disease

internationally standardized examination/quantification of dystonia

Familial DystoniaHealthy ControlsNeurodegeneration with brain iron acc.Parkinson´s disease, juvenileSporadic Dystoniamitochondrial disease

most recent, internationally standardized examination/quantification of bradykinesia / rigidity according to the Movement Disorder Society

Familial DystoniaHealthy ControlsNeurodegeneration with brain iron acc.Parkinson´s disease, juvenileSporadic Dystoniamitochondrial disease

internationally standardized examination to quantify traits of anxiety and depression

Familial DystoniaHealthy ControlsNeurodegeneration with brain iron acc.Parkinson´s disease, juvenileSporadic Dystoniamitochondrial disease

internationally standardized examination to quantify cognition, frequently used in studies of dystonia and parkinsonism

Familial DystoniaHealthy ControlsNeurodegeneration with brain iron acc.Parkinson´s disease, juvenileSporadic Dystoniamitochondrial disease

Eligibility Criteria

Age18 Years - 60 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64)
Sampling MethodNon-Probability Sample
Study Population

Patients from the National Hospital of Neurology, Queen Square, movement disorder outpatient clinic;

You may qualify if:

  • clinical diagnosis of parkinsonism and/or dystonia due to
  • dopa-responsive dystonia
  • sporadic or inherited/genetic dystonia
  • young-onset Parkinson's disease
  • NBIA
  • Mitochondrial disease
  • OR healthy controls
  • to 60 years of age
  • able to give informed consent

You may not qualify if:

  • Inability to tolerate 35min in an MRI machine
  • Contra-indications to 3T MRI on MRI safety grounds, such as presence of contra-indicated medical implants, as according to the established routine operating procedures for clinical MRI in the Lysholm Department of Neuroradiology at the National Hospital for Neurology and Neurosurgery.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Dystonic DisordersParkinsonian DisordersMitochondrial Diseases

Condition Hierarchy (Ancestors)

Movement DisordersCentral Nervous System DiseasesNervous System DiseasesBasal Ganglia DiseasesBrain DiseasesMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • Bhatia P Kailash, MD, DM, FRCP

    UCL, Institute of Neurology, Sobell Department

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Sebastian R Schreglmann, MD

CONTACT

Bhatia P Kailash, MD, DM, FRCP

CONTACT

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
CROSS SECTIONAL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 8, 2018

First Posted

June 28, 2018

Study Start

July 1, 2018

Primary Completion

July 1, 2021

Study Completion

July 1, 2021

Last Updated

June 28, 2018

Record last verified: 2018-06

Data Sharing

IPD Sharing
Will not share