NCT03509194

Brief Summary

The aim of this study is to validate and develop a new diagnostic and prognostic approach for assessment of liver function in children and adolescents with acute liver failure and chronic liver insufficiency. A carefully selected panel of functional and genomic tests along with diagnostic imaging and analysis of the microbiota will be performed in children and adolescents with acute liver failure and chronic liver insufficiency at Rigshospitalet. The tests will be performed in a serial manner in order to detect changes in outcomes. The study is an unblinded descriptive study, and approximately 20 patients with acute liver failure and 100 patients with chronic liver disease will be included in the project. This study will be the first of it's kind worldwide. The investigators expect the study to improve future diagnostic and prognostic accuracy and help the clinicians in identifying those patients in which the liver will regenerate itself, from those patients in which a liver transplantation will be lifesaving. Furthermore this study aims to help the clinicians in defining the optimal time for pediatric liver transplant in a narrow window of opportunity.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
120

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Dec 2017

Typical duration for all trials

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 11, 2017

Completed
6 days until next milestone

Study Start

First participant enrolled

December 17, 2017

Completed
4 months until next milestone

First Posted

Study publicly available on registry

April 26, 2018

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 17, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 17, 2020

Completed
Last Updated

April 26, 2018

Status Verified

April 1, 2018

Enrollment Period

3 years

First QC Date

December 11, 2017

Last Update Submit

April 25, 2018

Conditions

Keywords

liverchildrenliver transplantationliver cirrhosis

Outcome Measures

Primary Outcomes (1)

  • LTX free survival

    in days

    3 years

Secondary Outcomes (9)

  • HIDA

    3 years

  • ICG

    3 years

  • Cirrhosis

    3 years

  • MR

    3 years

  • fibroscan

    3 years

  • +4 more secondary outcomes

Study Arms (1)

Pediatric liver disease patients

Comparison of outcome of pediatric liver disease and prognostic functional liver test results and gene expression in liver biopsies.

Eligibility Criteria

Age1 Hour - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodNon-Probability Sample
Study Population

All cause liver disease in pediatric patients.

You may qualify if:

  • Children with Acute liver failure or children with Chronic Liver disease or Children with transplanted liver

You may not qualify if:

  • Non stable patients

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Dept of Pediatrics, Rigshospitalet

Copenhagen, 2100, Denmark

RECRUITING

MeSH Terms

Conditions

Liver DiseasesLiver Cirrhosis

Condition Hierarchy (Ancestors)

Digestive System DiseasesFibrosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Central Study Contacts

VIbeke B christensen, MD

CONTACT

Lise Borgwardt

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
MD, PhD, DmSc

Study Record Dates

First Submitted

December 11, 2017

First Posted

April 26, 2018

Study Start

December 17, 2017

Primary Completion

December 17, 2020

Study Completion

December 17, 2020

Last Updated

April 26, 2018

Record last verified: 2018-04

Locations